Clinical trials

  • plitidepsin for Viral diseases|Other specified diseases due to viruses
  • GSK5764227 for Advanced solid tumours
  • Regorafenib for Bone sarcoma | Osteosarcoma metastatic | Chondrosarcoma metastatic | Ewing sarcoma metastatic | Chordoma | CIC-rearranged sarcoma
  • ISTEM-01 (hESC-derived retinal pigment epithelium cells) for Retinitis pigmentosa|RPE-related retinal dystrophy
  • Ensartinib (X-396) for Non-small cell lung cancer
  • Acetylsalicylic acid for High risk for lung cancer|Systemic inflammatory state|Tobacco dependence
  • Allogeneic peripheral blood mononuclear cells incubated in vitro with mitomycin C for Living donor kidney transplantation | Kidney transplant
  • FLUDARABINE PHOSPHATE for Relapsed/refractory aggressive B-cell non-Hodgkin lymphoma | Diffuse large B-cell lymphoma (DLBCL) | High-grade B-cell lymphoma (HGBL) | Follicular lymphoma Grade 3B | Primary mediastinal B-cell lymphoma
  • PIRTOBRUTINIB for Richter transformation (DLBCL-type) | Chronic lymphocytic leukaemia (CLL)
  • nimotuzumab for Diffuse intrinsic pontine glioma | Brain stem glioma
  • Silymarin for Metabolic dysfunction-associated steatotic liver disease (MASLD)|Chronic liver disease
  • Autologous CD34+ haematopoietic stem and progenitor cells transduced with a lentiviral vector containing the human DCLRE1C gene for Severe combined immunodeficiency (SCID) due to biallelic DCLRE1C (Artemis) mutation