Clinical trial • Phase III • Ophthalmology

CENEGERMIN for Persistent corneal epithelial defect

Phase III trial of CENEGERMIN for Persistent corneal epithelial defect.

Overview

Trial Therapeutic Area
Ophthalmology
Trial Disease
Persistent corneal epithelial defect
Trial Stage
Phase III
Drug Modality
Peptide/protein/enzyme

Key dates

Initial CTIS Submission Date
08-01-2026
First CTIS Authorization Date
05-05-2026

Trial design

Randomised, oxervate 20 micrograms/ml eye drops, solution (active product; dose: 20 micrograms/ml) and vehicle for cenegermin drug product (placebo/control). dose schedule not specified in the ctis record. Phase III trial in Czechia, France, Germany and others.

Randomised
Yes
Comparator
OXERVATE 20 micrograms/ml eye drops, solution (active product; dose: 20 micrograms/ml) and Vehicle for cenegermin drug product (placebo/control). Dose schedule not specified in the CTIS record.
Target Sample Size
124

Eligibility

Recruits 124 No vulnerable populations selected. Participants must be able to sign the informed consent as described in the protocol (ICF). No provisions for assent of minors are provided because the study enrols adults (≥18 years)..

Pregnancy Exclusion
Contraception: a. Females of child-bearing age (defined as not surgically sterilized or post-menopausal for at least 1 year) are excluded if they meet any 1 of the following conditions: − Are known to be pregnant − Have a positive urine pregnancy test at baseline visit − Are planning to become pregnant during study period − Are breastfeeding − Are unwilling to use acceptable form of contraception until 30 days after the study treatment period is complete b. Male fertile participants (ie, not surgically sterilized by vasectomy) unwilling to use an acceptable form of contraception (male condom with spermicidal cream or jelly) until 30 days after the study treatment period is complete
Vulnerable Population
No vulnerable populations selected. Participants must be able to sign the informed consent as described in the protocol (ICF). No provisions for assent of minors are provided because the study enrols adults (≥18 years).

Inclusion criteria

  • {"criterion_text":"- Men or women aged 18 years or above"}
  • {"criterion_text":"- Participants with PCED in the study eye with the following characteristics: a. PCED ≥ 1.0 mm in greatest diameter b. PCED of at least 14 days duration, refractory to 1 or more conventional nonsurgical treatments (ocular lubricants, discontinuation of preserved drops and medications, bandage contact lens) showing no clinical resolution."}
  • {"criterion_text":"- Use of most ophthalmic medications (including glaucoma medications) indicated for ocular conditions other than PCED is permitted in the study eye, if the participant has been on a stable dose for at least 30 days and does not expect to have change in dosing regimen throughout the entire duration of the study. Please see exclusion criteria list for exceptions."}
  • {"criterion_text":"- Use of prophylactic antibiotics in the study eye is permitted if the participant is already receiving them prior to enrollment."}
  • {"criterion_text":"- Able to sign the inform consent as described in the protocol, which includes compliance with the requirements and restrictions listed in the informed consent form (ICF)."}

Exclusion criteria

  • {"criterion_text":"- Contralateral eye with vision of no light perception or anatomic absence of contralateral eye."}
  • {"criterion_text":"- Known active substance abuse or dependency, including but not limited to alcohol, illicit drugs, marijuana, or misuse of prescription medications within 30 days of randomization"}
  • {"criterion_text":"- Known or suspected ocular malignancy (e.g., ocular surface, intraocular, ocular adnexa), or presence of cancer or any other systemic disease that may affect the ability to participate in the clinical study in the opinion of the investigator including basal cell carcinoma of the head"}
  • {"criterion_text":"- Any ocular or systemic disorder that might hinder the efficacy of the study treatment or its evaluation or could be judged by the investigator to be incompatible with the study visit schedule or conduct"}
  • {"criterion_text":"- Concurrent participation in another investigational study"}
  • {"criterion_text":"- Hypersensitivity: a. Known or suspected allergy to any components of the cenegermin formulation b. Known hypersensitivity to 1 of the components of the study or procedural medications (eg, fluorescein)"}
  • {"criterion_text":"- Active ocular infection or inflammation in the study eye as follows: a. Bacterial, fungal, or protozoal infection at screening b. Active infectious stromal infiltrates or edema at screening c. Acute anterior uveitis of grade 2 or greater (SUN 2025) within 30 days of screening d. Acute intermediate uveitis or posterior uveitis within 30 days of screening e. Acute inflammation of the sclera or conjunctiva if it is not associated with the PCED"}
  • {"criterion_text":"- Corneal epithelial defect associated with stromal thinning greater than 30% (estimated on clinical slit lamp exam) or if associated with stromal infiltrate (corneal haze is acceptable), in the study eye."}
  • {"criterion_text":"- Severe eyelid disease in the study eye, such as: a. Mechanical eyelid abnormalities that have direct contact with the PCED (e.g., trichiasis, severe entropion with lid margin keratinization, etc, if in direct contact with the PCED) b. Lagophthalmos greater than 2 mm as measured in the clinic c. Existing diagnosis of nocturnal lagophthalmos or Parkinson’s disease d. Inability to fully close eyelids despite voluntary eyelid closure e. Severe ectropion with abnormal eyelid-globe congruity (e.g., the lower eyelid does not come into contact with the globe due to severe ectropion)"}
  • {"criterion_text":"- Severe end-stage ocular surface disease in the study eye, including but not limited to: a. Severe limbal stem cell deficiency, defined as involvement of more than 270 cumulative degrees or more of limbal stem cell deficiency b. Keratinization of the bulbar conjunctiva or lid margin"}
  • {"criterion_text":"- Use of the following medications and devices within the indicated time window prior to randomization: a. Local medications in study eye: − Any prior use of cenegermin − Blood-derived (autologous serum) or other ocular surface re-epithelizing agents, anesthetic use by the participant outside of the clinical exam setting, insulin, or steroids (unless associated with post-operative treatment regimen) within 7 days − Botox (botulinum toxin) injections for pharmacologic tarsorrhaphy within 90 days b. Systemic medications: − High-dose systemic corticosteroids (greater than 0.5 mg/kg/day) within 30 days − Any changes in oral medication regimen intended for the treatment of the ocular surface (eg, oral doxycycline) within 30 days, or planned changes during the study period − Systemic opioid use within 30 days − Use of any systemic investigational product, ocular investigational product in the study eye, radiation of the head or neck, or systemic chemotherapy within 90 days, or planned to occur during the study period c. Devices: − Use of contact lens (including therapeutic contact lens) within 7 days, or planned use of contact lens during the study period, in the study eye − Anticipated need for punctal occlusion in the study eye during the study period. Participants with punctal occlusion or punctal plugs inserted prior to the study are eligible for enrolment provided that the punctual occlusion is maintained throughout the study."}
  • {"criterion_text":"- Presence of acute severe systemic disease as follows: a. Any acute or active severe systemic inflammatory disease (eg, acute systemic Stevens-Johnson Syndrome, acute systemic GVHD, severe systemic Sjogren’s, mucous membrane pemphigoid) b. Presence of any systemic disease that may affect ability to participate in the clinical study according to the clinical judgment of the investigator"}
  • {"criterion_text":"- Recent surgery or amniotic membrane therapy as follows: a. Recent major surgical procedure for the treatment of PCED (eg, conjunctival flap, complete tarsorrhaphy, superficial keratectomy for epithelial defect revision, etc) within 14 days of randomization b. Presence of amniotic membrane from AMT for ocular surface indication if not dissolved within area of PCED within 14 days of randomization. Examples include: − Sutured AMT − Self-retaining AMT −Contact lens combined with AMT −Other AMT treatment for the ocular surface c. Partial tarsorrhaphy (temporary or permanent) placed within 14 days of randomization. If a participant is enrolled with partial tarsorrhaphy placed more than 14 days prior to randomization, then the tarsorrhaphy must not be removed for the entire duration of the study."}
  • {"criterion_text":"- Contraception: a. Females of child-bearing age (defined as not surgically sterilized or post-menopausal for at least 1 year) are excluded if they meet any 1 of the following conditions: − Are known to be pregnant − Have a positive urine pregnancy test at baseline visit − Are planning to become pregnant during study period − Are breastfeeding − Are unwilling to use acceptable form of contraception until 30 days after the study treatment period is complete b. Male fertile participants (ie, not surgically sterilized by vasectomy) unwilling to use an acceptable form of contraception (male condom with spermicidal cream or jelly) until 30 days after the study treatment period is complete"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Achieving complete epithelial healing at week 4 and maintained at week 8.","definition_or_measurement_approach":""}

Secondary endpoints

  • {"endpoint_text":"- Percentage change from baseline in maximum diameter of PCED at week 4","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Percentage change from baseline in maximum diameter of PCED at week 8","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Achieving complete epithelial healing at week 8 and maintained at week 10","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Linear change from baseline in maximum diameter (in mm) of the PCED at week 4","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
124
Recruitment Window Months
28
Consent Approach
Informed consent must be signed by the participant (able to sign the informed consent as described in the protocol). Study enrols adults (≥18 years). Country-specific ICFs and related documents are provided (examples in Czech, French, German, Hungarian, Italian, Spanish, Dutch, Polish and English). Pregnant-participant and pregnant-partner forms are available where applicable. No assent of minors (study population excludes <18).

Geography

Total Number Of Sites
38
Total Number Of Participants
91

Czechia

Earliest CTIS Part Ii Submission Date
21-04-2026
Latest Decision Or Authorization Date
05-05-2026
Processing Time Days
14
Number Of Sites
2
Number Of Participants
7

Sites

Site Name
Vseobecna Fakultni Nemocnice V Praze
Department Name
552: Ocni klinika
Principal Investigator Name
Pavlina Skalicka
Principal Investigator Email
pavlina.skalicka@vfn.cz
Contact Person Name
Pavlina Skalicka
Contact Person Email
pavlina.skalicka@vfn.cz
Site Name
Fakultni Nemocnice Brno
Department Name
551: Ocni klinika
Principal Investigator Name
Dominika Ivanisova
Principal Investigator Email
ivanisova.dominika@fnbrno.cz
Contact Person Name
Dominika Ivanisova
Contact Person Email
ivanisova.dominika@fnbrno.cz

France

Earliest CTIS Part Ii Submission Date
24-04-2026
Latest Decision Or Authorization Date
11-05-2026
Processing Time Days
17
Number Of Sites
5
Number Of Participants
12

Sites

Site Name
Centre Hospitalier Universitaire De Saint Etienne
Department Name
302; Département d’Ophtalmologie
Principal Investigator Name
Philippe Gain
Principal Investigator Email
philippe.gain@univ-st-etienne.fr
Contact Person Name
Philippe Gain
Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
306; Service d’Ophtalmologie
Principal Investigator Name
Béatrice Cochener
Principal Investigator Email
beatrice.cochener@ophtalmologie-chu29.fr
Contact Person Name
Béatrice Cochener
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
305; Service d’Ophtalmologie
Principal Investigator Name
Pierre-Jean Pisella
Principal Investigator Email
PJ.PISELLA@chu-tours.fr
Contact Person Name
Pierre-Jean Pisella
Contact Person Email
PJ.PISELLA@chu-tours.fr
Site Name
Fondation A De Rothschild
Department Name
304; Service d’Ophtalmologie
Principal Investigator Name
Eric Gabison
Principal Investigator Email
egabison@for.paris
Contact Person Name
Eric Gabison
Contact Person Email
egabison@for.paris
Site Name
Assistance Publique Hopitaux De Paris
Department Name
303; OphtalmoPôle
Principal Investigator Name
Jean-Louie Bourges
Principal Investigator Email
Jean-louis.bourges@aphp.fr
Contact Person Name
Jean-Louie Bourges
Contact Person Email
Jean-louis.bourges@aphp.fr

Germany

Earliest CTIS Part Ii Submission Date
07-04-2026
Latest Decision Or Authorization Date
06-05-2026
Processing Time Days
29
Number Of Sites
8
Number Of Participants
11

Sites

Site Name
Universitaet Des Saarlandes
Department Name
402: Klinik für Augenheilkunde
Principal Investigator Name
Berthold Seitz
Principal Investigator Email
berthold.seitz@uks.eu
Contact Person Name
Berthold Seitz
Contact Person Email
berthold.seitz@uks.eu
Site Name
Kliniken der Stadt Koeln gGmbH
Department Name
407: Augenklinik
Principal Investigator Name
Norbert Schrage
Principal Investigator Email
schrageN@kliniken-koeln.de
Contact Person Name
Norbert Schrage
Contact Person Email
schrageN@kliniken-koeln.de
Site Name
Universitaetsklinikum Erlangen AöR
Department Name
406: Augenklinik
Principal Investigator Name
Theofilos Tourtas
Principal Investigator Email
Theofilos.Tourtas@uk-erlangen.de
Contact Person Name
Theofilos Tourtas
Site Name
Goethe University Frankfurt
Department Name
403: Klinik für Augenheilkunde
Principal Investigator Name
Thomas Kohnen
Principal Investigator Email
Thomas.kohnen@unimedizin-ffm.de
Contact Person Name
Thomas Kohnen
Site Name
Philipps-Universitaet Marburg
Department Name
405: Klinik für Augenheilkunde
Principal Investigator Name
Walter Sekundo
Principal Investigator Email
sekundo@staff.uni-marburg.de
Contact Person Name
Walter Sekundo
Contact Person Email
sekundo@staff.uni-marburg.de
Site Name
Universitaetsklinikum Duesseldorf AöR
Department Name
401: Klinik für Augenheilkunde
Principal Investigator Name
Gerd Geerling
Principal Investigator Email
geerling@med.uni-duesseldorf.de
Contact Person Name
Gerd Geerling
Site Name
Universitaetsklinikum Koeln AöR
Department Name
404: Zentrum für Augenheilkunde
Principal Investigator Name
Claus Cursiefen
Principal Investigator Email
claus.cursiefen@uk-koeln.de
Contact Person Name
Claus Cursiefen
Contact Person Email
claus.cursiefen@uk-koeln.de
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
408: Klinik für Augenheilkunde
Principal Investigator Name
Eckart Bertelmann
Principal Investigator Email
Eckart.bertelmann@charite.de
Contact Person Name
Eckart Bertelmann
Contact Person Email
Eckart.bertelmann@charite.de

Hungary

Earliest CTIS Part Ii Submission Date
21-04-2026
Latest Decision Or Authorization Date
11-05-2026
Processing Time Days
20
Number Of Sites
2
Number Of Participants
7

Sites

Site Name
Semmelweis University
Department Name
652 :Szemészeti Klinika
Principal Investigator Name
Zoltán Nagy
Principal Investigator Email
nagy.zoltan.zsolt@semmelweis.hu
Contact Person Name
Zoltán Nagy
Site Name
Vididit Kft.
Department Name
651: NAP
Principal Investigator Name
Ákos Vadnay
Principal Investigator Email
vadnayszemeszet@gmail.com
Contact Person Name
Ákos Vadnay
Contact Person Email
vadnayszemeszet@gmail.com

Italy

Earliest CTIS Part Ii Submission Date
21-04-2026
Latest Decision Or Authorization Date
08-05-2026
Processing Time Days
17
Number Of Sites
7
Number Of Participants
17

Sites

Site Name
Hospital Santa Maria Della Misericordia
Department Name
102; Oculistica
Principal Investigator Name
Carlo Cagini
Principal Investigator Email
carlo.cagini@unipg.it
Contact Person Name
Carlo Cagini
Contact Person Email
carlo.cagini@unipg.it
Site Name
ASST Fatebenefratelli Sacco
Department Name
101; SC Oculistica
Principal Investigator Name
Stefano Barabino
Principal Investigator Email
stebarabi@gmail.com
Contact Person Name
Stefano Barabino
Contact Person Email
stebarabi@gmail.com
Site Name
Ospedale San Raffaele S.r.l.
Department Name
107; Unità di Oculistica
Principal Investigator Name
Francesco Bandello
Principal Investigator Email
bandello.francesco@hsr.it
Contact Person Name
Francesco Bandello
Contact Person Email
bandello.francesco@hsr.it
Site Name
Fondazione G.B.Bietti Per Lo Studio E La Ricerca In Oftalmologia
Department Name
103; UOS Cornea, cristallino e oftalmoplastica
Principal Investigator Name
Domenico Schiano Lomoriello
Principal Investigator Email
domenico.schiano@fondazionebietti.it
Contact Person Name
Domenico Schiano Lomoriello
Site Name
Fondazione IRCCS Policlinico San Matteo
Department Name
105; Oculistica
Principal Investigator Name
Giovanni Milano
Principal Investigator Email
gmilano@unipv.it
Contact Person Name
Giovanni Milano
Contact Person Email
gmilano@unipv.it
Site Name
Azienda Ospedaliero Universitaria Careggi
Department Name
106: Oculistica
Principal Investigator Name
Rita Mencucci
Principal Investigator Email
rita.mencucci@unifi.it
Contact Person Name
Rita Mencucci
Contact Person Email
rita.mencucci@unifi.it
Site Name
Ospedale San Raffaele S.r.l.
Department Name
107; Unità di Oculistica

Spain

Earliest CTIS Part Ii Submission Date
24-04-2026
Latest Decision Or Authorization Date
07-05-2026
Processing Time Days
13
Number Of Sites
8
Number Of Participants
16

Sites

Site Name
Hospital Germans Trias I Pujol
Department Name
202: Oftalmología
Principal Investigator Name
Antoni Sabala Llopart
Principal Investigator Email
asabala.germanstrias@gencat.cat
Contact Person Name
Antoni Sabala Llopart
Site Name
Fundacion De Oftalmologia Medica De La Comunitat Valenciana
Department Name
205: Oftalmología
Principal Investigator Name
Marta Cerda Ibañez
Principal Investigator Email
marta.cerda@fom.es
Contact Person Name
Marta Cerda Ibañez
Contact Person Email
marta.cerda@fom.es
Site Name
Hospital Universitario Regional De Malaga
Department Name
203: Oftalmología
Principal Investigator Name
Carlos Rocha de Lossada
Principal Investigator Email
carlosrochadelossada5@gmail.com
Contact Person Name
Carlos Rocha de Lossada
Site Name
Instituto Universitario De Oftalmobiologia Aplicada
Department Name
206: Oftalmología
Principal Investigator Name
Margarita Calonge
Principal Investigator Email
calonge@ioba.med.uva.es
Contact Person Name
Margarita Calonge
Contact Person Email
calonge@ioba.med.uva.es
Site Name
Instituto De Microcirugia Ocular Dos S.L.
Department Name
204: Oftalmología
Principal Investigator Name
Jose Luis Güell Villanueva
Principal Investigator Email
jose.guell@imo.es
Contact Person Name
Jose Luis Güell Villanueva
Contact Person Email
jose.guell@imo.es
Site Name
Clinica De Oftalmologia De Cordoba S.L.
Department Name
201: Oftalmología
Principal Investigator Name
Alberto Villarrubia Cuadrado
Principal Investigator Email
alvillarrubia@yahoo.com
Contact Person Name
Alberto Villarrubia Cuadrado
Contact Person Email
alvillarrubia@yahoo.com
Site Name
Centro De Ojos De La Coruna S.L.
Department Name
207: Oftalmología
Principal Investigator Name
Carlos Mendez Mangana
Principal Investigator Email
cmendezmangana@gmail.com
Contact Person Name
Carlos Mendez Mangana
Contact Person Email
cmendezmangana@gmail.com
Site Name
Hospital Universitario Regional De Malaga (duplicate entry?)

Netherlands

Earliest CTIS Part Ii Submission Date
22-04-2026
Latest Decision Or Authorization Date
05-05-2026
Processing Time Days
13
Number Of Sites
3
Number Of Participants
7

Sites

Site Name
The Rotterdam Eye Hospital
Department Name
502: Ophthalmology
Principal Investigator Name
Anna Randag
Principal Investigator Email
a.randag@oogziekenhuis.nl
Contact Person Name
Anna Randag
Contact Person Email
a.randag@oogziekenhuis.nl
Site Name
Amsterdam UMC Stichting
Department Name
501: Ophthalmology
Principal Investigator Name
Ruth Lapid-Gortzak
Principal Investigator Email
r.lapid@amsterdamumc.nl
Contact Person Name
Ruth Lapid-Gortzak
Contact Person Email
r.lapid@amsterdamumc.nl
Site Name
Universitair Medisch Centrum Utrecht
Department Name
503: Ophthalmology
Principal Investigator Name
Mor Dickman
Principal Investigator Email
m.m.dickman@umcutrecht.nl
Contact Person Name
Mor Dickman
Contact Person Email
m.m.dickman@umcutrecht.nl

Poland

Earliest CTIS Part Ii Submission Date
21-04-2026
Latest Decision Or Authorization Date
08-05-2026
Processing Time Days
17
Number Of Sites
3
Number Of Participants
14

Sites

Site Name
Gabinet Okulistyczny Prof Edward Wylegala
Department Name
601:Ophtalmology
Principal Investigator Name
Adam Wylegala
Principal Investigator Email
adam.wylegala@gmail.com
Contact Person Name
Adam Wylegala
Contact Person Email
adam.wylegala@gmail.com
Site Name
Samodzielny Publiczny Kliniczny Szpital Okulistyczny W Warszawie
Department Name
602:Ophtalmology
Principal Investigator Name
Jacek Szaflik
Principal Investigator Email
jacek.szaflik@wum.edu.pl
Contact Person Name
Jacek Szaflik
Contact Person Email
jacek.szaflik@wum.edu.pl
Site Name
Gabinety Okulistyczne Sp. z o.o.
Department Name
603:Opthalmology
Principal Investigator Name
Agnieszka Cwiklinska-Haszcz
Principal Investigator Email
acwiklinskahaszcz@ocho.pl
Contact Person Name
Agnieszka Cwiklinska-Haszcz
Contact Person Email
acwiklinskahaszcz@ocho.pl

Sponsor

Primary sponsor

Full Name
Dompe' Farmaceutici S.p.A.
Organisation Type
Pharmaceutical company
Country Of Registered Address
Italy

Contract research organisations

Name
Parexel International (IRL) Limited
Responsibilities
sponsorDuties codes: 1,10,11,12,13,14,5,6,8
Name
Merit CRO Inc.
Responsibilities
reading centre, rater training
Name
CluePoints
Responsibilities
Central data monitoring platform
Name
BAP Pharma GmbH
Responsibilities
sponsorDuties code: 14
Name
Medidata Solutions Inc.
Responsibilities
sponsorDuties codes: 3,7

Third parties

  • {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"sponsorDuties codes: 1,10,11,12,13,14,5,6,8","organisation_type":"Pharmaceutical company"}
  • {"country":"Belgium","full_name":"CluePoints","duties_or_roles":"Central data monitoring platform","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Merit CRO Inc.","duties_or_roles":"reading centre, rater training","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"BAP Pharma GmbH","duties_or_roles":"sponsorDuties code: 14","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"sponsorDuties codes: 3,7","organisation_type":"Non-Pharmaceutical company"}

Investigational products

Investigational Product Name
OXERVATE 20 micrograms/ml eye drops, solution
Active Substance
CENEGERMIN
Modality
Peptide/protein/enzyme
Routes Of Administration
OCULAR USE
Route
ocular
Authorisation Status
Marketing authorisation EU/1/17/1197/001 (prodAuthStatus 2)
Starting Dose
20 micrograms/ml
Investigational Product Name
Vehicle for cenegermin drug product
Modality
Other

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