Clinical trial • Phase III • Neurology|Rare Disease
BEXICASERIN HYDROCHLORIDE for Dravet syndrome | Severe myoclonic epilepsy of infancy
Phase III trial of BEXICASERIN HYDROCHLORIDE for Dravet syndrome | Severe myoclonic epilepsy of infancy.
Overview
- Trial Therapeutic Area
- Neurology|Rare Disease
- Trial Disease
- Dravet syndrome | Severe myoclonic epilepsy of infancy
- Trial Stage
- Phase III
- Drug Modality
- Small molecule
- Paediatric Trial
- Yes
Key dates
- Initial CTIS Submission Date
- 18-12-2024
- First CTIS Authorization Date
- 30-04-2025
Trial design
Randomised, placebo comparator: lp352 (bexicaserin) placebo oral solution — matching placebo administered orally or via g-tube/percutaneous endoscopic gastrostomy (peg) tube. experimental arm: lp352 (bexicaserin) oral solution, titrated up to the highest tolerated dose during the titration period (specific dose titration schedule described in protocol; maximum daily dose amount recorded as 36 mg in product data).-controlled, adaptive Phase III trial across 39 sites in Italy, Latvia, Belgium and others.
- Randomised
- Yes
- Comparator
- Placebo Comparator: LP352 (bexicaserin) Placebo Oral Solution — matching placebo administered orally or via G-tube/percutaneous endoscopic gastrostomy (PEG) tube. Experimental arm: LP352 (bexicaserin) oral solution, titrated up to the highest tolerated dose during the Titration period (specific dose titration schedule described in protocol; maximum daily dose amount recorded as 36 mg in product data).
- Adaptive
- True: study uses dose titration/escalation elements — participants are titrated up to the highest tolerated dose of LP352 during the Titration period (Visit 2–Visit 5); reverse titration described in taper for discontinuation. (No additional adaptive interim analysis/stopping rule detail available in the provided record.)
- Single Multiple Or Escalation Dose Combined
- Yes
- Target Sample Size
- 73
Eligibility
Recruits 73 paediatric patients.
- Vulnerable Population
- The trial includes vulnerable populations (paediatric subjects; isVulnerablePopulationSelected = true). Consent procedures include written informed consent from the participant where capable, or from parent/legal guardian/ caregiver (Caregiver-ICF, Main-Parents_Leg_Guardian-ICF, LAR substudy ICF). Age-appropriate assent forms are provided (assent forms for 6–11 years and 12–17 years, picturebooks and assent materials for younger children). Subject information and consent/assent documents and caregiver/LAR forms are provided in multiple country/language versions (examples: Italian, Latvian, Russian, German, French, Spanish, Portuguese, Dutch, English) as indicated in the published ICF and assent documents.
Inclusion criteria
- {"criterion_text":"-Participant is ≥2 to ≤65 years of age at the time of Screening"}
- {"criterion_text":"-Diagnosis of Dravet Syndrome according to International League Against Epilepsy definition and must fulfill all of the following criteria: a. Onset of seizures age >1 and <20 months in an otherwise healthy infant. b. History of at least 1 of the following seizure type(s): i. Prolonged generalized tonic-clonic ii. Hemiclonic iii. Myoclonic iv. Tonic v. Atonic vi. Atypical absence vii. Focal awareness viii. Nonconvulsive status epilepticus"}
- {"criterion_text":"-The following countable motor seizure types: a. Generalized tonic-clonic b. Tonic (bilateral) c. Clonic (bilateral) d. Atonic (bilateral) with truncal/leg involvement e. Focal motor (including hemiclonic) f. Focal to bilateral tonic-clonic"}
- {"criterion_text":"-Demonstrated an average of at least 4 countable motor seizures (as per inclusion criterion 3) per month for the 3 months prior to Screening"}
- {"criterion_text":"-Has been taking 1 to 4 ASMs at a stable dose for at least 4 weeks prior to Screening"}
- {"criterion_text":"-The participant must be willing and able to provide written informed consent."}
- {"criterion_text":"-The participant, parent, or caregiver is willing and able (in the judgment of the investigator) to comply with completion of the diaries throughout the study."}
Exclusion criteria
- {"criterion_text":"-The participant has a history of infantile/epileptic spasms."}
- {"criterion_text":"-The participant has been admitted to a medical facility for treatment of status epilepticus requiring mechanical ventilation within 3 months prior to Screening."}
- {"criterion_text":"-The participant has a neurodegenerative disorder as indicated by magnetic resonance imaging or genetic testing."}
- {"criterion_text":"-The participant has an acquired lesion/injury unrelated to the primary etiology that could contribute as a secondary cause of seizures."}
- {"criterion_text":"-The participant is receiving exclusionary medications, as described in the protocol."}
- {"criterion_text":"-The participant has used any cannabis product or cannabidiol that is not in oral solution/capsule/tablet form, not obtained from a government-approved dispensary, or contains ≥50% Delta-9-tetrahydrocannabinol (THC)"}
- {"criterion_text":"-The participant has unstable, clinically significant neurologic (other than the disease being studied; e.g., recurrent strokes), psychiatric, cardiovascular (e.g., pulmonary arterial hypertension, cardiac valvulopathy, orthostatic hypotension/tachycardia), pulmonary, hepatic, renal, metabolic, gastrointestinal, urologic, immunologic, hematopoietic, or endocrine disease or other abnormality which may impact the ability of the participant to participate or potentially confound the study results."}
- {"criterion_text":"-The participant is unwilling to comply with any of the study requirements or timelines."}
Endpoints
Primary endpoints
- {"endpoint_text":"-Frequency percent change in countable motor seizures during Maintenance compared to Baseline","definition_or_measurement_approach":"Percent change in countable motor seizures during the Maintenance period compared with Baseline. Countable motor seizure types (per inclusion criterion 3) are: Generalized tonic-clonic; Tonic (bilateral); Clonic (bilateral); Atonic (bilateral) with truncal/leg involvement; Focal motor (including hemiclonic); Focal to bilateral tonic-clonic."}
Secondary endpoints
- {"endpoint_text":"-Safety laboratory parameters","definition_or_measurement_approach":"Standard safety laboratory assessments as per protocol (laboratory parameters listed as secondary endpoint)."}
- {"endpoint_text":"-Physical examination findings","definition_or_measurement_approach":"Routine physical examinations recorded during study visits."}
- {"endpoint_text":"-Vital signs","definition_or_measurement_approach":"Standard vital signs measurements (e.g., blood pressure, heart rate, temperature) per protocol."}
- {"endpoint_text":"-Growth parameters (height and weight)","definition_or_measurement_approach":"Measurement of participant height and weight at specified visits to assess growth parameters."}
- {"endpoint_text":"-12-lead Electrocardiogram (ECGs)","definition_or_measurement_approach":"12-lead ECG assessments per schedule; ECG data collected and analyzed for cardiac safety."}
- {"endpoint_text":"-Columbia-Suicide Severity Rating Scale (C-SSRS) responses","definition_or_measurement_approach":"C-SSRS questionnaire responses collected per protocol to assess suicidality."}
- {"endpoint_text":"-Patient Health Questionnaire-9 (PHQ-9) total score and Question 9 score","definition_or_measurement_approach":"PHQ-9 instrument total score and item 9 score collected to monitor depressive symptoms and suicidal ideation."}
- {"endpoint_text":"-50% responder rate (the percentage of participants with a ≥50% reduction in countable motor seizures) during Maintenance compared to Baseline","definition_or_measurement_approach":"Proportion of participants achieving ≥50% reduction in countable motor seizures during Maintenance versus Baseline."}
- {"endpoint_text":"-Frequency percent change in countable motor seizures during Treatment compared to Baseline","definition_or_measurement_approach":"Percent change in countable motor seizures during the Treatment period compared with Baseline (treatment period defined in protocol)."}
Recruitment
- Digital Remote Recruitment
- True: digital/remote methods include study websites (DEEp-studies and country pages), online brochures and flyers, cookie/privacy policies for web recruitment, telephone pre-screening (Pre-ICF Telephone Data Consent), and eCOA/eDiary platforms (WCG Clinical; Medidata).
- Planned Sample Size
- 73
- Recruitment Window Months
- 12
- Consent Approach
- Written informed consent is required. Consent is obtained from participants able to provide written informed consent; for minors or participants lacking capacity, consent is obtained from parent/legal guardian or caregiver (Caregiver-ICF, Main-Parents/Legal Guardian ICF, LAR substudy ICF). Age-appropriate assent materials are provided (assent forms for 6–11 years and 12–17 years, picturebooks and assent materials for younger children, and substudy assent forms). Consent and assent documents are available in multiple country/language versions as published (examples include Italian, Latvian, Russian, German, French, Spanish, Portuguese, Dutch, English).
Methods
- Study-specific websites and online content (DEEp-studies website and country-specific recruitment website content; multiple languages) — recruitment webpages and images documented in recruitment materials.
- Brochures and patient flyers distributed as recruitment materials (country- and language-specific brochures and flyers listed for BE, DE, ES, FR, IT, LV, PT, NL, FI, DK).
- Pre-screening telephone data consent procedures (Pre-ICF Telephone Data Consent documents present) indicating telephone pre-screening/contact method.
- Patient-facing materials and study information sheets (country-specific ICF and study information documents) used for participant information and recruitment.
- Patient recruitment support and website/promo items provided by third-party vendors (e.g., Elligo Health Research Inc. listed with responsibilities for patient recruitment and website/promo items).
- Use of electronic diaries/eCOA and vendor-managed digital tools (WCG Clinical Inc., Medidata) to support data capture and remote engagement.
Geography
- Total Number Of Sites
- 39
- Total Number Of Participants
- 110
Italy
- Earliest CTIS Part Ii Submission Date
- 14-04-2025
- Latest Decision Or Authorization Date
- 21-01-2026
- Processing Time Days
- 282
- Number Of Sites
- 6
- Number Of Participants
- 10
Sites
- Site Name
- Azienda Ospedaliera Universitaria Meyer IRCCS
- Department Name
- Neuroscience and Medical Genetics Department
- Principal Investigator Name
- Renzo Guerrini
- Principal Investigator Email
- renzo.guerrini@meyer.it
- Contact Person Name
- Renzo Guerrini
- Contact Person Email
- renzo.guerrini@meyer.it
- Site Name
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Department Name
- U.O.C. Pediatric Neuropsychiatry
- Principal Investigator Name
- Domenica Immacolata Battaglia
- Principal Investigator Email
- domenicaimmacolata.battaglia@policlinicogemelli.it
- Contact Person Name
- Domenica Immacolata Battaglia
- Contact Person Email
- domenicaimmacolata.battaglia@policlinicogemelli.it
- Site Name
- Fondazione Istituto Neurologico Nazionale Casimiro Mondino
- Department Name
- SC Neuropsichiatria Infantile
- Principal Investigator Name
- Valentina Valentina De Giorgis
- Principal Investigator Email
- valentina.degiorgis@mondino.it
- Contact Person Name
- Valentina Valentina De Giorgis
- Contact Person Email
- valentina.degiorgis@mondino.it
- Site Name
- Azienda Ospedaliera Universitaria Integrata Verona
- Department Name
- UOC Neuropsichiatria infantile
- Principal Investigator Name
- Francesca Darra
- Principal Investigator Email
- francesca.darra@univr.it
- Contact Person Name
- Francesca Darra
- Contact Person Email
- francesca.darra@univr.it
- Site Name
- IRCCS Istituto Giannina Gaslini
- Department Name
- UOC Pediatric Neurology and Muscolar Diseases
- Principal Investigator Name
- Pasquale Striano
- Principal Investigator Email
- strianop@gmail.com
- Contact Person Name
- Pasquale Striano
- Contact Person Email
- strianop@gmail.com
- Site Name
- Ospedale Pediatrico Bambino Gesu
- Department Name
- UOC Neurologia dell'epilessia e disturbi del movimento
- Principal Investigator Name
- Nicola Specchio
- Principal Investigator Email
- nicola.specchio@opbg.net
- Contact Person Name
- Nicola Specchio
- Contact Person Email
- nicola.specchio@opbg.net
Latvia
- Earliest CTIS Part Ii Submission Date
- 21-01-2025
- Latest Decision Or Authorization Date
- 20-01-2026
- Processing Time Days
- 364
- Number Of Sites
- 1
- Number Of Participants
- 3
Sites
- Site Name
- Bernu Kliniska Universitates Slimnica VSIA
- Department Name
- Children‘s Neurology and Neurosurgery Clinic
- Principal Investigator Name
- Jurgis Strautmanis
- Principal Investigator Email
- jurgis.strautmanis@gmail.com
- Contact Person Name
- Jurgis Strautmanis
- Contact Person Email
- jurgis.strautmanis@gmail.com
Belgium
- Earliest CTIS Part Ii Submission Date
- 16-04-2025
- Latest Decision Or Authorization Date
- 20-01-2026
- Processing Time Days
- 279
- Number Of Sites
- 2
- Number Of Participants
- 10
Sites
- Site Name
- Universitair Ziekenhuis Antwerpen
- Department Name
- Kinderneurologie
- Principal Investigator Name
- An-Sofie Schoonjans
- Principal Investigator Email
- an-sofie.schoonjans@uza.be
- Contact Person Name
- An-Sofie Schoonjans
- Contact Person Email
- an-sofie.schoonjans@uza.be
- Site Name
- UZ Leuven
- Department Name
- Kinderneurologie
- Principal Investigator Name
- Lieven Lagae
- Principal Investigator Email
- lieven.lagae@uzleuven.be
- Contact Person Name
- Lieven Lagae
- Contact Person Email
- lieven.lagae@uzleuven.be
Germany
- Earliest CTIS Part Ii Submission Date
- 11-04-2025
- Latest Decision Or Authorization Date
- 21-01-2026
- Processing Time Days
- 285
- Number Of Sites
- 6
- Number Of Participants
- 16
Sites
- Site Name
- Zentrum für Psychiatrie Südwürttemberg Epilepsy Centre Bodensee
- Department Name
- Department of Neurology and Epileptology
- Principal Investigator Name
- Christian Tilz
- Principal Investigator Email
- Christian.Tilz@ZfP-Zentrum.de
- Contact Person Name
- Christian Tilz
- Contact Person Email
- Christian.Tilz@ZfP-Zentrum.de
- Site Name
- Schoen Klinik Vogtareuth SE & Co. KG
- Principal Investigator Name
- Milka Pringsheim
- Principal Investigator Email
- MPringsheim@schoen-klinik.de
- Contact Person Name
- Milka Pringsheim
- Contact Person Email
- MPringsheim@schoen-klinik.de
- Site Name
- Universitaetsklinikum Schleswig-Holstein AöR
- Department Name
- Klinik für Kinder- und Jugendmedizin II Abteilung für Neuropädiatrie und Sozialpädiatrie
- Principal Investigator Name
- Hiltrud Muhle
- Principal Investigator Email
- hiltrud.muhle@uksh.de
- Contact Person Name
- Hiltrud Muhle
- Contact Person Email
- hiltrud.muhle@uksh.de
- Site Name
- Gesellschaft Fuer Epilepsieforschung
- Department Name
- Epilepsieambulanz
- Principal Investigator Name
- Christian Brandt
- Principal Investigator Email
- christian.brandt@mara.de
- Contact Person Name
- Christian Brandt
- Contact Person Email
- christian.brandt@mara.de
- Site Name
- Universitaetsklinikum Bonn AöR
- Department Name
- Neuropädiatrie @ Sozialpädiatrisches Zentrum (SPZ)
- Principal Investigator Name
- Kerstin Alexandra Klotz
- Principal Investigator Email
- kerstin.alexandra.klotz@uniklinik-freiburg.de
- Contact Person Name
- Kerstin Alexandra Klotz
- Contact Person Email
- kerstin.alexandra.klotz@uniklinik-freiburg.de
- Site Name
- Universitaetsklinikum Frankfurt AöR
- Department Name
- ZNN – Epilepsy Center Rhine-Main
- Principal Investigator Name
- Adam Strzelczyk
- Principal Investigator Email
- strzelczyk@med.uni-frankfurt.de
- Contact Person Name
- Adam Strzelczyk
- Contact Person Email
- strzelczyk@med.uni-frankfurt.de
Portugal
- Earliest CTIS Part Ii Submission Date
- 21-01-2025
- Latest Decision Or Authorization Date
- 20-01-2026
- Processing Time Days
- 364
- Number Of Sites
- 3
- Number Of Participants
- 10
Sites
- Site Name
- Unidade Local De Saude De Coimbra E.P.E.
- Department Name
- Child development Center Service - Hospital Pediátrico - ULS Coimbra
- Principal Investigator Name
- Cristina Pereira
- Principal Investigator Email
- cristina.d.pereira@gmail.com
- Contact Person Name
- Cristina Pereira
- Contact Person Email
- cristina.d.pereira@gmail.com
- Site Name
- Unidade Local De Saude De Santa Maria E.P.E.
- Department Name
- Paediatrics Department
- Principal Investigator Name
- Sofia Quintas
- Principal Investigator Email
- sofiamendesquintas@gmail.com
- Contact Person Name
- Sofia Quintas
- Contact Person Email
- sofiamendesquintas@gmail.com
- Site Name
- Unidade Local De Saude De Santo Antonio E.P.E.
- Department Name
- Paediatrics - NeuroPediatric Unit
- Principal Investigator Name
- Cristina Garrido
- Principal Investigator Email
- cristinagarrido@ulssa.min-saude.pt
- Contact Person Name
- Cristina Garrido
- Contact Person Email
- cristinagarrido@ulssa.min-saude.pt
Spain
- Earliest CTIS Part Ii Submission Date
- 14-04-2025
- Latest Decision Or Authorization Date
- 29-01-2026
- Processing Time Days
- 290
- Number Of Sites
- 8
- Number Of Participants
- 18
Sites
- Site Name
- Hospital Universitario De Navarra
- Department Name
- Pediatrics
- Principal Investigator Name
- Sergio Aguilera Albesa
- Principal Investigator Email
- saguilea@navarra.es
- Contact Person Name
- Sergio Aguilera Albesa
- Contact Person Email
- saguilea@navarra.es
- Site Name
- Hospital La Milagrosa S.A.
- Department Name
- Neurology
- Principal Investigator Name
- Maria del Mar Carreño Martinez
- Principal Investigator Email
- maria.carreno@ext.vithas.es
- Contact Person Name
- Maria del Mar Carreño Martinez
- Contact Person Email
- maria.carreno@ext.vithas.es
- Site Name
- Hospital Universitari Vall D Hebron
- Department Name
- Neurology
- Principal Investigator Name
- Manuel Toledo Argany
- Principal Investigator Email
- manuel.toledo@vallhebron.cat
- Contact Person Name
- Manuel Toledo Argany
- Contact Person Email
- manuel.toledo@vallhebron.cat
- Site Name
- Hospital Sant Joan De Deu Barcelona
- Department Name
- Neurology
- Principal Investigator Name
- Maria del Carmen Fons Estupiña
- Principal Investigator Email
- carmen.fons@sjd.es
- Contact Person Name
- Maria del Carmen Fons Estupiña
- Contact Person Email
- carmen.fons@sjd.es
- Site Name
- Hospital Ruber Internacional
- Department Name
- Neurology
- Principal Investigator Name
- Antonio Gil-Nagel Rein
- Principal Investigator Email
- gilnagel.ensayos@neurologiaclinica.es
- Contact Person Name
- Antonio Gil-Nagel Rein
- Contact Person Email
- gilnagel.ensayos@neurologiaclinica.es
- Site Name
- Hospital Vithas Parque San Antonio
- Department Name
- Neurology
- Principal Investigator Name
- Pablo Cabezudo Garcia
- Principal Investigator Email
- pablocabezudogcp@gmail.com
- Contact Person Name
- Pablo Cabezudo Garcia
- Contact Person Email
- pablocabezudogcp@gmail.com
- Site Name
- Hospital Universitario Regional De Malaga
- Department Name
- Neurology
- Principal Investigator Name
- Pedro J. Serrano Castro
- Principal Investigator Email
- p.serrano.eecc@gmail.com
- Contact Person Name
- Pedro J. Serrano Castro
- Contact Person Email
- p.serrano.eecc@gmail.com
- Site Name
- Hospital De La Santa Creu I Sant Pau
- Department Name
- Neurology
- Principal Investigator Name
- Alba Sierra Marcos
- Principal Investigator Email
- asierram@santpau.cat
- Contact Person Name
- Alba Sierra Marcos
- Contact Person Email
- asierram@santpau.cat
France
- Earliest CTIS Part Ii Submission Date
- 15-04-2025
- Latest Decision Or Authorization Date
- 12-02-2026
- Processing Time Days
- 303
- Number Of Sites
- 8
- Number Of Participants
- 16
Sites
- Site Name
- Les Hopitaux Universitaires De Strasbourg
- Department Name
- Neuropédiatrie
- Principal Investigator Name
- Anne DE SAINT MARTIN
- Principal Investigator Email
- Anne.desaintmartin@chru-strasbourg.fr
- Contact Person Name
- Anne DE SAINT MARTIN
- Contact Person Email
- Anne.desaintmartin@chru-strasbourg.fr
- Site Name
- Hospices Civils De Lyon
- Department Name
- Neurologie fonctionnelle et épileptologie
- Principal Investigator Name
- Sylvain RHEIMS
- Principal Investigator Email
- sylvain.rheims@chu-lyon.fr
- Contact Person Name
- Sylvain RHEIMS
- Contact Person Email
- sylvain.rheims@chu-lyon.fr
- Site Name
- Centre Hospitalier Universitaire De Lille
- Department Name
- Neuropédiatrie
- Principal Investigator Name
- Sylvie NGUYEN THE TICH
- Principal Investigator Email
- sylvie.nguyenthetich@chru-lille.fr
- Contact Person Name
- Sylvie NGUYEN THE TICH
- Contact Person Email
- sylvie.nguyenthetich@chru-lille.fr
- Site Name
- Hopital Des Enfants
- Department Name
- Neurologie, Infectiologie Pédiatrique
- Principal Investigator Name
- Caroline HACHON LE CAMUS
- Principal Investigator Email
- hachonlecamus.c@chu-toulouse.fr
- Contact Person Name
- Caroline HACHON LE CAMUS
- Contact Person Email
- hachonlecamus.c@chu-toulouse.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Neurologie pédiatrique
- Principal Investigator Name
- Rima EL NABBOUT
- Principal Investigator Email
- Rima.Nabbout@aphp.fr
- Contact Person Name
- Rima EL NABBOUT
- Contact Person Email
- Rima.Nabbout@aphp.fr
- Site Name
- Centre Hospitalier Universitaire De Rennes
- Department Name
- Pédiatrie
- Principal Investigator Name
- Silvia NAPURI PEIRANO
- Principal Investigator Email
- silvia.napuri@chu-rennes.fr
- Contact Person Name
- Silvia NAPURI PEIRANO
- Contact Person Email
- silvia.napuri@chu-rennes.fr
- Site Name
- Centre Hospitalier Regional De Marseille
- Department Name
- Neurologie Pédiatrique et Epileptologie Pédiatrique
- Principal Investigator Name
- Mathieu MILH
- Principal Investigator Email
- mathieu.milh@ap-hm.fr
- Contact Person Name
- Mathieu MILH
- Contact Person Email
- mathieu.milh@ap-hm.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Neurologie Pédiatrique
- Principal Investigator Name
- Stéphane AUVIN
- Principal Investigator Email
- stephane.auvin@aphp.fr
- Contact Person Name
- Stéphane AUVIN
- Contact Person Email
- stephane.auvin@aphp.fr
Denmark
- Earliest CTIS Part Ii Submission Date
- 07-05-2026
- Latest Decision Or Authorization Date
- 11-05-2026
- Processing Time Days
- 4
- Number Of Sites
- 2
- Number Of Participants
- 8
Sites
- Site Name
- Filadelfia
- Department Name
- Neuropaediatric Department
- Principal Investigator Name
- Kern Olofsson
- Principal Investigator Email
- kol@filadelfia.dk
- Contact Person Name
- Kern Olofsson
- Contact Person Email
- kol@filadelfia.dk
- Site Name
- Region Midtjylland
- Department Name
- Department of Neurology, Neurological Research Unit
- Principal Investigator Name
- Jakob Christensen
- Principal Investigator Email
- jakob@farm.au.dk
- Contact Person Name
- Jakob Christensen
- Contact Person Email
- jakob@farm.au.dk
Finland
- Earliest CTIS Part Ii Submission Date
- 20-04-2026
- Latest Decision Or Authorization Date
- 12-05-2026
- Processing Time Days
- 22
- Number Of Sites
- 2
- Number Of Participants
- 9
Sites
- Site Name
- Pohjois-Savon hyvinvointialue
- Department Name
- Epilepsy Center
- Principal Investigator Name
- Reetta Kälviäinen
- Principal Investigator Email
- reetta.kalviainen@pshyvinvointialue.fi
- Contact Person Name
- Reetta Kälviäinen
- Contact Person Email
- reetta.kalviainen@pshyvinvointialue.fi
- Site Name
- HUS-yhtymae
- Department Name
- General Child Neurology Clinic and Children and Adolescents, Pediatric Clinical Trial Unit
- Principal Investigator Name
- Eeva-Liisa Metsähonkala
- Principal Investigator Email
- eeva-liisa.metsahonkala@hus.fi
- Contact Person Name
- Eeva-Liisa Metsähonkala
- Contact Person Email
- eeva-liisa.metsahonkala@hus.fi
Netherlands
- Earliest CTIS Part Ii Submission Date
- 15-04-2025
- Latest Decision Or Authorization Date
- 24-03-2026
- Processing Time Days
- 343
- Number Of Sites
- 1
- Number Of Participants
- 10
Sites
- Site Name
- Epilepsie Instellingen Nederland Stichting
- Department Name
- Epilepsy
- Principal Investigator Name
- Aysun Altinbas
- Principal Investigator Email
- polikliniek.heemstede@sein.nl
- Contact Person Name
- Aysun Altinbas
- Contact Person Email
- polikliniek.heemstede@sein.nl
Sponsor
Primary sponsor
- Full Name
- Longboard Pharmaceuticals Inc.
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- United States
Contract research organisations
- Name
- PPD Development LP
- Responsibilities
- Multiple sponsor duties (codes: 1,11,12,13,14,2,4,5,6,7,8) as listed in third-party duties
- Name
- PPD International Holdings LLC
- Responsibilities
- Sponsor duties (code: 4) as listed in third-party duties
- Name
- WCG Clinical Inc.
- Responsibilities
- eCoa/eDiary; other sponsor duties (code: 7)
- Name
- Endpoint Clinical Inc.
- Responsibilities
- Sponsor duties (code: 3)
Third parties
- {"country":"Germany","full_name":"Centogene GmbH","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"United States","full_name":"PPD Development LP","duties_or_roles":"sponsorDuties codes: 1,11,12,13,14,2,4,5,6,7,8","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Scout Clinical","duties_or_roles":"Patient travel and reimbursements, stipends","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"Belgium","full_name":"PPD International Holdings LLC","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Endpoint Clinical Inc.","duties_or_roles":"sponsorDuties codes: 3","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"WCG Clinical Inc.","duties_or_roles":"eCoa/eDiary; sponsorDuties codes: 7","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"ECG, cardiac services","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Azenta US Inc.","duties_or_roles":"Longterm sample storage","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Marken LLP","duties_or_roles":"Courier, DTP/DFP Shipment","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"URL; sponsorDuties codes: 7","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"Elligo Health Research Inc.","duties_or_roles":"Patient recruitment and website, promo items","organisation_type":"Laboratory/Research/Testing facility"}
Investigational products
- Investigational Product Name
- Bexicaserin
- Active Substance
- BEXICASERIN HYDROCHLORIDE
- Modality
- Small molecule
- Routes Of Administration
- ORAL, NASOGASTRIC TUBE OR PERCUTANEOUS ENDOSCOPIC GASTROSTOMY TUBE USE
- Route
- ORAL or via G-tube/PEG
- Authorisation Status
- prodAuthStatus: 1
- Maximum Dose
- 36 mg (maxDailyDoseAmount)
- Dose Escalation Increase
- Participants are titrated up to highest tolerated dose during Titration period (specific initial and subsequent dose levels not provided in CTIS record)
- Investigational Product Name
- LP352 (bexicaserin) Placebo Oral Solution
- Modality
- Other
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