Clinical trial • Phase II/III • Neurology|Rare Disease
NIPOCALIMAB for Chronic inflammatory demyelinating polyneuropathy
Phase II/III trial of NIPOCALIMAB for Chronic inflammatory demyelinating polyneuropathy.
Overview
- Trial Therapeutic Area
- Neurology|Rare Disease
- Trial Disease
- Chronic inflammatory demyelinating polyneuropathy
- Trial Stage
- Phase II/III
- Drug Modality
- Monoclonal antibody|Other antibody
Key dates
- Initial CTIS Submission Date
- 22-03-2024
- First CTIS Authorization Date
- 13-05-2024
Trial design
Randomised, open-label, placebo (saline, 0.9% sodium chloride solution for injection); standard of care ivig (privigen 100 mg/ml solution for infusion) - doses/schedules not specified in provided metadata.-controlled Phase II/III trial in France, Italy, Portugal and others.
- Randomised
- Yes
- Open Label
- Yes
- Comparator
- Placebo (Saline, 0.9% Sodium Chloride Solution for Injection); Standard of care IVIg (Privigen 100 mg/ml solution for infusion) - doses/schedules not specified in provided metadata.
- Target Sample Size
- 116
Eligibility
Recruits 116 Vulnerable population selection flag is set in the trial record. Participants must be adults (≥18) and consent is required from the participant; specific details on assent/consent handling for vulnerable subgroups are not available in the provided metadata..
- Vulnerable Population
- Vulnerable population selection flag is set in the trial record. Participants must be adults (≥18) and consent is required from the participant; specific details on assent/consent handling for vulnerable subgroups are not available in the provided metadata.
Inclusion criteria
- {"criterion_text":"-Adults ≥18 years of age at the time of consent and as applicable, must also meet the legal age of consent and in the jurisdiction in which the study is taking place."}
- {"criterion_text":"-Diagnosed with CIDP according to criteria of the EAN/PNS 2021, progressing or relapsing forms. CIDP diagnosis to be adjudicated by independent committee during screening period."}
- {"criterion_text":"-INCAT disability score between 2 and 9 at the Run-In Baseline visit for participants entering Run-In, or Stage A Baseline visit for participants directly entering Stage A. Participants with an INCAT score of 2 at trial entry must have this score exclusively from the leg disability score."}
Exclusion criteria
- {"criterion_text":"-Has a history of severe and/or uncontrolled hepatic (e.g. viral/alcoholic/ autoimmune hepatitis/cirrhosis and or metabolic liver disease), gastrointestinal, renal, pulmonary, cardiovascular, psychiatric, neurological or musculoskeletal disorder, hypertension and/ or any other medical or uncontrolled autoimmune disorder(s) (e.g. diabetes mellitus) or clinically significant abnormalities in screening laboratory that might interfere with the patient's full participation in the study, or might jeopardize the safety of the participant or the validity of the study results. Note: Any condition for which, in the opinion of the investigator, participation would not be in the best interest of the participants (e.g., compromise well-being) or that could prevent, limit, or confound the protocol-specified assessments."}
- {"criterion_text":"-Pure sensory CIDP or CISP (EAN/PNS definition)."}
- {"criterion_text":"-Polyneuropathy of other causes, including the following: Multifocal motor neuropathy (MMN); Monoclonal gammopathy of uncertain significance with antimyelin associated glycoprotein (anti-MAG) immunoglobulin M (IgM) antibodies; Hereditary motor neuropathy; Hereditary neuropathy with liability to pressure palsies (HNPP); Polyneuropathy, organomegaly, endocrinopathy, monoclonal protein and skin change syndromes; Lumbosacral radiculoplexus neuropathy; Polyneuropathy most likely due to diabetes mellitus; Polyneuropathy most likely due to systemic illnesses; Drug- or toxin-induced polyneuropathy. Note: A concomitant polyneuropathy of other causes (e.g. a mild, stable diabetic polyneuropathy) is not necessarily exclusionary if CIDP is confirmed as the main diagnosis, as determined by the investigator and confirmed by the adjudication committee."}
Endpoints
Primary endpoints
- {"endpoint_text":"-Time to first occurrence of a relapse event, where relapse is defined by the deterioration in either adjusted INCAT disability score relative to Stage B baseline or the switch to IVIg or other SoC as a result of investigator-assessed lack of efficacy as confirmed by an independent RAC","definition_or_measurement_approach":"Relapse defined as deterioration in adjusted INCAT disability score relative to Stage B baseline OR switch to IVIg or other standard-of-care due to investigator-assessed lack of efficacy, confirmed by an independent Relapse Adjudication Committee (RAC). Time-to-event analysis."}
Secondary endpoints
- {"endpoint_text":"-Time to initial confirmed ECI","definition_or_measurement_approach":"Time from baseline to initial confirmed Evidence of Clinical Improvement (ECI)."}
- {"endpoint_text":"-Percentage of responders as determined by ECI","definition_or_measurement_approach":"Proportion of participants meeting ECI criteria as defined by protocol."}
- {"endpoint_text":"-Change from Stage A baseline over time in adjusted INCAT disability score","definition_or_measurement_approach":"Longitudinal change from Stage A baseline in adjusted INCAT disability score."}
- {"endpoint_text":"-Change from Stage A baseline over time in MRC Muscle Grading Scale Sum score","definition_or_measurement_approach":"Longitudinal change from Stage A baseline in Medical Research Council (MRC) muscle strength sum score."}
- {"endpoint_text":"-Change from Stage A baseline over time in I-RODS centile score","definition_or_measurement_approach":"Longitudinal change from Stage A baseline in I-RODS centile score (Inflammatory Rasch-built Overall Disability Scale)."}
- {"endpoint_text":"-Change from Stage A baseline over time in mean grip strength (dominant hand)","definition_or_measurement_approach":"Longitudinal change from Stage A baseline in mean grip strength measured in the dominant hand."}
- {"endpoint_text":"-Change from Stage A baseline over time in mean grip strength (non-dominant hand)","definition_or_measurement_approach":"Longitudinal change from Stage A baseline in mean grip strength measured in the non-dominant hand."}
- {"endpoint_text":"-Time to first adjusted INCAT disability score deterioration relative to Stage B baseline","definition_or_measurement_approach":"Time-to-event: first deterioration in adjusted INCAT disability score compared to Stage B baseline."}
- {"endpoint_text":"-Time to first switch to IVIg or other SoC as a result of investigator-assessed lack of efficacy as confirmed by an independent RAC relative to Stage B baseline","definition_or_measurement_approach":"Time-to-event: first switch to IVIg or other standard-of-care due to investigator-assessed lack of efficacy, confirmed by independent RAC, relative to Stage B baseline."}
- {"endpoint_text":"-Change from Stage B baseline over time in adjusted INCAT disability score","definition_or_measurement_approach":"Longitudinal change from Stage B baseline in adjusted INCAT disability score."}
- {"endpoint_text":"-Change from Stage B baseline over time in MRC Muscle Grading Scale Sum score","definition_or_measurement_approach":"Longitudinal change from Stage B baseline in MRC muscle grading sum score."}
- {"endpoint_text":"-Change from Stage B baseline over time in I-RODS centile score","definition_or_measurement_approach":"Longitudinal change from Stage B baseline in I-RODS centile score."}
- {"endpoint_text":"-Change from Stage B baseline over time in mean grip strength (dominant hand)","definition_or_measurement_approach":"Longitudinal change from Stage B baseline in mean grip strength (dominant hand)."}
- {"endpoint_text":"-Change from Stage B baseline over time in mean grip strength (non-dominant hand)","definition_or_measurement_approach":"Longitudinal change from Stage B baseline in mean grip strength (non-dominant hand)."}
- {"endpoint_text":"-Binary response endpoint satisfying all 4 conditions: (1) an improved adjusted INCAT disability score compared to Stage B baseline, (2) not relapsing, (3) not switching to SoC, (4) not discontinuing treatment","definition_or_measurement_approach":"Composite binary responder endpoint requiring all four specified conditions relative to Stage B baseline."}
- {"endpoint_text":"-Percentage of participants with TEAEs and SAEs","definition_or_measurement_approach":"Proportion of participants experiencing treatment-emergent adverse events (TEAEs) and serious adverse events (SAEs)."}
- {"endpoint_text":"-Change in ECG, vital signs and clinical laboratory values over time","definition_or_measurement_approach":"Assessment of longitudinal changes in ECG, vital signs and laboratory values."}
- {"endpoint_text":"-Incidence of clinically significant ECG, vital signs and clinical laboratory abnormalities","definition_or_measurement_approach":"Incidence of clinically significant abnormalities in ECG, vital signs and laboratory tests."}
- {"endpoint_text":"-Percentage of participants with suicidal ideation or suicidal behavior based on the C-SSRS","definition_or_measurement_approach":"Proportion of participants with suicidal ideation or behavior as measured by the Columbia-Suicide Severity Rating Scale (C-SSRS)."}
- {"endpoint_text":"-Serum nipocalimab concentrations over time in participants receiving active study intervention","definition_or_measurement_approach":"Pharmacokinetic assessment: serum concentrations of nipocalimab over time."}
- {"endpoint_text":"-Incidence and titers of ADA to nipocalimab and the presence of NAb to nipocalimab","definition_or_measurement_approach":"Immunogenicity assessment: incidence and titers of anti-drug antibodies (ADA) and presence of neutralizing antibodies (NAb) to nipocalimab."}
- {"endpoint_text":"-Changes in total serum IgG concentrations over time","definition_or_measurement_approach":"Longitudinal assessment of total serum IgG concentrations."}
Recruitment
- Digital Remote Recruitment
- True - e-mail communication materials are present (e.g. L2_S491_SC_PFD_E-mail Communication and other electronic participant communications referenced in recruitment documents).
- Planned Sample Size
- 116
- Recruitment Window Months
- 90
- Consent Approach
- Informed consent is obtained from participants who are adults (≥18 years). Subject information and informed consent forms (L1_SIS-ICF_Main and related ICF documents, including pregnancy/withdrawal/privacy forms) are provided in the trial documentation. Specific assent procedures for minors are not applicable (minors excluded); exact language lists and age-specific consent form details are not available in the provided metadata.
Methods
- Print advertisements (K2_Print-Ad-Color templates listed in recruitment documents)
- Participant materials: flyer, brochure, poster (K2_Participant-Flyer / Participant-Brochure / Participant-Poster)
- Dear Participant Letter (K2_Dear-Participant-Letter)
- Advocacy / outreach text materials (K2_Advocacy-Outreach-Text)
- Recruitment and informed consent process documentation (K1_Recruit-ICF process)
Geography
- Total Number Of Sites
- 43
- Total Number Of Participants
- 116
France
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 11-06-2024
- Processing Time Days
- 61
- Number Of Sites
- 9
- Number Of Participants
- 5
Sites
- Site Name
- Centre Hospitalier Universitaire De Nice
- Department Name
- Système Nerveux Périphérique & Muscle
- Principal Investigator Name
- Sabrina Sacconi
- Principal Investigator Email
- sacconi.s@chu-nice.fr
- Contact Person Name
- Sabrina Sacconi
- Contact Person Email
- sacconi.s@chu-nice.fr
- Site Name
- Centre Hospitalier Universitaire De Nimes
- Department Name
- Neurologie
- Principal Investigator Name
- Giovanni Castelnovo
- Principal Investigator Email
- giovanni.castelnovo@chu-nimes.fr
- Contact Person Name
- Giovanni Castelnovo
- Contact Person Email
- giovanni.castelnovo@chu-nimes.fr
- Site Name
- Hospital Pierre Wertheimer
- Department Name
- Neurologie
- Principal Investigator Name
- Juliette Svahn
- Principal Investigator Email
- juliette.svahn@chu-lyon.fr
- Contact Person Name
- Juliette Svahn
- Contact Person Email
- juliette.svahn@chu-lyon.fr
- Site Name
- Centre Hospitalier Regional De Marseille
- Department Name
- Centre de reference des maladies neuromusculaires rares et de la SLA
- Principal Investigator Name
- Shahram Attarian
- Principal Investigator Email
- shahram.attarian@ap-hm.fr
- Contact Person Name
- Shahram Attarian
- Contact Person Email
- shahram.attarian@ap-hm.fr
- Site Name
- Les Hopitaux Universitaires De Strasbourg
- Department Name
- Neurologie
- Principal Investigator Name
- Jérôme De Seze
- Principal Investigator Email
- Jerome.DESEZE@chru-strasbourg.fr
- Contact Person Name
- Jérôme De Seze
- Contact Person Email
- Jerome.DESEZE@chru-strasbourg.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Neurologie
- Principal Investigator Name
- Karine Viala
- Principal Investigator Email
- karine.viala@aphp.fr
- Contact Person Name
- Karine Viala
- Contact Person Email
- karine.viala@aphp.fr
- Site Name
- Fondation A De Rothschild
- Department Name
- Neurologie
- Principal Investigator Name
- Antoine Gueguen
- Principal Investigator Email
- agueguen@for.paris
- Contact Person Name
- Antoine Gueguen
- Contact Person Email
- agueguen@for.paris
- Site Name
- Assistance Publique Hopitaux De Paris (Le Kremlin-Bicetre)
- Department Name
- Neurologie
- Principal Investigator Name
- Andoni Echaniz-Laguna
- Principal Investigator Email
- andoni.echaniz-laguna@aphp.fr
- Contact Person Name
- Andoni Echaniz-Laguna
- Contact Person Email
- andoni.echaniz-laguna@aphp.fr
- Site Name
- Centre Hospitalier Universitaire De Bordeaux
- Department Name
- Neurologie
- Principal Investigator Name
- Gwendal Le Masson
- Principal Investigator Email
- gwendal.le-masson@chu-bordeaux.fr
- Contact Person Name
- Gwendal Le Masson
- Contact Person Email
- gwendal.le-masson@chu-bordeaux.fr
Italy
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 29-05-2024
- Processing Time Days
- 413
- Number Of Sites
- 11
- Number Of Participants
- 5
Sites
- Site Name
- Casa Di Cura Igea S.p.A.
- Department Name
- Dipartimento di Scienze Neuroriabilitative
- Principal Investigator Name
- Elda Judica
- Principal Investigator Email
- e.judica@casadicuraigea.it
- Contact Person Name
- Elda Judica
- Contact Person Email
- e.judica@casadicuraigea.it
- Site Name
- IRCCS Ospedale Policlinico San Martino
- Department Name
- Clinica neurologica
- Principal Investigator Name
- Angelo Schenone
- Principal Investigator Email
- aschenone@neurologia.unige.it
- Contact Person Name
- Angelo Schenone
- Contact Person Email
- aschenone@neurologia.unige.it
- Site Name
- Humanitas Mirasole S.p.A.
- Department Name
- UO Malattie Neuromuscolari e Neuroimmunologiche
- Principal Investigator Name
- Giuseppe Liberatore
- Principal Investigator Email
- giuseppe.liberatore@humanitas.it
- Contact Person Name
- Giuseppe Liberatore
- Contact Person Email
- giuseppe.liberatore@humanitas.it
- Site Name
- Azienda Ospedaliero-Universitaria Policlinico G. Rodolico-San Marco Di Catania
- Department Name
- UO clinica neurologica
- Principal Investigator Name
- Francesco Patti
- Principal Investigator Email
- patti@unict.it
- Contact Person Name
- Francesco Patti
- Contact Person Email
- patti@unict.it
- Site Name
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Department Name
- UOC Neurologia
- Principal Investigator Name
- Marco Luigetti
- Principal Investigator Email
- marco.luigetti@policlinicogemelli.it
- Contact Person Name
- Marco Luigetti
- Contact Person Email
- marco.luigetti@policlinicogemelli.it
- Site Name
- Azienda Ospedaliera Di Rilievo Nazionale Antonio Cardarelli
- Department Name
- UOC Neurofisiopatologia
- Principal Investigator Name
- Francesco Habetswallner
- Principal Investigator Email
- francesco.habetswallner@aocardarelli.it
- Contact Person Name
- Francesco Habetswallner
- Contact Person Email
- francesco.habetswallner@aocardarelli.it
- Site Name
- IRCCS Foundation Istituto Neurologico Carlo Besta
- Department Name
- Unità Neurologia – SC Neurologia 3 - Neuralgologia
- Principal Investigator Name
- Eleonora Dalla Bella
- Principal Investigator Email
- Eleonora.dallabella@istituto-besta.it
- Contact Person Name
- Eleonora Dalla Bella
- Contact Person Email
- Eleonora.dallabella@istituto-besta.it
- Site Name
- Fondazione Istituto Neurologico Nazionale Casimiro Mondino
- Department Name
- U.O. Neuroncologia
- Principal Investigator Name
- Luca Diamanti
- Principal Investigator Email
- Luca.diamandi@mondino.it
- Contact Person Name
- Luca Diamanti
- Contact Person Email
- Luca.diamandi@mondino.it
- Site Name
- Azienda Ospediera Policlinico Universitario Tor Vergata
- Department Name
- UOS Studio e Terapia delle Neuropatie Disimmuni
- Principal Investigator Name
- Girolama Marfia
- Principal Investigator Email
- marfia@med.uniroma2.it
- Contact Person Name
- Girolama Marfia
- Contact Person Email
- marfia@med.uniroma2.it
- Site Name
- Azienda Ospedaliero-Universitaria San Luigi Gonzaga
- Department Name
- SSD Patologie Neurologiche Specialistiche
- Principal Investigator Name
- Marinella Clerico
- Principal Investigator Email
- Marinella.clerico@unito.it
- Contact Person Name
- Marinella Clerico
- Contact Person Email
- Marinella.clerico@unito.it
- Site Name
- Azienda Ospedaliero Universitaria Pisana
- Department Name
- UO Neurologia
- Principal Investigator Name
- Gabriele Siciliano
- Principal Investigator Email
- g.siciliano@med.unipi.it
- Contact Person Name
- Gabriele Siciliano
- Contact Person Email
- g.siciliano@med.unipi.it
Portugal
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 13-05-2024
- Processing Time Days
- 31
- Number Of Sites
- 3
- Number Of Participants
- 6
Sites
- Site Name
- Centro Hospitalar Universitario Sao Joao E.P.E.
- Department Name
- Neurology
- Principal Investigator Name
- Luis Braz
- Principal Investigator Email
- luis.braz@chsj.min-saude.pt
- Contact Person Name
- Luis Braz
- Contact Person Email
- luis.braz@chsj.min-saude.pt
- Site Name
- Unidade Local De Saude De Almada-Seixal E.P.E.
- Department Name
- Neurology
- Principal Investigator Name
- Pedro Pereira
- Principal Investigator Email
- gacic@hgo.min-saude.pt
- Contact Person Name
- Pedro Pereira
- Contact Person Email
- gacic@hgo.min-saude.pt
- Site Name
- CCAB Centro Clinico Academico Braga Associacao
- Department Name
- Neurology
- Principal Investigator Name
- Ricardo Maré
- Principal Investigator Email
- 2ca@ccabraga.org
- Contact Person Name
- Ricardo Maré
- Contact Person Email
- 2ca@ccabraga.org
Greece
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 10-06-2024
- Processing Time Days
- 425
- Number Of Sites
- 3
- Number Of Participants
- 6
Sites
- Site Name
- General Hospital Of Thessaloniki Papageorgiou
- Department Name
- Neurology Clinic
- Principal Investigator Name
- Athanasios Tichalas
- Principal Investigator Email
- atichalas@yahoo.com
- Contact Person Name
- Athanasios Tichalas
- Contact Person Email
- atichalas@yahoo.com
- Site Name
- University General Hospital Of Thessaloniki Ahepa
- Department Name
- 1st Department of Neurology
- Principal Investigator Name
- Vasilios Kimiskidis
- Principal Investigator Email
- kimiskid@auth.gr
- Contact Person Name
- Vasilios Kimiskidis
- Contact Person Email
- kimiskid@auth.gr
- Site Name
- University General Hospital Attikon
- Department Name
- B’ Neurology Clinic
- Principal Investigator Name
- Georgios Tsivgoulis
- Principal Investigator Email
- gtsivou@med.uoa.gr
- Contact Person Name
- Georgios Tsivgoulis
- Contact Person Email
- gtsivou@med.uoa.gr
Germany
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 21-05-2024
- Processing Time Days
- 410
- Number Of Sites
- 8
- Number Of Participants
- 10
Sites
- Site Name
- Martha-Maria Krankenhaus Halle-Doelau gGmbH
- Department Name
- Department of Neurology
- Principal Investigator Name
- Frank Hoffmann
- Principal Investigator Email
- frank.hoffmann@martha-maria.de
- Contact Person Name
- Frank Hoffmann
- Contact Person Email
- frank.hoffmann@martha-maria.de
- Site Name
- Universitaetsklinikum Leipzig AöR
- Department Name
- Studienambulanz Neurologie
- Principal Investigator Name
- Petra Baum
- Principal Investigator Email
- Petra.Baum@medizin.uni-leipzig.de
- Contact Person Name
- Petra Baum
- Contact Person Email
- Petra.Baum@medizin.uni-leipzig.de
- Site Name
- Medizinische Hochschule Hannover
- Department Name
- Klinik für Neurologie
- Principal Investigator Name
- Thomas Skripuletz
- Principal Investigator Email
- skripuletz.thomas@mh-hannover.de
- Contact Person Name
- Thomas Skripuletz
- Contact Person Email
- skripuletz.thomas@mh-hannover.de
- Site Name
- Medizinische Versorgungszentren St. Josefs-Krankenhaus Potsdam GmbH
- Department Name
- Neurology
- Principal Investigator Name
- Alexander Gawlitza
- Principal Investigator Email
- a.gawlitza@alexianer.de
- Contact Person Name
- Alexander Gawlitza
- Contact Person Email
- a.gawlitza@alexianer.de
- Site Name
- Universitaetsmedizin Goettingen
- Department Name
- Dept. of Neurology, University Medical Center Göttingen (UMG)
- Principal Investigator Name
- Jana Zschüntzsch
- Principal Investigator Email
- j.zschuentzsch@med.uni-goettingen.de
- Contact Person Name
- Jana Zschüntzsch
- Contact Person Email
- j.zschuentzsch@med.uni-goettingen.de
- Site Name
- Deutsches Zentrum Fuer Neurodegenerative Erkrankungen e.V.
- Department Name
- Department of Neurology, University of Ulm, and Department of Neurological Rehabilitation
- Principal Investigator Name
- Angela Rosenbohm
- Principal Investigator Email
- angela.rosenbohm@uni-ulm.de
- Contact Person Name
- Angela Rosenbohm
- Contact Person Email
- angela.rosenbohm@uni-ulm.de
- Site Name
- Juedisches Krankenhaus Berlin Stiftung Des Buergerlichen Rechts
- Department Name
- Klinik für Neurologie
- Principal Investigator Name
- Juliane Klehmet
- Principal Investigator Email
- juliane.klehmet@charite.de
- Contact Person Name
- Juliane Klehmet
- Contact Person Email
- juliane.klehmet@charite.de
- Site Name
- Katholisches Klinikum Bochum gGmbH
- Department Name
- Neurologische Universitätsklinik am St. Josef Hospital
- Principal Investigator Name
- Kalliopi Pitarokoili
- Principal Investigator Email
- kalliopi.pitarokoili@ruhr-uni-bochum.de
- Contact Person Name
- Kalliopi Pitarokoili
- Contact Person Email
- kalliopi.pitarokoili@ruhr-uni-bochum.de
Poland
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 13-05-2024
- Processing Time Days
- 397
- Number Of Sites
- 2
- Number Of Participants
- 6
Sites
- Site Name
- Clinical Research Center Sp. z o.o. Medic-R sp.k.
- Principal Investigator Name
- Artur Drużdż
- Principal Investigator Email
- artur.druzdz@cr-center.pl
- Contact Person Name
- Artur Drużdż
- Contact Person Email
- artur.druzdz@cr-center.pl
- Site Name
- Clinirem Sp. z o.o.
- Department Name
- Galen Clinic
- Principal Investigator Name
- Urszula Chyrchel-Paszkiewicz
- Principal Investigator Email
- pgluchyrchel@gmail.com
- Contact Person Name
- Urszula Chyrchel-Paszkiewicz
- Contact Person Email
- pgluchyrchel@gmail.com
Czechia
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 14-05-2024
- Processing Time Days
- 393
- Number Of Sites
- 1
- Number Of Participants
- 8
Sites
- Site Name
- Fakultni Nemocnice Hradec Kralove
- Department Name
- Neurologická klinika
- Principal Investigator Name
- Pavel Kunc
- Principal Investigator Email
- pavel.kunc@fnhk.cz
- Contact Person Name
- Pavel Kunc
- Contact Person Email
- pavel.kunc@fnhk.cz
Spain
- Earliest CTIS Part Ii Submission Date
- 12-04-2024
- Latest Decision Or Authorization Date
- 13-05-2024
- Processing Time Days
- 397
- Number Of Sites
- 6
- Number Of Participants
- 14
Sites
- Site Name
- Hospital Universitari Vall D Hebron
- Department Name
- Neurology
- Principal Investigator Name
- María Salvado Figueras
- Principal Investigator Email
- maria.salvado@vhir.org
- Contact Person Name
- María Salvado Figueras
- Contact Person Email
- maria.salvado@vhir.org
- Site Name
- Hospital Universitario Donostia
- Department Name
- Neurology
- Principal Investigator Name
- Roberto Fernández Torron
- Principal Investigator Email
- roberto.fernandeztorron@osakidetza.eus
- Contact Person Name
- Roberto Fernández Torron
- Contact Person Email
- roberto.fernandeztorron@osakidetza.eus
- Site Name
- Hospital General Universitario Dr. Balmis
- Department Name
- Neurology
- Principal Investigator Name
- Carmen Díaz Marin
- Principal Investigator Email
- ensayosneralicante@gmail.com
- Contact Person Name
- Carmen Díaz Marin
- Contact Person Email
- ensayosneralicante@gmail.com
- Site Name
- Hospital Clinico San Carlos
- Department Name
- Neurology
- Principal Investigator Name
- Lucía Galán Dávila
- Principal Investigator Email
- lgaland@salud.madrid.org
- Contact Person Name
- Lucía Galán Dávila
- Contact Person Email
- lgaland@salud.madrid.org
- Site Name
- Hospital Universitario Virgen De La Macarena
- Department Name
- Neurology
- Principal Investigator Name
- Eva María Martínez Fernández
- Principal Investigator Email
- evam.martinez.sspa@juntadeandalucia.es
- Contact Person Name
- Eva María Martínez Fernández
- Contact Person Email
- evam.martinez.sspa@juntadeandalucia.es
- Site Name
- Hospital Universitario Basurto
- Department Name
- Neurology
- Principal Investigator Name
- Solange Kapetanovic Garcia
- Principal Investigator Email
- solange.kapetanovicgarcia@osakidetza.eus
- Contact Person Name
- Solange Kapetanovic Garcia
- Contact Person Email
- solange.kapetanovicgarcia@osakidetza.eus
Sponsor
Primary sponsor
- Full Name
- Janssen Cilag International
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- Belgium
Contract research organisations
- Name
- Icon Clinical Research Limited
- Responsibilities
- Multiple sponsor duties (codes: 1,12,13,14,2,4,5,6,8,9) - per sponsor duties list
- Name
- PRA Hellas CRO A.E.
- Responsibilities
- Local/regional CRO activities (codes: 12,2,8)
- Name
- Bioclinica Inc.
- Responsibilities
- Adjudication
- Name
- Iqvia Inc.
- Responsibilities
- Clinical Outcome Assessments / Rater Services
Third parties
- {"country":"Switzerland","full_name":"MindMaze SA","duties_or_roles":"Provider of Gait Assessment (code 15 / value: Provider of Gait Assessment)","organisation_type":"Pharmaceutical company"}
- {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"Codes: 1,12,13,14,2,4,5,6,8,9 (multiple sponsor duties codes listed)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"Adjudication (code 15 / value: Adjudication)","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"Greece","full_name":"PRA Hellas CRO A.E.","duties_or_roles":"Codes: 12,2,8","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Almac Clinical Services LLC","duties_or_roles":"Drug Destruction (code 15 / value: Drug Destruction)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"Code: 4","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"The Andwin Corp.","duties_or_roles":"Vigorimeter (code 15 / value: Vigorimeter)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Meeting Protocol Worldwide LP","duties_or_roles":"patient reimbursement and Investigator meeting planning (code 15 / value: patient reimbursement and Investigator meeting planning)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Ancillare LP","duties_or_roles":"Ancillary supplies (code 15 / value: Ancillary supplies)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Iqvia Inc.","duties_or_roles":"Clinical Outcome Assessments / Rater Services (code 15 / value: Clinical Outcome Assessments / Rater Services)","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Imperial Clinical Research Services International Limited","duties_or_roles":"printing services (code 15 / value: printing services)","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"EDC (code 15 / value: EDC)","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"4g Clinical LLC","duties_or_roles":"Code: 3","organisation_type":"Non-Pharmaceutical company"}
Investigational products
- Investigational Product Name
- JNJ-80202135
- Active Substance
- NIPOCALIMAB
- Modality
- Monoclonal antibody
- Routes Of Administration
- Solution for infusion / Intravenous use
- Route
- Intravenous
- Authorisation Status
- Not authorised (investigational product; no marketing authorisation number listed)
- Investigational Product Name
- Privigen 100 mg/ml solution for infusion
- Active Substance
- HUMAN NORMAL IMMUNOGLOBULIN
- Modality
- Other antibody
- Routes Of Administration
- Intravenous use / Solution for infusion
- Route
- Intravenous
- Authorisation Status
- Authorised (marketing authorisation EU/1/08/446/001)
- Investigational Product Name
- Saline, 0.9% Sodium Chloride Solution for Injection
- Modality
- Other
- Authorisation Status
- Not specified (placebo/control)
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