Clinical trials

  • BEZAFIBRATE for Primary sclerosing cholangitis
  • Pasireotide for Synovial sarcoma | Desmoplastic small round cell tumor
  • OXALIPLATIN for Rectal cancer | Intermediate and high-risk rectal cancer
  • BMN 351 for Duchenne muscular dystrophy
  • ARIPIPRAZOLE for Autism spectrum disorder
  • APITEGROMAB for Spinal muscular atrophy (Type 2)|Spinal muscular atrophy (Type 3)
  • RMC-6291 for Non-small cell lung cancer | Pancreatic ductal adenocarcinoma | Advanced solid tumor | Colorectal cancer
  • QUEMLICLUSTAT for Upper gastrointestinal tract cancer | Advanced upper gastrointestinal tract malignancies | Gastrointestinal tract malignancies
  • IDROXIOLEIC ACID for Glioblastoma (newly diagnosed)
  • CEMIPLIMAB for Cutaneous squamous cell carcinoma
  • DARATUMUMAB for Rheumatoid arthritis
  • 5,8-DICHLORO-2-[(4-METHOXY-6-METHYL-2-OXO-1,2-DIHYDROPYRIDIN-3-YL)METHYL]-7-[(R)-METHOXY(OXETAN-3-YL)METHYL]-3,4-DIHYDROISOQUINOLIN-1(2H)-ONE for Metastatic castration-resistant prostate cancer