Clinical trial • Phase III • Oncology

CEMIPLIMAB for Cutaneous squamous cell carcinoma

Phase III trial of CEMIPLIMAB for Cutaneous squamous cell carcinoma.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Cutaneous squamous cell carcinoma
Trial Stage
Phase III
Drug Modality
Monoclonal antibody

Key dates

Initial CTIS Submission Date
21-05-2024
First CTIS Authorization Date
26-06-2024

Trial design

Randomised, libtayo (cemiplimab) 350 mg concentrate for solution for infusion; matching placebo with r2810 — dosing schedule not specified in the provided data.-controlled Phase III trial across 43 sites in France, Italy, Germany and others.

Randomised
Yes
Comparator
LIBTAYO (cemiplimab) 350 mg concentrate for solution for infusion; matching Placebo with R2810 — dosing schedule not specified in the provided data.
Target Sample Size
279

Eligibility

Recruits 279 Vulnerable population selected (isVulnerablePopulationSelected = true). Country-specific subject information and informed consent forms are listed in the trial documents (multiple L1_SIS-ICF documents for different countries/languages). No explicit text about assent or specific consent-by-proxy procedures for vulnerable subgroups is available in the provided CTIS JSON..

Vulnerable Population
Vulnerable population selected (isVulnerablePopulationSelected = true). Country-specific subject information and informed consent forms are listed in the trial documents (multiple L1_SIS-ICF documents for different countries/languages). No explicit text about assent or specific consent-by-proxy procedures for vulnerable subgroups is available in the provided CTIS JSON.

Inclusion criteria

  • {"criterion_text":"- Patient with resection of pathologically confirmed CSCC (primary CSCC lesion only, or primary CSCC with nodal involvement, or CSCC nodal metastasis with known primary CSCC lesion previously treated within the draining lymph node echelon), with macroscopic gross resection of all disease"}
  • {"criterion_text":"- High risk CSCC"}
  • {"criterion_text":"- Completion of curative intent post-operative radiation therapy (RT) within 2 to 10 weeks of randomization"}
  • {"criterion_text":"- Eastern Cooperative Oncology Group performance status (ECOG PS) ≤1"}
  • {"criterion_text":"- Adequate hepatic, renal, and bone marrow function as defined in the protocol"}

Exclusion criteria

  • {"criterion_text":"- Squamous cell carcinomas (SCCs) arising in non-cutaneous sites as defined in the protocol Concurrent malignancy other than localized CSCC and/or history of malignancy other than localized CSCC within 3 years of date of randomization as defined in the protocol"}
  • {"criterion_text":"- Patients with hematologic malignancies (note: patients with chronic lymphocytic leukemia (CLL) are not excluded if they have not required systemic therapy for CLL within 6 months of enrollment)"}
  • {"criterion_text":"- Patients with history of distantly metastatic CSCC (visceral or distant nodal), unless the disease-free interval is at least 3 years (regional nodal involvement of disease in draining lymph node basin that was resected and radiated prior to enrollment will not be exclusionary)"}
  • {"criterion_text":"- Ongoing or recent (within 5 years of randomization date) evidence of significant autoimmune disease that required treatment with systemic immunosuppressive treatments, which may suggest risk for immune-related adverse events (irAEs). The following are not exclusionary: vitiligo, childhood asthma that has resolved, type 1 diabetes, residual hypothyroidism that required only hormone replacement, or psoriasis that does not require systemic treatment."}
  • {"criterion_text":"- Has had prior systemic anti-cancer immunotherapy for CSCC"}
  • {"criterion_text":"- Note: Other protocol defined Inclusion/Exclusion criteria apply"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- DFS defined as time from randomization to the first documented disease recurrence (local, regional and/or distant); or death due to any cause.","definition_or_measurement_approach":"Defined as time from randomization to the first documented disease recurrence (local, regional and/or distant) or death from any cause (time-to-event)."}

Secondary endpoints

  • {"endpoint_text":"- Overall survival (OS), defined as time from randomization to the date of death.","definition_or_measurement_approach":"Defined as time from randomization to date of death (time-to-event)."}
  • {"endpoint_text":"- FFLRR defined as time from randomization to the date of first locoregional recurrence (LRR).","definition_or_measurement_approach":"Defined as time from randomization to date of first locoregional recurrence (time-to-event)."}
  • {"endpoint_text":"- Freedom from distant recurrence (FFDR), defined as time from randomization to the date of first distant recurrence (DR). Patients who died without a preceding DR will be censored on the date of death.","definition_or_measurement_approach":"Defined as time from randomization to date of first distant recurrence; patients who die without prior distant recurrence are censored at death (time-to-event with censoring rules specified)."}
  • {"endpoint_text":"- Cumulative occurrence of second primary cutaneous squamous cell carcinoma tumor (SPTs) for each patient from randomization to occurrence of first primary endpoint event or end of study.","definition_or_measurement_approach":"Cumulative incidence of second primary CSCC from randomization until the first primary endpoint event or end of study."}
  • {"endpoint_text":"- Safety, as measured by the incidence and severity of treatment-emergent adverse events (TEAE), deaths, and laboratory abnormalities.","definition_or_measurement_approach":"Safety assessed by incidence and severity of TEAEs, deaths, and laboratory abnormalities (standard safety reporting)."}
  • {"endpoint_text":"- Cemiplimab concentrations in serum and immunogenicity as measured in ADA in serum","definition_or_measurement_approach":"Pharmacokinetic assessment of cemiplimab serum concentrations and immunogenicity measured by anti-drug antibodies (ADA) in serum."}

Recruitment

Planned Sample Size
279
Recruitment Window Months
117
Consent Approach
Informed consent is obtained using country-specific subject information and informed consent form documents (multiple L1_SIS-ICF documents listed for France, Italy, Germany, Poland, Spain, Greece, Belgium, Ireland etc.). Documents include main ICF parts, pregnant partner information forms and specific local-language versions. The CTIS JSON lists functional contact 'Clinical Trial Information' and country-specific ICF document files but the provided data does not contain verbatim consent/assent process text or explicit age-specific assent procedures.

Geography

Total Number Of Sites
43
Total Number Of Participants
279

France

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
26-06-2024
Processing Time Days
22
Number Of Sites
10
Number Of Participants
16

Sites

Site Name
Hopital Ambroise Pare
Department Name
Dermatology and Oncology
Contact Person Name
Philippe Saiag
Contact Person Email
philippe.saiag@uvsq.fr
Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Dermato-oncology
Contact Person Name
Marie Beylot-Barry
Site Name
Centre Leon Berard
Department Name
Medical Oncology
Contact Person Name
Eve-Marie Neidhardt
Site Name
Centre Hospitalier Universitaire Rouen
Department Name
Dermatology
Contact Person Name
Anne Bendicte Duval Modeste
Contact Person Email
ab.duval-modeste@chu-rouen.fr
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Dermatology
Contact Person Name
Henri Montaudie
Contact Person Email
montaudie.h@chu-nice.fr
Site Name
Hospices Civils De Lyon
Department Name
Dermatology
Contact Person Name
Stephane Dalle
Contact Person Email
stephane.dalle@chu-lyon.fr
Site Name
Hospital Hotel Dieu
Department Name
Dermatology
Contact Person Name
Gaelle Quereux
Contact Person Email
gaelle.quereux@chu-nantes.fr
Site Name
Centre Hospitalier Universitaire Grenoble Alpes
Department Name
Dermatology
Contact Person Name
Marie Enquebecq
Contact Person Email
menquebecq@chu-grenoble.fr
Site Name
Centre Hospitalier Universitaire De Dijon
Department Name
Dermatology
Contact Person Name
Geraldine Jeudy
Contact Person Email
geraldine.jeudy@chu-dijon.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Dermatology
Contact Person Name
Laurent Mortier
Contact Person Email
laurent.mortier@chru-lille.fr

Italy

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
01-07-2024
Processing Time Days
27
Number Of Sites
8
Number Of Participants
21

Sites

Site Name
Azienda USL Toscana Centro
Department Name
Medical Oncology
Contact Person Name
Vincenzo De Giorgi
Contact Person Email
vincenzo.degiorgi@unifi.it
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
Dermatology
Contact Person Name
Ketty Peris
Contact Person Email
ketty.peris@unicatt.it
Site Name
Universita Degli Studi Di Brescia
Department Name
Oncology
Contact Person Name
Valeria Tovazzi
Contact Person Email
valeria.tovazzi@gmail.com
Site Name
Alma Mater Studiorum Universita Di Bologna
Department Name
Dermatology
Contact Person Name
Emi Dika
Contact Person Email
emi.dika3@unibo.it
Site Name
Istituto Europeo Di Oncologia S.r.l.
Department Name
Oncology Melanoma, Sarcoma and Rare Tumors
Contact Person Name
Carolina Cimminiello
Contact Person Email
carolina.cimminiello@ieo.it
Site Name
Humanitas Mirasole S.p.A.
Department Name
Medical Oncology
Contact Person Name
Paolo Bossi
Contact Person Email
paolo.bossi@hunimed.eu
Site Name
Istituto Nazionale Dei Tumori
Department Name
Oncology
Contact Person Name
Paolo Antonio Ascierto
Contact Person Email
paolo.ascierto@gmail.com
Site Name
Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
Department Name
Dermatology
Contact Person Name
Pietro Quaglino
Contact Person Email
pietro.quaglino@unito.it

Germany

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
27-06-2024
Processing Time Days
23
Number Of Sites
9
Number Of Participants
18

Sites

Site Name
SLK-Kliniken Heilbronn GmbH
Department Name
Hematology/Oncology
Contact Person Name
Uwe Martens
Contact Person Email
uwe.martens@slk-kliniken.de
Site Name
University Hospital Cologne AöR
Department Name
Dermatology
Contact Person Name
Nicole Kreuzberg
Contact Person Email
nicole.kreuzberg@uk-koeln.de
Site Name
Klinikum der Universitaet Muenchen AöR
Department Name
Dermato-oncology
Contact Person Name
Lucie Heinzerling
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Dermatology
Contact Person Name
Lukas Flatz
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Dermato-oncology
Contact Person Name
Axel Hauschild
Site Name
Universitaetsklinikum Heidelberg AöR
Department Name
Dermato-oncology
Contact Person Name
Jessica Cecile Hassel
Site Name
Universitaetsklinikum Carl Gustav Carus Dresden
Department Name
Dermatology
Contact Person Name
Friedegund Meier
Site Name
Universitaetsklinikum Essen AöR
Department Name
Dermatology
Contact Person Name
Dirk Schadendorf
Contact Person Email
dirk.schadendorf@uk-essen.de
Site Name
Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
Department Name
Dermatology
Contact Person Name
Stephan Grabbe

Poland

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
23-07-2024
Processing Time Days
49
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy
Department Name
Nowotwór Tkanek Miękkich, Kości i Czerniaków
Contact Person Name
Piotr Rutkowski
Contact Person Email
rutkowskip@coi.waw.pl

Spain

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
26-06-2024
Processing Time Days
22
Number Of Sites
9
Number Of Participants
11

Sites

Site Name
Instituto De Investigacion En Ciencias De La Salud Germans Trias I Pujol
Department Name
Oncology
Contact Person Name
Cristina Buges Sanchez
Contact Person Email
cbuges@iconcologia.net
Site Name
Clinica Universidad De Navarra
Department Name
Clinical Oncology
Contact Person Name
Eduardo Castanon Alvarez
Contact Person Email
ecastanon@unav.es
Site Name
Hospital General Universitario Gregorio Maranon
Department Name
Medical Oncology
Contact Person Name
Ivan Marquez Rodas
Contact Person Email
ivanpantic@hotmail.com
Site Name
Genesis Care Hospital San Francisco de Asis
Department Name
Medical Oncology
Contact Person Name
Jose Angel Garcia Cuesta
Contact Person Email
jose.garcia@genesiscare.es
Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Medical Oncology
Contact Person Name
Roberto Pedro Diaz Beveridge
Contact Person Email
diaz_rob@gva.es
Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Dermatology
Contact Person Name
Lucia Turrion Merino
Contact Person Email
luciaturrion@gmail.com
Site Name
Hospital Clinic De Barcelona
Department Name
Dermatology
Contact Person Name
Susana Puig Sarda
Contact Person Email
susipuig@gmail.com
Site Name
Fundacion Instituto Valenciano De Oncologia
Department Name
Medical Oncology
Contact Person Name
Hector Augusto Aguilar Andino
Contact Person Email
haguilar@fivo.org
Site Name
Hospital Universitario De Salamanca
Department Name
Dermatology
Contact Person Name
Javier Canueto Alvarez
Contact Person Email
jcanueto@usal.es

Greece

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
19-07-2024
Processing Time Days
45
Number Of Sites
2
Number Of Participants
3

Sites

Site Name
Andreas Syngros Hospital Of Venereal And Dermatological Diseases
Department Name
University Dermatology and Venereology Clinic
Contact Person Name
Alexander Stratigos
Contact Person Email
msm@syggros.gr
Site Name
Ippokratio General Hospital Of Thessaloniki
Department Name
1st Department of Dermatology Clinic AUTH
Contact Person Name
Aimilios Lallas

Belgium

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
26-06-2024
Processing Time Days
22
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
UZ Leuven
Department Name
Oncology
Contact Person Name
Oliver Bechter
Contact Person Email
oliver.bechter@uzleuven.be

Ireland

Earliest CTIS Part Ii Submission Date
04-06-2024
Latest Decision Or Authorization Date
26-06-2024
Processing Time Days
22
Number Of Sites
3
Number Of Participants
5

Sites

Site Name
University Hospital Galway
Department Name
Medical Oncology
Contact Person Name
Paul Donnellan
Contact Person Email
paul.donnellan@hse.ie
Site Name
Cork University Maternity Hospital
Department Name
Medical Oncology
Contact Person Name
Derek Power
Contact Person Email
derek.power1@hse.ie
Site Name
St Vincent's University Hospital
Department Name
Medical Oncology
Contact Person Name
John Crown
Contact Person Email
john.crown@ccrt.ie

Sponsor

Primary sponsor

Full Name
Regeneron Pharmaceuticals Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Icon Clinical Research Limited
Responsibilities
CRO, Clinical database Management and Independent Data Monitoring Committee
Name
Icon Public Limited Company
Responsibilities
Reading Centers - Reading CT Scans and MRIs
Name
Excelya Greece CRO Single Member S.A.
Responsibilities
Start-up, RA and EC submissions, site contracting and site payments management

Third parties

  • {"country":"Slovakia","full_name":"SanaClis s.r.o.","duties_or_roles":"Investigational Product Distribution to Sites, Return, and Destruction","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Ventana Medical Systems Inc.","duties_or_roles":"Speciality laboratory - PDL1 IHC Testing","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Icon Public Limited Company","duties_or_roles":"Reading Centers - Reading CT Scans and MRIs","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Fisher Clinical Services Inc.","duties_or_roles":"Investigational Product Packaging","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Q Squared Solutions LLC","duties_or_roles":"Central Laboratory - sample analysis and storage","organisation_type":"Industry"}
  • {"country":"United States","full_name":"Yprime LLC","duties_or_roles":"Interactive Voice Response System/ Interactive Web Response System","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Icon Clinical Research (U.K.) Limited","duties_or_roles":"Pharmacovigilience Services","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Personalis Inc.","duties_or_roles":"Specialty Lab (MRD ctDNA analysis)","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Andersonbrecon Inc.","duties_or_roles":"Investigational Product Distribution to Sites, Return, and Destruction","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Q Squared Solutions LLC","duties_or_roles":"Central Laboratory - sample analysis and storage","organisation_type":"Industry"}
  • {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"CRO, Clinical database Management and Independent Data Monitoring Committee","organisation_type":"Pharmaceutical company"}
  • {"country":"Greece","full_name":"Excelya Greece CRO Single Member S.A.","duties_or_roles":"Start-up, RA and EC submissions, site contracting and site payments management","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"University Of Wisconsin","duties_or_roles":"Independent Statistics Vendor","organisation_type":"Educational Institution"}
  • {"country":"United States","full_name":"Yprime LLC","duties_or_roles":"eCOA","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Acumen Medical Communications LLC","duties_or_roles":"Patient Safety narratives","organisation_type":"Pharmaceutical company"}
  • {"country":"Australia","full_name":"Trans Tasman Radiation Oncology Group Limited","duties_or_roles":"RT Plan data collection and review","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Ireland","full_name":"Icon (Lr) Limited","duties_or_roles":"Pharmaceutical Research Associates Greece A.E (Affiliated company of ICON Clinical Research Limited) - Site visits and monitoring activities","organisation_type":"Non-Pharmaceutical company"}

Investigational products

Investigational Product Name
LIBTAYO 350 mg concentrate for solution for infusion.
Active Substance
CEMIPLIMAB
Modality
Monoclonal antibody
Routes Of Administration
IV INFUSION
Route
IV INFUSION
Authorisation Status
Authorised (marketing authorisation present: EU/1/19/1376/001)
Maximum Dose
700 mg (maxDailyDoseAmount indicated in product data)
Investigational Product Name
matching Placebo with R2810
Modality
Other
Authorisation Status
Not authorised / N/A

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