Clinical trial • Phase II|Phase IV • Ophthalmology

SURABGENE LOMPARVOVEC for Neovascular age-related macular degeneration

Phase II|Phase IV trial of SURABGENE LOMPARVOVEC for Neovascular age-related macular degeneration. None/Not specified-controlled. 1301 participants.

Overview

Trial Therapeutic Area
Ophthalmology
Trial Disease
Neovascular age-related macular degeneration
Trial Stage
Phase II|Phase IV
Drug Modality
Gene therapy

Key dates

Initial CTIS Submission Date
28-03-2025
First CTIS Authorization Date
14-07-2025

Trial design

None/Not specified-controlled Phase II|Phase IV trial in France, Hungary, Italy and others.

Comparator
None/Not specified
Target Sample Size
1301
Trial Duration For Participant
1831

Eligibility

Recruits 1301 No vulnerable population selected; participants must be able and willing to provide written, signed informed consent for this study..

Vulnerable Population
No vulnerable population selected; participants must be able and willing to provide written, signed informed consent for this study.

Inclusion criteria

  • {"criterion_text":"- Able and willing to provide written, signed informed consent for this study"}
  • {"criterion_text":"- Previously enrolled in a clinical study of ABBV-RGX-314 subretinal administration for the treatment of nAMD and must have received treatment in that study"}
  • {"criterion_text":"- Must be willing and able to comply with all study procedures"}

Exclusion criteria

  • {"criterion_text":"- Not Applicable"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Incidence of ocular adverse events (AEs) and any serious adverse events (SAEs)","definition_or_measurement_approach":"Incidence (count/rate) of ocular AEs and any SAEs as reported in study follow-up (no further definition provided in source JSON)"}

Secondary endpoints

  • {"endpoint_text":"- Incidence of non-ocular AEs and any adverse events of special interest (AESIs)","definition_or_measurement_approach":"Incidence (count/rate) of non-ocular AEs and AESIs as reported in study follow-up"}
  • {"endpoint_text":"- Mean change from baseline (ie, prior to ABBV-RGX-314 administration in the parent study) in BCVA","definition_or_measurement_approach":"Mean change in BCVA from baseline (prior to ABBV-RGX-314 in parent study); BCVA measured (translations reference ETDRS scoring in related translation)"}
  • {"endpoint_text":"- Proportion of participants losing letters in BCVA compared with baseline (ie, prior to ABBV-RGX 314 administration in the parent study) in the study eye at assessed timepoints","definition_or_measurement_approach":"Proportion losing ≥5, 10 and 15 letters in BCVA compared with baseline at assessed timepoints (BCVA/ETDRS)"}
  • {"endpoint_text":"- Mean change from baseline (ie, prior to ABBV-RGX-314 administration in the parent study) in CRT as measured by SD-OCT in the study eye at assessed timepoints","definition_or_measurement_approach":"Mean change in central retinal thickness (CRT) measured by spectral domain optical coherence tomography (SD-OCT) from baseline"}
  • {"endpoint_text":"- Mean supplemental anti-VEGF injection annualized rate through years 2, 3, 4, and 5 based on ongoing chart review in the study eye","definition_or_measurement_approach":"Annualized rate of supplemental anti-VEGF injections through years 2–5 based on ongoing chart review"}
  • {"endpoint_text":"- Mean supplemental anti-VEGF injection annualized rate in years 2, 3, 4, and 5 based on ongoing chart review in the study eye","definition_or_measurement_approach":"Annualized rate of supplemental anti-VEGF injections in years 2–5 based on ongoing chart review"}
  • {"endpoint_text":"- Mean number of supplemental anti-VEGF injections through years 2, 3, 4, and 5 based on ongoing chart review in the study eye","definition_or_measurement_approach":"Mean number of supplemental anti-VEGF injections through years 2–5 based on chart review"}
  • {"endpoint_text":"- Mean number of supplemental anti-VEGF injections in years 2, 3, 4, and 5 based on ongoing chart review in the study eye","definition_or_measurement_approach":"Mean number of supplemental anti-VEGF injections in years 2–5 based on chart review"}
  • {"endpoint_text":"- Mean number of retina specialist visits attended for nAMD through years 2, 3, 4, and 5 based on ongoing chart review","definition_or_measurement_approach":"Mean number of retina specialist visits for nAMD through years 2–5 based on chart review"}
  • {"endpoint_text":"- Mean number of retina specialist visits attended for nAMD in years 2, 3, 4, and 5 based on ongoing chart review","definition_or_measurement_approach":"Mean number of retina specialist visits for nAMD in years 2–5 based on chart review"}

Recruitment

Planned Sample Size
1301
Recruitment Window Months
60
Consent Approach
Participants must be able and willing to provide written, signed informed consent for this study. Subject information and informed consent documents are provided (country-specific versions listed for FR, HU, IT, ES, DE). No assent/parental consent procedures listed (no paediatric population selected).

Geography

Total Number Of Sites
39
Total Number Of Participants
84

France

Earliest CTIS Part Ii Submission Date
03-07-2025
Latest Decision Or Authorization Date
16-07-2025
Processing Time Days
13
Number Of Sites
10
Number Of Participants
19

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Ophtalmopole de Paris
Contact Person Name
Francine Behar-Cohen
Contact Person Email
Francine.behar@gmail.com
Site Name
Hospices Civils De Lyon
Department Name
Ophthalmology
Contact Person Name
Laurent Kodjikian
Contact Person Email
Laurent.kodjikian@chu-lyon.fr
Site Name
Centre Monticelli Paradis D Ophtalmologie
Department Name
Ophthalmology
Contact Person Name
Francois Devin
Contact Person Email
Fdbm.retine@gmail.com
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Ophthalmology
Contact Person Name
Aude Couturier
Contact Person Email
Aude.couturier@aphp.fr
Site Name
Centre Hospitalier Intercommunal Creteil
Department Name
Ophthalmology
Contact Person Name
Eric Souied
Contact Person Email
Eric.souied@chicreteil.fr
Site Name
Clinique Honore Cave
Department Name
Ophthalmology
Contact Person Name
Vincent Gualiano
Contact Person Email
Recherche-chc@hotmail.com
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Ophthalmology
Contact Person Name
Stephanie Baillif
Contact Person Email
Baillif.s@chu-nice.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Ophthalmology Department
Contact Person Name
Vincent Soler
Contact Person Email
Soler.v@chu-toulouse.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Ophthalmology Department
Contact Person Name
Olivier Lebreton
Contact Person Email
Olivier.lebreton@chu-nantes.fr
Site Name
Centre Hospitalier Universitaire De Dijon
Department Name
Ophthalmology
Contact Person Name
Catherine Creuzot-Garcher

Hungary

Earliest CTIS Part Ii Submission Date
15-05-2025
Latest Decision Or Authorization Date
18-07-2025
Processing Time Days
64
Number Of Sites
3
Number Of Participants
7

Sites

Site Name
Nozologen Kft.
Contact Person Name
Balazs Varsanyi
Contact Person Email
varsanyi.balazs@gmail.com
Site Name
Budapest Retina Associates Kft.
Contact Person Name
András Seres
Contact Person Email
seres@budapestretina.hu
Site Name
University Of Debrecen
Contact Person Name
Attila Vajas
Contact Person Email
vajasa@gmail.com

Italy

Earliest CTIS Part Ii Submission Date
08-07-2025
Latest Decision Or Authorization Date
06-02-2026
Processing Time Days
213
Number Of Sites
10
Number Of Participants
24

Sites

Site Name
University Hospital Of Ferrara
Department Name
Unità Operativa di Clinica Oculistica
Contact Person Name
Marco Mura
Contact Person Email
mrumrc@unife.it
Site Name
Azienda Universitaria Ospedaliera Consorziale Policlinico Bari
Department Name
UO Oftalmologia Universitaria
Contact Person Name
Francesco Boscia
Contact Person Email
francescoboscia@hotmail.com
Site Name
Azienda Ospedaliera Universitaria Universita' Degli Studi Della Campania Luigi Vanvitelli
Department Name
D.A.I. Medico-Chirurgico ad Alta Specialità — Clinica Oculistica
Contact Person Name
Michele Della Corte
Site Name
Azienda Sanitaria Universitaria Friuli Centrale
Department Name
SOC Clinica oculistica
Contact Person Name
Paolo Lanzetta
Contact Person Email
paolo.lanzetta@uniud.it
Site Name
Azienda Sanitaria Locale 2 Lanciano Vasto Chieti
Department Name
U.O.C. Riabilitazione Visiva Chirurgica
Contact Person Name
Rodolfo Mastropasqua
Contact Person Email
rodolfo.mastropasqua@unich.it
Site Name
ASST Fatebenefratelli Sacco
Department Name
Eye Clinic
Contact Person Name
Matteo Giuseppe Cereda
Site Name
IRCCS Ospedale Sacro Cuore Don Calabria
Department Name
Oculistica
Contact Person Name
Grazia Pertile
Contact Person Email
grazia.pertile@gmail.com
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
UOC Oculistica
Contact Person Name
Angelo Maria Minnella
Site Name
Ospedale San Raffaele S.r.l.
Department Name
Unità di Oculistica
Contact Person Name
Francesco Bandello
Contact Person Email
bandello.francesco@hsr.it
Site Name
Fondazione G.B.Bietti Per Lo Studio E La Ricerca In Oftalmologia
Department Name
UOC di Oftalmologia
Contact Person Name
Tommaso Rossi

Spain

Earliest CTIS Part Ii Submission Date
12-06-2025
Latest Decision Or Authorization Date
16-07-2025
Processing Time Days
34
Number Of Sites
10
Number Of Participants
22

Sites

Site Name
Clinica Baviera S.A.
Department Name
Ophthalmology
Contact Person Name
Marta Suárez de Figueroa
Contact Person Email
figueroa.marta@outlook.es
Site Name
Metavision Arruzafa S.L.
Department Name
Ophthalmology
Contact Person Name
Juan Manuel Cubero Parra
Contact Person Email
jmcubero@hospitalarruzafa.com
Site Name
Bellvitge University Hospital
Department Name
Ophthalmology
Contact Person Name
Luis Arias Barquet
Contact Person Email
luisariasbarquet@gmail.com
Site Name
Hospital Clinic De Barcelona
Department Name
Ophthalmology
Contact Person Name
Anna Sala Puigdollers
Contact Person Email
ansala@clinic.cat
Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Ophthalmology
Contact Person Name
Jose María Ruíz Moreno
Contact Person Email
josemaria.ruiz@uclm.es
Site Name
Hospital Universitario 12 De Octubre
Department Name
Ophthalmology
Contact Person Name
Luis Francisco Moreno García
Site Name
Hospital Provincial De Conxo
Department Name
Ophthalmology
Contact Person Name
Maximino José Abraldes López-Veiga
Contact Person Email
maxiabraldes@gmail.com
Site Name
Complejo Hospitalario Universitario Insular Materno Infantil
Department Name
Ophthalmology
Contact Person Name
Francisco Cabrera López
Contact Person Email
pacooft@gmail.com
Site Name
Instituto De Microcirugia Ocular Dos S.L.
Department Name
Ophthalmology
Contact Person Name
Rafael Navarro Alemany
Contact Person Email
rafael.navarro@imo.es
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Ophthalmology
Contact Person Name
José Ignacio Vela Segarra
Contact Person Email
ivela@santpau.cat

Germany

Earliest CTIS Part Ii Submission Date
26-06-2025
Latest Decision Or Authorization Date
23-01-2026
Processing Time Days
211
Number Of Sites
6
Number Of Participants
12

Sites

Site Name
Medical Center - University Of Freiburg
Contact Person Name
Hansjuergen Agostini
Site Name
Klinikum der Stadt Ludwigshafen am Rhein gGmbH
Contact Person Name
Lars-Olof Hattenbach
Contact Person Email
Hattenbach.studien@klilu.de
Site Name
Universitaetsklinikum Ulm AöR
Department Name
Abteilung für Augenheilkunde
Contact Person Name
Armin Wolf
Contact Person Email
Armin.wolf@uniklinikum-ulm.de
Site Name
Universitaet Muenster
Department Name
Klinik fuer Augenheilkunde
Contact Person Name
Nicole Eter
Site Name
Universitaetsklinikum Bonn AöR
Department Name
Department Ophthalmology
Contact Person Name
Kristina Pfau
Contact Person Email
kristina.pfau@ukbonn.de
Site Name
University Medical Center Hamburg-Eppendorf
Department Name
Klinik und Poliklinik für Augenheilkunde
Contact Person Name
Martin Spitzer
Contact Person Email
m.spitzer@uke.de

Sponsor

Primary sponsor

Full Name
AbbVie Deutschland GmbH & Co. KG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Germany

Contract research organisations

Name
Syneos Health Netherlands B.V.
Name
Merit CRO Inc.
Responsibilities
Imaging center

Third parties

  • {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Patient compensation","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Transperfect Translations International Inc.","duties_or_roles":"Translation services","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Optymedge LLC","duties_or_roles":"Visual acuity examiner and lane certification","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Netherlands","full_name":"Syneos Health Netherlands B.V.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Merit CRO Inc.","duties_or_roles":"Imaging center","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Surabgene Lomparvovec (ABBV-RGX-314)
Active Substance
SURABGENE LOMPARVOVEC
Modality
Gene therapy
Routes Of Administration
SUBRETINAL USE
Route
Subretinal

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