Clinical trial • Phase III | Phase IV • Ophthalmology

FARICIMAB for Neovascular age-related macular degeneration

Phase III | Phase IV trial of FARICIMAB for Neovascular age-related macular degeneration.

Overview

Trial Therapeutic Area
Ophthalmology
Trial Disease
Neovascular age-related macular degeneration
Trial Stage
Phase III | Phase IV
Drug Modality
Bispecific antibody

Key dates

Initial CTIS Submission Date
12-02-2025
First CTIS Authorization Date
02-06-2025

Trial design

Randomised, open-label, faricimab regimens in two arms: arm a (regimen exploring potential to reduce treatment burden associated with the initial loading period) vs arm b (treatment regimen based on the design of the lucerne and tenaya studies). specific doses and schedules not specified in the provided record.-controlled Phase III | Phase IV trial across 24 sites in France, Germany, Italy and others.

Randomised
Yes
Open Label
Yes
Comparator
Faricimab regimens in two arms: Arm A (regimen exploring potential to reduce treatment burden associated with the initial loading period) vs Arm B (treatment regimen based on the design of the Lucerne and Tenaya studies). Specific doses and schedules not specified in the provided record.
Target Sample Size
185

Eligibility

Recruits 185 Vulnerable population selected. Subject information and informed consent documents listed include 'L1_SIS and IAF infant authorization' and 'L1_SIS and ICF Infant Health' (infant authorization documents) and multiple ICF/SIS documents for adults, indicating specific consent/authorization materials for infants and other subjects are provided..

Vulnerable Population
Vulnerable population selected. Subject information and informed consent documents listed include 'L1_SIS and IAF infant authorization' and 'L1_SIS and ICF Infant Health' (infant authorization documents) and multiple ICF/SIS documents for adults, indicating specific consent/authorization materials for infants and other subjects are provided.

Inclusion criteria

  • {"criterion_text":"- Age ≥50 years at the time of signing Informed Consent Form"}
  • {"criterion_text":"- Overtly healthy as determined by medical evaluation that includes medical history and physical examination."}
  • {"criterion_text":"- Agreement to adhere to the contraception requirements described"}
  • {"criterion_text":"- Ocular Inclusion Criteria for Study Eye: Active treatment-naïve macular neovascularization (MNV) secondary to age-related macular degeneration (AMD), confirmed by the Investigator based on the presence of intraretinal fluid (IRF) or subretinal fluid (SRF) affecting the central subfield on OCT."}
  • {"criterion_text":"- Ocular Inclusion Criteria for Study Eye: BCVA of 83 to 24 letters, inclusive (20/25 to 20/320 approximate Snellen equivalent, using the early treatment diabetic retinopathy study (ETDRS) protocol and addressed at the initial testing distance of 4 meters on Day 1)."}
  • {"criterion_text":"- Ocular Inclusion Criteria for Study Eye:Sufficiently clear ocular media and adequate pupillary dilation to allow acquisition of good quality retinal images to confirm diagnosis."}

Exclusion criteria

  • {"criterion_text":"- Macular neovascularization due to causes other than AMD, such as ocular histoplasmosis, trauma, pathological myopia, angioid streaks, choroidal rupture, or uveitis."}
  • {"criterion_text":"- Retinal pigment epithelial tear involving the macula on Day 1"}
  • {"criterion_text":"- Current vitreous hemorrhage on Day 1"}
  • {"criterion_text":"- Prior periocular pharmacological or IVT treatment (including faricimab, anti-vascular endothelial growth factor (VEGF), or complement inhibitor medication) for other retinal diseases"}
  • {"criterion_text":"- Ocular Exclusion Criteria for Fellow (Non-Study) Eye Participants who have a nonfunctioning fellow (non-study) eye, defined as either BCVA of hand motion or worse, or no physical presence of non-study eye (i.e., monocular), at both the screening and study Day 1 visits will be excluded from study entry"}
  • {"criterion_text":"- Ocular Exclusion for Both Eyes Potential participants are excluded from the study if any of the following criteria apply: – History of idiopathic or autoimmune associated uveitis in either eye – Active ocular inflammation or suspected or active ocular or periocular infection in either eye on study Day 1"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Change from baseline in BCVA score as measured using the ETDRS VA chart at a starting distance of 4 meters","definition_or_measurement_approach":"BCVA measured using the ETDRS VA chart at a starting distance of 4 meters; endpoint is change from baseline averaged over specified weeks per protocol."}

Secondary endpoints

  • {"endpoint_text":"- Change from baseline in BCVA averaged over Weeks 92, 96, and 100","definition_or_measurement_approach":"BCVA change from baseline averaged over Weeks 92, 96 and 100 (BCVA measurement per ETDRS protocol as used for primary endpoint)."}
  • {"endpoint_text":"- Change from baseline in BCVA over time","definition_or_measurement_approach":"BCVA change from baseline measured over time (ETDRS VA chart protocol)."}
  • {"endpoint_text":"- Change from baseline in central subfield thickness (CST) averaged over Weeks 44, 48, and 52","definition_or_measurement_approach":"Central subfield thickness (CST) change from baseline averaged over Weeks 44, 48 and 52; anatomical assessments are specified in protocol (e.g., OCT)."}
  • {"endpoint_text":"- Change from baseline in CST averaged over Weeks 92, 96, and 100","definition_or_measurement_approach":"CST change from baseline averaged over Weeks 92, 96 and 100 (anatomic measurement using OCT per protocol)."}
  • {"endpoint_text":"- Change from baseline in CST over time","definition_or_measurement_approach":"CST change from baseline measured over time (anatomical measurement, e.g., OCT)."}
  • {"endpoint_text":"- Proportion of participants on a Q4W, Q8W, Q12W, Q16W, Q20W, and Q24W treatment interval at Weeks 52 and 100","definition_or_measurement_approach":"Proportion of participants assigned/maintaining specified dosing intervals (every 4, 8, 12, 16, 20, 24 weeks) at Weeks 52 and 100 as recorded in treatment schedule."}
  • {"endpoint_text":"- Incidence and severity of ocular adverse events","definition_or_measurement_approach":"Recorded incidence and severity of ocular adverse events per safety reporting procedures in protocol."}
  • {"endpoint_text":"- Incidence and severity of non-ocular adverse events","definition_or_measurement_approach":"Recorded incidence and severity of non-ocular adverse events per safety reporting procedures in protocol."}

Recruitment

Planned Sample Size
185
Recruitment Window Months
30
Consent Approach
Informed consent obtained using subject information sheets and informed consent forms (multiple ICF/SIS documents listed). Documents include main ICFs and infant authorization forms (e.g., 'L1_SIS and IAF infant authorization', 'L1_SIS and ICF Infant Health') and patient-facing study brochures in multiple languages (English, Spanish, French, Italian, German). Infant authorization/authorization forms are listed where applicable.

Methods

  • K1_Recruitment arrangement (documented recruitment arrangements)
  • K2_Recruitment material Advert
  • K2_Recruitment material Clinical Trials Brochure (graphics and photos)
  • K2_Recruitment material Flyer Light Creative 1
  • K2_Recruitment material Flyer Light Creative 2
  • K2_Recruitment material Poster 1
  • K2_Recruitment material Poster 2
  • K2_Recruitment material Study Brochure
  • Flyers, posters and study brochures available in multiple languages (as per listed documents)

Geography

Total Number Of Sites
24
Total Number Of Participants
89

France

Earliest CTIS Part Ii Submission Date
12-03-2025
Latest Decision Or Authorization Date
14-07-2025
Processing Time Days
124
Number Of Sites
6
Number Of Participants
22

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Ophtalmology
Principal Investigator Name
Aude Couturier
Principal Investigator Email
aude.couturier@aphp.fr
Contact Person Name
Aude Couturier
Contact Person Email
aude.couturier@aphp.fr
Site Name
Clinique De L'Union
Department Name
Ophtalmology
Principal Investigator Name
Xavier Benouaich
Principal Investigator Email
benouaich_xavier@yahoo.fr
Contact Person Name
Xavier Benouaich
Contact Person Email
benouaich_xavier@yahoo.fr
Site Name
Retina
Department Name
Ophtalmology
Principal Investigator Name
Hessam Razavi
Principal Investigator Email
centrestexupery37@gmail.com
Contact Person Name
Hessam Razavi
Contact Person Email
centrestexupery37@gmail.com
Site Name
Societe Civile De Moyens Des Docteurs Maury-Francais-Coscas-Favard-Krivosic
Department Name
Ophtalmology
Principal Investigator Name
Elise Philippakis
Principal Investigator Email
elise.philippakis@gmail.com
Contact Person Name
Elise Philippakis
Contact Person Email
elise.philippakis@gmail.com
Site Name
Selarl Retine Tourny
Department Name
Ophtalmology
Principal Investigator Name
Eric Fourmaux
Principal Investigator Email
arc@retinegallien.com
Contact Person Name
Eric Fourmaux
Contact Person Email
arc@retinegallien.com
Site Name
Hospices Civils De Lyon
Department Name
Ophtalmology
Principal Investigator Name
Corinne Dot
Principal Investigator Email
corinnedot.pro@hotmail.fr
Contact Person Name
Corinne Dot
Contact Person Email
corinnedot.pro@hotmail.fr

Germany

Earliest CTIS Part Ii Submission Date
12-03-2025
Latest Decision Or Authorization Date
21-01-2026
Processing Time Days
315
Number Of Sites
6
Number Of Participants
22

Sites

Site Name
Universitaetsklinikum Wuerzburg AöR
Department Name
Augenklinik und Poliklinik
Principal Investigator Name
Andreas Berlin
Principal Investigator Email
augenklinik@ukw.de
Contact Person Name
Andreas Berlin
Contact Person Email
augenklinik@ukw.de
Site Name
Augenzentrum Am St Franziskus-Hospital Muenster
Department Name
Augenzentrum
Principal Investigator Name
Albrecht Lommatzsch
Principal Investigator Email
info@augen-franziskus.de
Contact Person Name
Albrecht Lommatzsch
Contact Person Email
info@augen-franziskus.de
Site Name
Universitaetsklinikum Ulm AöR
Department Name
Klinik für Augenheilkunde
Principal Investigator Name
Armin Wolf
Principal Investigator Email
sekretariat.augenklinik@uniklinik-ulm.de
Contact Person Name
Armin Wolf
Site Name
Rostock University Medical Center
Department Name
Klinik und Poliklinik für Augenheilkunde
Principal Investigator Name
Friederike Schaub
Principal Investigator Email
Friederike.Schaub@med.uni-rostock.de
Contact Person Name
Friederike Schaub
Site Name
Augenzentrum Prof. Dr. Koch GmbH
Department Name
Augenzentrum
Principal Investigator Name
Svenja Deuchler
Principal Investigator Email
info@augenzentrumfrankfurt.de
Contact Person Name
Svenja Deuchler
Contact Person Email
info@augenzentrumfrankfurt.de
Site Name
Medizinische Hochschule Hannover
Department Name
Klinik für Augenheilkunde
Principal Investigator Name
Ekaterina Sokolenko
Principal Investigator Email
augenklinik.sekretariat@mh-hannover.de
Contact Person Name
Ekaterina Sokolenko

Italy

Earliest CTIS Part Ii Submission Date
14-04-2025
Latest Decision Or Authorization Date
03-06-2025
Processing Time Days
50
Number Of Sites
6
Number Of Participants
23

Sites

Site Name
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Department Name
Scienze Cliniche e di Comunità
Principal Investigator Name
Francesco Viola
Principal Investigator Email
francesco.viola@unimi.it
Contact Person Name
Francesco Viola
Contact Person Email
francesco.viola@unimi.it
Site Name
Azienda Ospedaliero-Universitaria Sant Andre
Department Name
UOD Oculistica
Principal Investigator Name
Gianluca Scuderi
Principal Investigator Email
gianluca.scuderi@uniroma1.it
Contact Person Name
Gianluca Scuderi
Contact Person Email
gianluca.scuderi@uniroma1.it
Site Name
Azienda Ospedaliero Universitaria Ospedali Riuniti Umberto I G M Lancisi G Salesi
Department Name
Medicina sperimentale e clinica, clinica oculistica
Principal Investigator Name
Marco Lupidi
Principal Investigator Email
marco.lupidi@ospedaliriuniti.marche.it
Contact Person Name
Marco Lupidi
Site Name
Azienda Ospedaliero Universitaria Ospedali Riuniti
Department Name
Scienze Mediche e Chirurgiche
Principal Investigator Name
Cristiana Iaculli
Principal Investigator Email
cristiana.iaculli@unifg.it
Contact Person Name
Cristiana Iaculli
Contact Person Email
cristiana.iaculli@unifg.it
Site Name
Azienda Ospedaliera Universitaria Universita' Degli Studi Della Campania Luigi Vanvitelli
Department Name
Dipartimento Multidisciplinare di Specialità Medico-Chirurgiche e Odontoiatriche
Principal Investigator Name
Settimio Rossi
Principal Investigator Email
settimio.rossi@unicampania.it
Contact Person Name
Settimio Rossi
Contact Person Email
settimio.rossi@unicampania.it
Site Name
Multimedica S.p.A.
Department Name
Clinica Oculistica Universitaria
Principal Investigator Name
Stela Vujosevic
Principal Investigator Email
stela.vujosevic@unimi.it
Contact Person Name
Stela Vujosevic
Contact Person Email
stela.vujosevic@unimi.it

Spain

Earliest CTIS Part Ii Submission Date
28-05-2025
Latest Decision Or Authorization Date
04-06-2025
Processing Time Days
7
Number Of Sites
6
Number Of Participants
22

Sites

Site Name
Oftalmologia Vistahermosa S.L.
Department Name
Ophthalmology
Principal Investigator Name
Rosa Dolz Marco
Principal Investigator Email
rosadolzmarco@gmail.com
Contact Person Name
Rosa Dolz Marco
Contact Person Email
rosadolzmarco@gmail.com
Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Ophthalmology
Principal Investigator Name
Jose Maria Ruiz Moreno
Principal Investigator Email
josemaria.ruiz@uclm.es
Contact Person Name
Jose Maria Ruiz Moreno
Contact Person Email
josemaria.ruiz@uclm.es
Site Name
Hospital Clinic De Barcelona
Department Name
Ophthalmology
Principal Investigator Name
Maria Socorro Alforja Castiella
Principal Investigator Email
ALFORJA@clinic.cat
Contact Person Name
Maria Socorro Alforja Castiella
Contact Person Email
ALFORJA@clinic.cat
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Ophthalmology
Principal Investigator Name
Andres Romero Martinez
Principal Investigator Email
romeroverte@gmail.com
Contact Person Name
Andres Romero Martinez
Contact Person Email
romeroverte@gmail.com
Site Name
Clinica Baviera S.A.
Department Name
Ophthalmology
Principal Investigator Name
Marta Sanchez Figueroa
Principal Investigator Email
figueroa.marta@outlook.es
Contact Person Name
Marta Sanchez Figueroa
Contact Person Email
figueroa.marta@outlook.es
Site Name
Hospital Universitari General De Catalunya
Department Name
Ophthalmology
Principal Investigator Name
Laura Sararols Ramsay
Principal Investigator Email
lsararols@omiq.es
Contact Person Name
Laura Sararols Ramsay
Contact Person Email
lsararols@omiq.es

Sponsor

Primary sponsor

Full Name
F. Hoffmann-La Roche AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
IQVIA Limited
Responsibilities
Monitoring
Name
Drugdev Inc.
Responsibilities
Site portal
Name
Perceptive Informatics Inc.
Responsibilities
IxRS Provider

Third parties

  • {"country":"United States","full_name":"Prime Realty Holdings LLC","duties_or_roles":"Patient Transportation","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Perceptive Informatics Inc.","duties_or_roles":"IxRS Provider","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Optymedge LLC","duties_or_roles":"Central Visual Acuity Provider","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United Kingdom","full_name":"Q2q Communications Limited","duties_or_roles":"Investigator Meeting","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Patient Reimbursement Provider","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Drugdev Inc.","duties_or_roles":"Site portal","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"Monitoring","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Duke University","duties_or_roles":"Vendor Imaging","organisation_type":"Educational Institution"}
  • {"country":"United Kingdom","full_name":"Ashfield Healthcare Limited","duties_or_roles":"","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Vabysmo 120 mg/mL solution for injection
Active Substance
FARICIMAB
Modality
Bispecific antibody
Routes Of Administration
Intravitreal use
Route
Intravitreal
Authorisation Status
Authorised (marketing authorisation EU/1/22/1683/001)
Maximum Dose
6 mg (maxDailyDoseAmount: 6 mg) as recorded in product entry

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