Clinical trial • Phase III • Immunology

RITLECITINIB TOSILATE for Alopecia areata

Phase III trial of RITLECITINIB TOSILATE for Alopecia areata. Placebo to match ritlecitinib 50 mg; Placebo to match ritlecitinib 30 mg-controlled.

Overview

Trial Therapeutic Area
Immunology
Trial Disease
Alopecia areata
Trial Stage
Phase III
Drug Modality
Small molecule
Paediatric Trial
Yes

Key dates

Initial CTIS Submission Date
07-07-2025
First CTIS Authorization Date
14-10-2025

Trial design

Placebo to match ritlecitinib 50 mg; Placebo to match ritlecitinib 30 mg-controlled Phase III trial across 33 sites in Poland, France, Czechia and others.

Comparator
Placebo to match ritlecitinib 50 mg; Placebo to match ritlecitinib 30 mg
Target Sample Size
62
Trial Duration For Participant
1080

Eligibility

Recruits 62 paediatric patients.

Vulnerable Population
Pediatric participants are explicitly included. Age-specific informed consent/assent handling is provided: parent/guardian informed consent and separate assent/ICF documents for minors (examples: Minor ICF 6-12; Minor/Assent 13-17; Parent/Guardian ICF). Country-specific ICFs and assent forms are available (documents listed for PL, FR, CZ, ES, IT).

Inclusion criteria

  • {"criterion_text":"- a)For participants originating from Study B7981031: 1.Participants with AA (including alopecia totalis [AT] and alopecia universalis [AU]) who completed the B7981031 study.\n- 2.\tAt least 50% scalp hair loss due to AA (ie, a SALT score of ≥50) at both the Screening and Baseline visits.\n- b)For participants originating from Study B7981027: 3.\tParticipants with AA (including AT and AU) who completed the B7981027 study."}

Exclusion criteria

  • {"criterion_text":"- a)Exclusion criteria for participants originating from Study B7981027 with ≤ 30 Days between last dose in Study B7981027 and first visit of Study B7981028: 1.During Study B7981027 or in the period between the last dose of study intervention in Study B7981027 and the first dose of study intervention of Study B7981028, presence of safety events that would require permanent discontinuation based on the B7981028 protocol.\n- 2. Study participants discontinued from Study B7981027 due to issues other than safety-related events and considered by the investigator for enrolment in Study B7981028 must have resolution of the issue(s) resulting in discontinuation from the parent study prior to enrolment in Study B7981028.\n- b)Exclusion criteria for participants originating from Study B7981031 or from Study B7981027 with >30 Days between last dose in Study B7981027 and first visit of Study B7981028: 1. During Study B7981031 or Study B7981027 or in the period between the last dose of study intervention in Study B7981031 or Study B7981027 and the first dose of study intervention of Study B7981028, presence of safety events that would require permanent discontinuation based on the B7981028 protocol.\n- 2. Any present malignancies or history of malignancies or lymphoproliferative disorders.\n- 3. Evidence of untreated or inadequately treated active or latent Mycobacterium tuberculosis (TB) infection.\n- 4. History (one or more episodes) of severe or serious cytomegalovirus (CMV), herpes zoster (shingles) or disseminated herpes simplex.\n- 5. Any infection requiring hospitalization, parenteral antimicrobial therapy, or as otherwise judged clinically significant within prior 3 months.\n- 6. Infection with hepatitis B virus (HBV) or hepatitis C virus (HCV)."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- • Incidence of treatment-emergent adverse events (AEs).\n- • Incidence of serious AEs (SAEs) and AEs leading to permanent discontinuation from the study.","definition_or_measurement_approach":""}

Secondary endpoints

  • {"endpoint_text":"- • Response based on achieving absolute Severity of Alopecia Tool (SALT) score ≤10 at all visits.\n- • Response based on achieving absolute SALT score ≤20 at all visits\n- •\tChange from baseline (CFB) in SALT score at all visits.\n- • Response based on achieving at least 2 grade improvement or a score of 3 in eyebrow assessment (EBA) score at all visits in participants with an abnormal EBA at baseline.\n- • Response based on achieving at least 2 grade improvement or a score of 3 in eyelash assessment (ELA) score at all visits in participants with an abnormal ELA at baseline.\n- • Patient Global Impression of Change (PGI-C) response defined as score of “moderately improved or greatly improved” at all time points.\n- • CFB in Patient Reported Outcomes Measurement Information System (PROMIS) Parent Proxy Depressive Symptoms T-score at all visits.\n- • CFB in PROMIS Parent Proxy Anxiety Symptoms T-score at all visits.\n- • CFB in Behavior Rating Inventory of Executive Function®2 (BRIEF®2) T-scores for the three index scores (Behavior Regulation Index [BRI], Emotional Regulation Index [ERI], Cognitive Regulation Index [CRI]) at all visits.\n- • CFB in modified Children's Dermatology Life Quality Index (CDLQI) total score at all visits.\n- • CFB# in Wechsler Intelligence Scale for Children® Fifth Edition (WISC-V) at end of study (Month 36).","definition_or_measurement_approach":""}

Recruitment

Registry Or Advocacy Recruitment
True, Advocacy Group Study Alert (country-specific materials present for PL, FR, CZ, ES, IT; specific organisations not named)
Digital Remote Recruitment
True, digital methods include Digital Adverts Pack, Animated Video/Study animation and Media Board materials (country-specific digital/online recruitment materials listed).
Planned Sample Size
62
Recruitment Window Months
48
Consent Approach
Informed consent obtained from adult participants; for pediatric participants parent/guardian informed consent required, with separate assent/ICF documents for minors. Age-specific assent/ICF documents are provided (examples: Assent 6-11; Assent 12-17; Parent/Guardian ICF). Country- and language-specific ICFs/assents are provided (documents present in PL, FR, CZ, ES, IT and English versions where noted).

Methods

  • Printed materials: study posters, flyers and patient brochures (country-specific versions listed for PL, FR, CZ, ES, IT).
  • Advocacy Group alerts / Study alerts (documents titled 'Advocacy Group Study Alert' available for multiple countries) targeted to patient advocacy groups.
  • Digital media: Digital Adverts Pack, Animated Video and Study animation (country-specific) for online/digital recruitment.
  • Media materials / Media Board (country-specific) for broader outreach.
  • Recruitment arrangements documents (K1) describing recruitment procedure at country level (K1 files present for PL, FR, CZ, ES, IT).

Geography

Total Number Of Sites
33
Total Number Of Participants
78

Poland

Earliest CTIS Part Ii Submission Date
10-09-2025
Latest Decision Or Authorization Date
23-12-2025
Processing Time Days
104
Number Of Sites
14
Number Of Participants
31

Sites

Site Name
Cityclinic Przychodnia Lekarsko-Psychologiczna Matusiak sp.p.
Principal Investigator Name
Jacek Szepietowski
Principal Investigator Email
jacek.szepietowski.work@gmail.com
Contact Person Name
Jacek Szepietowski
Site Name
Uniwersyteckie Centrum Kliniczne Warszawskiego Uniwersytetu Medycznego
Department Name
Klinika Dermatologiczna
Principal Investigator Name
Lidia Rudnicka
Principal Investigator Email
lidiarudnicka@gmail.com
Contact Person Name
Lidia Rudnicka
Contact Person Email
lidiarudnicka@gmail.com
Site Name
Dermedic Iwona Zdybska
Principal Investigator Name
Jacek Zdybski
Principal Investigator Email
jacek_z@icloud.com
Contact Person Name
Jacek Zdybski
Contact Person Email
jacek_z@icloud.com
Site Name
Panstwowy Instytut Medyczny Ministerstwa Spraw Wewnetrznych I Administracji
Department Name
Klinika Dermatologii
Principal Investigator Name
Irena Walecka Herniczek
Principal Investigator Email
irena.walecka@cskmswia.gov.pl
Contact Person Name
Irena Walecka Herniczek
Contact Person Email
irena.walecka@cskmswia.gov.pl
Site Name
Royalderm Agnieszka Nawrocka
Principal Investigator Name
Witold Owczarek
Principal Investigator Email
witold.owczarek@dermedicus.pl
Contact Person Name
Witold Owczarek
Contact Person Email
witold.owczarek@dermedicus.pl
Site Name
Labderm Essence Sp. z o.o.
Principal Investigator Name
Beata Bergler-Czop
Principal Investigator Email
bbergler-czop@sum.edu.pl
Contact Person Name
Beata Bergler-Czop
Contact Person Email
bbergler-czop@sum.edu.pl
Site Name
Provita Sp. z o.o.
Principal Investigator Name
Anita Lewartowska-Bialek
Principal Investigator Email
a.bialek@angelius.org
Contact Person Name
Anita Lewartowska-Bialek
Contact Person Email
a.bialek@angelius.org
Site Name
Klinika Ambroziak Sp. z o.o.
Principal Investigator Name
Justyna Skibinska
Principal Investigator Email
principalskibinska@klinikaambroziak.pl
Contact Person Name
Justyna Skibinska
Site Name
Uniwersytecki Szpital Kliniczny Im.Fryderyka Chopina W Rzeszowie
Principal Investigator Name
Adam Reich
Principal Investigator Email
adamandrzejreich@gmail.com
Contact Person Name
Adam Reich
Contact Person Email
adamandrzejreich@gmail.com
Site Name
Dermoklinika-Centrum Medyczne s.c. M. Kierstan J. Narbutt A. Lesiak
Principal Investigator Name
Joanna Narbutt
Principal Investigator Email
joanna.narbutt@onet.pl
Contact Person Name
Joanna Narbutt
Contact Person Email
joanna.narbutt@onet.pl
Site Name
Provita Poliklinika Sp. z o.o.
Principal Investigator Name
Mariusz Sikora
Principal Investigator Email
drmariuszsikora@gmail.com
Contact Person Name
Mariusz Sikora
Contact Person Email
drmariuszsikora@gmail.com
Site Name
Specjalistyczny gabinet dermatologiczny Aplikacyjno-Badawczy Marek Brzewski Pawel Brzewski SC
Principal Investigator Name
Pawel Brzewski
Principal Investigator Email
brzewski@gmail.com
Contact Person Name
Pawel Brzewski
Contact Person Email
brzewski@gmail.com
Site Name
NZOZ Specjalistyczny Osrodek Dermatologiczny ”Dermal”
Principal Investigator Name
Adam Wronski
Principal Investigator Email
adam.wronski@dermal.pl
Contact Person Name
Adam Wronski
Contact Person Email
adam.wronski@dermal.pl
Site Name
Klinika Osipowicz & Turkowski Sp. z o.o.
Principal Investigator Name
Katarzyna Osipowicz
Principal Investigator Email
osipowicz.kasia@gmail.com
Contact Person Name
Katarzyna Osipowicz
Contact Person Email
osipowicz.kasia@gmail.com

France

Earliest CTIS Part Ii Submission Date
12-09-2025
Latest Decision Or Authorization Date
07-01-2026
Processing Time Days
117
Number Of Sites
8
Number Of Participants
15

Sites

Site Name
Centre Hospitalier Universitaire Rouen
Department Name
Service de Dermatologie
Principal Investigator Name
Vivien HEBERT
Principal Investigator Email
vivien.hebert@chu-rouen.fr
Contact Person Name
Vivien HEBERT
Contact Person Email
vivien.hebert@chu-rouen.fr
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
service de Dermatologie
Principal Investigator Name
Thierry PASSERON
Principal Investigator Email
passeron.t@chu-nice.fr
Contact Person Name
Thierry PASSERON
Contact Person Email
passeron.t@chu-nice.fr
Site Name
Centre Hospitalier Universitaire De Dijon
Department Name
Service de Dermatologie
Principal Investigator Name
Bertille BONNIAUD
Principal Investigator Email
bertille.bonniaud@chu-dijon.fr
Contact Person Name
Bertille BONNIAUD
Contact Person Email
bertille.bonniaud@chu-dijon.fr
Site Name
Hospices Civils De Lyon
Department Name
Service de Dermatologie Pedriatrique
Principal Investigator Name
Alice PHAN
Principal Investigator Email
alice.phan@chu-lyon.fr
Contact Person Name
Alice PHAN
Contact Person Email
alice.phan@chu-lyon.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Service de Dermatologie
Principal Investigator Name
Juliette MAZEREEUW_HAUTIER
Principal Investigator Email
mazereeuw-hautier.j@chu-toulouse.fr
Contact Person Name
Juliette MAZEREEUW_HAUTIER
Site Name
Hopital Necker-Enfants Malades
Department Name
Service de Dermatologie
Principal Investigator Name
Chrisitine BODEMER
Principal Investigator Email
chrisitine.bodemer@aphp.fr
Contact Person Name
Chrisitine BODEMER
Contact Person Email
chrisitine.bodemer@aphp.fr
Site Name
Hopitaux Drome Nord
Department Name
Service de Dermatologie
Principal Investigator Name
Francois SKOWRON
Principal Investigator Email
f.skowron@ch-hdn.fr
Contact Person Name
Francois SKOWRON
Contact Person Email
f.skowron@ch-hdn.fr
Site Name
Groupement Des Hopitaux De L'Institut Catholique De Lille
Department Name
Service de Dermatologie
Principal Investigator Name
Audrey LASEK
Principal Investigator Email
Lasek.Audrey@ghicl.net
Contact Person Name
Audrey LASEK
Contact Person Email
Lasek.Audrey@ghicl.net

Czechia

Earliest CTIS Part Ii Submission Date
29-08-2025
Latest Decision Or Authorization Date
25-11-2025
Processing Time Days
88
Number Of Sites
4
Number Of Participants
8

Sites

Site Name
Fakultni Nemocnice Brno
Department Name
Detska nemocnice Detske kozni oddeleni PeK
Principal Investigator Name
Blanka Pinkova
Principal Investigator Email
pinkova.blanka@fnbrno.cz
Contact Person Name
Blanka Pinkova
Contact Person Email
pinkova.blanka@fnbrno.cz
Site Name
Fakultni Nemocnice Bulovka
Department Name
Dermatovenerologicka klinika
Principal Investigator Name
Filip Rob
Principal Investigator Email
filip.rob@gmail.com
Contact Person Name
Filip Rob
Contact Person Email
filip.rob@gmail.com
Site Name
Fakultni Nemocnice Plzen
Department Name
Dermatovenerologicka klinika
Principal Investigator Name
Jan Ricar
Principal Investigator Email
ricarj@fnplzen.cz
Contact Person Name
Jan Ricar
Contact Person Email
ricarj@fnplzen.cz
Site Name
Prof. MUDr. Petr Arenberger, DrSc., MBA
Principal Investigator Name
Monika Arenbergerová
Principal Investigator Email
arenbergerova@email.cz
Contact Person Name
Monika Arenbergerová
Contact Person Email
arenbergerova@email.cz

Spain

Earliest CTIS Part Ii Submission Date
09-09-2025
Latest Decision Or Authorization Date
04-03-2026
Processing Time Days
176
Number Of Sites
3
Number Of Participants
6

Sites

Site Name
Hospital Sant Joan De Deu Barcelona
Department Name
Pediatric Dermatology
Principal Investigator Name
Carolina Prat Torres
Principal Investigator Email
carolinasusana.prat@sjd.es
Contact Person Name
Carolina Prat Torres
Contact Person Email
carolinasusana.prat@sjd.es
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Dermatology
Principal Investigator Name
Caridad Elena Morales Múnera
Principal Investigator Email
CMorales@santpau.cat
Contact Person Name
Caridad Elena Morales Múnera
Contact Person Email
CMorales@santpau.cat
Site Name
Hospital Universitario Miguel Servet
Department Name
Dermatology
Principal Investigator Name
Fermina Yolanda Gilaberte Calzada
Principal Investigator Email
ygilaberte@salud.aragon.es
Contact Person Name
Fermina Yolanda Gilaberte Calzada
Contact Person Email
ygilaberte@salud.aragon.es

Italy

Earliest CTIS Part Ii Submission Date
24-04-2025
Latest Decision Or Authorization Date
23-04-2026
Processing Time Days
364
Number Of Sites
4
Number Of Participants
18

Sites

Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
UO Dermatologia - IRCCS Policlinico S. Orsola-Malpighi, Bologna
Principal Investigator Name
Michela Starace
Principal Investigator Email
michela.starace2@unibo.it
Contact Person Name
Michela Starace
Contact Person Email
michela.starace2@unibo.it
Site Name
Azienda Ospedaliero-Universitaria Policlinico G. Rodolico-San Marco Di Catania
Department Name
Azienda Ospedaliero-Universitaria Policlinico “G. Rodolico - San Marco" Di Catania
Principal Investigator Name
Giuseppe Micali
Principal Investigator Email
gmicalitrial@gmail.com
Contact Person Name
Giuseppe Micali
Contact Person Email
gmicalitrial@gmail.com
Site Name
Azienda Ospedaliera Universita' Degli Studi Della Campania Luigi Vanvitelli
Department Name
Universita degli Studi della Campania "Luigi Vanvitelli"
Principal Investigator Name
Giuseppe Argenziano
Principal Investigator Email
g.argenziano@gmail.com
Contact Person Name
Giuseppe Argenziano
Contact Person Email
g.argenziano@gmail.com
Site Name
Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
Department Name
ASST Spedali Civili di Brescia
Principal Investigator Name
Valeria Boccaletti
Principal Investigator Email
valeria.boccaletti@gmail.com
Contact Person Name
Valeria Boccaletti
Contact Person Email
valeria.boccaletti@gmail.com

Sponsor

Primary sponsor

Full Name
Pfizer Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Almac Pharmaceutical Services Pte Ltd
Responsibilities
code:14; code:15 (IP Description)
Name
Almac Clinical Services LLC
Responsibilities
IP Destruction; IP Description (various locations)
Name
Syneos Health UK Limited / Syneos Health Inc.
Responsibilities
codes:1 and 5 (responsibilities per sponsorDuties entries)
Name
Icon Clinical Research Limited
Responsibilities
Training
Name
Pharmaceutical Product Development LLC (PPD) and affiliated PPD organisations
Responsibilities
code:4 (multiple PPD entities listed for site services/lab services)
Name
QPS LLC
Responsibilities
code:4
Name
Signant Health Global LLC
Responsibilities
code:7
Name
Canfield Scientific Inc.
Responsibilities
code:7

Third parties

  • {"country":"Singapore","full_name":"Almac Pharmaceutical Services Pte Ltd","duties_or_roles":"code:14; code:15 (IP Description)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Scout Clinical","duties_or_roles":"code:15 (Participant Reimbursement)","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United Kingdom","full_name":"Syneos Health UK Limited","duties_or_roles":"code:1","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Services LLC","duties_or_roles":"code:14; code:15 (IP Destruction)","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"code:15 (Training)","organisation_type":"Pharmaceutical company"}
  • {"country":"China","full_name":"Ppd Laboratories (Suzhou) Co. Ltd.","duties_or_roles":"code:4","organisation_type":"Pharmaceutical company"}
  • {"country":"Belgium","full_name":"PPD International Holdings LLC","duties_or_roles":"code:4","organisation_type":"Pharmaceutical company"}
  • {"country":"Singapore","full_name":"PPD Global Central Labs (S) Pte Ltd","duties_or_roles":"code:4","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Pharmaceutical Product Development LLC","duties_or_roles":"code:4","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Services LLC (Durham address)","duties_or_roles":"code:14; code:15 (IP Destruction)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Canfield Scientific Inc.","duties_or_roles":"code:7","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"QPS LLC","duties_or_roles":"code:4","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Almac Clinical Services (Ireland) Limited","duties_or_roles":"code:14; code:15 (IP Destruction)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Syneos Health Inc.","duties_or_roles":"code:5","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Services LLC (4238 Technology Drive)","duties_or_roles":"code:14; code:15 (IP Description)","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Innovative Trials Limited","duties_or_roles":"code:15 (Recruitment Materials)","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom (Northern Ireland)","full_name":"Almac Clinical Services Limited","duties_or_roles":"code:14; code:15 (IP Destruction)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Signant Health Global LLC","duties_or_roles":"code:7","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Services LLC (4204 Technology Drive)","duties_or_roles":"code:14; code:15 (IP Description)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Services LLC (4228 Technology Drive)","duties_or_roles":"code:14; code:15 (IP Destruction)","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Ritlecitinib tosilate
Active Substance
RITLECITINIB TOSILATE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Authorised
Starting Dose
50 mg
Dose Levels
50 mg
Maximum Dose
50 mg
Investigational Product Name
Ritlecitinib
Active Substance
RITLECITINIB TOSILATE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Authorised
Starting Dose
30 mg
Dose Levels
30 mg
Maximum Dose
30 mg
Investigational Product Name
Placebo to match ritlecitinib 50 mg
Modality
Other
Investigational Product Name
Placebo to match ritlecitinib 30 mg
Modality
Other

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