Clinical trial • Phase II • Dermatology

AMLITELIMAB for Alopecia areata

Phase II trial of AMLITELIMAB for Alopecia areata.

Overview

Trial Therapeutic Area
Dermatology
Trial Disease
Alopecia areata
Trial Stage
Phase II
Drug Modality
Monoclonal antibody

Key dates

Initial CTIS Submission Date
29-04-2024
First CTIS Authorization Date
23-08-2024

Trial design

Randomised, amlitelimab matching placebo (placebo control). dose and schedule not specified in the ctis public data. Phase II trial in Bulgaria, Netherlands, Italy and others.

Randomised
Yes
Comparator
Amlitelimab matching placebo (placebo control). Dose and schedule not specified in the CTIS public data.
Target Sample Size
147
Trial Duration For Participant
252

Eligibility

Recruits 147 No vulnerable population selected in the Part I population. The trial is restricted to adult participants; informed consent from adult participants is required. No assent/parental consent procedures are described in the public CTIS record..

Vulnerable Population
No vulnerable population selected in the Part I population. The trial is restricted to adult participants; informed consent from adult participants is required. No assent/parental consent procedures are described in the public CTIS record.

Inclusion criteria

  • {"criterion_text":"- Definitive diagnosis of AA of more than 6 months."}
  • {"criterion_text":"- Diagnosis of severe AA, as determined by all of the following: a) Hair loss affecting ≥50% of the scalp, as measured by Severity of Alopecia Tool (SALT) at both screening and baseline visits. b) Current episode of severe hair loss of less than 8 years. Participants with a history of AA of more than 8 years who have observed episodes of terminal hair regrowth over their scalp (“moving patches” spontaneously or following treatment) in the past 8 years can be included. c) Stable disease: no evidence of terminal hair regrowth within 6 months (ie, equivalent to less than 10% improvement points spontaneous reduction in SALT over the past 6 months). (guidance: if participant reports to have quite a bit more hair than 6 months prior, then patient cannot be included)."}
  • {"criterion_text":"- Willingness in maintaining a consistent hair style and hair care, including hair products, and to refrain from weaves, extensions, adhesive wigs, other than banded perimeter devices, refrain from shaving of scalp hair for 2 weeks prior to each study visit from baseline to the EOS."}

Exclusion criteria

  • {"criterion_text":"- Participants that are currently experiencing other forms of alopecia, including but not limited to: androgenetic alopecia, trichotillomania, telogen effluvium, traction alopecia, scarring alopecia."}
  • {"criterion_text":"- Participants currently with any local or systemic active medical conditions which in the opinion of the Investigator would interfere with evaluations of the IMP effect on AA due to scalp inflammation, including but not limited to seborrheic dermatitis requiring topical treatment to the scalp, lupus erythematosus, lichen planus, psoriasis, secondary syphilis, tinea capitis, thyroiditis, systemic sclerosis, hair transplants, micropigmentation/tattoo of the scalp"}
  • {"criterion_text":"- Received the specified treatment regimens within the timeframe outlined in the protocol."}
  • {"criterion_text":"- Prior use of any oral JAKi or the topical JAKi ruxolitinib for more than 24 months, regardless if washout period is respected."}
  • {"criterion_text":"- Subjects with shaved heads must not enter the study until hair has grown back and SALT score can be reliably administered."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Change from baseline in SALT score at Week 36","definition_or_measurement_approach":"Change from baseline in Severity of Alopecia Tool (SALT) score measured at Week 36 (SALT instrument referenced elsewhere in protocol and inclusion criteria)."}

Secondary endpoints

  • {"endpoint_text":"- Change from the baseline in SALT score at Week 24 (key secondary)","definition_or_measurement_approach":"Change from baseline in SALT score measured at Week 24."}
  • {"endpoint_text":"- Proportion of participants achieving a SALT score ≤20 at Weeks 24 and 36","definition_or_measurement_approach":"Proportion achieving SALT ≤20 at Weeks 24 and 36."}
  • {"endpoint_text":"- Time to SALT score ≤20","definition_or_measurement_approach":"Time-to-event analysis for achieving SALT ≤20."}
  • {"endpoint_text":"- Proportion of participants achieving a SALT score ≤10 at Weeks 24 and 36","definition_or_measurement_approach":"Proportion achieving SALT ≤10 at Weeks 24 and 36."}
  • {"endpoint_text":"- Time to SALT score ≤10","definition_or_measurement_approach":"Time-to-event analysis for achieving SALT ≤10."}
  • {"endpoint_text":"- Proportion of participants achieving ClinRO Measure for eyebrow (EB) Hair Loss 0 or 1 with ≥2-point improvement from baseline at Weeks 24 and 36 (among participants with ClinRO Measure for EB Hair Loss ≥2 at Baseline)","definition_or_measurement_approach":"Clinician-reported outcome for eyebrow hair loss (EB); proportion achieving grade 0 or 1 with ≥2-point improvement at Weeks 24 and 36 among those with baseline EB ≥2."}
  • {"endpoint_text":"- Proportion of participants achieving ClinRO Measure for Eyelash (EL) Hair Loss 0 or 1 with ≥2-point improvement from baseline (among participants with ClinRO Measure for EL Hair Loss ≥2 at Baseline)","definition_or_measurement_approach":"Clinician-reported outcome for eyelash hair loss (EL); proportion achieving grade 0 or 1 with ≥2-point improvement among those with baseline EL ≥2."}
  • {"endpoint_text":"- Proportion of participants achieving a PGI-C response defined as a score of “moderately improved” or “greatly improved” at Weeks 24 and 36","definition_or_measurement_approach":"Patient Global Impression of Change (PGI-C); proportion with response of 'moderately improved' or 'greatly improved' at Weeks 24 and 36."}
  • {"endpoint_text":"- Proportion of participants achieving a PGI-S response defined as a score of “mild“ or “none” at Weeks 24 and 36","definition_or_measurement_approach":"Patient Global Impression of Severity (PGI-S); proportion scoring 'mild' or 'none' at Weeks 24 and 36."}
  • {"endpoint_text":"- Mean changes from baseline in SKINDEX-16AA at Weeks 24 and 36","definition_or_measurement_approach":"Mean change from baseline in SKINDEX-16AA (quality of life instrument) at Weeks 24 and 36."}
  • {"endpoint_text":"- Proportion of participants with PRO Scalp Hair Assessment score of 0 to 1 with ≥2-point improvement from baseline (among participants with PRO Scalp Hair Assessment score ≥3 at Baseline)","definition_or_measurement_approach":"Patient-reported outcome (Scalp Hair Assessment); proportion achieving score 0–1 with ≥2-point improvement among those with baseline ≥3."}
  • {"endpoint_text":"- Proportion of participants achieving grade 0 or 1 with ≥2­point improvement from baseline PRO Measure for EB Hair Loss (among participants with PRO Measure for EB Hair Loss ≥2 at Baseline)","definition_or_measurement_approach":"Patient-reported eyebrow hair loss measure; proportion achieving grade 0 or 1 with ≥2-point improvement among those with baseline ≥2."}
  • {"endpoint_text":"- Proportion of participants achieving grade 0 or 1 with ≥2­point improvement from baseline PRO Measure for EL Hair Loss at Weeks 24 and 36 (among participants with PRO Measure for EL Hair Loss ≥2 at Baseline)","definition_or_measurement_approach":"Patient-reported eyelash hair loss measure; proportion achieving grade 0 or 1 with ≥2-point improvement among those with baseline ≥2 at Weeks 24 and 36."}
  • {"endpoint_text":"- Proportion of participants who experienced treatment-emergent adverse events (TEAEs), experienced treatment-emergent serious adverse event (TESAEs) and/or Treatment-Emergent adverse event of special interest (AESIs)","definition_or_measurement_approach":"Safety endpoints: incidence of TEAEs, TESAEs and AESIs during treatment."}
  • {"endpoint_text":"- Serum amlitelimab concentrations measured at prespecified timepoints","definition_or_measurement_approach":"Pharmacokinetic endpoint: serum amlitelimab concentrations at prespecified timepoints."}
  • {"endpoint_text":"- Incidence of ADAs) of amlitelimab at prespecified timepoints","definition_or_measurement_approach":"Immunogenicity endpoint: incidence of anti-drug antibodies (ADAs) at prespecified timepoints."}

Recruitment

Digital Remote Recruitment
True, video scripts and electronic recruitment assets are included in the recruitment materials (suggesting use of digital/video content), languages and materials prepared for online or digital distribution.
Planned Sample Size
147
Recruitment Window Months
41
Consent Approach
Informed consent obtained from adult participants; multiple ICF and subject information documents are provided (adult main ICF and partner/pregnancy ICFs). Consent documents are available in multiple languages (English, Romanian, Bulgarian, Dutch, French, Spanish, Italian, German, Czech as shown in CTIS document listings). No assent or parental consent procedures are described in the public CTIS record.

Methods

  • Flyers (K2 recruitment material flyers available in multiple languages as listed in CTIS documents).
  • Posters (K2 recruitment material posters available in multiple languages).
  • Placebo fact sheets for recruitment (documents labelled placebo fact sheet for multiple countries).
  • Video scripts for recruitment (K2 recruitment material placebo video script documents).
  • Doctor-to-doctor letters (K2 recruitment material dr-to-dr letters referenced).
  • Country-specific K1 recruitment arrangements documents (country-specific recruitment arrangement PDFs available).

Geography

Total Number Of Sites
30
Total Number Of Participants
74

Bulgaria

Earliest CTIS Part Ii Submission Date
17-05-2024
Latest Decision Or Authorization Date
27-10-2025
Processing Time Days
528
Number Of Sites
2
Number Of Participants
5

Sites

Site Name
Medical Center Comac Medical Ltd.
Principal Investigator Name
Minoo Mehrabian
Principal Investigator Email
minoo.mehrabian@comac-medical.com
Contact Person Name
Minoo Mehrabian
Site Name
Medical Center Comac Medical Ltd.
Principal Investigator Name
Minoo Mehrabian
Principal Investigator Email
minoo.mehrabian@comac-medical.com
Contact Person Name
Minoo Mehrabian

Netherlands

Earliest CTIS Part Ii Submission Date
29-07-2024
Latest Decision Or Authorization Date
12-03-2026
Processing Time Days
591
Number Of Sites
1
Number Of Participants
8

Sites

Site Name
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Department Name
Dermatology Department
Principal Investigator Name
Rick Waalboer-Spuij
Principal Investigator Email
r.waalboer@erasmusmc.nl
Contact Person Name
Rick Waalboer-Spuij
Contact Person Email
r.waalboer@erasmusmc.nl

Italy

Earliest CTIS Part Ii Submission Date
25-07-2024
Latest Decision Or Authorization Date
23-03-2026
Processing Time Days
606
Number Of Sites
4
Number Of Participants
5

Sites

Site Name
Ospedale San Raffaele S.r.l.
Department Name
Dermatologia
Principal Investigator Name
Franco Rongioletti
Principal Investigator Email
rongioletti.franco@hsr.it
Contact Person Name
Franco Rongioletti
Contact Person Email
rongioletti.franco@hsr.it
Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
DIMEC, Department of Medical and Surgical Sciences
Principal Investigator Name
Michela Starace
Principal Investigator Email
michela.starace2@unibo.it
Contact Person Name
Michela Starace
Contact Person Email
michela.starace2@unibo.it
Site Name
Azienda Ospedaliera Universitaria Federico II Di Napoli
Department Name
Dipartimento di Medicina Clinica e Chirurgia
Principal Investigator Name
Paola Nappa
Principal Investigator Email
paonappa@unina.it
Contact Person Name
Paola Nappa
Contact Person Email
paonappa@unina.it
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
U.O.C. Dermatologia
Principal Investigator Name
Ketty Peris
Principal Investigator Email
ketty.peris@unicatt.it
Contact Person Name
Ketty Peris
Contact Person Email
ketty.peris@unicatt.it

France

Earliest CTIS Part Ii Submission Date
12-07-2024
Latest Decision Or Authorization Date
13-03-2026
Processing Time Days
609
Number Of Sites
4
Number Of Participants
8

Sites

Site Name
Centre Hospitalier Universitaire Rouen
Department Name
Dermatologie
Principal Investigator Name
Vivien Hebert
Principal Investigator Email
vivien.hebert@chu-rouen.fr
Contact Person Name
Vivien Hebert
Contact Person Email
vivien.hebert@chu-rouen.fr
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Service de Dermatologie
Principal Investigator Name
Thierry PASSERON
Principal Investigator Email
thierry.passeron@unice.fr
Contact Person Name
Thierry PASSERON
Contact Person Email
thierry.passeron@unice.fr
Site Name
Centre SABOURAUD
Department Name
Dermatologie
Principal Investigator Name
Mira Pavlovic
Principal Investigator Email
m.pavlovic-ganascia@centresabouraud.fr
Contact Person Name
Mira Pavlovic
Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
Service de Dermatologie
Principal Investigator Name
Claire Abasq-Thomas
Principal Investigator Email
claire.abasq@chu-brest.fr
Contact Person Name
Claire Abasq-Thomas
Contact Person Email
claire.abasq@chu-brest.fr

Germany

Earliest CTIS Part Ii Submission Date
29-07-2024
Latest Decision Or Authorization Date
20-03-2026
Processing Time Days
599
Number Of Sites
7
Number Of Participants
14

Sites

Site Name
Universitaetsklinikum Muenster AöR
Department Name
Dermatologie
Principal Investigator Name
Nina Magnolo
Principal Investigator Email
nina.magnolo@ukmuenster.de
Contact Person Name
Nina Magnolo
Contact Person Email
nina.magnolo@ukmuenster.de
Site Name
Klinische Forschung Osnabrueck
Principal Investigator Name
Sylvia Pauser
Principal Investigator Email
sylvia.pauser@klifos.de
Contact Person Name
Sylvia Pauser
Contact Person Email
sylvia.pauser@klifos.de
Site Name
Emovis GmbH
Department Name
Dermatology
Principal Investigator Name
Guido Burbach
Principal Investigator Email
guido.burbach@futuremeds.com
Contact Person Name
Guido Burbach
Contact Person Email
guido.burbach@futuremeds.com
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
Dermatologie/Venerologie/Allergologie
Principal Investigator Name
Ulrike Blume-Peytavi
Principal Investigator Email
ulrike.blume-peytavi@charite.de
Contact Person Name
Ulrike Blume-Peytavi
Site Name
Thermalsole und Schwefelbad Bentheim GmbH
Department Name
Dermatologie
Principal Investigator Name
Athanasios Tsianakas
Principal Investigator Email
a.tsianakas@fk-bentheim.de
Contact Person Name
Athanasios Tsianakas
Contact Person Email
a.tsianakas@fk-bentheim.de
Site Name
Hautarztpraxis Dr. Mihaescu
Principal Investigator Name
Virgil-Oreste Mihaescu
Principal Investigator Email
info@dr-mihaescu.de
Contact Person Name
Virgil-Oreste Mihaescu
Contact Person Email
info@dr-mihaescu.de
Site Name
Eurofins bioskin GmbH
Principal Investigator Name
Swarna Ekanayake-Bohlig
Principal Investigator Email
Swarna.Ekanayake@cpt.eurofinseu.com
Contact Person Name
Swarna Ekanayake-Bohlig

Romania

Earliest CTIS Part Ii Submission Date
29-07-2024
Latest Decision Or Authorization Date
23-03-2026
Processing Time Days
602
Number Of Sites
1
Number Of Participants
8

Sites

Site Name
Spitalul Clinic Judetean De Urgenta Cluj
Department Name
Medical II
Principal Investigator Name
Adrian Lucian Baican
Principal Investigator Email
adrian.baican.ext@arensia-em.com
Contact Person Name
Adrian Lucian Baican

Czechia

Earliest CTIS Part Ii Submission Date
30-07-2024
Latest Decision Or Authorization Date
13-03-2026
Processing Time Days
591
Number Of Sites
3
Number Of Participants
17

Sites

Site Name
Praglandia s.r.o.
Department Name
Dermatology
Principal Investigator Name
Andrea Vocilkova
Principal Investigator Email
a.voc@praglandia.cz
Contact Person Name
Andrea Vocilkova
Contact Person Email
a.voc@praglandia.cz
Site Name
CCR Ostrava s.r.o.
Department Name
dermatology
Principal Investigator Name
Sylva Zajicova
Principal Investigator Email
sylva.zajicova@ccrostrava.com
Contact Person Name
Sylva Zajicova
Contact Person Email
sylva.zajicova@ccrostrava.com
Site Name
Sanixtra CZ s.r.o.
Department Name
dermatology
Principal Investigator Name
Lucia Mansfeldova
Principal Investigator Email
lucia.mansfeldova@sanixtra.eu
Contact Person Name
Lucia Mansfeldova
Contact Person Email
lucia.mansfeldova@sanixtra.eu

Spain

Earliest CTIS Part Ii Submission Date
08-08-2024
Latest Decision Or Authorization Date
17-03-2026
Processing Time Days
586
Number Of Sites
7
Number Of Participants
9

Sites

Site Name
Hospital General Universitario Dr. Balmis
Department Name
Servicio de Dermatologia
Principal Investigator Name
Maria del Mar Blanes Martinez
Principal Investigator Email
marblanes76@gmail.com
Contact Person Name
Maria del Mar Blanes Martinez
Contact Person Email
marblanes76@gmail.com
Site Name
Hospital Clinico San Carlos
Department Name
Servicio de Dermatologia
Principal Investigator Name
Eduardo Lopez Bran
Principal Investigator Email
lopezbran@salud.madrid.org
Contact Person Name
Eduardo Lopez Bran
Contact Person Email
lopezbran@salud.madrid.org
Site Name
Hospital Universitario Reina Sofia
Department Name
Servicio de Dermatologia
Principal Investigator Name
Juan Alberto Ruano Ruiz
Principal Investigator Email
juanruanoruiz@mac.com
Contact Person Name
Juan Alberto Ruano Ruiz
Contact Person Email
juanruanoruiz@mac.com
Site Name
Hospital Universitario Infanta Leonor
Department Name
Servicio de Dermatologia
Principal Investigator Name
Pablo de la Cueva Dobao
Principal Investigator Email
pdelacueva@yahoo.com
Contact Person Name
Pablo de la Cueva Dobao
Contact Person Email
pdelacueva@yahoo.com
Site Name
Hospital Clinic De Barcelona
Department Name
Servicio de Dermatologia
Principal Investigator Name
Andrea Combalia Escudero
Principal Investigator Email
acombalia@clinic.cat
Contact Person Name
Andrea Combalia Escudero
Contact Person Email
acombalia@clinic.cat
Site Name
Hospital Universitari Vall D Hebron
Department Name
Servicio de Dermatologia
Principal Investigator Name
Victor Cabezas Calderon
Principal Investigator Email
vcabezas91@gmail.com
Contact Person Name
Victor Cabezas Calderon
Contact Person Email
vcabezas91@gmail.com
Site Name
Hospital Universitario Quironsalud Madrid
Department Name
Dermatology
Principal Investigator Name
Javier Pedraz Munoz
Principal Investigator Email
javierpedraz78@gmail.com
Contact Person Name
Javier Pedraz Munoz
Contact Person Email
javierpedraz78@gmail.com

Sponsor

Primary sponsor

Full Name
Sanofi-Aventis Recherche & Developpement
Organisation Type
Pharmaceutical company
Country Of Registered Address
France

Contract research organisations

Name
Endpoint Clinical Inc.
Name
PPD Development LP
Name
Pharmaceutical Product Development LLC
Name
Inato

Third parties

  • {"country":"United States","full_name":"Endpoint Clinical Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"France","full_name":"Mapi Research Trust","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Icahn School Of Medicine At Mount Sinai","duties_or_roles":"","organisation_type":"Educational Institution"}
  • {"country":"Germany","full_name":"Azenta Germany GmbH","duties_or_roles":"Biorepository Storage","organisation_type":"Pharmaceutical company"}
  • {"country":"France","full_name":"Inato","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"PPD Development LP","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Rules Based Medicine Inc.","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Canfield Scientific Inc.","duties_or_roles":"Handling the optional photography (no central reading activities performed)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Transperfect Translations International Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"ARENSIA Exploratory Medicine GmbH","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Pharmaceutical Product Development LLC","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Bulgaria","full_name":"Comac Medical Ltd.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"ESMS Global Limited","duties_or_roles":"Emergency Services 24/7","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Amlitelimab
Active Substance
AMLITELIMAB
Modality
Monoclonal antibody
Routes Of Administration
SUBCUTANEOUS INJECTION
Route
SUBCUTANEOUS INJECTION
Authorisation Status
1
Maximum Dose
500 mg
Investigational Product Name
Amlitelimab matching placebo to test product
Modality
Other

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