Clinical trial • Phase III • Gastroenterology

RISANKIZUMAB for Ulcerative colitis

Phase III trial of RISANKIZUMAB for Ulcerative colitis.

Overview

Trial Therapeutic Area
Gastroenterology
Trial Disease
Ulcerative colitis
Trial Stage
Phase III
Drug Modality
Monoclonal antibody
Paediatric Trial
Yes

Key dates

Initial CTIS Submission Date
08-05-2025
First CTIS Authorization Date
29-08-2025

Trial design

Randomised, open-label, risankizumab placebo (placebo comparator); dose and schedule not specified in provided data-controlled Phase III trial in Belgium, Greece, Italy and others.

Randomised
Yes
Open Label
Yes
Comparator
risankizumab placebo (placebo comparator); dose and schedule not specified in provided data
Target Sample Size
87

Eligibility

Recruits 87 paediatric patients.

Vulnerable Population
Pediatric subjects aged 2 to <18 years are included. The study uses age-appropriate assent and parent/guardian consent procedures: assent forms and ICFs are provided for age groups (titles indicate assent/ICF for ages 2-5, 6-11, 12-17) and parental/guardian consent forms are provided. Country- and language-specific ICF/assent documents are available (examples in the file list: English, Dutch, French for BE; German for DE; Italian for IT; Spanish for ES; Greek for GR; Swedish for SE). Consent is provided by parent/guardian with assent from the child as appropriate to age.

Inclusion criteria

  • {"criterion_text":"- Active ulcerative colitis (UC) with an modified Mayo Score (mMS) of 5 to 9 points and endoscopic subscore of 2 to 3 (confirmed by central reader).\n- Demonstrated intolerance or inadequate response (IR) to one or more of the following categories of drugs: aminosalicylates (except in countries where failure of this drug class is not sufficient for eligibility), oral locally acting corticosteroids, systemic steroids (prednisone or equivalent), immunomodulators (IMMs), and/or biologic therapies, as outlined in the protocol.\n- Subjects must have a documented history of UC for at least 3 months prior to Baseline, confirmed by colonoscopy during the screening period, with exclusion of current infection, colonic dysplasia and/or malignancy. Documentation of pathology results consistent with the diagnosis of UC must be available."}

Exclusion criteria

  • {"criterion_text":"- Subjects who have had a major surgery performed within 12 weeks prior to Baseline or planned during the conduct of the study (e.g., inguinal hernia repair, cholecystectomy, intestinal resection).\n- Subjects who have concurrent clinically significant medical conditions other than the indication being studied or any other reason that the investigator determines would interfere with the subject's participation in this study, would make the subject an unsuitable candidate to receive study treatment, or would put the subject at risk by participating in the study."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- PK Lead-in Cohort 1 and Cohort 2: Maximum Observed Serum Concentration (Cmax)","definition_or_measurement_approach":"Measured by serum concentrations (pharmacokinetic assessment)."}
  • {"endpoint_text":"- PK Lead-in Cohort 1 and Cohort 2: Time to Maximum Serum Concentration (Tmax)","definition_or_measurement_approach":"Measured by serum concentration-time profile to determine time to peak concentration."}
  • {"endpoint_text":"- PK Lead-in Cohort 1 and Cohort 2: Area Under the Serum Concentration-Time Curve Over the Dosing Interval (AUCtau)","definition_or_measurement_approach":"Calculated from serum concentration-time data over the dosing interval (AUCtau)."}
  • {"endpoint_text":"- Expansion Cohort 3: Achievement of Clinical Remission per Modified Mayo Score (mMS) at Week 64 Among Week 12 Clinical Responders per mMS","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) to determine clinical remission at Week 64 among Week 12 responders."}

Secondary endpoints

  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Achievement of clinical remission per mMS at Week 64 among Week 12 responders per mMS","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) at Weeks 12 and 64."}
  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Achievement of clinical remission per mMS at Week 12","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) at Week 12."}
  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Achievement of clinical response per mMS at Week 12","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) to define clinical response at Week 12."}
  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Achievement of endoscopic improvement at Week 12","definition_or_measurement_approach":"Endoscopic assessment to evaluate improvement at Week 12."}
  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Symptomatic response per partial mMS at Week 12","definition_or_measurement_approach":"Assessed using the partial Modified Mayo Score (partial mMS) for symptomatic response at Week 12."}
  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Achievement of clinical response per mMS at Week 64 among Week 12 responders per mMS","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) at Weeks 12 and 64."}
  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Achievement of endoscopic improvement at Week 64 among Week 12 responders per mMS","definition_or_measurement_approach":"Endoscopic assessment at Week 64 among Week 12 responders."}
  • {"endpoint_text":"- PK Lead-In Cohort 1 and Cohort 2: Ability to discontinue corticosteroids prior to Week 64 (at least 90 days without corticosteroid exposure) and achievement of clinical remission per mMS among Week 12 responders per mMS","definition_or_measurement_approach":"Defined as at least 90 days without corticosteroid exposure prior to Week 64 and assessment of clinical remission by mMS among Week 12 responders."}
  • {"endpoint_text":"- Expansion Cohort 3: Achievement of clinical remission per mMS at Week 12","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) at Week 12."}
  • {"endpoint_text":"- Expansion Cohort 3: Achievement of clinical response per mMS at Week 12","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) at Week 12."}
  • {"endpoint_text":"- Expansion Cohort 3: Achievement of endoscopic improvement at Week 12","definition_or_measurement_approach":"Endoscopic assessment to evaluate improvement at Week 12."}
  • {"endpoint_text":"- Expansion Cohort 3: Symptomatic response per partial mMS at Week 12","definition_or_measurement_approach":"Assessed using the partial Modified Mayo Score (partial mMS) for symptomatic response at Week 12."}
  • {"endpoint_text":"- Expansion Cohort 3: Achievement of clinical response per mMS at Week 64 among Week 12 responders per mMS","definition_or_measurement_approach":"Assessed using the Modified Mayo Score (mMS) at Week 64 among Week 12 responders."}
  • {"endpoint_text":"- Expansion Cohort 3: Achievement of endoscopic improvement at Week 64 among Week 12 responders per mMS","definition_or_measurement_approach":"Endoscopic assessment at Week 64 among Week 12 responders."}
  • {"endpoint_text":"- Expansion Cohort 3: Achievement of corticosteroid-free clinical remission per mMS at Week 64 among Week 12 responders per mMS","definition_or_measurement_approach":"Corticosteroid-free remission assessed by mMS at Week 64 among Week 12 responders (corticosteroid-free defined as no corticosteroid exposure for the specified period in the protocol)."}

Recruitment

Planned Sample Size
87
Recruitment Window Months
106
Consent Approach
Informed consent is provided by parent(s)/legal guardian(s); assent is obtained from pediatric participants using age-appropriate assent forms. ICF and assent documents are prepared by country and age group (documents in the file list include assent/ICF for ages 2-5, 6-11, 12-17 and parental/guardian ICFs). Country/language-specific documents are available (examples include English, Dutch, French for Belgium; German for Germany; Italian for Italy; Spanish for Spain; Greek for Greece; Swedish for Sweden).

Geography

Total Number Of Sites
20
Total Number Of Participants
33

Belgium

Earliest CTIS Part Ii Submission Date
06-08-2025
Latest Decision Or Authorization Date
29-08-2025
Processing Time Days
23
Number Of Sites
3
Number Of Participants
5

Sites

Site Name
Association Hospitaliere De Bruxelles Hopital Universitaire Des Enfants Reine Fabiola
Department Name
Gastroenterology (Pediatric)
Principal Investigator Name
Patrick Bontems
Principal Investigator Email
patrick.bontems@huderf.be
Contact Person Name
Patrick Bontems
Contact Person Email
patrick.bontems@huderf.be
Site Name
Centre Hospitalier Regional De La Citadelle
Department Name
Gastroenterology (Pediatric)
Principal Investigator Name
Emeline Bequet
Principal Investigator Email
emeline.bequet@chrcitadelle.be
Contact Person Name
Emeline Bequet
Contact Person Email
emeline.bequet@chrcitadelle.be
Site Name
Cliniques Universitaires Saint-Luc
Department Name
Gastroenterology (Pediatric)
Principal Investigator Name
Isabelle Scheers
Principal Investigator Email
isabelle.scheers@saintluc.uclouvain.be
Contact Person Name
Isabelle Scheers

Greece

Earliest CTIS Part Ii Submission Date
28-07-2025
Latest Decision Or Authorization Date
02-09-2025
Processing Time Days
36
Number Of Sites
3
Number Of Participants
6

Sites

Site Name
Thoracic General Hospital Of Athens I Sotiria
Department Name
3rd University Internal Medicine department
Principal Investigator Name
Georgios Bamias
Principal Investigator Email
gastro.sotiria@gmail.com
Contact Person Name
Georgios Bamias
Contact Person Email
gastro.sotiria@gmail.com
Site Name
University General Hospital Attikon
Department Name
Paediatric gastroenterology unit, Hepatology and Dietetics, 3rd University Paediatric Clinic
Principal Investigator Name
Smaragdi Fessatou
Principal Investigator Email
sfessatou@yahoo.gr
Contact Person Name
Smaragdi Fessatou
Contact Person Email
sfessatou@yahoo.gr
Site Name
Hippokration Hospital
Department Name
3rd Pediatric
Principal Investigator Name
Ioannis Xinias
Principal Investigator Email
xinias@auth.gr
Contact Person Name
Ioannis Xinias
Contact Person Email
xinias@auth.gr

Italy

Earliest CTIS Part Ii Submission Date
07-08-2025
Latest Decision Or Authorization Date
02-09-2025
Processing Time Days
26
Number Of Sites
4
Number Of Participants
6

Sites

Site Name
Azienda Ospedaliera Universitaria Federico II Di Napoli
Department Name
Pediatrics
Principal Investigator Name
Annamaria Staiano
Principal Investigator Email
staiano@unina.it
Contact Person Name
Annamaria Staiano
Contact Person Email
staiano@unina.it
Site Name
Casa Sollievo Della Sofferenza
Department Name
Pediatric department
Principal Investigator Name
Maria Rosa Pastore
Principal Investigator Email
m.pastore@operapadrepio.it
Contact Person Name
Maria Rosa Pastore
Contact Person Email
m.pastore@operapadrepio.it
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
UOC Medicina Interna e Gastroenterologia
Principal Investigator Name
Antonio Gasbarrini
Principal Investigator Email
antonio.gasbarrini@unicatt.it
Contact Person Name
Antonio Gasbarrini
Contact Person Email
antonio.gasbarrini@unicatt.it
Site Name
Istituto Di Ricovero E Cura A Carattere Scientifico Materno Infantile Burlo Garofolo
Department Name
Paediatric Gastroenterology
Principal Investigator Name
Matteo Bramuzzo
Principal Investigator Email
matteo.bramuzzo@burlo.trieste.it
Contact Person Name
Matteo Bramuzzo

Spain

Earliest CTIS Part Ii Submission Date
03-06-2025
Latest Decision Or Authorization Date
03-09-2025
Processing Time Days
92
Number Of Sites
2
Number Of Participants
4

Sites

Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Pediatric Gastroenterology Unit
Principal Investigator Name
Carolina Gutierrez Junquera
Principal Investigator Email
carolina.gutijun@salud.madrid.org
Contact Person Name
Carolina Gutierrez Junquera
Site Name
Complexo Hospitalario Universitario A Coruna
Department Name
Servicio de Pediatría
Principal Investigator Name
Ana Moreno Alvarez
Principal Investigator Email
Ana.Moreno.Alvarez@sergas.es
Contact Person Name
Ana Moreno Alvarez
Contact Person Email
Ana.Moreno.Alvarez@sergas.es

Sweden

Earliest CTIS Part Ii Submission Date
08-08-2025
Latest Decision Or Authorization Date
01-09-2025
Processing Time Days
24
Number Of Sites
3
Number Of Participants
5

Sites

Site Name
Queen Silvia Childrens Hospital - Sahlgrenska University Hospital - Vaestra Goetalandsregionen
Department Name
Sektionen för Pediatrisk Gastroenterologi, Hepatologi och Nutrition
Principal Investigator Name
Robert Saalman
Principal Investigator Email
robert.saalman@vgregion.se
Contact Person Name
Robert Saalman
Contact Person Email
robert.saalman@vgregion.se
Site Name
Soedersjukhuset AB
Department Name
Sachsska Barn- och Ungdomssjukhuset
Principal Investigator Name
Petter Malmborg
Principal Investigator Email
petter.malmborg@regionstockholm.se
Contact Person Name
Petter Malmborg
Site Name
Karolinska University Hospital
Department Name
Astrid Lindgren's Children Hospital
Principal Investigator Name
Henrik Arnell
Principal Investigator Email
henrik.arnell@regionstockholm.se
Contact Person Name
Henrik Arnell

Germany

Earliest CTIS Part Ii Submission Date
22-08-2025
Latest Decision Or Authorization Date
30-01-2026
Processing Time Days
161
Number Of Sites
5
Number Of Participants
7

Sites

Site Name
Medical University Of Lausitz Carl Thiem
Principal Investigator Name
Simone Stolz
Principal Investigator Email
m.loebel@mul-ct.de
Contact Person Name
Simone Stolz
Contact Person Email
m.loebel@mul-ct.de
Site Name
Klinikum Westbrandenburg GmbH
Department Name
Klinik für Gastroenterologie, Hepatologie, Infektiologie und Rheumatologie
Principal Investigator Name
Daniel Baumgart
Principal Investigator Email
daniel.baumgart@klinikumevb.de
Contact Person Name
Daniel Baumgart
Contact Person Email
daniel.baumgart@klinikumevb.de
Site Name
Klinikum Kassel GmbH
Principal Investigator Name
Ralph Melchior
Principal Investigator Email
ralph.melchior@gnh.net
Contact Person Name
Ralph Melchior
Contact Person Email
ralph.melchior@gnh.net
Site Name
Universitaetsklinikum Muenster AöR
Principal Investigator Name
Thomas Kaiser
Principal Investigator Email
Thomas.Kaiser@ukmuenster.de
Contact Person Name
Thomas Kaiser
Contact Person Email
Thomas.Kaiser@ukmuenster.de
Site Name
Universitaetsklinikum Erlangen AöR
Department Name
Medizinische Klinik 4
Principal Investigator Name
André Hörning
Principal Investigator Email
gastroenterologie.kinder@uk-erlangen.de
Contact Person Name
André Hörning

Sponsor

Primary sponsor

Full Name
AbbVie Deutschland GmbH & Co. KG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Germany

Contract research organisations

Name
Labcorp Central Laboratory Services SARL
Responsibilities
sponsorDuties codes: 4
Name
Signant Health Management Limited
Responsibilities
sponsorDuties codes: 7
Name
Alimentiv Inc.
Responsibilities
Imaging (sponsorDuties id 15)
Name
WCG Clinical Inc.
Responsibilities
Data monitoring committee (sponsorDuties id 15)
Name
IQVIA Limited
Responsibilities
sponsorDuties codes: 3

Third parties

  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Signant Health Management Limited","duties_or_roles":"sponsorDuties codes: 7","organisation_type":"Pharmaceutical company"}
  • {"country":"Canada","full_name":"Alimentiv Inc.","duties_or_roles":"sponsorDuties: 15 (Imaging)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"WCG Clinical Inc.","duties_or_roles":"sponsorDuties: 15 (Data monitoring committee)","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"sponsorDuties codes: 3","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Risankizumab
Active Substance
RISANKIZUMAB
Modality
Monoclonal antibody
Routes Of Administration
SUBCUTANEOUS
Route
SUBCUTANEOUS
Authorisation Status
Authorised
Investigational Product Name
ABBV-066 / Risankizumab
Active Substance
RISANKIZUMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Authorisation Status
Authorised
Investigational Product Name
ABBV-066
Active Substance
RISANKIZUMAB
Modality
Monoclonal antibody
Routes Of Administration
SUBCUTANEOUS
Route
SUBCUTANEOUS
Authorisation Status
Authorised
Investigational Product Name
risankizumab placebo
Modality
Other

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