Clinical trial • Phase III • Oncology

PIRTOBRUTINIB for Chronic lymphocytic leukemia | Small lymphocytic lymphoma

Phase III trial of PIRTOBRUTINIB for Chronic lymphocytic leukemia | Small lymphocytic lymphoma.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Chronic lymphocytic leukemia | Small lymphocytic lymphoma
Trial Stage
Phase III
Drug Modality
Small molecule | Monoclonal antibody

Key dates

Initial CTIS Submission Date
14-05-2024
First CTIS Authorization Date
12-06-2024

Trial design

Randomised, open-label, venetoclax plus rituximab (comparator arm) — venetoclax (film-coated tablet, oral, max daily dose reported 400 mg) and rituximab (solution for infusion, iv, dose reported up to 500 mg/m2)-controlled Phase III trial in Sweden, Denmark, Belgium and others.

Randomised
Yes
Open Label
Yes
Comparator
Venetoclax plus Rituximab (comparator arm) — Venetoclax (FILM-COATED TABLET, oral, max daily dose reported 400 mg) and Rituximab (SOLUTION FOR INFUSION, IV, dose reported up to 500 mg/m2)
Target Sample Size
377
Trial Duration For Participant
784

Eligibility

Recruits 377 adults.

Inclusion criteria

  • {"criterion_text":"- Age 18 and older at time of enrollment\n- Confirmed diagnosis of CLL/SLL requiring therapy per iwCLL 2018 criteria\n- Previous treatment with at least one line of therapy that may include a covalent Bruton's tyrosine kinase (BTK) inhibitor\n- Platelets greater than or equal to (≥)50 x 10⁹/liter (L), hemoglobin ≥8 grams/deciliter (g/dL) and absolute neutrophil count ≥1.0 x 10⁹/L\n- Adequate organ function\n- Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2\n- Estimated creatinine clearance ≥30 milliliters per minute (mL/min)"}

Exclusion criteria

  • {"criterion_text":"- Known or suspected Richter's transformation at any time preceding enrollment\n- Patients with the following hypersensitivity: 1. Known hypersensitivity to any component or excipient of pirtobrutinib and venetoclax 2. Prior significant hypersensitivity to rituximab 3. Known allergy to allopurinol and inability to take uric acid lowering agent\n- Prior therapy with a non-covalent (reversible) BTK inhibitor\n- Patients requiring therapeutic anticoagulation with warfarin or another Vitamin K antagonist\n- Current treatment with strong cytochrome P450 (CYP) 3A4 (CYP3A4) inhibitors or inducers\n- Prior therapy with venetoclax\n- Central nervous system (CNS) involvement\n- Active uncontrolled systemic bacterial, viral, fungal, or parasitic infection\n- Known human immunodeficiency virus (HIV) infection, regardless of cluster of differentiation 4 (CD4) count\n- Allogeneic stem cell transplantation (SCT) or chimeric antigen receptor (CAR)-T within 60 days\n- Active hepatitis B or hepatitis C\n- Known active cytomegalovirus (CMV) infection\n- Uncontrolled immune thrombocytopenic purpura (ITP) or autoimmune hemolytic anemia (AIHA)\n- Significant cardiovascular disease\n- Vaccination with a live vaccine within 28 days prior to randomization"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- PFS per International Workshop on Chronic Lymphocytic Leukemia (iwCLL) Criteria 2018, assessed by Independent Review Committee (IRC)","definition_or_measurement_approach":"Assessed per iwCLL 2018 criteria and evaluated by an Independent Review Committee (IRC)"}

Recruitment

Planned Sample Size
377
Recruitment Window Months
62
Consent Approach
Adults (age ≥18) provide informed consent. Subject information and informed consent forms (ICFs) are submitted in multiple country/language versions (documents available in English, French, Spanish, Hungarian, Polish, Italian, Swedish, Czech, Dutch per submitted ICF documents).

Geography

Total Number Of Sites
69
Total Number Of Participants
262

Sweden

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
12-06-2024
Processing Time Days
9
Number Of Sites
2
Number Of Participants
10

Sites

Site Name
Region Skane Skanes Universitetssjukhus
Department Name
Hematology
Principal Investigator Name
Daniel Roth
Principal Investigator Email
Daniel.Roth@skane.se
Contact Person Name
Daniel Roth
Contact Person Email
Daniel.Roth@skane.se
Site Name
Karolinska University Hospital
Department Name
Hematology
Principal Investigator Name
Anders Osterborg
Principal Investigator Email
anders.osterborg@regionstockholm.se
Contact Person Name
Anders Osterborg

Denmark

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
14-06-2024
Processing Time Days
11
Number Of Sites
1
Number Of Participants
7

Sites

Site Name
Rigshospitalet
Department Name
Hematology
Principal Investigator Name
Caspar Cunha-Bang M.D
Principal Investigator Email
caspar.da.cunha-bang@regionh.dk
Contact Person Name
Caspar Cunha-Bang M.D

Belgium

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
17-06-2024
Processing Time Days
14
Number Of Sites
3
Number Of Participants
4

Sites

Site Name
Universitair Ziekenhuis Gent
Department Name
Hematology
Principal Investigator Name
Fritz Offnner
Principal Investigator Email
fritz.offner@ugent.be
Contact Person Name
Fritz Offnner
Contact Person Email
fritz.offner@ugent.be
Site Name
Centre Hospitalier Universitaire Dinant Godinne Sainte-Elisabeth-UCL-Namur
Department Name
Hematology
Principal Investigator Name
Hélène Vellemans
Principal Investigator Email
helene.vellemans@chuuclnamur.uclouvain.be
Contact Person Name
Hélène Vellemans
Site Name
Pole Hospitalier Jolimont
Department Name
Hematology
Principal Investigator Name
Vanessa Delrieu
Principal Investigator Email
vanessa.delrieu@helora.be
Contact Person Name
Vanessa Delrieu
Contact Person Email
vanessa.delrieu@helora.be

Italy

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
01-07-2024
Processing Time Days
28
Number Of Sites
13
Number Of Participants
40

Sites

Site Name
Azienda Ospedaliera Santa Croce E Carle
Department Name
SC Ematologia
Principal Investigator Name
Elia Boccellato
Principal Investigator Email
elia.boccellato@gmail.com
Contact Person Name
Elia Boccellato
Contact Person Email
elia.boccellato@gmail.com
Site Name
Careggi University Hospital
Department Name
SODc Ematologia
Principal Investigator Name
Alessandro Sanna
Principal Investigator Email
sannaa@aou-careggi.toscana.it
Contact Person Name
Alessandro Sanna
Contact Person Email
sannaa@aou-careggi.toscana.it
Site Name
Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
Department Name
Hematology
Principal Investigator Name
Candida Vitale
Principal Investigator Email
candida.vitale@unito.it
Contact Person Name
Candida Vitale
Contact Person Email
candida.vitale@unito.it
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
UOC Oncologia Medica
Principal Investigator Name
Luca Laurenti
Principal Investigator Email
luca.laurenti@unicatt.it
Contact Person Name
Luca Laurenti
Contact Person Email
luca.laurenti@unicatt.it
Site Name
Ospedale San Raffaele S.r.l.
Department Name
Oncologia
Principal Investigator Name
Pierpaolo Ghia
Principal Investigator Email
ghia.paolo@hsr.it
Contact Person Name
Pierpaolo Ghia
Contact Person Email
ghia.paolo@hsr.it
Site Name
Azienda Ospedaliero Universitaria Di Modena
Department Name
SC Ematologia
Principal Investigator Name
Roberto Marasca
Principal Investigator Email
roberto.marasca@unimore.it
Contact Person Name
Roberto Marasca
Contact Person Email
roberto.marasca@unimore.it
Site Name
ASST Grande Ospedale Metropolitano Niguarda
Department Name
SC Ematologia
Principal Investigator Name
Anna Maria Frustaci
Principal Investigator Email
annamaria.frustaci@ospedaleniguarda.it
Contact Person Name
Anna Maria Frustaci
Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
UO Ematologia
Principal Investigator Name
Pier Luigi Zinzani
Principal Investigator Email
pierluigi.zinzani@unibo.it
Contact Person Name
Pier Luigi Zinzani
Contact Person Email
pierluigi.zinzani@unibo.it
Site Name
Azienda Ospedaliero-Universitaria Maggiore Della Carita
Department Name
SCDU Ematologia
Principal Investigator Name
Gianluca Gaidano
Principal Investigator Email
gianluca.gaidano@med.uniupo.it
Contact Person Name
Gianluca Gaidano
Contact Person Email
gianluca.gaidano@med.uniupo.it
Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
Oncologia medica
Principal Investigator Name
Gerardo Musuraca
Principal Investigator Email
gerardo.musuraca@irst.emr.it
Contact Person Name
Gerardo Musuraca
Contact Person Email
gerardo.musuraca@irst.emr.it
Site Name
Azienda ospedaliera universitaria Renato Dulbecco
Department Name
Oncoematologia
Principal Investigator Name
Marco Rossi
Principal Investigator Email
rossim@unicz.it
Contact Person Name
Marco Rossi
Contact Person Email
rossim@unicz.it
Site Name
Azienda Ospedaliero-Universitaria Policlinico Umberto I
Department Name
Divisione di Ematologia
Principal Investigator Name
Maurizio Martelli
Principal Investigator Email
martelli@bce.uniroma1.it
Contact Person Name
Maurizio Martelli
Contact Person Email
martelli@bce.uniroma1.it
Site Name
University Hospital Of Ferrara
Department Name
UO Ematologia
Principal Investigator Name
Antonio Cuneo
Principal Investigator Email
cut@unife.it
Contact Person Name
Antonio Cuneo
Contact Person Email
cut@unife.it

Poland

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
01-07-2024
Processing Time Days
28
Number Of Sites
7
Number Of Participants
63

Sites

Site Name
Uniwersytecki Szpital Kliniczny Nr 1 W Lublinie
Department Name
Klinika Hematoonkologii i Transplantacji Szpiku
Principal Investigator Name
Marek Hus
Principal Investigator Email
markhus@o2.pl
Contact Person Name
Marek Hus
Contact Person Email
markhus@o2.pl
Site Name
Pratia S.A.
Principal Investigator Name
Wojciech Jurczak
Principal Investigator Email
wojciech.jurczak@pratia.com
Contact Person Name
Wojciech Jurczak
Contact Person Email
wojciech.jurczak@pratia.com
Site Name
Instytut Hematologii I Transfuzjologii
Department Name
Klinika Hematologii
Principal Investigator Name
Ewa Lech-Marańda
Principal Investigator Email
emaranda@ihit.waw.pl
Contact Person Name
Ewa Lech-Marańda
Contact Person Email
emaranda@ihit.waw.pl
Site Name
Pratia Hematologia Sp. z o.o.
Principal Investigator Name
Sebastian Grosicki
Principal Investigator Email
sgrosicki@wp.pl
Contact Person Name
Sebastian Grosicki
Contact Person Email
sgrosicki@wp.pl
Site Name
Medicover Integrated Clinical Services Sp. z o.o.
Principal Investigator Name
Dominik Chraniuk
Principal Investigator Email
d.chraniuk@naszlekarz.pl
Contact Person Name
Dominik Chraniuk
Contact Person Email
d.chraniuk@naszlekarz.pl
Site Name
Szpitale Pomorskie Sp. z o.o.
Department Name
Oddział Hematologii i Transplantologii Szpiku
Principal Investigator Name
Adam Witkowski
Principal Investigator Email
adam.wit12@gmail.com
Contact Person Name
Adam Witkowski
Contact Person Email
adam.wit12@gmail.com
Site Name
Wojewodzkie Wielospecjalistyczne Centrum Onkologii I Traumatologii Im M.Kopernika W Lodzi
Department Name
Oddział Hematologii z Pododdziałem Chemoterapii - Klinika Hematologii
Principal Investigator Name
Tadeusz Robak
Principal Investigator Email
robaktad@csk.umed.lodz.pl
Contact Person Name
Tadeusz Robak
Contact Person Email
robaktad@csk.umed.lodz.pl

Hungary

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
12-06-2024
Processing Time Days
9
Number Of Sites
3
Number Of Participants
3

Sites

Site Name
University Of Debrecen
Department Name
Belgyógyászati Klinika. B épület. Hematológia
Principal Investigator Name
Árpád Illés
Principal Investigator Email
illes@IIIbel.dote.hu
Contact Person Name
Árpád Illés
Contact Person Email
illes@IIIbel.dote.hu
Site Name
Orszagos Onkologiai Intezet
Department Name
Hematológia és Lymphoma osztály "Kemoterápia A"
Principal Investigator Name
András Masszi
Principal Investigator Email
masszi.andras@oncol.hu
Contact Person Name
András Masszi
Contact Person Email
masszi.andras@oncol.hu
Site Name
Somogy Varmegyei Kaposi Mor Oktato Korhaz
Department Name
Haematológiai Osztály
Principal Investigator Name
Balázs Kollár
Principal Investigator Email
kollarbalazs@yahoo.com
Contact Person Name
Balázs Kollár
Contact Person Email
kollarbalazs@yahoo.com

Ireland

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
14-06-2024
Processing Time Days
11
Number Of Sites
2
Number Of Participants
1

Sites

Site Name
University Hospital Waterford
Department Name
Haem
Principal Investigator Name
Ezzat Elhassadi
Principal Investigator Email
ezzat.elhassadi@hse.ie
Contact Person Name
Ezzat Elhassadi
Contact Person Email
ezzat.elhassadi@hse.ie
Site Name
Mater Misericordiae University Hospital
Department Name
Haematology
Principal Investigator Name
Anne Fortune
Principal Investigator Email
afortune@mater.ie
Contact Person Name
Anne Fortune
Contact Person Email
afortune@mater.ie

Germany

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
13-06-2024
Processing Time Days
10
Number Of Sites
6
Number Of Participants
12

Sites

Site Name
University Hospital Cologne AöR
Department Name
Klinik I für innere Medizin
Principal Investigator Name
Paula Cramer
Principal Investigator Email
paula.cramer@uk-koeln.de
Contact Person Name
Paula Cramer
Contact Person Email
paula.cramer@uk-koeln.de
Site Name
Rostock University Medical Center
Department Name
ZIM III für Hämatologie
Principal Investigator Name
Sebastian Boettcher
Principal Investigator Email
sebastian.boettcher@med.uni-rostock.de
Contact Person Name
Sebastian Boettcher
Site Name
Muenchen Klinik gGmbH
Department Name
Klinik für Hämatologie und Onkologie
Principal Investigator Name
Clemens-Martin Wendtner
Principal Investigator Email
clemens.wendtner@muenchen-klinik.de
Contact Person Name
Clemens-Martin Wendtner
Site Name
Haematologisch Onkologische Schwerpunktpraxis
Department Name
Gemeinschaftspraxis Dres. Schöttker & Pretscher
Principal Investigator Name
Bjoern Schoettker
Principal Investigator Email
b.schoettker@onkopraxis-wuerzburg.de
Contact Person Name
Bjoern Schoettker
Site Name
Universitaet Leipzig
Department Name
Klinik und Poliklinik für Hämatologie, Zelltherapie und Hämostaseologie
Principal Investigator Name
Carmen Herling
Principal Investigator Email
Carmen.Herling@medizin.uni-leipzig.de
Contact Person Name
Carmen Herling
Site Name
Universitaetsklinikum Essen AöR
Department Name
Klinik für Hämatologie und Stammzelltransplantation
Principal Investigator Name
Julia von Tresckow
Principal Investigator Email
Julia.vonTresckow@uk-essen.de
Contact Person Name
Julia von Tresckow
Contact Person Email
Julia.vonTresckow@uk-essen.de

Czechia

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
13-06-2024
Processing Time Days
10
Number Of Sites
4
Number Of Participants
36

Sites

Site Name
Vseobecna Fakultni Nemocnice V Praze
Department Name
1st Dep. of Medicine - Dep. of Hematology
Principal Investigator Name
Marek Trněný
Principal Investigator Email
trneny@cesnet.cz
Contact Person Name
Marek Trněný
Contact Person Email
trneny@cesnet.cz
Site Name
Fakultni Nemocnice Hradec Kralove
Department Name
4th Department of Internal Medicine – Haematology
Principal Investigator Name
Martin Šimkovič
Principal Investigator Email
martin.simkovic@fnhk.cz
Contact Person Name
Martin Šimkovič
Contact Person Email
martin.simkovic@fnhk.cz
Site Name
Fakultni Nemocnice Kralovske Vinohrady
Department Name
Internal Hematology Clinic
Principal Investigator Name
Heidi Móciková
Principal Investigator Email
heidi.mocikova@fnkv.cz
Contact Person Name
Heidi Móciková
Contact Person Email
heidi.mocikova@fnkv.cz
Site Name
Fakultni Nemocnice Brno
Department Name
Internal hematology and oncology clinic
Principal Investigator Name
Anna Panovská
Principal Investigator Email
panovska.anna@fnbrno.cz
Contact Person Name
Anna Panovská
Contact Person Email
panovska.anna@fnbrno.cz

Spain

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
17-06-2024
Processing Time Days
14
Number Of Sites
14
Number Of Participants
38

Sites

Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Hematologia
Principal Investigator Name
Rafael Andreu Lapiedra
Principal Investigator Email
andreu_raflap@gva.es
Contact Person Name
Rafael Andreu Lapiedra
Contact Person Email
andreu_raflap@gva.es
Site Name
Hospital Universitario Fundacion Jimenez Diaz
Department Name
oncology
Principal Investigator Name
Sergio Ramos
Principal Investigator Email
sergio.ramos@startmadrid.com
Contact Person Name
Sergio Ramos
Contact Person Email
sergio.ramos@startmadrid.com
Site Name
Hospital Universitari Vall D Hebron
Department Name
Hematologia
Principal Investigator Name
Francesc Bosch Albareda
Principal Investigator Email
fbosch@vhebron.net
Contact Person Name
Francesc Bosch Albareda
Contact Person Email
fbosch@vhebron.net
Site Name
Hospital Clinic De Barcelona
Department Name
hematologia
Principal Investigator Name
Pablo Javier Mozas Fernández
Principal Investigator Email
MOZAS@clinic.cat
Contact Person Name
Pablo Javier Mozas Fernández
Contact Person Email
MOZAS@clinic.cat
Site Name
Hospital Universitario De Toledo
Department Name
Hematologia
Principal Investigator Name
Maria Isabel Gomez Roncero
Principal Investigator Email
mgroncero@telefonica.net
Contact Person Name
Maria Isabel Gomez Roncero
Contact Person Email
mgroncero@telefonica.net
Site Name
Hospital Universitario Central De Asturias
Department Name
hematologia
Principal Investigator Name
Angel Ramirez Payer
Principal Investigator Email
apayer.angel@gmail.com
Contact Person Name
Angel Ramirez Payer
Contact Person Email
apayer.angel@gmail.com
Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Hematologia
Principal Investigator Name
Jose Antonio Garcia Vela
Principal Investigator Email
garciavela.joseantonio@gmail.com
Contact Person Name
Jose Antonio Garcia Vela
Site Name
MD Anderson Cancer Center
Department Name
oncologia-hematologia
Principal Investigator Name
Adolfo De la Fuente Burguera
Principal Investigator Email
afuente@mdanderson.es
Contact Person Name
Adolfo De la Fuente Burguera
Contact Person Email
afuente@mdanderson.es
Site Name
Hospital Universitario De La Princesa
Department Name
oncologia
Principal Investigator Name
Javier Loscertales Pueyo
Principal Investigator Email
jloscertales@gmail.com
Contact Person Name
Javier Loscertales Pueyo
Contact Person Email
jloscertales@gmail.com
Site Name
Hospital Costa Del Sol
Department Name
Hematologia
Principal Investigator Name
Maria Angeles Medina Perez
Principal Investigator Email
amedinaperez@gmail.com
Contact Person Name
Maria Angeles Medina Perez
Contact Person Email
amedinaperez@gmail.com
Site Name
Hospital Universitario Infanta Leonor
Department Name
hematologia y hematoterapia
Principal Investigator Name
JOSE ANGEL HERNANDEZ RIVAS
Principal Investigator Email
jahernandezr@salud.madrid.org
Contact Person Name
JOSE ANGEL HERNANDEZ RIVAS
Contact Person Email
jahernandezr@salud.madrid.org
Site Name
Hospital Universitario Quironsalud Madrid
Department Name
Hematologia
Principal Investigator Name
Carmen Martinez Chamorro
Principal Investigator Email
carmenmartinezchamorro@hotmail.com
Contact Person Name
Carmen Martinez Chamorro
Site Name
Hospital Universitario Virgen De La Macarena
Department Name
hematologia y hematoterapia
Principal Investigator Name
Alicia Rodriguez Fernandez
Contact Person Name
Alicia Rodriguez Fernandez
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Unidad de ensayos clinicos
Principal Investigator Name
Fatima de la Cruz Vicente
Principal Investigator Email
fatimadelacruzv@gmail.com
Contact Person Name
Fatima de la Cruz Vicente
Contact Person Email
fatimadelacruzv@gmail.com

France

Earliest CTIS Part Ii Submission Date
03-06-2024
Latest Decision Or Authorization Date
17-06-2024
Processing Time Days
14
Number Of Sites
14
Number Of Participants
48

Sites

Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
Hématologie
Principal Investigator Name
Luc-Matthieu FORNECKER
Principal Investigator Email
Luc-matthieu.fornecker@chru-strasbourg.fr
Contact Person Name
Luc-Matthieu FORNECKER
Site Name
Centre Henri Becquerel
Department Name
Hématologie
Principal Investigator Name
Stéphane LEPRETRE
Principal Investigator Email
stephane.lepretre@chb.unicancer.fr
Contact Person Name
Stéphane LEPRETRE
Site Name
Centre Hospitalier Et Universitaire De Limoges
Department Name
Hématologie
Principal Investigator Name
Natalia DMYTRUK
Principal Investigator Email
nataliya.dmytuk@chu-limoges.fr
Contact Person Name
Natalia DMYTRUK
Contact Person Email
nataliya.dmytuk@chu-limoges.fr
Site Name
Institut Universitaire Du Cancer Toulouse-Oncopole
Department Name
Hématologie
Principal Investigator Name
Loic YSEBAERT
Principal Investigator Email
ysebaert.loic@iuct-oncopole.fr
Contact Person Name
Loic YSEBAERT
Contact Person Email
ysebaert.loic@iuct-oncopole.fr
Site Name
Hopital Saint Louis
Department Name
Hématologie - Oncologie
Principal Investigator Name
Catherine THIEBLEMONT
Principal Investigator Email
catherine.thieblemont@aphp.fr
Contact Person Name
Catherine THIEBLEMONT
Contact Person Email
catherine.thieblemont@aphp.fr
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Hématologie
Principal Investigator Name
Cécile TOMOWIAK
Principal Investigator Email
cecile.tomowiak@chu-poitiers.fr
Contact Person Name
Cécile TOMOWIAK
Site Name
Centre Hospitalier Lyon Sud
Department Name
Hématologie option maladies du sang
Principal Investigator Name
Emmanuelle FERRANT
Principal Investigator Email
emmanuelle.ferrant2@chu-lyon.fr
Contact Person Name
Emmanuelle FERRANT
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Hématologie Option Maladies du sang
Principal Investigator Name
Emmanuelle TCHERNONOG
Principal Investigator Email
e-tchernonog@chu-montpellier.fr
Contact Person Name
Emmanuelle TCHERNONOG
Site Name
CHRU De Nancy
Department Name
Médecine Interne
Principal Investigator Name
Pierre FEUGIER
Principal Investigator Email
p.feugier@chru-nancy.fr
Contact Person Name
Pierre FEUGIER
Contact Person Email
p.feugier@chru-nancy.fr
Site Name
Centre Hospitalier Universitaire De Tours
Department Name
Hématologie
Principal Investigator Name
Caroline DARTIGEAS
Principal Investigator Email
c.dartigeas@chu-tours.fr
Contact Person Name
Caroline DARTIGEAS
Contact Person Email
c.dartigeas@chu-tours.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Hématologie option maladies du sang
Principal Investigator Name
Damien ROOS-WEIL
Principal Investigator Email
damien.roosweil@aphp.fr
Contact Person Name
Damien ROOS-WEIL
Contact Person Email
damien.roosweil@aphp.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Hématologie option oncohématologie
Principal Investigator Name
Anne LOK
Principal Investigator Email
anne.lok@chu-nantes.fr
Contact Person Name
Anne LOK
Contact Person Email
anne.lok@chu-nantes.fr
Site Name
Centre Hospitalier Universitaire De Rennes
Department Name
Hématologie
Principal Investigator Name
Sophie DE GUIBERT
Principal Investigator Email
sophie.de.guibert@chu-rennes.fr
Contact Person Name
Sophie DE GUIBERT
Site Name
Clinique Victor Hugo
Department Name
Biologie médicale
Principal Investigator Name
Kamel LARIBI
Principal Investigator Email
klaribi@ch-lemans.fr
Contact Person Name
Kamel LARIBI
Contact Person Email
klaribi@ch-lemans.fr

Sponsor

Primary sponsor

Full Name
Loxo Oncology Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
IQVIA Limited
Responsibilities
IVRS – treatment randomisation; various operational roles (multiple sponsorDuties codes)
Name
Perceptive Eclinical Limited
Responsibilities
Medical Imaging Analysis
Name
Eresearchtechnology Inc.
Responsibilities
eCOA, ePRO compliance, eCOA data collection

Third parties

  • {"country":"United States","full_name":"Infinity Biologix LLC","duties_or_roles":"Correlative studies & storage (bone marrow biopsy and aspirate, optional saliva DNA, MRD, cfDNA, PBM)","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"Azenta Germany GmbH","duties_or_roles":"Long term Sample storage","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Perceptive Eclinical Limited","duties_or_roles":"Medical Imaging Analysis","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Unisphere Travel Ltd. Inc.","duties_or_roles":"Patient travel assistance","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Eli Lilly & Co.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"eCOA, ePRO compliance, eCOA data collection","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Neogenomics Inc.","duties_or_roles":"Deletion 17p Kit (FISH), IGHV, Bone Marrow","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"IVRS – treatment randomisation","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
PIRTOBRUTINIB
Active Substance
PIRTOBRUTINIB
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
200 mg
Investigational Product Name
VENETOCLAX
Active Substance
VENETOCLAX
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
400 mg
Investigational Product Name
RITUXIMAB
Active Substance
RITUXIMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Maximum Dose
500 mg/m2
Combination Treatment
Yes

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