Clinical trial • Phase III • Immunology

Obinutuzumab for Lupus nephritis | Systemic lupus erythematosus

Phase III trial of Obinutuzumab for Lupus nephritis | Systemic lupus erythematosus.

Overview

Trial Therapeutic Area
Immunology
Trial Disease
Lupus nephritis | Systemic lupus erythematosus
Trial Stage
Phase III
Drug Modality
Monoclonal antibody | Small molecule

Key dates

Initial CTIS Submission Date
24-11-2023
First CTIS Authorization Date
12-01-2024

Trial design

Randomised, open-label, placebo arm: obinutuzumab placebo (placebo infusions) plus background mycophenolate mofetil (mmf) and corticosteroids; investigational arm: obinutuzumab (gazyvaro) 1000 mg intravenous infusion on day 1 and weeks 2, 24, 26, 50, and 52 plus background mmf and corticosteroids.-controlled Phase III trial across 23 sites in France, Poland, Germany and others.

Randomised
Yes
Open Label
Yes
Comparator
Placebo arm: Obinutuzumab placebo (placebo infusions) plus background mycophenolate mofetil (MMF) and corticosteroids; Investigational arm: Obinutuzumab (Gazyvaro) 1000 mg intravenous infusion on Day 1 and Weeks 2, 24, 26, 50, and 52 plus background MMF and corticosteroids.
Target Sample Size
219

Eligibility

Recruits 219 Vulnerable population selected (isVulnerablePopulationSelected = true). Subject information sheets and informed consent forms (SIS and ICF) are provided (multiple versions listed, including language-specific documents and partner/pregnant-partner documents). No explicit assent or age-specific consent handling text is available in the provided data..

Pregnancy Exclusion
1. Pregnant or breastfeeding, or intending to become pregnant during the study or within 18 months after the final dose of obinutuzumab or placebo or within 6 weeks after the final dose of MMF
Vulnerable Population
Vulnerable population selected (isVulnerablePopulationSelected = true). Subject information sheets and informed consent forms (SIS and ICF) are provided (multiple versions listed, including language-specific documents and partner/pregnant-partner documents). No explicit assent or age-specific consent handling text is available in the provided data.

Inclusion criteria

  • {"criterion_text":"- 1. Active or active/chronic International Society of Nephrology/Renal Pathology Society (ISN/RPS) 2003 Class III or IV proliferative LN by renal biopsy performed in the 6 months prior to screening or during screening"}
  • {"criterion_text":"- 2. Systemic lupus erythematosus (SLE) according to the 2019 European League Against Rheumatism/American College of Rheumatology (EULAR/ACR) Classification Criteria, which are met by the presence of Class III or IV LN (above) and current or past positive antinuclear antibody (ANA), as evidenced by ANA at a titer of >= 1:80 on hEp-2 cells or an equivalent positive ANA test at least once"}
  • {"criterion_text":"- 3. Urinary protein-to-creatinine ratio (UPCR) ≥ 1 g/g on a 24-hour collection at screening"}
  • {"criterion_text":"- 4. Receipt of at least one dose of pulse methylprednisolone IV (≥ 250 mg) or equivalent for treatment of the current episode of active LN during the 6 months prior to screening or during screening; or to be given on Day 1 prior to the first infusion. A maximum of 3 g methylprednisolone IV or equivalent during the 4 weeks prior to screening or during screening is allowed"}

Exclusion criteria

  • {"criterion_text":"- 1. Pregnant or breastfeeding, or intending to become pregnant during the study or within 18 months after the final dose of obinutuzumab or placebo or within 6 weeks after the final dose of MMF"}
  • {"criterion_text":"- 2. Severe renal impairment, as defined by eGFR < 30 mL/min/1.73 m2 or the need for dialysis or renal transplantation"}
  • {"criterion_text":"- 3. Sclerosis in > 50% of glomeruli on renal biopsy"}
  • {"criterion_text":"- 4. Presence of rapidly progressive glomerulonephritis"}
  • {"criterion_text":"- 5. Severe, active central nervous system SLE, including retinitis, poorly controlled seizure disorder, acute confusional state, myelitis, stroke, cerebellar ataxia, or dementia"}
  • {"criterion_text":"- 6. High risk for clinically-significant bleeding or any condition requiring plasmapheresis, intravenous immunoglobulin, or acute blood product transfusions"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- 1. Proportion of patients who achieve a CRR at Week 76","definition_or_measurement_approach":"Based on the proportion of patients who achieve a complete renal response (CRR) at Week 76 (assessed at Week 76)."}

Secondary endpoints

  • {"endpoint_text":"- 1. Proportion of patients who achieve a proteinuric response at Week 76","definition_or_measurement_approach":"Assessed at Week 76 (proteinuric response at Week 76)."}
  • {"endpoint_text":"- 2. Proportion of patients who achieve CRR with successful prednisone taper at Week 76","definition_or_measurement_approach":"Assessed at Week 76 (CRR with successful prednisone taper at Week 76)."}
  • {"endpoint_text":"- 3. Proportion of patients who achieve an ORR evaluated at Week 50","definition_or_measurement_approach":"Overall renal response (ORR) evaluated at Week 50."}
  • {"endpoint_text":"- 4. Proportion of patients who experience death or renal-related events through Week 76","definition_or_measurement_approach":"Observed through Week 76 (death or renal-related events through Week 76)."}
  • {"endpoint_text":"- 5. Mean change in eGFR from baseline to Week 76","definition_or_measurement_approach":"Mean change in estimated glomerular filtration rate (eGFR) from baseline to Week 76."}
  • {"endpoint_text":"- 6. Change in anti-dsDNA titer from baseline to Week 50","definition_or_measurement_approach":"Change in anti-double stranded DNA (anti-dsDNA) titer from baseline to Week 50."}
  • {"endpoint_text":"- 7. Change in C3 from baseline to Week 50","definition_or_measurement_approach":"Change in complement C3 from baseline to Week 50."}
  • {"endpoint_text":"- 8. Change in SLEDAI-2K from baseline to Week 76","definition_or_measurement_approach":"Change in Systemic Lupus Erythematosus Disease Activity Index 2000 (SLEDAI-2K) from baseline to Week 76."}
  • {"endpoint_text":"- 9. Time to onset of CRR over the course of 76 weeks","definition_or_measurement_approach":"Time-to-event: time to onset of complete renal response (CRR) over 76 weeks."}
  • {"endpoint_text":"- 10. Change in FACIT-F scale from baseline to Week 76","definition_or_measurement_approach":"Change in Functional Assessment of Chronic Illness Therapy-Fatigue (FACIT-F) from baseline to Week 76."}
  • {"endpoint_text":"- 11. Proportion of patients who achieve CRR with serum creatinine criteria at Week 76","definition_or_measurement_approach":"Assessed at Week 76 (CRR using serum creatinine criteria)."}
  • {"endpoint_text":"- 12. Incidence and severity of adverse events, with severity determined according to National Cancer Institute Common Terminology Criteria for Adverse Events version 5.0 (NCI CTCAE v5.0)","definition_or_measurement_approach":"Incidence and severity of AEs measured and graded per NCI CTCAE v5.0."}
  • {"endpoint_text":"- 13. To characterize adverse events of special interest, including, among others, infusion-related reactions (IRRs), neutropenia, infections, and thrombocytopenia","definition_or_measurement_approach":"Characterisation of prespecified adverse events of special interest (including IRRs, neutropenia, infections, thrombocytopenia)."}
  • {"endpoint_text":"- 14. Change from baseline in targeted vital signs","definition_or_measurement_approach":"Change from baseline in selected vital sign measurements."}
  • {"endpoint_text":"- 15. Change from baseline in targeted clinical laboratory test results","definition_or_measurement_approach":"Change from baseline in specified clinical laboratory tests."}
  • {"endpoint_text":"- 16. Maximum observed concentration (Cmax) of obinutuzumab","definition_or_measurement_approach":"Pharmacokinetic endpoint: observed Cmax of obinutuzumab."}
  • {"endpoint_text":"- 17. Minimum observed concentration (Cmin) of obinutuzumab","definition_or_measurement_approach":"Pharmacokinetic endpoint: observed Cmin of obinutuzumab."}
  • {"endpoint_text":"- 18. Area under concentration-time curve (AUC) of obinutuzumab","definition_or_measurement_approach":"Pharmacokinetic endpoint: AUC of obinutuzumab."}
  • {"endpoint_text":"- 19. Clearance (CL) of obinutuzumab","definition_or_measurement_approach":"Pharmacokinetic endpoint: clearance of obinutuzumab."}
  • {"endpoint_text":"- 20. Prevalence of anti-drug antibodies (ADAs) at baseline and incidence of ADAs post-treatment during the study","definition_or_measurement_approach":"Immunogenicity endpoint: prevalence and incidence of anti-drug antibodies at baseline and post-treatment."}
  • {"endpoint_text":"- 21. Total peripheral B-cell count at specified timepoints","definition_or_measurement_approach":"Total peripheral B-cell counts measured at prespecified timepoints."}
  • {"endpoint_text":"- 22. Time to lupus nephritis (LN) flare","definition_or_measurement_approach":"Time-to-event: time to LN flare."}
  • {"endpoint_text":"- 23. Time to unfavorable kidney outcome","definition_or_measurement_approach":"Time-to-event: time to unfavorable renal outcome."}
  • {"endpoint_text":"- 24. Mean change in eGFR from baseline, eGFR slope and proportion of participants achieving CRR over time","definition_or_measurement_approach":"Mean change and slope of eGFR from baseline and longitudinal proportion achieving CRR over time."}

Recruitment

Planned Sample Size
219
Recruitment Window Months
99
Consent Approach
Participants provide informed consent prior to screening ("Consenting patients will enter a screening period"). Subject information sheets and informed consent forms (SIS and ICF) are provided; multiple language and country-specific ICF/SIS documents are listed (including Russian versions, country-specific ICFs, pregnancy/partner ICFs, biopsy optional ICFs, mobile nursing ICFs). No explicit assent process or age-specific consent handling is described in the provided data.

Geography

Total Number Of Sites
23
Total Number Of Participants
52

France

Earliest CTIS Part Ii Submission Date
05-12-2023
Latest Decision Or Authorization Date
27-01-2026
Processing Time Days
784
Number Of Sites
5
Number Of Participants
13

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Internal Medicine
Principal Investigator Name
Zahir Amoura
Principal Investigator Email
zahir.amoura@aphp.fr
Contact Person Name
Zahir Amoura
Contact Person Email
zahir.amoura@aphp.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Nephrology
Principal Investigator Name
Dominique Chauveau
Principal Investigator Email
chauveau.d@chu-toulouse.fr
Contact Person Name
Dominique Chauveau
Contact Person Email
chauveau.d@chu-toulouse.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Nephrology
Principal Investigator Name
Eric DAUGAS
Principal Investigator Email
eric.daugas@aphp.fr
Contact Person Name
Eric DAUGAS
Contact Person Email
eric.daugas@aphp.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Internal Medicine
Principal Investigator Name
Eric HACHULLA
Principal Investigator Email
Eric.HACHULLA@chu-lille.fr
Contact Person Name
Eric HACHULLA
Contact Person Email
Eric.HACHULLA@chu-lille.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Nephrology
Principal Investigator Name
Nizar JOHER
Principal Investigator Email
nizar.joher@aphp.fr
Contact Person Name
Nizar JOHER
Contact Person Email
nizar.joher@aphp.fr

Poland

Earliest CTIS Part Ii Submission Date
05-12-2023
Latest Decision Or Authorization Date
30-01-2026
Processing Time Days
787
Number Of Sites
5
Number Of Participants
10

Sites

Site Name
Narodowy Instytut Geriatrii Reumatologii I Rehabilitacji Im Prof. Dr Hab. Med. Eleonory Reicher
Department Name
Klinika Wczesnego Zapalenia Stawów
Principal Investigator Name
Brygida Kwiatkowska
Principal Investigator Email
brygida.kwiatkowska@spartanska.pl
Contact Person Name
Brygida Kwiatkowska
Site Name
Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu
Department Name
Klinika Nefrologii, Medycyny Transplantacyjnej i Chorob Wewnetrznych
Principal Investigator Name
Miroslaw Banasik
Principal Investigator Email
kln@usk.wroc.pl
Contact Person Name
Miroslaw Banasik
Contact Person Email
kln@usk.wroc.pl
Site Name
Medyczne Centrum Hetmańska
Principal Investigator Name
Piotr Leszczyński
Principal Investigator Email
piotr.leszczynski@centrum-hetmanska.pl
Contact Person Name
Piotr Leszczyński
Site Name
Rheuma Medicus Zaklad Opieki Zdrowotnej
Principal Investigator Name
Maria Rell-Bakalarska
Principal Investigator Email
rell-bakalarska@wp.pl
Contact Person Name
Maria Rell-Bakalarska
Contact Person Email
rell-bakalarska@wp.pl
Site Name
Szpital Kliniczny Dzieciątka Jezus
Department Name
Klinika Medycyny Transplantacyjnej, Nefrologii i Chorób Wewnętrznych
Principal Investigator Name
Teresa Baczkowska
Principal Investigator Email
teresa.baczkowska@wum.edu.pl
Contact Person Name
Teresa Baczkowska
Contact Person Email
teresa.baczkowska@wum.edu.pl

Germany

Earliest CTIS Part Ii Submission Date
05-12-2023
Latest Decision Or Authorization Date
28-01-2026
Processing Time Days
785
Number Of Sites
5
Number Of Participants
12

Sites

Site Name
Universitaetsklinikum Carl Gustav Carus Dresden an der Technischen Universitaet Dresden AöR
Department Name
Medizinische Klinik und Poliklinik III Nephrologie
Principal Investigator Name
Christian Hugo
Principal Investigator Email
christian.hugo@uniklinikum-dresden.de
Contact Person Name
Christian Hugo
Site Name
Staedtisches Klinikum Dresden
Department Name
1. Medizinische Klinik
Principal Investigator Name
Olaf Nestler
Principal Investigator Email
olaf.nestler@klinikum-dresden.de
Contact Person Name
Olaf Nestler
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Medizinische Klinik II
Principal Investigator Name
Joerg Henes
Principal Investigator Email
joerg.henes@med.uni-tuebingen.de
Contact Person Name
Joerg Henes
Site Name
Medical Center - University Of Freiburg
Department Name
Klinik für Rheumatologie und Klinische Immunologie
Principal Investigator Name
Stephanie Finzel
Principal Investigator Email
stephanie.finzel@uniklinik-freiburg.de
Contact Person Name
Stephanie Finzel
Site Name
Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
Department Name
I. Medizinische Klinik und Poliklinik
Principal Investigator Name
Andreas Schwarting
Principal Investigator Email
Andreas.Schwarting@unimedizin-Mainz.de
Contact Person Name
Andreas Schwarting

Spain

Earliest CTIS Part Ii Submission Date
05-12-2023
Latest Decision Or Authorization Date
02-02-2026
Processing Time Days
790
Number Of Sites
3
Number Of Participants
10

Sites

Site Name
Hospital Universitari Vall D Hebron
Department Name
Servicio de Medicina Interna
Principal Investigator Name
Josefina Cortés Hernández
Principal Investigator Email
fina.cortes@vhir.org
Contact Person Name
Josefina Cortés Hernández
Contact Person Email
fina.cortes@vhir.org
Site Name
Hospital Clinic De Barcelona
Department Name
Servicio de Nefrología
Principal Investigator Name
Luis Quintana Porras
Principal Investigator Email
mmr@clinic.cat
Contact Person Name
Luis Quintana Porras
Contact Person Email
mmr@clinic.cat
Site Name
Hospital Universitario 12 De Octubre
Department Name
Servicio de Reumatología
Principal Investigator Name
María Galindo Izquierdo
Principal Investigator Email
mgalindo@h12o.es
Contact Person Name
María Galindo Izquierdo
Contact Person Email
mgalindo@h12o.es

Italy

Earliest CTIS Part Ii Submission Date
05-12-2023
Latest Decision Or Authorization Date
13-05-2026
Processing Time Days
890
Number Of Sites
5
Number Of Participants
7

Sites

Site Name
IRCCS Ospedale Policlinico San Martino
Department Name
Nefrologia
Principal Investigator Name
Francesca Viazzi
Principal Investigator Email
francesca.viazzi@unige.it
Contact Person Name
Francesca Viazzi
Contact Person Email
francesca.viazzi@unige.it
Site Name
Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
Department Name
U.O. Nefrologia
Principal Investigator Name
Federica Mescia
Principal Investigator Email
federica.mescia@unibs.it
Contact Person Name
Federica Mescia
Contact Person Email
federica.mescia@unibs.it
Site Name
Careggi University Hospital
Department Name
Medicina Interna Interdisciplinare
Principal Investigator Name
Elena Silvestri
Principal Investigator Email
elena.silvestri@unifi.it
Contact Person Name
Elena Silvestri
Contact Person Email
elena.silvestri@unifi.it
Site Name
University Hospital Consorziale Policlinico
Department Name
SC Nefrologia, Dialisi e Trapianto
Principal Investigator Name
Loreto Gesualdo
Principal Investigator Email
loreto.gesualdo@uniba.it
Contact Person Name
Loreto Gesualdo
Contact Person Email
loreto.gesualdo@uniba.it
Site Name
Azienda Ospedale-Universita Padova
Department Name
UOC Reumatologia
Principal Investigator Name
Luca Iaccarino
Principal Investigator Email
luca.iaccarino@unipd.it
Contact Person Name
Luca Iaccarino
Contact Person Email
luca.iaccarino@unipd.it

Sponsor

Primary sponsor

Full Name
F. Hoffmann-La Roche AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
Medical Research Network Limited
Responsibilities
Home nursing
Name
Almac Clinical Technologies LLC
Responsibilities
Drug Management, Randomization
Name
Labcorp Central Laboratory Services LP
Responsibilities
Central laboratory services

Third parties

  • {"country":"United Kingdom","full_name":"Medical Research Network Limited","duties_or_roles":"Home nursing","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Technologies LLC","duties_or_roles":"Drug Management, Randomization","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Gazyvaro 1,000 mg concentrate for solution for infusion.
Active Substance
Obinutuzumab
Modality
Monoclonal antibody
Routes Of Administration
Intravenous infusion
Route
Intravenous infusion
Authorisation Status
Marketing authorisation exists (EU/1/14/937/001) - relabeled & repackaged for clinical trial use
Starting Dose
1000 mg IV (Day 1)
Dose Levels
1000 mg per infusion; maximum total dose amount 6000 mg
Frequency
Day 1 and Weeks 2, 24, 26, 50, and 52
Maximum Dose
1000 mg per infusion; max total 6000 mg
Investigational Product Name
Myfenax 500 mg film-coated tablets
Active Substance
Mycophenolate mofetil
Modality
Small molecule
Routes Of Administration
Oral
Route
Oral
Authorisation Status
Marketing authorisation exists (PRD3931840) - relabeled and repackaged for clinical trial use
Frequency
Background immunosuppression (MMF) per protocol (not specified in dataset)
Maximum Dose
Max daily dose amount 2500 mg (as listed)
Combination Treatment
Yes

Related trials

Other published trials that may interest you.