Clinical trial • Phase IV • Gastroenterology

METFORMIN EMBONATE for Portal hypertension | Cirrhosis

Phase IV trial of METFORMIN EMBONATE for Portal hypertension | Cirrhosis. Randomised, placebo 515 (placebo)-controlled. 76 participants.

Overview

Trial Therapeutic Area
Gastroenterology
Trial Disease
Portal hypertension | Cirrhosis
Trial Stage
Phase IV
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
07-06-2024
First CTIS Authorization Date
04-09-2024

Trial design

Randomised, placebo 515 (placebo)-controlled Phase IV trial across 10 sites in France.

Randomised
Yes
Comparator
Placebo 515 (placebo)
Target Sample Size
76
Trial Duration For Participant
28

Eligibility

Recruits 76 No vulnerable populations selected. Written informed consent to participate is required from participants. Study population restricted to adults (Age ≥ 18 years). No assent or parental consent procedures described..

Pregnancy Exclusion
- For child-bearing aged women, contraception using oestroprogestative, progestative, intrauterine device, or mechanical contraception
Vulnerable Population
No vulnerable populations selected. Written informed consent to participate is required from participants. Study population restricted to adults (Age ≥ 18 years). No assent or parental consent procedures described.

Inclusion criteria

  • {"criterion_text":"- Age ≥ 18 years\n- Absence of hepatocellular carcinoma outside at least one nodule > 3 cm in diameter, or more than 3 nodules, on ultrasound, CT-scan or MRI performed during the previous 6 months\n- Written informed consent to participate in the study\n- Medical insurance coverage\n- For child-bearing aged women, contraception using oestroprogestative, progestative, intrauterine device, or mechanical contraception\n- Diagnosis of cirrhosis based on a liver biopsy, or on clinical, biological, endoscopic, and radiological evidence\n- Active cause of cirrhosis, or resolution (alcohol cessation, sustained virological response to direct-acting antiviral treatment for HCV, initiation of nucleoside/nucleotide analog treatment for HBV) for at least 6 months\n- Child-Pugh A or B\n- High likelihood of HVPG ≥ 12 mm Hg based on investigator’s judgement, _confer criteria in the protocole\n- Treatment with carvedilol (≥ 6,25 mg/day) at a stable dose for at least one month"}

Exclusion criteria

  • {"criterion_text":"- Serum total bilirubin > 50 µmol/L\n- Prothrombin ratio < 50 %\n- Transaminases > 5 ULN\n- Need for at least one paracentesis for ascites fluid evacuation in the last 6 months"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- the hepatic venous pressure gradient (HVPG) after 28 days of treatment","definition_or_measurement_approach":"Measurement of hepatic venous pressure gradient (HVPG) after 28 days of treatment"}
  • {"endpoint_text":"- Endpoints of the ancillary study: Changes in systemic haemodynamics and HVPG 30 minutes after a meal consisting of two 200 mL bottles of hypercaloric/hyperprotic Fortimel Energy","definition_or_measurement_approach":"Postprandial assessment: changes in systemic haemodynamics and HVPG measured 30 minutes after a standardized meal (two 200 mL bottles of Fortimel Energy)"}

Recruitment

Planned Sample Size
76
Recruitment Window Months
24
Consent Approach
Written informed consent is required from participants. Subject information and informed consent form document available (L1_SIS-ICF_2023-504831-42-00_adults). Study restricted to adults (Age ≥ 18 years). No assent or multiple-language consent details provided.

Geography

Total Number Of Sites
10
Total Number Of Participants
76

France

Earliest CTIS Part Ii Submission Date
14-08-2024
Latest Decision Or Authorization Date
02-07-2025
Processing Time Days
322
Number Of Sites
10
Number Of Participants
76

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hépatologie
Principal Investigator Name
BLAISE Lorraine
Principal Investigator Email
lorraine.blaise@aphp.fr
Contact Person Name
BLAISE Lorraine
Contact Person Email
lorraine.blaise@aphp.fr
Site Name
Hospital Foch
Department Name
service de médecine interne
Principal Investigator Name
Sophie HILLAIRE
Principal Investigator Email
s.hillaire@hopital-foch.com
Contact Person Name
Sophie HILLAIRE
Contact Person Email
s.hillaire@hopital-foch.com
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hépatologie
Principal Investigator Name
Anna SESSA
Principal Investigator Email
anna.sessa@aphp.fr
Contact Person Name
Anna SESSA
Contact Person Email
anna.sessa@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hépatologie
Principal Investigator Name
OZENNE Violaine
Principal Investigator Email
violaine.ozenne@aphp.fr
Contact Person Name
OZENNE Violaine
Contact Person Email
violaine.ozenne@aphp.fr
Site Name
Centre Hospitalier General De St Denis
Department Name
Service d'Hépatogastro-entérologie.
Principal Investigator Name
Marion JAGER
Principal Investigator Email
marion.jager@ch-stdenis.fr
Contact Person Name
Marion JAGER
Contact Person Email
marion.jager@ch-stdenis.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hépatologie
Principal Investigator Name
Vincent MALLET
Principal Investigator Email
vincent.mallet@aphp.fr
Contact Person Name
Vincent MALLET
Contact Person Email
vincent.mallet@aphp.fr
Site Name
Centre Hospitalier Intercommunal Creteil
Department Name
Service d'Hépatologie
Principal Investigator Name
ROSA Isabelle
Principal Investigator Email
isabelle.rosa@chicreteil.fr
Contact Person Name
ROSA Isabelle
Contact Person Email
isabelle.rosa@chicreteil.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hépatogastro-entérologie.
Principal Investigator Name
Dominique THABUT Dominique
Principal Investigator Email
dominique.thabut@aphp.fr
Contact Person Name
Dominique THABUT Dominique
Contact Person Email
dominique.thabut@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hépatologie
Principal Investigator Name
Ilias KOUNIS
Principal Investigator Email
ilias.kounis@aphp.fr
Contact Person Name
Ilias KOUNIS
Contact Person Email
ilias.kounis@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hépatologie
Principal Investigator Name
MOGA Lucile
Principal Investigator Email
lucile.moga@aphp.fr
Contact Person Name
MOGA Lucile
Contact Person Email
lucile.moga@aphp.fr

Sponsor

Primary sponsor

Full Name
Assistance Publique Hopitaux De Paris
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
France

Investigational products

Investigational Product Name
METFORMIN
Active Substance
METFORMIN EMBONATE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL USE
Authorisation Status
Authorised (product with EU MP number SCP10310250 listed)
Maximum Dose
1 g/day
Investigational Product Name
Placebo 515
Modality
Other

Related trials

Other published trials that may interest you.