Clinical trial • Phase III • Oncology

Lenalidomide for Multiple myeloma

Phase III trial of Lenalidomide for Multiple myeloma.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Multiple myeloma
Trial Stage
Phase III
Drug Modality
Small molecule | Monoclonal antibody | Cell therapy
Orphan Drug
Yes

Key dates

Initial CTIS Submission Date
28-03-2024
First CTIS Authorization Date
01-05-2024

Trial design

Randomised, dvrd (daratumumab + bortezomib + lenalidomide + dexamethasone) followed by autologous stem cell transplant (asct) (comparator arm); dvrd followed by ciltacabtagene autoleucel (cilta-cel) and lenalidomide therapy (investigational arm). dose/schedule details not specified in the ctis record.-controlled Phase III trial across 45 sites in Czechia, Greece, Norway and others.

Randomised
Yes
Comparator
DVRd (daratumumab + bortezomib + lenalidomide + dexamethasone) followed by Autologous Stem Cell Transplant (ASCT) (comparator arm); DVRd followed by ciltacabtagene autoleucel (cilta-cel) and lenalidomide therapy (investigational arm). Dose/schedule details not specified in the CTIS record.
Target Sample Size
366

Eligibility

Recruits 366 Vulnerable population flag selected. Trial enrols adults (minimum age 18 years) only; informed consent is obtained using subject information and informed consent forms (multiple L1_ICF Main Adult documents). Specific 'Other Pregnant Partner' ICF documents are provided. Participant information/consent materials are available in multiple country/language versions (examples in the public documents include English, Dutch, French, German, Spanish, Czech, Greek, Norwegian, Swedish). No assent process for minors is indicated (minors are excluded)..

Vulnerable Population
Vulnerable population flag selected. Trial enrols adults (minimum age 18 years) only; informed consent is obtained using subject information and informed consent forms (multiple L1_ICF Main Adult documents). Specific 'Other Pregnant Partner' ICF documents are provided. Participant information/consent materials are available in multiple country/language versions (examples in the public documents include English, Dutch, French, German, Spanish, Czech, Greek, Norwegian, Swedish). No assent process for minors is indicated (minors are excluded).

Inclusion criteria

  • {"criterion_text":"- 18 years of age or older\n- Participants with documented NDMM according to IMWG diagnostic criteria, for whom high-dose therapy and ASCT are part of the intended initial treatment plan.\n- Measurable disease, as assessed by central laboratory, at screening as defined by any of the following: 1) Serum monoclonal paraprotein (M-protein) level ≥1.0 g/dL or urine M-protein level ≥200 mg/24 hours; or 2) Light chain MM without measurable disease in serum or urine: serum Ig free-light chain (FLC) ≥10 mg/dL and abnormal serum Ig kappa lambda FLC ratio.\n- ECOG performance status of grade 0 or 1\n- Clinical laboratory values within prespecified range as listed in 5.1.1, page 55 of the protocol."}

Exclusion criteria

  • {"criterion_text":"- Prior treatment with CAR-T therapy directed at any target.\n- Any prior BCMA target therapy.\n- Any prior therapy for MM or smoldering myeloma other than a short course of corticosteroids\n- Received a strong cytochrome P450 (CYP)3A4 inducer within 5 halflives prior to randomization\n- Received or plans to receive any live, attenuated vaccine (except for COVID-19 vaccines) within 4 weeks prior to randomization.\n- Known active, or prior history of central nervous system (CNS) involvement or clinical signs of meningeal involvement of MM\n- Stroke or seizure within 6 months of signing Informed Consent Form (ICF)"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- PFS","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Sustained MRD-negative CR, defined as MRD-negative CR for at a minimum 12 months duration, with MRD status determined by NGS with a sensitivity of at least 10-5","definition_or_measurement_approach":"MRD status determined by NGS with a sensitivity of at least 10-5"}

Secondary endpoints

  • {"endpoint_text":"- Overall response (PR or better) status and CR or better status","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Overall MRD-negative CR with a sensitivity of at least 10-5","definition_or_measurement_approach":"MRD assessed by NGS with sensitivity ≥10-5"}
  • {"endpoint_text":"- Time to subsequent antimyeloma therapy","definition_or_measurement_approach":""}
  • {"endpoint_text":"- PFS on next-line therapy (PFS2)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Incidence, severity, and type of AEs, clinical laboratory results, and other safety parameters","definition_or_measurement_approach":""}
  • {"endpoint_text":"- OS","definition_or_measurement_approach":""}
  • {"endpoint_text":"- PK and pharmacodynamic markers by protein, DNA, or RNA analyses, including but not limited to, systemic inflammatory cytokine concentrations, markers of CAR-T cell expansion (proliferation) and persistence via monitoring of cilta-cel-positive cellular concentrations, and cilta-cel transgene levels","definition_or_measurement_approach":"PK and pharmacodynamic markers measured by protein/DNA/RNA analyses including systemic inflammatory cytokine concentrations and CAR-T expansion/persistence (cilta-cel-positive cellular concentrations and transgene levels)"}
  • {"endpoint_text":"- Mean change from baseline in the EORTC-QLQ-C30, MySIm-Q, and EQ-5D-5L subscale scores and the PROCTCAE items","definition_or_measurement_approach":"PRO instruments: EORTC-QLQ-C30, MySIm-Q, EQ-5D-5L and PRO-CTCAE"}
  • {"endpoint_text":"- Time to improvement or worsening of symptoms, functioning, and overall well-being","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Improvement or worsening in the EORTC-QLQ- C30 and MySIm-Q subscale scores using the PGIS to calculate the meaningful change threshold","definition_or_measurement_approach":"Use PGIS to calculate meaningful change thresholds for EORTC-QLQ-C30 and MySIm-Q subscales"}
  • {"endpoint_text":"- Presence of RCL","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
366
Recruitment Window Months
180
Consent Approach
Informed consent is obtained from each adult participant using subject information and informed consent forms (L1_ICF Main Adult and related L1/L2 documents). Country-specific ICFs and patient-facing information documents are provided (multiple language versions available in the public documents list, e.g., English, Dutch, French, German, Spanish, Czech, Greek, Norwegian, Swedish). Specific 'Other Pregnant Partner' information/ICF documents are also available.

Geography

Total Number Of Sites
45
Total Number Of Participants
440

Czechia

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
08-10-2025
Processing Time Days
534
Number Of Sites
5
Number Of Participants
41

Sites

Site Name
Vseobecna Fakultni Nemocnice V Praze
Department Name
Z97CZ10004: I. Interni klinika - klinika hematologie VFN a 1. LF UK v Praze
Principal Investigator Name
Ivan Spicka
Principal Investigator Email
spicka@cesnet.cz
Contact Person Name
Ivan Spicka
Contact Person Email
spicka@cesnet.cz
Site Name
Fakultni Nemocnice Plzen
Department Name
Z97CZ10005: Hematologicko-onkologicke odd.
Principal Investigator Name
Alexandra Jungova
Principal Investigator Email
jungovaa@fnplzen.cz
Contact Person Name
Alexandra Jungova
Contact Person Email
jungovaa@fnplzen.cz
Site Name
Fakultni Nemocnice Ostrava
Department Name
Z97CZ10001: Klinika hematoonkologie
Principal Investigator Name
Roman Hajek
Principal Investigator Email
roman.hajek@fno.cz
Contact Person Name
Roman Hajek
Contact Person Email
roman.hajek@fno.cz
Site Name
Fakultni Nemocnice Brno
Department Name
Z97CZ10002: Int. hemat. a onkol. klinika
Principal Investigator Name
Ludek Pour
Principal Investigator Email
pour.ludek@fnbrno.cz
Contact Person Name
Ludek Pour
Contact Person Email
pour.ludek@fnbrno.cz
Site Name
Fakultni Nemocnice Hradec Kralove
Department Name
Z97CZ10003: IV. interni hematologicka klinika
Principal Investigator Name
Jakub Radocha
Principal Investigator Email
jakub.radocha@centrum.cz
Contact Person Name
Jakub Radocha
Contact Person Email
jakub.radocha@centrum.cz

Greece

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
09-10-2025
Processing Time Days
535
Number Of Sites
2
Number Of Participants
23

Sites

Site Name
Geniko Nosokomeio Thessalonikis George Papanikolaou
Department Name
Z97GR10001:Hematology and HCT unit
Principal Investigator Name
Ioanna Sakellari
Principal Investigator Email
ioannamarilena@gmail.com
Contact Person Name
Ioanna Sakellari
Contact Person Email
ioannamarilena@gmail.com
Site Name
Alexandra Hospital
Department Name
Z97GR10002:Clinical Therapeutics
Principal Investigator Name
Evangelos Terpos
Principal Investigator Email
eterpos@med.uoa.gr
Contact Person Name
Evangelos Terpos
Contact Person Email
eterpos@med.uoa.gr

Norway

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
09-10-2025
Processing Time Days
535
Number Of Sites
1
Number Of Participants
18

Sites

Site Name
Oslo University Hospital HF
Department Name
Z97NO10001: Avdeling for blodsykdommer
Principal Investigator Name
Ingerid Weum Abrahamsen
Principal Investigator Email
inabra@ous-hf.no
Contact Person Name
Ingerid Weum Abrahamsen
Contact Person Email
inabra@ous-hf.no

Belgium

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
13-10-2025
Processing Time Days
539
Number Of Sites
4
Number Of Participants
40

Sites

Site Name
Institut Jules Bordet
Department Name
Oncologie Médicale
Principal Investigator Name
Marie Vercruyssen
Principal Investigator Email
Marie.Vercruyssen@bordet.be
Contact Person Name
Marie Vercruyssen
Contact Person Email
Marie.Vercruyssen@bordet.be
Site Name
Universitair Ziekenhuis Gent
Department Name
Z97BE10004;Hematology
Principal Investigator Name
Nicolas KINT
Principal Investigator Email
nicolas.kint@uzgent.be
Contact Person Name
Nicolas KINT
Contact Person Email
nicolas.kint@uzgent.be
Site Name
Antwerp University Hospital
Department Name
Z97BE10001;Hematology
Principal Investigator Name
Sebastien Anguille
Principal Investigator Email
sebastien.anguille@uza.be
Contact Person Name
Sebastien Anguille
Contact Person Email
sebastien.anguille@uza.be
Site Name
UZ Leuven
Department Name
Z97BE10003;Hematology
Principal Investigator Name
Michel Delforge
Principal Investigator Email
Michel.delforge@uzleuven.be
Contact Person Name
Michel Delforge
Contact Person Email
Michel.delforge@uzleuven.be

Netherlands

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
06-10-2025
Processing Time Days
532
Number Of Sites
5
Number Of Participants
81

Sites

Site Name
Radboud universitair medisch centrum / RADBOUDUMC
Department Name
Z97NL10002: Hematology
Principal Investigator Name
Elizabeth de Kort
Principal Investigator Email
Elizabeth.deKort@radboudumc.nl
Contact Person Name
Elizabeth de Kort
Contact Person Email
Elizabeth.deKort@radboudumc.nl
Site Name
Universitair Medisch Centrum Utrecht
Department Name
Z97NL10003: Hematology
Principal Investigator Name
Monique Minnema
Principal Investigator Email
m.c.minnema@umcutrecht.nl
Contact Person Name
Monique Minnema
Contact Person Email
m.c.minnema@umcutrecht.nl
Site Name
Universitair Medisch Centrum Groningen
Department Name
Z97NL10004: Hematology
Principal Investigator Name
Wilfried Roeloffzen
Principal Investigator Email
w.w.h.roeloffzen@umcg.nl
Contact Person Name
Wilfried Roeloffzen
Contact Person Email
w.w.h.roeloffzen@umcg.nl
Site Name
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Department Name
Z97NL10001: Hematology
Principal Investigator Name
Annemiek Broijl
Principal Investigator Email
a.broyl@erasmusmc.nl
Contact Person Name
Annemiek Broijl
Contact Person Email
a.broyl@erasmusmc.nl
Site Name
Amsterdam UMC Stichting
Department Name
Z97NL10005: Hematology
Principal Investigator Name
Niels van de Donk
Principal Investigator Email
n.vandedonk@amsterdamumc.nl
Contact Person Name
Niels van de Donk
Contact Person Email
n.vandedonk@amsterdamumc.nl

France

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
10-10-2025
Processing Time Days
536
Number Of Sites
7
Number Of Participants
29

Sites

Site Name
Centre Hospitalier Lyon Sud
Department Name
Z97FR10005: Service d'Hématologie Clinique
Principal Investigator Name
Lionel Karlin
Principal Investigator Email
lionel.karlin@chu-lyon.fr
Contact Person Name
Lionel Karlin
Contact Person Email
lionel.karlin@chu-lyon.fr
Site Name
Institut Universitaire Du Cancer Toulouse-Oncopole
Department Name
Z97FR10004: Hématologie
Principal Investigator Name
Aurore Perrot
Principal Investigator Email
perrot.aurore@iuct-oncopole.fr
Contact Person Name
Aurore Perrot
Contact Person Email
perrot.aurore@iuct-oncopole.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Z97FR10002: Service des Maladies du Sang
Principal Investigator Name
Salomon MANIER
Principal Investigator Email
salomon.manier@chru-lille.fr
Contact Person Name
Salomon MANIER
Contact Person Email
salomon.manier@chru-lille.fr
Site Name
Hopital Saint Louis
Department Name
Z97FR10001: Immunologie-Hematologie Clinique
Principal Investigator Name
Bertrand MANIER
Principal Investigator Email
bertrand.arnulf@aphp.fr
Contact Person Name
Bertrand MANIER
Contact Person Email
bertrand.arnulf@aphp.fr
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Z97FR10006: Service d’Hématologie et Thérapie Cellulaire
Principal Investigator Name
Xavier Leleu
Principal Investigator Email
xavier.leleu@chu-poitiers.fr
Contact Person Name
Xavier Leleu
Contact Person Email
xavier.leleu@chu-poitiers.fr
Site Name
Hopital Saint Antoine
Department Name
Z97FR10007: Service d'Hématologie Clinique et Thérapie Cellulaire
Principal Investigator Name
Mohamad Mohty
Principal Investigator Email
mohamad.mohty@inserm.fr
Contact Person Name
Mohamad Mohty
Contact Person Email
mohamad.mohty@inserm.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Z97FR10003: Hématologie Clinique
Principal Investigator Name
Philippe Moreau
Principal Investigator Email
philippe.moreau@chu-nantes.fr
Contact Person Name
Philippe Moreau
Contact Person Email
philippe.moreau@chu-nantes.fr

Germany

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
03-11-2025
Processing Time Days
560
Number Of Sites
6
Number Of Participants
51

Sites

Site Name
Universitaetsklinikum Leipzig AöR
Department Name
Z97DE10006: University Cancer Center Dpt.
Principal Investigator Name
Vladan Vucinic
Principal Investigator Email
vladan.vucinic@medizin.uni-leipzig.de
Contact Person Name
Vladan Vucinic
Site Name
Universitaetsklinikum Wuerzburg AöR
Department Name
Z97DE10002:Medizinische Klinik und Poliklinik II
Principal Investigator Name
Hermann Einsele
Principal Investigator Email
einsele_h@ukw.de
Contact Person Name
Hermann Einsele
Contact Person Email
einsele_h@ukw.de
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Z97DE10001: Onkologie, Hämatologie, Klinische Immunologie, Rheumatologie und Pulmologie
Principal Investigator Name
Britta Besemer
Principal Investigator Email
britta.besemer@med.uni-tuebingen
Contact Person Name
Britta Besemer
Site Name
University Hospital Cologne AöR
Department Name
Z97DE10004: Innere Medizin I
Principal Investigator Name
Christoph Scheid
Principal Investigator Email
c.scheid@uni-koeln.de
Contact Person Name
Christoph Scheid
Contact Person Email
c.scheid@uni-koeln.de
Site Name
Universitaetsklinikum Heidelberg AöR
Department Name
Z97DE10003: Abteilung Innere Medizin V, Haematologie, Onkologie, Rheumatologie
Principal Investigator Name
Marc Steffen Raab
Principal Investigator Email
marc.raab@med.uni-heidelberg.de
Contact Person Name
Marc Steffen Raab
Site Name
University Medical Center Hamburg-Eppendorf
Department Name
Z97DE10007: Innere Medizin
Principal Investigator Name
Katja Weisel
Principal Investigator Email
k.weisel@uke.de
Contact Person Name
Katja Weisel
Contact Person Email
k.weisel@uke.de

Spain

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
04-11-2025
Processing Time Days
561
Number Of Sites
11
Number Of Participants
141

Sites

Site Name
Clinica Universidad De Navarra
Department Name
Z97ES10010: Hematología
Principal Investigator Name
Paula Rodríguez Otero
Principal Investigator Email
paurodriguez@unav.es
Contact Person Name
Paula Rodríguez Otero
Contact Person Email
paurodriguez@unav.es
Site Name
Hospital Universitario De Salamanca
Department Name
Z97ES10007: Hematología
Principal Investigator Name
María Mateos Manteca
Principal Investigator Email
mvmateos@usal.es
Contact Person Name
María Mateos Manteca
Contact Person Email
mvmateos@usal.es
Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Z97ES10005: Hematología
Principal Investigator Name
Maria Jesus Blanchard Rodriguez
Principal Investigator Email
mariajesus.blanchard@salud.madrid.org
Contact Person Name
Maria Jesus Blanchard Rodriguez
Site Name
Institut Catala D'oncologia
Department Name
Z97ES10011: Hematologia
Principal Investigator Name
Anna Sureda Balari
Principal Investigator Email
asureda@iconcologia.net
Contact Person Name
Anna Sureda Balari
Contact Person Email
asureda@iconcologia.net
Site Name
Complexo Hospitalario Universitario De Santiago
Department Name
Z97ES10004: Hematología
Principal Investigator Name
Marta González Pérez
Principal Investigator Email
marta.sonia.gonzalez.perez@sergas.es
Contact Person Name
Marta González Pérez
Site Name
Hospital Universitario 12 De Octubre
Department Name
Z97ES10006: Hematología y Hemoterápia
Principal Investigator Name
Joaquin Martinez Lopez
Principal Investigator Email
jmarti01@med.ucm.es
Contact Person Name
Joaquin Martinez Lopez
Contact Person Email
jmarti01@med.ucm.es
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Z97ES10009: Hematologia y Hemoterapia
Principal Investigator Name
Juan Reguera Ortega
Principal Investigator Email
juanl.reguera.sspa@juntadeandalucia.es
Contact Person Name
Juan Reguera Ortega
Site Name
Hospital Clinic De Barcelona
Department Name
Z97ES10002: Hematología
Principal Investigator Name
Carlos Fernández De Larrea Rodríguez
Principal Investigator Email
cfernan1@clinic.cat
Contact Person Name
Carlos Fernández De Larrea Rodríguez
Contact Person Email
cfernan1@clinic.cat
Site Name
Institut Catala D'oncologia (Badalona)
Department Name
Z97ES10008: Hematología
Principal Investigator Name
Albert Oriol-Rocafiguera
Principal Investigator Email
aoriol@iconcologia.net
Contact Person Name
Albert Oriol-Rocafiguera
Contact Person Email
aoriol@iconcologia.net
Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Z97ES10001: Hematología
Principal Investigator Name
Javier De la Rubia Comos
Principal Investigator Email
delarubia_jav@gva.es
Contact Person Name
Javier De la Rubia Comos
Contact Person Email
delarubia_jav@gva.es
Site Name
Hospital General Universitario Gregorio Maranon
Department Name
Z97ES10003: Hematologia
Principal Investigator Name
Cristina Encinas Rodriguez
Principal Investigator Email
cristina.encinas@salud.madrid.org
Contact Person Name
Cristina Encinas Rodriguez

Sweden

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
13-01-2026
Processing Time Days
631
Number Of Sites
4
Number Of Participants
16

Sites

Site Name
Sahlgrenska University Hospital-Vaestra Goetalandsregionen
Department Name
Z97SE10002:Sektionen för Hematologi och K
Principal Investigator Name
Markus Hansson
Principal Investigator Email
markus.hansson.2@gu.se
Contact Person Name
Markus Hansson
Contact Person Email
markus.hansson.2@gu.se
Site Name
University Of Skane
Department Name
Z97SE10001:Outpatient department
Principal Investigator Name
Stina Wichert
Principal Investigator Email
stina.wichert@skane.se
Contact Person Name
Stina Wichert
Contact Person Email
stina.wichert@skane.se
Site Name
Linkoping University Hospital Region Ostergotland
Department Name
Z97SE10003:Hematologiska Kliniken
Principal Investigator Name
Love Tätting
Principal Investigator Email
Love.Tatting@regionostergotland.se
Contact Person Name
Love Tätting
Site Name
Uppsala University Hospital
Department Name
Z97SE10004:Oncology
Principal Investigator Name
Kristina Carlson
Principal Investigator Email
Kristina.Carlson@akademiska.se
Contact Person Name
Kristina Carlson
Contact Person Email
Kristina.Carlson@akademiska.se

Sponsor

Primary sponsor

Full Name
European Myeloma Network B.V.
Organisation Type
Patient organisation/association
Country Of Registered Address
Netherlands

Contract research organisations

Name
Parexel International (IRL) Limited
Responsibilities
Codes listed in sponsorDuties (1,12,6,7,8) - contact: clinicaltrial.enquiries@parexel.com
Name
Excelya Greece CRO Single Member S.A.
Responsibilities
Codes listed in sponsorDuties (1,12) - contact: clinicalRa-greece@excelya.com

Third parties

  • {"country":"United States","full_name":"Charles River Laboratories International Inc.","duties_or_roles":"SPM (Second Primary Malignancy)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Frontage Laboratories Inc.","duties_or_roles":"Cytokines (serum)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Eurofins Pharma Bioanalytics Services US Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Smithers PDS LLC","duties_or_roles":"Immunogenicity","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":": PK Daratumumab, Immunogenicity Daratumumab, Sample storage time: until end of study.","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Netherlands","full_name":"Amsterdam UMC Stichting","duties_or_roles":"Clinical haematology, Histopathology","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"Belgium","full_name":"Cerba Research","duties_or_roles":"Immunophenotyping, Flowcytometry (bone marrow aspirate)","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Greece","full_name":"Excelya Greece CRO Single Member S.A.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Italy","full_name":"Ospedale San Raffaele S.r.l.","duties_or_roles":"scRNAseq (single cell RNA sequencing), TCR (T Cell receptor) sequencing, cfMeDIP (Cell-free methylated DNA immunoprecipitation) sequencing, LiBIS (liquid biopsy integration site) seqencing, IS (Integration Site) sequencing","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"Netherlands","full_name":"Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)","duties_or_roles":"Clinical haematology, Histopathology","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United States","full_name":"Adaptive Biotechnologies Corp.","duties_or_roles":"MRD negativity status","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Hematogenix Laboratory Services LLC","duties_or_roles":"New (Second) primary malignancy, Biopsy, Fish testing, PBMC processing, BMMC processing.","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Belgium","full_name":"CellCarta","duties_or_roles":"RCL Testing","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"Central labs","organisation_type":"Pharmaceutical company"}
  • {"country":"Belgium","full_name":"Clinigen Clinical Supplies Management","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"Julius-Maximilians-Universitaet Wuerzburg","duties_or_roles":"Clinical haematology, Histopathology","organisation_type":"Educational Institution"}
  • {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"Buccal Swab scRNAseq, WES, CyTOF, plasma and BM","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Italy","full_name":"Universita' Degli Studi Di Torino","duties_or_roles":"Clinical haematology, Histopathology","organisation_type":"Educational Institution"}
  • {"country":"United States","full_name":"Phenopath Laboratories PLLC","duties_or_roles":": BIOPSY KIT : New malignancies (SPM), Plasmacytoma, Neurotoxicity event or any other time a biopsy","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Signant Health LLC","duties_or_roles":"IVRS30 – treatment randomisation","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"EPL Pathology Archives LLC","duties_or_roles":"Biomarkers","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Spain","full_name":"Complexo Hospitalario Universitario De Santiago","duties_or_roles":"Laboratory analysis: GrHeCo-Xen","organisation_type":"Hospital/Clinic/Other health care facility"}

Co-sponsors

  • Emn Trial Office S.r.l. Impresa Sociale

Investigational products

Investigational Product Name
Lenalidomide Accord (multiple strengths)
Active Substance
Lenalidomide
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
Oral
Authorisation Status
Authorised
Dose Levels
2.5 mg | 5 mg | 15 mg | 20 mg | 25 mg
Maximum Dose
25 mg per day
Investigational Product Name
DARZALEX 1800 mg solution for injection
Active Substance
Daratumumab
Modality
Monoclonal antibody
Routes Of Administration
SUBCUTANEOUS USE
Route
Subcutaneous
Authorisation Status
Authorised
Orphan Designation
Yes
Dose Levels
1800 mg
Maximum Dose
1800 mg
Investigational Product Name
CARVYKTI (ciltacabtagene autoleucel)
Active Substance
Ciltacabtagene autoleucel
Modality
Cell therapy
Routes Of Administration
INTRAVENOUS USE
Route
Intravenous
Authorisation Status
Authorised
Orphan Designation
Yes
Dose Levels
3.2 × 10^6 – 1.0 × 10^8 cells dispersion for infusion
Investigational Product Name
VELCADE 3.5 mg powder for solution for injection
Active Substance
Bortezomib
Modality
Small molecule
Routes Of Administration
SUBCUTANEOUS USE
Route
Subcutaneous (dose expressed in mg/m2)
Authorisation Status
Authorised
Dose Levels
3.5 mg (powder for solution)
Maximum Dose
1.3 mg/m2
Investigational Product Name
Dexamethasone (2 mg / 4 mg tablets)
Active Substance
Dexamethasone
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
Oral
Authorisation Status
Authorised
Dose Levels
2 mg | 4 mg
Maximum Dose
40 mg per day
Combination Treatment
Yes

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