Clinical trial • Phase I/II • Oncology

SURZETOCLAX for Multiple myeloma

Phase I/II trial of SURZETOCLAX for Multiple myeloma.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Multiple myeloma
Trial Stage
Phase I/II
Drug Modality
Small molecule|Monoclonal antibody

Key dates

Initial CTIS Submission Date
12-06-2025
First CTIS Authorization Date
06-10-2025

Trial design

open-label, antimyeloma agents (dexamethasone, pomalidomide, daratumumab) - doses and schedules not specified-controlled, adaptive Phase I/II trial across 27 sites in Belgium, Germany, Italy and others.

Open Label
Yes
Comparator
Antimyeloma agents (dexamethasone, pomalidomide, daratumumab) - doses and schedules not specified
Adaptive
True, includes dose-escalation based on DLT assessment to determine tolerability and appropriate dosing; specific escalation rules not provided in available data.
Single Multiple Or Escalation Dose Combined
Yes
Target Sample Size
43

Eligibility

Recruits 43 No vulnerable populations selected (isVulnerablePopulationSelected: false). Informed consent documents provided (multiple ICFs: main, prescreening, optional, pregnancy parts) in country-specific languages as listed in the study documents..

Vulnerable Population
No vulnerable populations selected (isVulnerablePopulationSelected: false). Informed consent documents provided (multiple ICFs: main, prescreening, optional, pregnancy parts) in country-specific languages as listed in the study documents.

Inclusion criteria

  • {"criterion_text":"- Documented diagnosis of multiple myeloma (MM) based on standard international myeloma working group (IMWG) diagnostic criteria.\n- All participants must have measurable disease per central laboratory with at least 1 of the following assessed within 28 days prior to enrollment: -- Serum M-protein >= 0.5 g/dL (>= 5g/L); OR -- Urine M-protein >= 200 mg/24 hours; OR -- For participants without measurable serum and urine M-protein: Serum free light chain (sFLC) ≥ 10 mg/dL (100 mg/L), provided sFLC ratio is abnormal.\n- B-cell lymphoma (BCL)-2 inhibitor treatment naïve."}

Exclusion criteria

  • {"criterion_text":"- Major surgery within 4 weeks of study treatment or planned during study participation.\n- Recent infection requiring systemic treatment that was completed <= 7 days before first dose of study treatment and/or uncontrolled active systemic infection."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Dose Limiting Toxicities (DLT)s of ABBV-453","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Safety and tolerability (AEs and SAEs, clinical laboratory parameters, vital sign measurements, and ECG results).","definition_or_measurement_approach":"Assessment of adverse events (AEs) and serious adverse events (SAEs), clinical laboratory parameters, vital sign measurements, and ECG results as measures of safety and tolerability."}

Secondary endpoints

  • {"endpoint_text":"- Overall Response Rate (ORR)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Progression-Free Survival (PFS)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Duration of Response (DOR)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Time-to-Progression (TTP)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Time to Next Treatment","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Rate and Depth of minimal residual disease (MRD) Negativity Determined Centrally","definition_or_measurement_approach":"MRD negativity determined by central laboratory assessment."}
  • {"endpoint_text":"- Overall survival (OS)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Pharmacokinetics (PK): Cmax, Tmax, t ½ , AUC.","definition_or_measurement_approach":"PK parameters to be measured: Cmax, Tmax, half-life (t½), and AUC."}

Recruitment

Planned Sample Size
43
Recruitment Window Months
41
Consent Approach
Informed consent obtained from adult participants using country-specific ICFs (main, prescreening, optional, pregnancy sections). ICF documents are available in multiple languages (examples from document list include English, French, Dutch, German, Italian, Portuguese, Swedish, Polish).

Geography

Total Number Of Sites
27
Total Number Of Participants
76

Belgium

Earliest CTIS Part Ii Submission Date
08-09-2025
Latest Decision Or Authorization Date
06-10-2025
Processing Time Days
28
Number Of Sites
3
Number Of Participants
9

Sites

Site Name
Centre hospitalier universitaire de Liege
Department Name
Hematology
Principal Investigator Name
Bernard De Prijck
Principal Investigator Email
bernard.deprijck@chuliege.be
Contact Person Name
Bernard De Prijck
Contact Person Email
bernard.deprijck@chuliege.be
Site Name
UZ Leuven
Department Name
Hematology
Principal Investigator Name
Michel Delforge
Principal Investigator Email
michel.delforge@uzleuven.be
Contact Person Name
Michel Delforge
Contact Person Email
michel.delforge@uzleuven.be
Site Name
Universitair Ziekenhuis Gent
Department Name
Hematology
Principal Investigator Name
Nicolas Kint
Principal Investigator Email
nicolas.kint@uzgent.be
Contact Person Name
Nicolas Kint
Contact Person Email
nicolas.kint@uzgent.be

Germany

Earliest CTIS Part Ii Submission Date
18-09-2025
Latest Decision Or Authorization Date
08-10-2025
Processing Time Days
20
Number Of Sites
4
Number Of Participants
16

Sites

Site Name
Universitaetsklinikum Heidelberg AöR
Department Name
Medizinische Klinik V
Principal Investigator Name
Marc-Steffen Raab
Principal Investigator Email
Marc.Raab@med.uni-heidelberg.de
Contact Person Name
Marc-Steffen Raab
Site Name
Universitaetsklinikum Wuerzburg AöR
Department Name
Medizinische Klinik und Poliklinik II
Principal Investigator Name
Martin Kortuem
Principal Investigator Email
Kortuem_M@ukw.de
Contact Person Name
Martin Kortuem
Contact Person Email
Kortuem_M@ukw.de
Site Name
LMU Klinikum Muenchen AöR
Department Name
Medizinische Klinik und Poliklinik III
Principal Investigator Name
Sebastian Theurich
Principal Investigator Email
sebastian.theurich@med.uni-muenchen.de
Contact Person Name
Sebastian Theurich
Site Name
University Medical Center Hamburg-Eppendorf
Department Name
II. Medizinische Klinik und Poliklinik
Principal Investigator Name
Katja Weisel
Principal Investigator Email
myelomstudien@uke.de
Contact Person Name
Katja Weisel
Contact Person Email
myelomstudien@uke.de

Italy

Earliest CTIS Part Ii Submission Date
18-09-2025
Latest Decision Or Authorization Date
06-10-2025
Processing Time Days
18
Number Of Sites
5
Number Of Participants
12

Sites

Site Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale
Department Name
SC Ematologia Oncologica e Trapianto di Cellule Staminali
Principal Investigator Name
Antonio Pinto
Principal Investigator Email
a.pinto@istitutotumori.na.it
Contact Person Name
Antonio Pinto
Contact Person Email
a.pinto@istitutotumori.na.it
Site Name
Azienda Socio Sanitaria Territoriale Papa Giovanni Xxiii
Department Name
Hematology and Bone Marrow Unit
Principal Investigator Name
Monica Galli
Principal Investigator Email
monicagalli@asst-pg23.it
Contact Person Name
Monica Galli
Contact Person Email
monicagalli@asst-pg23.it
Site Name
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Department Name
S.C. Ematologia
Principal Investigator Name
Matteo Claudio Da Via
Principal Investigator Email
matteo.davia@policlinico.mi.it
Contact Person Name
Matteo Claudio Da Via
Contact Person Email
matteo.davia@policlinico.mi.it
Site Name
Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
Department Name
Hematology U Division
Principal Investigator Name
Francesca Gay
Principal Investigator Email
francesca.gay@unito.it
Contact Person Name
Francesca Gay
Contact Person Email
francesca.gay@unito.it
Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
HEMATOLOGY UNIT
Principal Investigator Name
Claudio Cerchione
Principal Investigator Email
claudio.cerchione@irst.emr.it
Contact Person Name
Claudio Cerchione
Contact Person Email
claudio.cerchione@irst.emr.it

Portugal

Earliest CTIS Part Ii Submission Date
12-09-2025
Latest Decision Or Authorization Date
06-10-2025
Processing Time Days
24
Number Of Sites
3
Number Of Participants
7

Sites

Site Name
Instituto Portugues De Oncologia De Lisboa Francisco Gentil E.P.E.
Department Name
Oncology
Principal Investigator Name
Paulo Bernardo
Principal Investigator Email
pbernardo@ipolisboa.min-saude.pt
Contact Person Name
Paulo Bernardo
Site Name
CCAB Centro Clinico Academico Braga Associacao
Department Name
Oncology
Principal Investigator Name
Jose Freitas
Principal Investigator Email
jose.p.freitas@hb.min-saude.pt
Contact Person Name
Jose Freitas
Contact Person Email
jose.p.freitas@hb.min-saude.pt
Site Name
Instituto Portugues De Oncologia Do Porto Francisco Gentil E.P.E.
Department Name
Oncology
Principal Investigator Name
Claudia Moreira
Principal Investigator Email
csmoreira@ipoporto.min-saude.pt
Contact Person Name
Claudia Moreira

Sweden

Earliest CTIS Part Ii Submission Date
10-09-2025
Latest Decision Or Authorization Date
06-10-2025
Processing Time Days
26
Number Of Sites
3
Number Of Participants
7

Sites

Site Name
Soedra Aelvsborg Hospital Vaestra Goetalandsregionen
Department Name
Medicinkliniken, Hiss E plan 7
Principal Investigator Name
Ulf-Henrik Mellqvist
Principal Investigator Email
ulf-henrik.mellqvist@vgregion.se
Contact Person Name
Ulf-Henrik Mellqvist
Site Name
Sahlgrenska University Hospital-Vaestra Goetalandsregionen
Department Name
Department of Hematology
Principal Investigator Name
Markus Hansson
Principal Investigator Email
markus.hansson.2@gu.se
Contact Person Name
Markus Hansson
Contact Person Email
markus.hansson.2@gu.se
Site Name
Karolinska University Hospital
Department Name
Cancerstudieenheten M62
Principal Investigator Name
Katarina Uttervall
Principal Investigator Email
katarina.uttervall@regionstockholm.se
Contact Person Name
Katarina Uttervall

Poland

Earliest CTIS Part Ii Submission Date
25-09-2025
Latest Decision Or Authorization Date
10-10-2025
Processing Time Days
15
Number Of Sites
4
Number Of Participants
13

Sites

Site Name
Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy
Department Name
Klinika Nowotworow Układu Chlonnego
Principal Investigator Name
Joanna Romejko-Jarosinska
Principal Investigator Email
joanna.romejko-jarosinska@pib-nio.pl
Contact Person Name
Joanna Romejko-Jarosinska
Site Name
Uniwersytecki Szpital Kliniczny W Poznaniu
Department Name
Oddzial Hematologii i Transplantacji Szpiku
Principal Investigator Name
Dominik Dytfeld
Principal Investigator Email
dytfeld@me.com
Contact Person Name
Dominik Dytfeld
Contact Person Email
dytfeld@me.com
Site Name
Uniwersytecki Szpital Kliniczny Nr 4 W Lublinie
Department Name
Oddzial Wieloprofilowy Zachowawczy
Principal Investigator Name
Krzysztof Giannopoulos
Principal Investigator Email
krzysztofgiannopoulos@umlub.pl
Contact Person Name
Krzysztof Giannopoulos
Contact Person Email
krzysztofgiannopoulos@umlub.pl
Site Name
Uniwersytecki Szpital Kliniczny Nr 1 W Lublinie
Department Name
Klinika Hematoonkologii i Transplantacji Szpiku Oddział Hematoonkologii i Transplantacji Szpiku i Ch
Principal Investigator Name
Marek Hus
Principal Investigator Email
hematoonkologia@usk1.lublin.pl
Contact Person Name
Marek Hus
Contact Person Email
hematoonkologia@usk1.lublin.pl

France

Earliest CTIS Part Ii Submission Date
22-09-2025
Latest Decision Or Authorization Date
08-12-2025
Processing Time Days
77
Number Of Sites
5
Number Of Participants
12

Sites

Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Clinical Hematology
Principal Investigator Name
Laure VINCENT
Principal Investigator Email
l-vincent@chu-montpellier.fr
Contact Person Name
Laure VINCENT
Contact Person Email
l-vincent@chu-montpellier.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Adult Hematology Department
Principal Investigator Name
Laurent FRENZEL
Principal Investigator Email
laurent.frenzel@aphp.fr
Contact Person Name
Laurent FRENZEL
Contact Person Email
laurent.frenzel@aphp.fr
Site Name
Oncopole Claudius Regaud
Department Name
Medical Oncology - Early Phase Unit
Principal Investigator Name
Pierre BORIES
Principal Investigator Email
bories.pierre@iuct-oncopole.fr
Contact Person Name
Pierre BORIES
Contact Person Email
bories.pierre@iuct-oncopole.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Clinical Hematology
Principal Investigator Name
Cyrille TOUZEAU
Principal Investigator Email
cyrille.touzeau@chu-nantes.fr
Contact Person Name
Cyrille TOUZEAU
Contact Person Email
cyrille.touzeau@chu-nantes.fr
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Oncology Hematology
Principal Investigator Name
Xavier LELEU
Principal Investigator Email
xavier.leleu@chu-poitiers.fr
Contact Person Name
Xavier LELEU
Contact Person Email
xavier.leleu@chu-poitiers.fr

Sponsor

Primary sponsor

Full Name
AbbVie Deutschland GmbH & Co. KG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Germany

Contract research organisations

Name
Iqvia Biotech LLC
Responsibilities
sponsorDuties codes: [4]; operational/CRO services (contact els.vannylen@iqvia.com)
Name
Clario (formerly ERT)
Responsibilities
ECG machine for triplicate ECG which applicable for Substudy 2 Japan only; sponsorDuties code 15
Name
Advarra Inc.
Responsibilities
Central IRB for US

Third parties

  • {"country":"United States","full_name":"Abbott Molecular Inc.","duties_or_roles":"sponsorDuties codes: [4]; contact help@abbottmolecular.com","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Veeva Systems Inc.","duties_or_roles":"sponsorDuties codes: [6,7]; contact CDMS_Support@veeva.com","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services Sàrl","duties_or_roles":"sponsorDuties codes: [4]; contact Guillaume.Couffe@labcorp.com","organisation_type":"Health care"}
  • {"country":"United Kingdom","full_name":"Qiagen Manchester Limited","duties_or_roles":"sponsorDuties codes: [4]; contact customercare-us@qiagen.com","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Advarra Inc.","duties_or_roles":"Central IRB for US (sponsorDuties code 15); contact cirbi@advarra.com","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Clario (formerly ERT)","duties_or_roles":"sponsorDuties code 15; 'ECG machine for triplicate ECG which applicable for Substudy 2 Japan only'; contact customercare@clario.com","organisation_type":"Industry"}
  • {"country":"United States","full_name":"Iqvia Biotech LLC","duties_or_roles":"sponsorDuties codes: [4]; contact els.vannylen@iqvia.com","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Surzetoclax
Active Substance
SURZETOCLAX
Modality
Small molecule
Routes Of Administration
Oral
Route
Oral
Investigational Product Name
DARATUMUMAB
Active Substance
DARATUMUMAB
Modality
Monoclonal antibody
Routes Of Administration
Subcutaneous
Route
Subcutaneous
Investigational Product Name
POMALIDOMIDE
Active Substance
POMALIDOMIDE
Modality
Small molecule
Routes Of Administration
Oral (capsule)
Route
Oral
Investigational Product Name
DEXAMETHASONE
Active Substance
DEXAMETHASONE
Modality
Small molecule
Routes Of Administration
Oral (tablet)
Route
Oral
Combination Treatment
Yes

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