Clinical trial • Phase I • Rare Disease

GSK4771261 for Autosomal dominant polycystic kidney disease | Kidney disease

Phase I trial of GSK4771261 for Autosomal dominant polycystic kidney disease | Kidney disease. 63 participants.

Overview

Trial Therapeutic Area
Rare Disease
Trial Disease
Autosomal dominant polycystic kidney disease | Kidney disease
Trial Stage
Phase I

Key dates

Initial CTIS Submission Date
12-12-2024
First CTIS Authorization Date
30-04-2025

Trial design

Phase I trial across 15 sites in France, Spain, Germany and others.

Target Sample Size
63

Eligibility

Recruits 63 No vulnerable populations selected (isVulnerablePopulationSelected: false). No specific consent/assent handling for vulnerable groups is described..

Vulnerable Population
No vulnerable populations selected (isVulnerablePopulationSelected: false). No specific consent/assent handling for vulnerable groups is described.

Recruitment

Planned Sample Size
63
Recruitment Window Months
15

Geography

Total Number Of Sites
15
Total Number Of Participants
21

France

Earliest CTIS Part Ii Submission Date
13-02-2025
Latest Decision Or Authorization Date
23-03-2026
Processing Time Days
403
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Höpital Necker, Néphrologie Dialyse Adulte
Principal Investigator Name
Bertrand KNEBELMANN
Principal Investigator Email
bertrand.knebelmann@aphp.fr
Contact Person Name
Bertrand KNEBELMANN
Contact Person Email
bertrand.knebelmann@aphp.fr
Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
Nephrology, Renal Transplant and Hemodialysis
Principal Investigator Name
Emilie CORNEC-LE GALL
Principal Investigator Email
emilie.cornec.le-gall@hu-brest.fr
Contact Person Name
Emilie CORNEC-LE GALL

Spain

Earliest CTIS Part Ii Submission Date
31-03-2025
Latest Decision Or Authorization Date
26-03-2026
Processing Time Days
360
Number Of Sites
5
Number Of Participants
5

Sites

Site Name
Hospital Universitario Fundacion Jimenez Diaz
Department Name
Nephrology Service
Principal Investigator Name
Mª Vanessa Pérez Gómez
Principal Investigator Email
mvanessa@fjd.es
Contact Person Name
Mª Vanessa Pérez Gómez
Contact Person Email
mvanessa@fjd.es
Site Name
Fundacio Puigvert
Department Name
Nephrology Service
Principal Investigator Name
Mª Roser Torra Balcells
Principal Investigator Email
rtorra@fundacio-puigvert.es
Contact Person Name
Mª Roser Torra Balcells
Contact Person Email
rtorra@fundacio-puigvert.es
Site Name
Hospital Del Mar
Department Name
Nephrology Service
Principal Investigator Name
Melissa Pilco Teran
Principal Investigator Email
melissalorena.pilco.teran@hmar.cat
Contact Person Name
Melissa Pilco Teran
Site Name
Hospital Universitario 12 De Octubre
Department Name
Nephrology Service
Principal Investigator Name
Eduardo Gutiérrez Martínez
Principal Investigator Email
eduardogutmat90@gmail.com
Contact Person Name
Eduardo Gutiérrez Martínez
Contact Person Email
eduardogutmat90@gmail.com
Site Name
Hospital Universitari Vall D Hebron
Department Name
Nephrology Service
Principal Investigator Name
Laia Sans Atxer
Principal Investigator Email
laia.sans@vallhebron.cat
Contact Person Name
Laia Sans Atxer
Contact Person Email
laia.sans@vallhebron.cat

Germany

Earliest CTIS Part Ii Submission Date
09-04-2025
Latest Decision Or Authorization Date
25-03-2026
Processing Time Days
350
Number Of Sites
2
Number Of Participants
5

Sites

Site Name
University Hospital Cologne AöR
Department Name
Innere Medizin II - Nephrologie, Rheumatologie, Diabetologie und Allgemeine Innere Medizin
Principal Investigator Name
Roman-Ulrich Mueller
Principal Investigator Email
roman-ulrich.mueller@uk-koeln.de
Contact Person Name
Roman-Ulrich Mueller
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Campus Lübeck, Medizinische Klinik 1
Principal Investigator Name
Figen Cakiroglu
Principal Investigator Email
Figen.Cakiroglu@uksh.de
Contact Person Name
Figen Cakiroglu
Contact Person Email
Figen.Cakiroglu@uksh.de

Netherlands

Earliest CTIS Part Ii Submission Date
25-03-2025
Latest Decision Or Authorization Date
23-03-2026
Processing Time Days
363
Number Of Sites
3
Number Of Participants
6

Sites

Site Name
Leids Universitair Medisch Centrum (LUMC)
Department Name
Kidney disease
Principal Investigator Name
Siebe Spijker
Principal Investigator Email
h.s.spijker@lumc.nl
Contact Person Name
Siebe Spijker
Contact Person Email
h.s.spijker@lumc.nl
Site Name
Universitair Medisch Centrum Groningen
Department Name
Nefrologie
Principal Investigator Name
Ron Gansevoort
Principal Investigator Email
r.t.gansevoort@umcg.nl
Contact Person Name
Ron Gansevoort
Contact Person Email
r.t.gansevoort@umcg.nl
Site Name
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Department Name
Internal medicine
Principal Investigator Name
Mahdi Salih
Principal Investigator Email
m.salih@erasmusmc.nl
Contact Person Name
Mahdi Salih
Contact Person Email
m.salih@erasmusmc.nl

Belgium

Earliest CTIS Part Ii Submission Date
02-04-2025
Latest Decision Or Authorization Date
25-03-2026
Processing Time Days
357
Number Of Sites
3
Number Of Participants
3

Sites

Site Name
Cliniques Universitaires Saint-Luc
Department Name
Nephrology
Principal Investigator Name
Nathalie Demoulin
Principal Investigator Email
nathalie.demoulin@uclouvain.be
Contact Person Name
Nathalie Demoulin
Contact Person Email
nathalie.demoulin@uclouvain.be
Site Name
Universiteit Gent
Department Name
Nephrology
Principal Investigator Name
Francis Verbeke
Principal Investigator Email
Francis.Verbeke@UZGent.be
Contact Person Name
Francis Verbeke
Contact Person Email
Francis.Verbeke@UZGent.be
Site Name
UZ Leuven
Department Name
Nephrology
Principal Investigator Name
Bert Bammens
Principal Investigator Email
bert.bammens@uzleuven.be
Contact Person Name
Bert Bammens
Contact Person Email
bert.bammens@uzleuven.be

Sponsor

Primary sponsor

Full Name
Glaxosmithkline Research & Development Limited
Organisation Type
Pharmaceutical company
Country Of Registered Address
United Kingdom

Investigational products

Investigational Product Name
GSK4771261

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