Clinical trial • Phase II • Gastroenterology

GS-1427 for Ulcerative colitis

Phase II trial of GS-1427 for Ulcerative colitis.

Overview

Trial Therapeutic Area
Gastroenterology
Trial Disease
Ulcerative colitis
Trial Stage
Phase II
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
28-03-2024
First CTIS Authorization Date
22-07-2024

Trial design

Randomised, placebo tablets (ptm 25 mg, ptm 75 mg, ptm 100 mg) matching gs-1427 tablets (placebo arms listed as ptm 25 mg / 75 mg / 100 mg tablets).-controlled Phase II trial in Romania, Austria, Belgium and others.

Randomised
Yes
Comparator
Placebo tablets (PTM 25 mg, PTM 75 mg, PTM 100 mg) matching GS-1427 tablets (placebo arms listed as PTM 25 mg / 75 mg / 100 mg tablets).
Single Multiple Or Escalation Dose Combined
Yes
Target Sample Size
144
Trial Duration For Participant
812

Eligibility

Recruits 144 isVulnerablePopulationSelected: true; subject information and consent forms are available for pregnant participants, pregnant partner, infant follow-up and scout/infant ICFs; multiple country-specific main ICFs are provided. (Documents listed include Main ICFs, Pregnant Participant ICFs, Pregnant Partner ICFs, Infant Follow-up ICFs and Scout ICFs in multiple languages.).

Vulnerable Population
isVulnerablePopulationSelected: true; subject information and consent forms are available for pregnant participants, pregnant partner, infant follow-up and scout/infant ICFs; multiple country-specific main ICFs are provided. (Documents listed include Main ICFs, Pregnant Participant ICFs, Pregnant Partner ICFs, Infant Follow-up ICFs and Scout ICFs in multiple languages.)

Inclusion criteria

  • {"criterion_text":"- Participants have UC with symptoms of at least 90 days duration before randomization, with the diagnosis confirmed by endoscopy and histology at any time prior to randomization. Documentation of endoscopy and histology consistent with the diagnosis of UC must be available in the source documents."}
  • {"criterion_text":"- Participants have UC with minimum disease extent of 15 cm from the anal verge."}
  • {"criterion_text":"- Participants have moderately to severely active UC as determined by endoscopy occurring during screening with a total mMCS of 5 to 9 points, including a centrally read endoscopic subscore of at least 2."}
  • {"criterion_text":"- Participants have an inadequate response or loss of response or are intolerant to at least 1 of the following UC treatments:  Corticosteroids  Immunomodulators: azathioprine, 6-mercaptopurine, or 6-thioguanine (see full inclusion criteria for details)  Advanced therapy: have an inadequate response or loss of response or are intolerant to an advanced therapy (AT) for the treatment of UC: ○ Tumor necrosis factor-alpha (TNF-α) inhibitor: eg, infliximab, adalimumab, golimumab, or biosimilars ○ Interleukin-12/23 inhibitor: eg, Ustekinumab. Sphingosine 1-phosphate receptor modulator: eg, ozanimod ○ Janus kinase inhibitor: eg, tofacitinib, upadacitinib, filgotinib"}
  • {"criterion_text":"- Participants have an inadequate response or loss of response or are intolerant to < 3 AT mechanisms of action for UC (use of 2 or more AT with the same mechanism of action, eg, 2 TNF-α inhibitors, counts as 1 mechanism of action):"}

Exclusion criteria

  • {"criterion_text":"- Have a current diagnosis of Crohn’s disease (CD) or clinical findings suggestive of CD, diagnosis of indeterminate colitis due to causes such as an enteric pathogen, or lymphocytic or collagenous colitis."}
  • {"criterion_text":"- Have a current diagnosis of toxic megacolon, symptomatic colonic stricture, acute severe colitis, fulminant colitis, or abdominal abscess at screening or randomization."}
  • {"criterion_text":"- Have any history of exposure to vedolizumab or other integrin antagonists."}
  • {"criterion_text":"- Have any history of stroke, seizure disorder, multiple sclerosis, neurodegenerative disease of brain (such as Parkinson’s disease, dementias), or brain tumor."}
  • {"criterion_text":"- Have a positive progressive multifocal leukoencephalopathy subjective checklist at screening or at randomization prior to the administration of the first dose of study drug."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Clinical response at Week 12 Clinical response is defined as a decrease from baseline in the modified Mayo Clinic Score (mMCS) of ≥ 2 points and at least a 30% reduction from baseline, and a decrease in rectal bleeding subscore of ≥ 1 from baseline or an absolute rectal bleeding subscore of 0 or 1.","definition_or_measurement_approach":"Clinical response at Week 12 defined as decrease from baseline in mMCS of ≥2 points and ≥30% reduction from baseline AND decrease in rectal bleeding subscore ≥1 from baseline or absolute rectal bleeding subscore 0 or 1; assessed at Week 12 (mMCS and rectal bleeding subscore; endoscopy and central reads for endoscopic subscores where applicable)."}

Secondary endpoints

  • {"endpoint_text":"- Incidence of treatment-emergent adverse events, serious adverse events, or deaths, and treatment-emergent laboratory abnormalities","definition_or_measurement_approach":"Safety/tolerability assessed as incidence of treatment-emergent AEs, SAEs, deaths and treatment-emergent laboratory abnormalities (standard AE/SAE reporting and lab assessments)."}
  • {"endpoint_text":"- Clinical remission at Week 12","definition_or_measurement_approach":"Clinical remission defined (where provided for Week 52) as mMCS ≤ 2 with stool frequency subscore ≤1 not greater than baseline and rectal bleeding subscore of 0 and centrally-read endoscopic subscore ≤1; for Week 12 endpoint the study will use the corresponding Week 12 definition as per protocol."}
  • {"endpoint_text":"- Clinical remission at Week 52 Clinical remission is defined as an mMCS of ≤ 2 points, including a stool frequency subscore (SFS) ≤ 1 and not greater than baseline, rectal bleeding subscore of 0, and centrally-read endoscopic subscore ≤ 1 (score of 1 modified to exclude friability).","definition_or_measurement_approach":"Clinical remission at Week 52 defined explicitly as mMCS ≤2, SFS ≤1 and not greater than baseline, rectal bleeding subscore 0, and centrally-read endoscopic subscore ≤1 (with score of 1 modified to exclude friability)."}
  • {"endpoint_text":"- Histologic-endoscopic mucosal improvement at Week 12 Histologic-endoscopic mucosal improvement is defined as a Geboes score ≤ 3.1 and endoscopic subscore of ≤ 1.","definition_or_measurement_approach":"Defined as Geboes score ≤3.1 and endoscopic subscore ≤1 at Week 12 (histology + endoscopy central reads)."}
  • {"endpoint_text":"- Mucosal healing at Week 12 Mucosal healing is defined as a Geboes score ≤ 2B.1 and endoscopic subscore ≤ 1.","definition_or_measurement_approach":"Defined as Geboes score ≤2B.1 and endoscopic subscore ≤1 at Week 12."}
  • {"endpoint_text":"- Endoscopic improvement at Week 12 Endoscopic improvement is defined as an endoscopic subscore ≤ 1.","definition_or_measurement_approach":"Endoscopic subscore ≤1 at Week 12 (central endoscopic read)."}
  • {"endpoint_text":"- Partial mMCS remission at Week 52 Partial mMCS remission is defined as a SFS ≤ 1 and rectal bleeding subscore of 0.","definition_or_measurement_approach":"Partial mMCS remission at Week 52 defined as stool frequency subscore ≤1 and rectal bleeding subscore 0."}

Recruitment

Registry Or Advocacy Recruitment
True, Asociatia Oncohelp
Digital Remote Recruitment
True, documents indicate use of eCOA (digital self-complete), eCOA instruments (EQ-5D-5L, IBDQ, UC-PRO-SS), subject devices/site tablets (provided by Signant Health), and Scout email/digital communications.
Planned Sample Size
144
Recruitment Window Months
43
Consent Approach
Adult participants provide informed consent via country-specific Main ICFs; multiple language ICFs available (English and country languages across France, Germany, Spain, Italy, Poland, Romania, Hungary, Czech, Belgium variants etc.). Separate ICFs exist for pregnant participants, pregnant partners, infant follow-up, reimbursement-and-travel, optional future research and Scout participants. Parent/guardian consent procedures are provided for infant follow-up (Infant Follow-up ICFs).

Methods

  • Country-specific recruitment brochures and recruitment arrangements (multiple PDFs listed for each MSC e.g., Recruitment Brochure, Recruitment-Arrangements documents).
  • GP letters (documents titled GP letter available for some countries).
  • Scout outreach (Scout ICF, Scout email communications, Scout study brochure listed).
  • Site-based recruitment (site contact lists and patient advocacy contact lists listed).
  • Digital eCOA and electronic communications (eCOA instruments, digital self-complete forms and email communications referenced).

Geography

Total Number Of Sites
55
Total Number Of Participants
124

Romania

Earliest CTIS Part Ii Submission Date
18-04-2024
Latest Decision Or Authorization Date
10-11-2025
Processing Time Days
571
Number Of Sites
11
Number Of Participants
13

Sites

Site Name
Spitalul Clinic Colentina Bucuresti
Department Name
Gastroenterology Department
Principal Investigator Name
Radu-Bogdan Mateescu
Principal Investigator Email
gastrostudii@gmail.com
Contact Person Name
Radu-Bogdan Mateescu
Contact Person Email
gastrostudii@gmail.com
Site Name
Institutul Clinic Fundeni
Department Name
Gastroenterology 2
Principal Investigator Name
Carmen Monica Preda
Principal Investigator Email
Preda_monicaa@yahoo.com
Contact Person Name
Carmen Monica Preda
Contact Person Email
Preda_monicaa@yahoo.com
Site Name
Spitalul Universitar De Urgenta Militar Central Dr. Carol Davila
Department Name
Sectia Clinica Gastroenterologie
Principal Investigator Name
Sandica-Nicoleta Bucurica
Principal Investigator Email
bucuricasandy@yahoo.com
Contact Person Name
Sandica-Nicoleta Bucurica
Contact Person Email
bucuricasandy@yahoo.com
Site Name
Gastromed S.R.L.
Department Name
Gastroenterology
Principal Investigator Name
Florin-George Musat
Principal Investigator Email
florinmusat.trials@gmail.com
Contact Person Name
Florin-George Musat
Contact Person Email
florinmusat.trials@gmail.com
Site Name
Centrul Medical Medicum S.R.L.
Department Name
Gastroenterology
Principal Investigator Name
Theodor-Alexandru Voiosu
Principal Investigator Email
theodor.voiosu@gmail.com
Contact Person Name
Theodor-Alexandru Voiosu
Contact Person Email
theodor.voiosu@gmail.com
Site Name
Centrul Medical Monza S.R.L.
Department Name
Gastroenterolgy Department
Principal Investigator Name
Iulia Simionov
Principal Investigator Email
dr_simionov@yahoo.com
Contact Person Name
Iulia Simionov
Contact Person Email
dr_simionov@yahoo.com
Site Name
Spitalul Clinic Judetean De Urgenta Cluj
Department Name
Gastroenterology Department
Principal Investigator Name
Vlad-Andrei Ichim
Principal Investigator Email
vlad.ichim.ext@arensiaem.com
Contact Person Name
Vlad-Andrei Ichim
Contact Person Email
vlad.ichim.ext@arensiaem.com
Site Name
Asociatia Oncohelp
Department Name
Gastroenterology
Principal Investigator Name
Razvan-Gheorghe Diaconescu
Principal Investigator Email
diaconescu_razvan@yahoo.com
Contact Person Name
Razvan-Gheorghe Diaconescu
Contact Person Email
diaconescu_razvan@yahoo.com
Site Name
Centrul De Gastroenterologie Dr. Goldis S.R.L.
Department Name
Gastroenterolgy Department
Principal Investigator Name
Eugen-Adrian Goldis
Principal Investigator Email
goldisadi@yahoo.com
Contact Person Name
Eugen-Adrian Goldis
Contact Person Email
goldisadi@yahoo.com
Site Name
Spital Judetean De Urgenta Satu Mare
Department Name
Sectia Gastroenterologie
Principal Investigator Name
Bogdan-Calin Pintea
Principal Investigator Email
dr.bogdan.pintea@gmail.com
Contact Person Name
Bogdan-Calin Pintea
Contact Person Email
dr.bogdan.pintea@gmail.com
Site Name
Institutul Regional De Gastroenterologie Hepatologie Prof. Dr. Octavian Fodor Cluj
Department Name
Sectia Clinica Gastroenterologie I
Principal Investigator Name
Cristina Pojoga
Principal Investigator Email
cristinapojoga@yahoo.com
Contact Person Name
Cristina Pojoga
Contact Person Email
cristinapojoga@yahoo.com

Austria

Earliest CTIS Part Ii Submission Date
25-06-2024
Latest Decision Or Authorization Date
03-11-2025
Processing Time Days
496
Number Of Sites
3
Number Of Participants
3

Sites

Site Name
Gemeinnutzige Salzburger Landes kliniken Betriebsgesellschaft mbH
Department Name
University Clinic for Internal Medicine I
Principal Investigator Name
Sonja Heeren
Principal Investigator Email
s.heeren@salk.at
Contact Person Name
Sonja Heeren
Contact Person Email
s.heeren@salk.at
Site Name
Medical University Of Vienna
Department Name
Department of Internal Medicine III Division Gastroenterology and Hepatology
Principal Investigator Name
Walter Reinisch
Principal Investigator Email
walter.reinisch@meduniwien.ac.at
Contact Person Name
Walter Reinisch
Site Name
Medizinische Universitaet Innsbruck
Department Name
University Clinic for Internal Medicine I
Principal Investigator Name
Robert Koch
Principal Investigator Email
robert.koch@i-med.ac.at
Contact Person Name
Robert Koch
Contact Person Email
robert.koch@i-med.ac.at

Belgium

Earliest CTIS Part Ii Submission Date
24-06-2024
Latest Decision Or Authorization Date
03-11-2025
Processing Time Days
497
Number Of Sites
3
Number Of Participants
4

Sites

Site Name
Algemeen Ziekenhuis Groeninge
Department Name
Gastroenterology
Principal Investigator Name
Wouter Van Moerkercke
Principal Investigator Email
wouter.vanmoerkercke@azgroeninge.be
Contact Person Name
Wouter Van Moerkercke
Site Name
Vitaz
Department Name
Gastroenterology
Principal Investigator Name
Tom Holvoet
Principal Investigator Email
tom.holvoet@vitaz.be
Contact Person Name
Tom Holvoet
Contact Person Email
tom.holvoet@vitaz.be
Site Name
Imelda
Department Name
Gastroenterology
Principal Investigator Name
Lieven Pouillon
Principal Investigator Email
lieven.pouillon@imelda.be
Contact Person Name
Lieven Pouillon
Contact Person Email
lieven.pouillon@imelda.be

Hungary

Earliest CTIS Part Ii Submission Date
31-05-2024
Latest Decision Or Authorization Date
15-12-2025
Processing Time Days
563
Number Of Sites
4
Number Of Participants
4

Sites

Site Name
Semmelweis University
Department Name
2nd Dept. of Internal Medicine
Principal Investigator Name
Zsolt Tulassay
Principal Investigator Email
tulassay.zsolt@med.semmelweis-univ.hu
Contact Person Name
Zsolt Tulassay
Site Name
Vasutegeszseguegyi Nonprofit Koezhasznu Kft.
Principal Investigator Name
G. Kiss Gyula
Principal Investigator Email
gkissgyula@gmail.com
Contact Person Name
G. Kiss Gyula
Contact Person Email
gkissgyula@gmail.com
Site Name
Semmelweis University (Koranyi Sandor Utca)
Department Name
Internal Medicine and Oncology Clinic
Principal Investigator Name
Ákos Iliás
Principal Investigator Email
driliasakos@gmail.com
Contact Person Name
Ákos Iliás
Contact Person Email
driliasakos@gmail.com
Site Name
Bekes Varmegyei Koezponti Korhaz
Department Name
Department of Internal Medicine
Principal Investigator Name
Marta Varga
Principal Investigator Email
drvargamarta@gmail.com
Contact Person Name
Marta Varga
Contact Person Email
drvargamarta@gmail.com

Czechia

Earliest CTIS Part Ii Submission Date
24-06-2024
Latest Decision Or Authorization Date
07-11-2025
Processing Time Days
501
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
PreventaMed s.r.o.
Principal Investigator Name
Jiří Pumprla
Principal Investigator Email
research@vilazdravi.cz
Contact Person Name
Jiří Pumprla
Contact Person Email
research@vilazdravi.cz
Site Name
Nemocnice Slany
Department Name
Interní klinika
Principal Investigator Name
Martin Peterka
Principal Investigator Email
peterka.studie@seznam.cz
Contact Person Name
Martin Peterka
Contact Person Email
peterka.studie@seznam.cz

Spain

Earliest CTIS Part Ii Submission Date
15-07-2024
Latest Decision Or Authorization Date
03-11-2025
Processing Time Days
476
Number Of Sites
6
Number Of Participants
6

Sites

Site Name
Hospital Universitario Nuestra Senora De Candelaria
Department Name
Servicio de Aparato Digestivo
Principal Investigator Name
Milagros Vela
Principal Investigator Email
milvelillas@yahoo.es
Contact Person Name
Milagros Vela
Contact Person Email
milvelillas@yahoo.es
Site Name
Hospital Universitario Virgen De La Macarena
Department Name
Servicio de Gastroenterologia
Principal Investigator Name
Federico Arguelles-Arias
Principal Investigator Email
farguelles@telefonica.net
Contact Person Name
Federico Arguelles-Arias
Contact Person Email
farguelles@telefonica.net
Site Name
Hospital Universitario Juan Ramon Jimenez
Department Name
Servicio de Digestivo
Principal Investigator Name
Ana Bejarano Garcia
Contact Person Name
Ana Bejarano Garcia
Site Name
Hospital Universitario De Cabuenes
Department Name
Unidad de Enfermedad Inflamatoria Intestinal
Principal Investigator Name
Pilar Varela Trastoy
Principal Investigator Email
trastoy@hotmail.com
Contact Person Name
Pilar Varela Trastoy
Contact Person Email
trastoy@hotmail.com
Site Name
Area Sanitaria De Ferrol
Department Name
Servicio de Digestivo
Principal Investigator Name
Ana Isabel Echarri Piudo
Principal Investigator Email
ana.echarri.piudo@sergas.es
Contact Person Name
Ana Isabel Echarri Piudo
Contact Person Email
ana.echarri.piudo@sergas.es
Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Servicio de Gastroenterologia
Principal Investigator Name
Maria Isabel Iborra Colomino
Principal Investigator Email
marisaiborra@hotmail.com
Contact Person Name
Maria Isabel Iborra Colomino
Contact Person Email
marisaiborra@hotmail.com

Poland

Earliest CTIS Part Ii Submission Date
11-07-2024
Latest Decision Or Authorization Date
15-05-2026
Processing Time Days
673
Number Of Sites
21
Number Of Participants
81

Sites

Site Name
Bodyclinic Sp. z o.o. sp.k.
Principal Investigator Name
Piotr Gietka
Principal Investigator Email
piotrgietka@gmail.com
Contact Person Name
Piotr Gietka
Contact Person Email
piotrgietka@gmail.com
Site Name
Centrum Medyczne Plejady Magdalena Celinska Loewenhoff Michal Zolnowski sp.k.
Principal Investigator Name
Monika Augustyn
Principal Investigator Email
amonika@interia.pl
Contact Person Name
Monika Augustyn
Contact Person Email
amonika@interia.pl
Site Name
Medical Network Sp. z o.o.
Principal Investigator Name
Jarosław Kierkuś
Principal Investigator Email
j.kierkus@wip.waw.pl
Contact Person Name
Jarosław Kierkuś
Contact Person Email
j.kierkus@wip.waw.pl
Site Name
Centrum Medyczne Medyk Sp. z o.o.
Principal Investigator Name
Rafał Filip
Principal Investigator Email
r.s.filip@wp.pl
Contact Person Name
Rafał Filip
Contact Person Email
r.s.filip@wp.pl
Site Name
H-T. Centrum Medyczne-Endoterapia
Principal Investigator Name
Tomasz Romańczyk
Principal Investigator Email
romanczyk@htcentrum.pl
Contact Person Name
Tomasz Romańczyk
Contact Person Email
romanczyk@htcentrum.pl
Site Name
Futuremeds Sp. z o.o.
Principal Investigator Name
Szymon Wieczorek
Principal Investigator Email
szymon.wieczorek@futuremeds.com
Contact Person Name
Szymon Wieczorek
Site Name
Rivermed Sp. z o.o.
Principal Investigator Name
Łukasz Hordecki
Principal Investigator Email
l.hordecki@rivermed.pl
Contact Person Name
Łukasz Hordecki
Contact Person Email
l.hordecki@rivermed.pl
Site Name
Gyncentrum Sp. z o.o.
Principal Investigator Name
Marek Olakowski
Principal Investigator Email
m.olakowski@holsaclinical.com
Contact Person Name
Marek Olakowski
Contact Person Email
m.olakowski@holsaclinical.com
Site Name
Sonomed Sp. z o.o.
Principal Investigator Name
Anna Wiechowska Kozłowska
Principal Investigator Email
annamwk@wp.pl
Contact Person Name
Anna Wiechowska Kozłowska
Contact Person Email
annamwk@wp.pl
Site Name
Futuremeds Sp. z o.o. (Kraków)
Department Name
FutureMeds Kraków
Principal Investigator Name
Piotr Rozpondek
Principal Investigator Email
piotr.rozpondek@futuremeds.com
Contact Person Name
Piotr Rozpondek
Contact Person Email
piotr.rozpondek@futuremeds.com
Site Name
Centrum Medyczne Oporow
Principal Investigator Name
Radosław Kempiński
Principal Investigator Email
radoslaw.kempinski@cmoporow.com
Contact Person Name
Radosław Kempiński
Site Name
Vivamed Sp. z o.o.
Principal Investigator Name
Robert Petryka
Principal Investigator Email
robert@petrykamed.com
Contact Person Name
Robert Petryka
Contact Person Email
robert@petrykamed.com
Site Name
Centrum Innowacyjnych Terapii Sp. z o.o.
Principal Investigator Name
Witold Kucharski
Principal Investigator Email
witold.kucharski@citrials.pl
Contact Person Name
Witold Kucharski
Contact Person Email
witold.kucharski@citrials.pl
Site Name
Medrise Sp. z o.o.
Principal Investigator Name
Wit Danilkiewicz
Principal Investigator Email
wit.danilkiewicz@medrise.pl
Contact Person Name
Wit Danilkiewicz
Contact Person Email
wit.danilkiewicz@medrise.pl
Site Name
Manermed Sp. z o.o.
Department Name
Centrum Medyczne Medis
Principal Investigator Name
Maria Kłopocka
Principal Investigator Email
mariaklopocka@cm-medis.pl
Contact Person Name
Maria Kłopocka
Contact Person Email
mariaklopocka@cm-medis.pl
Site Name
EMC Instytut Medyczny S.A. (Wrocław)
Department Name
Penta Hospitals Przychodnie, Wrocław Wejherowska
Principal Investigator Name
Patryk Smoliński
Principal Investigator Email
psmolinski@poczta.onet.pl
Contact Person Name
Patryk Smoliński
Contact Person Email
psmolinski@poczta.onet.pl
Site Name
Twoja Przychodnia Szczecinskie Centrum Medyczne Sp. z o.o.
Principal Investigator Name
Beata Gawdis-Wojnarska
Principal Investigator Email
gawdis@twojaprzychodnia.com
Contact Person Name
Beata Gawdis-Wojnarska
Contact Person Email
gawdis@twojaprzychodnia.com
Site Name
Care Access Polska Sp. z o.o.
Principal Investigator Name
Łukasz Jałocha
Principal Investigator Email
s.borek@careaccess.com
Contact Person Name
Łukasz Jałocha
Contact Person Email
s.borek@careaccess.com
Site Name
Centrum Opieki Zdrowotnej Orkan-Med Stec - Michalska Sp. j.
Principal Investigator Name
Krystyna Stec-Michalska
Principal Investigator Email
stemii@wp.pl
Contact Person Name
Krystyna Stec-Michalska
Contact Person Email
stemii@wp.pl
Site Name
EMC Instytut Medyczny S.A. (Poznan)
Principal Investigator Name
Piotr Szabłowski
Principal Investigator Email
szapi@mp.pl
Contact Person Name
Piotr Szabłowski
Contact Person Email
szapi@mp.pl
Site Name
Endoskopia Sp. z o.o.
Principal Investigator Name
Dariusz Kleczkowski
Principal Investigator Email
szach999@wp.pl
Contact Person Name
Dariusz Kleczkowski
Contact Person Email
szach999@wp.pl

France

Earliest CTIS Part Ii Submission Date
11-07-2024
Latest Decision Or Authorization Date
12-05-2026
Processing Time Days
670
Number Of Sites
2
Number Of Participants
1

Sites

Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Service de Gastro-Entérologie
Principal Investigator Name
Arnaud Bourreille
Principal Investigator Email
arnaud.bourreille@chu-nantes.fr
Contact Person Name
Arnaud Bourreille
Site Name
Hospices Civils De Lyon
Department Name
Service de Gastro-Entérologie
Principal Investigator Name
Stéphane Nancey
Principal Investigator Email
stephane.nancey@chu-lyon.fr
Contact Person Name
Stéphane Nancey
Contact Person Email
stephane.nancey@chu-lyon.fr

Italy

Earliest CTIS Part Ii Submission Date
16-05-2024
Latest Decision Or Authorization Date
14-05-2026
Processing Time Days
728
Number Of Sites
2
Number Of Participants
9

Sites

Site Name
Ospedale San Raffaele S.r.l.
Department Name
Gastroenterology and Gastrointestinal Endoscopy Unit
Principal Investigator Name
Silvio Danese
Principal Investigator Email
danese.silvio@hsr.it
Contact Person Name
Silvio Danese
Contact Person Email
danese.silvio@hsr.it
Site Name
Azienda Ospedaliera di Padova
Department Name
U.O. Gastroenterologia
Principal Investigator Name
Edoardo Savarino
Principal Investigator Email
edoardo.savarino@unipd.it
Contact Person Name
Edoardo Savarino
Contact Person Email
edoardo.savarino@unipd.it

Germany

Earliest CTIS Part Ii Submission Date
28-06-2024
Latest Decision Or Authorization Date
13-05-2026
Processing Time Days
684
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Klinik für Innere Medizin I
Principal Investigator Name
Stefan Schreiber
Principal Investigator Email
stefan.schreiber@uksh.de
Contact Person Name
Stefan Schreiber
Contact Person Email
stefan.schreiber@uksh.de

Sponsor

Primary sponsor

Full Name
Gilead Sciences Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
PPD Development L.P.
Responsibilities
CRO

Third parties

  • {"country":"United States","full_name":"PPD Development L.P.","duties_or_roles":"CRO","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"Central laboratory services","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Signant Health Management Limited","duties_or_roles":"Subject devices/ site tablets","organisation_type":"Pharmaceutical company"}
  • {"country":"Canada","full_name":"Alimentiv Inc.","duties_or_roles":"Endoscopy imaging","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Signant Health Management Limited","duties_or_roles":"Blinded enrollment/randomization","organisation_type":"Pharmaceutical company"}
  • {"country":"Romania","full_name":"Arensia Exploratory Medicine S.R.L.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"ARENSIA Exploratory Medicine GmbH","duties_or_roles":"Contract negotiation with PI; Feasibility","organisation_type":"Laboratory/Research/Testing facility"}

Investigational products

Investigational Product Name
GS-1427 25 mg tablets
Active Substance
GS-1427
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Authorised
Starting Dose
25 mg
Dose Levels
25 mg
Maximum Dose
25 mg (maxDailyDoseAmount)
Dose Escalation Increase
25 mg; 75 mg; 100 mg
Investigational Product Name
GS-1427 75 mg tablets
Active Substance
GS-1427
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Authorised
Starting Dose
75 mg
Dose Levels
75 mg
Maximum Dose
75 mg (maxDailyDoseAmount)
Dose Escalation Increase
25 mg; 75 mg; 100 mg
Investigational Product Name
GS-1427 100 mg tablets
Active Substance
GS-1427
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Authorised
Starting Dose
100 mg
Dose Levels
100 mg
Maximum Dose
100 mg (maxDailyDoseAmount)
Dose Escalation Increase
25 mg; 75 mg; 100 mg
Investigational Product Name
PTM 25 mg Tablets (placebo)
Modality
Other
Dose Levels
25 mg (placebo match)
Investigational Product Name
PTM 75 mg Tablets (placebo)
Modality
Other
Dose Levels
75 mg (placebo match)
Investigational Product Name
PTM 100 mg Tablets (placebo)
Modality
Other
Dose Levels
100 mg (placebo match)

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