Clinical trial • Phase III • Nephrology

FINERENONE for Chronic kidney disease | Proteinuria

Phase III trial of FINERENONE for Chronic kidney disease | Proteinuria. open-label, none/not specified-controlled. 40 participants.

Overview

Trial Therapeutic Area
Nephrology
Trial Disease
Chronic kidney disease | Proteinuria
Trial Stage
Phase III
Drug Modality
Small molecule
Paediatric Trial
Yes

Key dates

Initial CTIS Submission Date
21-02-2024
First CTIS Authorization Date
27-03-2024

Trial design

open-label, none/not specified-controlled Phase III trial in Italy, Denmark, Austria and others.

Open Label
Yes
Comparator
None/Not specified
Target Sample Size
40
Trial Duration For Participant
540

Eligibility

Recruits 40 paediatric patients.

Pregnancy Exclusion
Pregnant or breastfeeding or intention to become pregnant during the study
Vulnerable Population
Participants are children and young adults aged 1–18 years. Consent/assent handling requires informed consent from parent(s)/legal guardian and assent from children as appropriate. Age‑specific information sheets, consent and assent forms (Core, Pre-teen, Teen, Parents, Expecting Parents, Study Update versions) and country/language-specific documents are provided (multiple country ICFs and assent templates are listed in the application documents). Decentralised trial (DCT) consent versions are also available where applicable.

Inclusion criteria

  • {"criterion_text":"- Participants must be ≥1 year to 18 years of age, at the time of signing the informed consent/assent."}
  • {"criterion_text":"- Prior participation in the finerenone Phase 3 study FIONA (19920) and not permanently discontinued from treatment by the end of treatment (EoT) visit in FIONA."}
  • {"criterion_text":"- Participants must have a clinical diagnosis of chronic kidney disease (CKD) at Visit 1 which is defined as - CKD stages 1-3 (estimated glomerular filtration rate [eGFR] ≥30 mL/min/1.73m^2) for children ≥1 year to <19 years of age at FIONA EoT and at Visit 1"}
  • {"criterion_text":"- Treated with an angiotensin-converting enzyme inhibitor (ACEI) or angiotensin receptor blocker (ARB) at optimized doses defined as maximally tolerable doses within the recommended dose range according to guidelines on blood pressure (BP) management (or local label / guidelines as applicable), unchanged for at least 30 days prior to Visit 1."}
  • {"criterion_text":"- K+ ≤5.0 mmol/L for children ≥2 years of age at both FIONA EoT and Visit 1, and ≤5.3 mmol/L for children <2 years of age at both FIONA EoT and Visit 1"}
  • {"criterion_text":"- Participant is able to receive enteral feeding (solid food, bottle or cup fed, feeding through nasogastric or gastric feeding tubes) with or without breastfeeding."}

Exclusion criteria

  • {"criterion_text":"- Planned urological surgery expected to influence renal function"}
  • {"criterion_text":"- Concomitant therapy with strong cytochrome P450 isoenzyme 3A4 (CYP3A4) inhibitors, moderate or strong CYP3A4 inducers"}
  • {"criterion_text":"- Previous assignment to treatment during this study"}
  • {"criterion_text":"- Simultaneous participation in another interventional clinical study (e.g., Phase 1 to 4 clinical studies)."}
  • {"criterion_text":"- Any suspected (S)AE related to the study intervention which led to permanent discontinuation of study intervention during the FIONA study"}
  • {"criterion_text":"- Pregnant or breastfeeding or intention to become pregnant during the study"}
  • {"criterion_text":"- Patients who are candidates for renal transplantation, i.e., a kidney transplantation scheduled within the study time frame"}
  • {"criterion_text":"- Systemic hypertension Stage 2 defined according to institutional guidelines on BP management at Visit 1."}
  • {"criterion_text":"- Systemic hypotension defined as symptomatic hypotension or a mean systolic BP below the 5th percentile for age, sex and height but no lower than 80 mmHg for participants <18 years and symptomatic hypotension or a mean systolic blood pressure (SBP) <90 mmHg in participants ≥18 years at Visit 1."}
  • {"criterion_text":"- Known hypersensitivity to the study treatment (active substance or excipients)"}
  • {"criterion_text":"- Severe hepatic insufficiency defined by e.g. Child-Pugh C or analogous scores."}
  • {"criterion_text":"- Participants with immune-mediated CKD using rituximab, cyclophosphamide, abatacept, or prolonged high-dose glucocorticoids (defined as ≥ 0.5 mg/kg/day of prednisolone or equivalent) for more than 7 days"}
  • {"criterion_text":"- Concomitant therapy with a mineralocorticoid receptor antagonist (MRA) (eplerenone, spironolactone, esaxerenone, canrenone), any renin inhibitor (aliskiren, enalkiren, remikiren), any sodium-glucose co-transporter-2 (SGLT2) inhibitor (SGLT2i), sacubitril/valsartan combination (ARNI), or potassium-sparing diuretic (amiloride, triamterene)"}
  • {"criterion_text":"- Concomitant therapy with both ACEI and ARBs together"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Number of participants with treatment emergent adverse events (TEAEs)","definition_or_measurement_approach":"Count of participants experiencing treatment-emergent adverse events (TEAEs) during the study."}
  • {"endpoint_text":"- Change in serum potassium levels from baseline to Day 540±7","definition_or_measurement_approach":"Change in measured serum potassium from baseline to Day 540 ± 7 days."}
  • {"endpoint_text":"- Change in systolic blood pressure (SBP) from baseline to Day 540±7","definition_or_measurement_approach":"Change in measured systolic blood pressure (SBP) from baseline to Day 540 ± 7 days."}

Secondary endpoints

  • {"endpoint_text":"- Change in urinary protein-to-creatinine ratio (UPCR) and urinary albumin-to-creatinine ratio (UACR) from baseline to Day 540±7","definition_or_measurement_approach":"Change in UPCR and UACR measured from baseline to Day 540 ± 7 days."}
  • {"endpoint_text":"- Change in estimated glomerular filtration rate (eGFR) from baseline to Day 540±7","definition_or_measurement_approach":"Change in estimated glomerular filtration rate (eGFR) from baseline to Day 540 ± 7 days."}

Recruitment

Digital Remote Recruitment
Yes
Planned Sample Size
40
Recruitment Window Months
75
Consent Approach
Informed consent is required from the parent(s)/legal guardian and assent from minors as appropriate; participants must sign the informed consent/assent. Age-specific information sheets and consent/assent forms are provided (Core, Pre-teen, Teen, Parents, Expecting Parents, Study Update versions) and country-specific language versions are available across participating Member States. Decentralised clinical trial (DCT) consent/materials are available for some countries (DCT-labelled ICFs present).

Geography

Total Number Of Sites
67
Total Number Of Participants
69

Italy

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
28-04-2026
Processing Time Days
785
Number Of Sites
6
Number Of Participants
5

Sites

Site Name
Ospedale Pediatrico Bambino Gesu'
Department Name
Division of Nephrology and Dialysis, Department of Pediatric Subspecialties
Principal Investigator Name
Marina Vivarelli
Principal Investigator Email
marina.vivarelli@opbg.net
Contact Person Name
Marina Vivarelli
Contact Person Email
marina.vivarelli@opbg.net
Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
U.O. Pediatria, Programma di Nefrologia Pediatrica – Pad. 13
Principal Investigator Name
Andrea Pasini
Principal Investigator Email
andrea.pasini@aosp.bo.it
Contact Person Name
Andrea Pasini
Contact Person Email
andrea.pasini@aosp.bo.it
Site Name
Giannina Gaslini Institute For Scientific Hospitalization And Care
Department Name
Department of Nephrology, dialysis and transplantation
Principal Investigator Name
Eugenio Verrina
Principal Investigator Email
enricoverrina@gaslini.org
Contact Person Name
Eugenio Verrina
Contact Person Email
enricoverrina@gaslini.org
Site Name
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Department Name
Pediatric Nephrology, Dialysis and Transplant Unit
Principal Investigator Name
William Morello
Principal Investigator Email
william.morello@policlinico.mi.it
Contact Person Name
William Morello
Site Name
Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
Department Name
Nephrology, Dialysis and TransplantaƟon Unit
Principal Investigator Name
Licia Peruzzi
Principal Investigator Email
lperuzzi@cittadellasalute.to.it
Contact Person Name
Licia Peruzzi
Site Name
Azienda Ospedaliera Universitaria Meyer IRCCS
Department Name
Pediatric Nephrology and Dialysis Unit
Principal Investigator Name
Francesca Becherucci
Principal Investigator Email
francesca.becherucci@meyer.it
Contact Person Name
Francesca Becherucci
Contact Person Email
francesca.becherucci@meyer.it

Denmark

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
26-04-2026
Processing Time Days
783
Number Of Sites
3
Number Of Participants
2

Sites

Site Name
Rigshospitalet
Department Name
BørneUngeAfdelingen Afsnit 4072 (opgang 4, 7. sal)
Principal Investigator Name
Ida Maria Schmidt
Principal Investigator Email
ida.maria.schmidt@regionh.dk
Contact Person Name
Ida Maria Schmidt
Contact Person Email
ida.maria.schmidt@regionh.dk
Site Name
Aarhus Universitetshospital
Department Name
Børn og Unge, Krydspunkt H301, Plan 3
Principal Investigator Name
Konstantinos Kamperis
Principal Investigator Email
konskamp@rm.dk
Contact Person Name
Konstantinos Kamperis
Contact Person Email
konskamp@rm.dk
Site Name
Odense University Hospital
Department Name
H.C. Andersen Børnehospital
Principal Investigator Name
Per Wittenhagen
Principal Investigator Email
per.wittenhagen@rsyd.dk
Contact Person Name
Per Wittenhagen
Contact Person Email
per.wittenhagen@rsyd.dk

Austria

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
28-04-2026
Processing Time Days
785
Number Of Sites
4
Number Of Participants
2

Sites

Site Name
Medical University Of Vienna
Department Name
Pediatrics and Adolescent Medicine
Principal Investigator Name
Krisztina Heindl-Rusai
Principal Investigator Email
krisztina.rusai@meduniwien.ac.at
Contact Person Name
Krisztina Heindl-Rusai
Site Name
Kepler Universitaetsklinikum GmbH
Department Name
Pediatrics and Adolescent Medicine
Principal Investigator Name
Roland Lanzersdorfer
Principal Investigator Email
roland.lanzersdorfer@kepleruniklinikum.at
Contact Person Name
Roland Lanzersdorfer
Site Name
Medical University Of Graz
Department Name
Pediatrics and Adolescent Medicine
Principal Investigator Name
Christoph Mache
Principal Investigator Email
christoph.mache@medunigraz.at
Contact Person Name
Christoph Mache
Contact Person Email
christoph.mache@medunigraz.at
Site Name
Gemeinnutzige Salzburger Landes kliniken Betriebsgesellschaft mbH
Department Name
Pediatrics and Adolescent Medicine
Principal Investigator Name
Monika Edelbauer-Wechselberger
Principal Investigator Email
m.edelbauer-wechselberger@salk.at
Contact Person Name
Monika Edelbauer-Wechselberger

Poland

Earliest CTIS Part Ii Submission Date
28-03-2024
Latest Decision Or Authorization Date
27-04-2026
Processing Time Days
784
Number Of Sites
4
Number Of Participants
8

Sites

Site Name
Instytut Centrum Zdrowia Matki Polki
Department Name
Klinika Pediatrii, Immunologii i Nefrologii
Principal Investigator Name
Marcin Tkaczyk
Principal Investigator Email
sek31@iczmp.edu.pl
Contact Person Name
Marcin Tkaczyk
Contact Person Email
sek31@iczmp.edu.pl
Site Name
Uniwersyteckie Centrum Kliniczne
Department Name
Klinika Chorob Nerek i Nadcisnienia Dzieci i Młodziezy
Principal Investigator Name
Aleksandra Zurowska
Principal Investigator Email
nefrologiadziecieca@uck.gda.pl
Contact Person Name
Aleksandra Zurowska
Contact Person Email
nefrologiadziecieca@uck.gda.pl
Site Name
Uniwersytecki Dzieciecy Szpital Kliniczny Im. L. Zamenhofa W Bialymstoku samodzielny publiczny zakład opieki zdrowotnej
Department Name
Klinika Pediatrii i Nefrologii
Principal Investigator Name
Anna Wasilewska
Principal Investigator Email
nefrologia@udsk.pl
Contact Person Name
Anna Wasilewska
Contact Person Email
nefrologia@udsk.pl
Site Name
Instytut Pomnik Centrum Zdrowia Dziecka
Department Name
Klinika Nefrologii, Transplantacji Nerek i Nadcisnienia Tetniczego
Principal Investigator Name
Malgorzata Podymniak-Grzeszykowska
Principal Investigator Email
oddzial.nefrologia@ipczd.pl
Contact Person Name
Malgorzata Podymniak-Grzeszykowska
Contact Person Email
oddzial.nefrologia@ipczd.pl

France

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
28-04-2026
Processing Time Days
785
Number Of Sites
6
Number Of Participants
8

Sites

Site Name
Hospices Civils De Lyon
Department Name
Service de néphrologie - rhumatologie - dermatologie pédiatrique
Principal Investigator Name
Justine Bacchetta
Principal Investigator Email
ghe.ciclyon@chu-lyon.fr
Contact Person Name
Justine Bacchetta
Contact Person Email
ghe.ciclyon@chu-lyon.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service de Néphrologie - Transplantation - Hémodialyse pédiatrique
Principal Investigator Name
Julien Hogan
Principal Investigator Email
sabrina.ouamdi@aphp.fr
Contact Person Name
Julien Hogan
Contact Person Email
sabrina.ouamdi@aphp.fr
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Service de Néphrologie pédiatrique
Principal Investigator Name
Marc Fila
Principal Investigator Email
cic@chu-montpellier.fr
Contact Person Name
Marc Fila
Contact Person Email
cic@chu-montpellier.fr
Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Unité de Néphrologie Service de Pédiatrie
Principal Investigator Name
Jérôme Harambat
Principal Investigator Email
cic-p.coordination@chu-bordeaux.fr
Contact Person Name
Jérôme Harambat
Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
Service de Néphrologie pédiatrique
Principal Investigator Name
Ariane Zaloszyc
Principal Investigator Email
cic@chru-strasbourg.fr
Contact Person Name
Ariane Zaloszyc
Contact Person Email
cic@chru-strasbourg.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Pédiatrie - Néphrologie, médecine interne et hypertension
Principal Investigator Name
Stéphane Decramer
Principal Investigator Email
Drci.toulouse@chu-toulouse.fr
Contact Person Name
Stéphane Decramer
Contact Person Email
Drci.toulouse@chu-toulouse.fr

Finland

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
23-04-2026
Processing Time Days
780
Number Of Sites
3
Number Of Participants
3

Sites

Site Name
Tampere University Hospital
Department Name
Lasten Lääketutkimuskeskus PeeTU
Principal Investigator Name
Sauli Palmu
Principal Investigator Email
sauli.palmu@pirha.fi
Contact Person Name
Sauli Palmu
Contact Person Email
sauli.palmu@pirha.fi
Site Name
HUS-Yhtymae
Department Name
Lasten Uusi Sairaala
Principal Investigator Name
Tuula Hölttä
Principal Investigator Email
tuula.holtta@hus.fi
Contact Person Name
Tuula Hölttä
Contact Person Email
tuula.holtta@hus.fi
Site Name
Turku University Hospital
Department Name
Majakkasairaala, Lasten ja Nuorten klinikka
Principal Investigator Name
Janne Kataja
Principal Investigator Email
janne.kataja@varha.fi
Contact Person Name
Janne Kataja
Contact Person Email
janne.kataja@varha.fi

Spain

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
24-04-2026
Processing Time Days
781
Number Of Sites
6
Number Of Participants
5

Sites

Site Name
Hospital Universitario Regional De Malaga
Department Name
Pediatric Nephrology
Principal Investigator Name
Verónica Martínez Rivera
Contact Person Name
Verónica Martínez Rivera
Site Name
Hospital Universitario La Paz
Department Name
Pediatric Nephrology
Principal Investigator Name
Marta Melgosa Hijosa
Principal Investigator Email
marta.melgosa@salud.madrid.org
Contact Person Name
Marta Melgosa Hijosa
Contact Person Email
marta.melgosa@salud.madrid.org
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Pediatric Nephrology
Principal Investigator Name
Francisco de la Cerda Ojeda
Principal Investigator Email
Francisco.cerda.sspa@juntadeandalucia.es
Contact Person Name
Francisco de la Cerda Ojeda
Site Name
Hospital Universitari Vall D Hebron
Department Name
Pediatric Nephrology
Principal Investigator Name
Gema Ariceta Iraola
Principal Investigator Email
gema.ariceta@vallhebron.cat
Contact Person Name
Gema Ariceta Iraola
Contact Person Email
gema.ariceta@vallhebron.cat
Site Name
Hospital Universitario 12 De Octubre
Department Name
Pediatric Nephrology
Principal Investigator Name
Maria del Mar Espino Hernández
Principal Investigator Email
mar.espino@salud.madrid.org
Contact Person Name
Maria del Mar Espino Hernández
Contact Person Email
mar.espino@salud.madrid.org
Site Name
Sant Joan De Deu Barcelona Hospital
Department Name
Pediatric Nephrology
Principal Investigator Name
Álvaro Domingo Madrid Aris
Principal Investigator Email
alvaro.madrid@sjd.es
Contact Person Name
Álvaro Domingo Madrid Aris
Contact Person Email
alvaro.madrid@sjd.es

Czechia

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
24-04-2026
Processing Time Days
781
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Fakultni Nemocnice V Motole
Department Name
Pediatrická klinika
Principal Investigator Name
Jakub Zieg
Principal Investigator Email
Jakub.Zieg@fnmotol.cz
Contact Person Name
Jakub Zieg
Contact Person Email
Jakub.Zieg@fnmotol.cz
Site Name
Vseobecna Fakultni Nemocnice V Praze
Department Name
Klinika pediatrie a dědičných poruch metabolismu
Principal Investigator Name
Šárka Doležalová
Principal Investigator Email
Sarka.Dolezalova@vfn.cz
Contact Person Name
Šárka Doležalová
Contact Person Email
Sarka.Dolezalova@vfn.cz

Portugal

Earliest CTIS Part Ii Submission Date
11-04-2024
Latest Decision Or Authorization Date
23-04-2026
Processing Time Days
780
Number Of Sites
2
Number Of Participants
1

Sites

Site Name
Unidade Local De Saude De Coimbra E.P.E.
Department Name
Pediatrics
Principal Investigator Name
Marta Machado
Principal Investigator Email
martamachado@ulscoimbra.min-saude.pt
Contact Person Name
Marta Machado
Site Name
Centro Hospitalar Universitario De Santo Antonio E.P.E.
Department Name
Unidade de Pediatria
Principal Investigator Name
Alberto Caldas Afonso
Principal Investigator Email
caldasafonso.cmin@chporto.min-saude.pt
Contact Person Name
Alberto Caldas Afonso

Sweden

Earliest CTIS Part Ii Submission Date
27-03-2024
Latest Decision Or Authorization Date
23-04-2026
Processing Time Days
780
Number Of Sites
3
Number Of Participants
2

Sites

Site Name
Karolinska University Hospital
Department Name
K88 Dagvård, Barnnefrologi, Karolinska universitetssjukhuset Huddinge
Principal Investigator Name
Peter Bárány
Contact Person Name
Peter Bárány
Site Name
Region Skane Skanes Universitetssjukhus
Department Name
Barnnefroenheten, Barnkliniken, Lasarettsgatan 48
Principal Investigator Name
Lisa Sartz
Principal Investigator Email
forumsoder@skane.se
Contact Person Name
Lisa Sartz
Contact Person Email
forumsoder@skane.se
Site Name
Uppsala University Hospital
Department Name
Njur- & urinvägsmottagningen för barn & ungdom, Akademiska barnsjukhuset, Ingång 95/96, NBV
Principal Investigator Name
Site Closed
Principal Investigator Email
site_closed@site-closed.se
Contact Person Name
Site Closed
Contact Person Email
site_closed@site-closed.se

Netherlands

Earliest CTIS Part Ii Submission Date
28-03-2024
Latest Decision Or Authorization Date
23-04-2026
Processing Time Days
780
Number Of Sites
2
Number Of Participants
1

Sites

Site Name
Universitair Medisch Centrum Groningen
Department Name
Pediatric Nephrology
Principal Investigator Name
Martine T. P. Besouw
Principal Investigator Email
m.t.p.besouw@umcg.nl
Contact Person Name
Martine T. P. Besouw
Contact Person Email
m.t.p.besouw@umcg.nl
Site Name
Universitair Medisch Centrum Utrecht
Department Name
Pediatric Nephrology
Principal Investigator Name
Mandy Gabriëlle Keijzer-Veen
Principal Investigator Email
m.g.veen-14@umcutrecht.nl
Contact Person Name
Mandy Gabriëlle Keijzer-Veen
Contact Person Email
m.g.veen-14@umcutrecht.nl

Germany

Earliest CTIS Part Ii Submission Date
27-03-2024
Latest Decision Or Authorization Date
24-04-2026
Processing Time Days
781
Number Of Sites
7
Number Of Participants
7

Sites

Site Name
University Medical Center Hamburg-Eppendorf
Department Name
Klinik für Kinder- und Jugendmedizin
Principal Investigator Name
Jun Oh
Principal Investigator Email
j.oh@uke.de
Contact Person Name
Jun Oh
Contact Person Email
j.oh@uke.de
Site Name
Universitaetsklinikum Heidelberg AöR
Department Name
Paediatrisches Klinisch-Pharmakologisches Studienzentrum (paedKliPS)
Principal Investigator Name
Elke Wuehl
Principal Investigator Email
Elke.Wuehl@med.uni-heidelberg.de
Contact Person Name
Elke Wuehl
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
Klinik für Pädiatrie mit Schwerpunkt Gastroenterologie, Nephrologie und Stoffwechselmedizin
Principal Investigator Name
Julia Thumfart
Principal Investigator Email
julia.thumfart@charite.de
Contact Person Name
Julia Thumfart
Contact Person Email
julia.thumfart@charite.de
Site Name
Kindernierenzentrum Bonn
Principal Investigator Name
Gesa Schalk
Principal Investigator Email
gesa.schalk@knz-bonn.de
Contact Person Name
Gesa Schalk
Contact Person Email
gesa.schalk@knz-bonn.de
Site Name
Medizinische Hochschule Hannover
Department Name
Klinik für Paediatrische Nieren-, Leber- und Stoffwechselerkrankungen
Principal Investigator Name
Nele Kanzelmeyer
Principal Investigator Email
Kanzelmeyer.Nele@mh-hannover.de
Contact Person Name
Nele Kanzelmeyer
Site Name
Universitaetsklinikum Muenster AöR
Department Name
Klinik fuer Kinder- und Jugendmedizin - Allgemeine Paediatrie
Principal Investigator Name
Martin Konrad
Principal Investigator Email
Martin.Konrad@ukmuenster.de
Contact Person Name
Martin Konrad
Contact Person Email
Martin.Konrad@ukmuenster.de
Site Name
Universitaetsklinikum Essen AöR
Department Name
Klinik für Kinderheilkunde II
Principal Investigator Name
Lars Pape
Principal Investigator Email
Lars.Pape@uk-essen.de
Contact Person Name
Lars Pape
Contact Person Email
Lars.Pape@uk-essen.de

Belgium

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
27-04-2026
Processing Time Days
785
Number Of Sites
5
Number Of Participants
5

Sites

Site Name
Association Hospitaliere De Bruxelles Hopital Universitaire Des Enfants Reine Fabiola
Department Name
Néphrologie - Dialyse
Principal Investigator Name
Elise Hennaut
Principal Investigator Email
elise.hennaut@hubruxelles.be
Contact Person Name
Elise Hennaut
Contact Person Email
elise.hennaut@hubruxelles.be
Site Name
UZ Leuven
Department Name
Kindernefrologie en orgaantransplantatie
Principal Investigator Name
Detlef Böckenhauer
Principal Investigator Email
detlef.bockenhauer@uzleuven.be
Contact Person Name
Detlef Böckenhauer
Contact Person Email
detlef.bockenhauer@uzleuven.be
Site Name
Cliniques Universitaires Saint-Luc
Department Name
Néphrologie Pédiatrique
Principal Investigator Name
Nathalie Godefroid
Principal Investigator Email
nathalie.godefroid@saintluc.uclouvain.be
Contact Person Name
Nathalie Godefroid
Site Name
Universitair Ziekenhuis Gent
Department Name
Kindernefrologie
Principal Investigator Name
Evelien Snauwaert
Principal Investigator Email
secretariaat.kindernefrologie@uzgent.be
Contact Person Name
Evelien Snauwaert
Site Name
CHC MontLegia
Department Name
Néphrologie pédiatrique
Principal Investigator Name
Laure Collard
Principal Investigator Email
LAURE.COLLARD@chc.be
Contact Person Name
Laure Collard
Contact Person Email
LAURE.COLLARD@chc.be

Lithuania

Earliest CTIS Part Ii Submission Date
08-05-2024
Latest Decision Or Authorization Date
23-04-2026
Processing Time Days
780
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Vilniaus Universiteto Ligonine Santaros Klinikos Vsi
Department Name
Pediatrijos centras
Principal Investigator Name
Augustina Jankauskienė
Principal Investigator Email
augustina.jankauskiene@santa.lt
Contact Person Name
Augustina Jankauskienė
Site Name
Lietuvos sveikatos mokslu universiteto ligonine Kauno klinikos
Department Name
I vaikų ligų skyrius
Principal Investigator Name
Jūratė Masalskienė
Principal Investigator Email
jurate.masalskiene@kaunoklinikos.lt
Contact Person Name
Jūratė Masalskienė

Bulgaria

Earliest CTIS Part Ii Submission Date
07-11-2025
Latest Decision Or Authorization Date
28-04-2026
Processing Time Days
172
Number Of Sites
3
Number Of Participants
9

Sites

Site Name
Specialized Hospital For Active Treatment Of Childrens Diseases Professor Ivan Mitev
Department Name
Clinic of Pediatric Nephrology and Dialysis – dialysis treatment
Principal Investigator Name
Galya Zlatanova
Principal Investigator Email
zlatanova_g@pediatrichospital.bg
Contact Person Name
Galya Zlatanova
Site Name
Umbal - Prof. D-R Stoyan Kirkovich AD
Department Name
Clinic of Pediatrics
Principal Investigator Name
Emiliya Kostadinova
Principal Investigator Email
kostadinovaemilia@abv.bg
Contact Person Name
Emiliya Kostadinova
Contact Person Email
kostadinovaemilia@abv.bg
Site Name
University Multiprofile Hospital For Active Treatment Saint Georgi EAD
Department Name
Clinic of Pediatrics
Principal Investigator Name
Petya Markova
Principal Investigator Email
klinikadetska@gmail.com
Contact Person Name
Petya Markova
Contact Person Email
klinikadetska@gmail.com

Hungary

Earliest CTIS Part Ii Submission Date
04-03-2024
Latest Decision Or Authorization Date
24-04-2026
Processing Time Days
781
Number Of Sites
4
Number Of Participants
2

Sites

Site Name
Semmelweis University
Department Name
I. Sz. Gyermekgyogyaszati Klinika
Principal Investigator Name
Balint Mikes
Principal Investigator Email
mikesbalint@gmail.com
Contact Person Name
Balint Mikes
Contact Person Email
mikesbalint@gmail.com
Site Name
University Of Debrecen
Department Name
Gyermekgyogyaszati Klinika
Principal Investigator Name
Tamas Szabo
Principal Investigator Email
gyermeknephrologia@gmail.com
Contact Person Name
Tamas Szabo
Contact Person Email
gyermeknephrologia@gmail.com
Site Name
University Of Szeged
Department Name
Gyermekgyogyaszati Klinika es Gyermekegeszsegugyi Kozpont
Principal Investigator Name
Csaba Bereczki
Principal Investigator Email
study.pedia@med.u-szeged.hu
Contact Person Name
Csaba Bereczki
Contact Person Email
study.pedia@med.u-szeged.hu
Site Name
University Of Pecs
Department Name
Gyermekgyogyaszati Klinika
Principal Investigator Name
Tamas Decsi
Principal Investigator Email
gyereknefrologia.pecs@pte.hu
Contact Person Name
Tamas Decsi
Contact Person Email
gyereknefrologia.pecs@pte.hu

Greece

Earliest CTIS Part Ii Submission Date
13-05-2024
Latest Decision Or Authorization Date
24-04-2026
Processing Time Days
781
Number Of Sites
5
Number Of Participants
5

Sites

Site Name
Nosokomeio Paidon I Agia Sofia
Department Name
1st Clinic of Pediatrics, Nephrology Department
Principal Investigator Name
Nikolaos Stergiou
Principal Investigator Email
pednephr@paidon-agiasofia.gr
Contact Person Name
Nikolaos Stergiou
Contact Person Email
pednephr@paidon-agiasofia.gr
Site Name
Ippokratio General Hospital Of Thessaloniki
Department Name
Pediatric Nephrology Unit, 3rd Department of Paediatrics
Principal Investigator Name
Ioannis Ntotis
Principal Investigator Email
doctors-gpaid@ippokratio.gr
Contact Person Name
Ioannis Ntotis
Contact Person Email
doctors-gpaid@ippokratio.gr
Site Name
Athens General Children's Hospital Panagioti And Aglaia Kyriakou
Department Name
Pediatric Nephrology Department
Principal Investigator Name
Varvara Askiti
Principal Investigator Email
mtnagkyriakou@gmail.com
Contact Person Name
Varvara Askiti
Contact Person Email
mtnagkyriakou@gmail.com
Site Name
University General Hospital Of Heraklion
Department Name
Department of Pediatrics
Principal Investigator Name
Maria Bitsori
Principal Investigator Email
paed@pagni.gr
Contact Person Name
Maria Bitsori
Contact Person Email
paed@pagni.gr
Site Name
University General Hospital Of Ioannina
Department Name
Child Health Sector
Principal Investigator Name
Aikaterini Siomou
Principal Investigator Email
ped.pgni@gmail.com
Contact Person Name
Aikaterini Siomou
Contact Person Email
ped.pgni@gmail.com

Sponsor

Primary sponsor

Full Name
Bayer AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Germany

Contract research organisations

Name
Eresearchtechnology Inc.
Responsibilities
ECG analysis/review, Echocardiography image analysis/review
Name
Labcorp Central Laboratory Services LP
Responsibilities
Central laboratory services
Name
Swiss BioQuant AG
Responsibilities
Pharmacokinetics analysis
Name
Fisher Clinical Services GmbH
Name
Suvoda LLC
Name
Illingworth Research Group Limited
Responsibilities
Decentralized Clinical Trial: Home Nursing
Name
DATAN Analytics GmbH

Third parties

  • {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"ECG analysis/review, Echocardiography image analysis/review","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Switzerland","full_name":"Swiss BioQuant AG","duties_or_roles":"Pharmacokinetics analysis","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Switzerland","full_name":"Fisher Clinical Services GmbH","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Suvoda LLC","duties_or_roles":"","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Illingworth Research Group Limited","duties_or_roles":"Decentralized Clinical Trial: Home Nursing","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"Germany","full_name":"Universitaetsklinikum Heidelberg AöR","duties_or_roles":"Expert consultation. ESCAPE sites will participate in the study","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"Italy","full_name":"Fondazione Penta ETS","duties_or_roles":"Expert consultation: Fondazione Penta Onlus - conect4children (c4c) expert have participated in expert panel discussion","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Germany","full_name":"DATAN Analytics GmbH","duties_or_roles":"","organisation_type":"Non-Pharmaceutical company"}

Investigational products

Investigational Product Name
Finerenone
Active Substance
FINERENONE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
Oral
Authorisation Status
Authorised
Dose Levels
max daily dose 10 mg (product record: maxDailyDoseAmount: 10 mg)
Maximum Dose
10 mg
Investigational Product Name
BAY 94-8862
Active Substance
FINERENONE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
Oral
Authorisation Status
Authorised
Dose Levels
max daily dose 20 mg (product record: maxDailyDoseAmount: 20 mg)
Maximum Dose
20 mg
Investigational Product Name
BAY 948862 (granules for oral suspension)
Active Substance
FINERENONE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
Oral (granules for oral suspension)
Authorisation Status
Authorised
Dose Levels
max daily dose 20 mg (product record: maxDailyDoseAmount: 20 mg)
Maximum Dose
20 mg
Investigational Product Name
Finerenone Bayer (paediatric granules for oral suspension)
Active Substance
FINERENONE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
Oral (granules)
Authorisation Status
Authorised
Dose Levels
max daily dose 20 mg (paediatric formulation record: maxDailyDoseAmount: 20 mg)
Maximum Dose
20 mg
Combination Treatment
Yes

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