Clinical trial • Phase III • Ophthalmology

FARICIMAB for Myopic choroidal neovascularization

Phase III trial of FARICIMAB for Myopic choroidal neovascularization.

Overview

Trial Therapeutic Area
Ophthalmology
Trial Disease
Myopic choroidal neovascularization
Trial Stage
Phase III
Drug Modality
Bispecific antibody|Monoclonal antibody

Key dates

Initial CTIS Submission Date
17-11-2023
First CTIS Authorization Date
26-03-2024

Trial design

Randomised, faricimab (intravitreal injection; dose/schedule not specified in the application)|ranibizumab (lucentis) (intravitreal injection; dose/schedule not specified in the application; product: lucentis 10 mg/ml solution for injection, marketing authorisation eu/1/06/374/004)-controlled Phase III trial across 40 sites in France, Germany, Italy and others.

Randomised
Yes
Comparator
FARICIMAB (intravitreal injection; dose/schedule not specified in the application)|RANIBIZUMAB (Lucentis) (intravitreal injection; dose/schedule not specified in the application; product: Lucentis 10 mg/ml solution for injection, marketing authorisation EU/1/06/374/004)
Target Sample Size
190
Trial Duration For Participant
336

Eligibility

Recruits 190 adults.

Inclusion criteria

  • {"criterion_text":"- 1. Overtly healthy as determined by medical evaluation that includes medical history, physical examination, and laboratory tests"}
  • {"criterion_text":"- 2. Treatment-naïve choroidal neovascularization (CNV) secondary to myopia"}
  • {"criterion_text":"- 3. Diagnosis of active myopic CNV in the study eye confirmed by ocular examination and CRC review"}
  • {"criterion_text":"- 4. BCVA of 78 to 24 letters, inclusive (20/32 to 20/320 approximate Snellen equivalent), using the Early Treatment Diabetic Retinopathy Study (ETDRS) protocol and assessed at the initial testing distance of 4 meters (see the BCVA manual for additional details) on Day 1"}
  • {"criterion_text":"- 5. Presence of at least 1 of the following lesion types (determined by CRC): Subfoveal (presence of abnormal neovasculature in the avascular central fovea) Juxtafoveal (presence of abnormal neovasculature not under the center of the fovea but ≤ 200 um from the center) with involvement of the central macular area Extrafoveal (presence of abnormal neovasculature > 200 um from the center of the fovea) with involvement of the central macular area Margin of the optic disc (presence of abnormal neovasculature at peripapillary area) with involvement of the central macular area"}
  • {"criterion_text":"- 6. Sufficiently clear ocular media and adequate pupillary dilatation to allow acquisition of good quality retinal images to confirm diagnosis"}

Exclusion criteria

  • {"criterion_text":"- 1. CNV due to causes other than pathologic myopia, such as neovascular age-related macular degeneration, ocular histoplasmosis, trauma, angioid streaks, choroidal rupture, or uveitis, etc"}
  • {"criterion_text":"- 2. Any history of macular pathology unrelated to pathologic myopia affecting vision or contributing to the presence of intraretinal or subretinal fluid"}
  • {"criterion_text":"- 3. Presence at screening of central serous chorioretinopathy or myopic tractional maculopathy. Retinal pigment epithelial tear involving the macula on Day 1"}
  • {"criterion_text":"- 4. Non-functioning non-study eye, defined as either: BCVA Snellen equivalent of 20/200 or worse No physical presence of non-study eye (i.e., monocular)"}
  • {"criterion_text":"- 5. Prior IVT administration of faricimab in either eye"}
  • {"criterion_text":"- 6. History of idiopathic or autoimmune-associated uveitis in either eye. Active ocular inflammation (anterior, intermediate or posterior uveitis, grade trace or above) or suspected or active ocular or periocular infection in either eye on Day 1"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- 1. Change from baseline in BCVA averaged over Weeks 4, 8, and 12","definition_or_measurement_approach":"BCVA measured using the ETDRS protocol at Weeks 4, 8 and 12; primary endpoint is change from baseline averaged over those weeks."}

Secondary endpoints

  • {"endpoint_text":"- 1. Change from baseline in BCVA over time","definition_or_measurement_approach":"BCVA measured over study visits (ETDRS) to assess change from baseline over time."}
  • {"endpoint_text":"- 2. Proportion of patients gaining ≥15 letters averaged over Weeks 4, 8, and 12","definition_or_measurement_approach":"Proportion based on ETDRS letter gain averaged across Weeks 4, 8 and 12."}
  • {"endpoint_text":"- 3. Proportion of patients gaining ≥15 letters in BCVA from baseline over time","definition_or_measurement_approach":"Proportion of subjects achieving ≥15-letter BCVA gain at scheduled timepoints."}
  • {"endpoint_text":"- 4. Proportion of patients avoiding loss of ≥15 letters in BCVA from baseline over time","definition_or_measurement_approach":"Proportion of subjects not losing ≥15 ETDRS letters at scheduled timepoints."}
  • {"endpoint_text":"- 5. Proportion of patients gaining ≥15 letters or achieving BCVA of ≥84 letters over time","definition_or_measurement_approach":"Composite endpoint using ETDRS letter thresholds over time."}
  • {"endpoint_text":"- 6. Proportion of patients with BCVA Snellen equivalent of 20/40 or better over time","definition_or_measurement_approach":"Proportion determined from ETDRS-to-Snellen-equivalent conversions at visits."}
  • {"endpoint_text":"- 7. Proportion of patients with BCVA Snellen equivalent of 20/200 or worse over time","definition_or_measurement_approach":"Proportion determined from ETDRS-to-Snellen-equivalent conversions at visits."}
  • {"endpoint_text":"- 8. Proportion of patients only receiving one injection from baseline to Week 12","definition_or_measurement_approach":"Count of IVT injections administered up to Week 12; proportion with only one injection."}
  • {"endpoint_text":"- 9. Proportion of patients only receiving one injection from baseline to Week 24","definition_or_measurement_approach":"Count of IVT injections administered up to Week 24; proportion with only one injection."}
  • {"endpoint_text":"- 10. Proportion of patients only receiving one injection from baseline to Week 48","definition_or_measurement_approach":"Count of IVT injections administered up to Week 48; proportion with only one injection."}
  • {"endpoint_text":"- 11. Number of IVT injections received by Week 12","definition_or_measurement_approach":"Total number of intravitreal injections received by each patient by Week 12."}
  • {"endpoint_text":"- 12. Number of IVT injections received by Week 24","definition_or_measurement_approach":"Total number of intravitreal injections received by each patient by Week 24."}
  • {"endpoint_text":"- 13. Number of IVT injections received by Week 48","definition_or_measurement_approach":"Total number of intravitreal injections received by each patient by Week 48."}
  • {"endpoint_text":"- 14. Change from baseline in central subfield thickness (CST) of the study eye averaged over Weeks 4, 8, and 12","definition_or_measurement_approach":"CST measured by OCT; change from baseline averaged over Weeks 4, 8 and 12."}
  • {"endpoint_text":"- 15. Change from baseline in CST of the study eye over time","definition_or_measurement_approach":"CST measured by OCT over scheduled visits to assess change from baseline."}
  • {"endpoint_text":"- 16. Change from baseline in total area of CNV lesion at Week 12 and Week 48","definition_or_measurement_approach":"Total lesion area measured (imaging assessment) at Weeks 12 and 48 compared to baseline."}
  • {"endpoint_text":"- 17. Change from baseline in total area of CNV leakage at Week 12 and Week 48","definition_or_measurement_approach":"Total leakage area measured (imaging/FFA) at Weeks 12 and 48 compared to baseline."}
  • {"endpoint_text":"- 18. Proportion of patients with absence of macular leakage at Week 12 and Week 48","definition_or_measurement_approach":"Determined by imaging (FFA/CFP/OCT) at Weeks 12 and 48."}
  • {"endpoint_text":"- 19. Incidence and severity of ocular adverse events","definition_or_measurement_approach":"Standard AE reporting and grading for ocular adverse events."}
  • {"endpoint_text":"- 20. Incidence and severity of non-ocular adverse events","definition_or_measurement_approach":"Standard AE reporting and grading for non-ocular adverse events."}
  • {"endpoint_text":"- 21. Prevalence of ADAs at baseline and incidence of ADA during the study","definition_or_measurement_approach":"Antidrug antibodies measured at baseline and during study visits using immunogenicity assays."}
  • {"endpoint_text":"- 22. Relationship between ADA status and efficacy or safety endpoints","definition_or_measurement_approach":"Exploratory analyses correlating ADA presence/status with efficacy (e.g., BCVA) and safety outcomes."}

Recruitment

Planned Sample Size
190
Recruitment Window Months
34
Consent Approach
Subject information sheets and informed consent forms are provided (documents listed: L1_SIS and ICF-Volunteer; L1_SIS and ICF-IAF; L1_SIS and ICF-Main; L1_SIS and ICF Infant Authorization). Multiple language materials/synopses are present (English, French, Spanish, Polish, Italian). Specific consent/assent text and age-specific consent handling are not extractable from the provided data.

Geography

Total Number Of Sites
40
Total Number Of Participants
90

France

Earliest CTIS Part Ii Submission Date
15-02-2024
Latest Decision Or Authorization Date
21-10-2025
Processing Time Days
614
Number Of Sites
11
Number Of Participants
27

Sites

Site Name
Pole Vision Val D'Ouest
Department Name
Ophtalmology
Contact Person Name
Pierre-Loïc Cornut
Contact Person Email
direction@polevision.fr
Site Name
Centre Monticelli Paradis D Ophtalmologie
Department Name
Ophtalmology
Contact Person Name
Frederic Matonti
Contact Person Email
fdbm.retine@gmail.com
Site Name
Quinze-Vingts National Ophthalmology Hospital
Department Name
Ophtalmology
Contact Person Name
Jean-François Girmens
Contact Person Email
jfgirmens@15-20.fr
Site Name
Hospital Hotel Dieu
Department Name
Ophtalmology
Contact Person Name
Hélène Massé
Contact Person Email
catherine.ivan@chu-nantes.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Ophtalmology
Contact Person Name
Aude Couturier
Contact Person Email
anfel.lemiti@aphp.fr
Site Name
Theorie Etudes Organisation Recherche En Retine Medicale S.A.R.L.
Department Name
Ophtalmology
Contact Person Name
Salomon Yves Cohen
Contact Person Email
b.maloberti@gmail.com
Site Name
Ophtalmologie Maison Rouge S.C.M.
Department Name
Ophtalmology
Contact Person Name
Benjamin Wolff
Contact Person Email
v.vasseur@comr.fr
Site Name
Centre Hospitalier Intercommunal Creteil
Department Name
Ophtalmology
Contact Person Name
Eric Souied
Contact Person Email
eva.guetta@chicreteil.fr
Site Name
Hopital Fondation Adolphe De Rothschild
Department Name
Ophtalmology
Contact Person Name
Sophie Bonnin
Contact Person Email
sbonnin@for.paris
Site Name
Hopital De La Croix Rousse
Department Name
Ophtalmology
Contact Person Name
Laurent Kodjikian
Contact Person Email
amelie.bouilloux@chu-lyon.fr
Site Name
Retina
Department Name
Ophtalmology
Contact Person Name
Hessam Razavi
Contact Person Email
centrestexupery37@gmail.com

Germany

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
31-07-2024
Processing Time Days
156
Number Of Sites
6
Number Of Participants
10

Sites

Site Name
Universitaetsmedizin Goettingen
Department Name
Klinik für Augenheilkunde
Contact Person Name
Sebastian Bemme
Site Name
University Hospital Cologne AöR
Department Name
Augenklinik
Contact Person Name
Tim Krohne
Contact Person Email
tim.krohne@uk-koeln.de
Site Name
Medical Center - University Of Freiburg
Department Name
Klinik für Augenheilkunde
Contact Person Name
Hansjürgen Agostini
Site Name
Universitaet Muenster
Department Name
Augenheilkunde
Contact Person Name
Nicole Eter
Site Name
Klinikum rechts der Isar der TU Muenchen AöR
Department Name
Augenklinik
Contact Person Name
Mathias Maier
Contact Person Email
mathias.maier@mri.tum.de
Site Name
Knappschaftsklinikum Saar GmbH
Department Name
Augenklinik Sulzbach
Contact Person Name
Boris Stanzel
Contact Person Email
boris.stanzel@kksaar.de

Italy

Earliest CTIS Part Ii Submission Date
01-12-2023
Latest Decision Or Authorization Date
01-08-2024
Processing Time Days
244
Number Of Sites
6
Number Of Participants
18

Sites

Site Name
Fondazione G.B.Bietti Per Lo Studio E La Ricerca In Oftalmologia
Department Name
UOC Oculistica Fondazione G.B.Bietti-IRCCS presso Ospedale Britannico
Contact Person Name
Mariacristina Parravano
Site Name
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Department Name
SSD Oftalmologia
Contact Person Name
Francesco Viola
Contact Person Email
francesco.viola@unimi.it
Site Name
Universita' Degli Studi G. D'annunzio Di Chieti
Department Name
UOC Riabilitazione Visiva Chirurgica
Contact Person Name
Rodolfo Mastropasqua
Contact Person Email
rodolfo.mastropasqua@unich.it
Site Name
Azienda Sanitaria Universitaria Friuli Centrale
Department Name
Oftalmologia
Contact Person Name
Paolo Lanzetta
Contact Person Email
paolo.lanzetta@uniud.it
Site Name
University Hospital Consorziale Policlinico
Department Name
UO Oftalmologia Universitaria
Contact Person Name
Francesco Boscia
Site Name
Azienda Ospedaliera Dei Colli
Department Name
Oftalmologia
Contact Person Name
Flavia Chiosi

Poland

Earliest CTIS Part Ii Submission Date
22-02-2024
Latest Decision Or Authorization Date
04-08-2024
Processing Time Days
164
Number Of Sites
11
Number Of Participants
19

Sites

Site Name
Pryzmat Sp. z o.o.
Department Name
not applicable
Contact Person Name
Karolina Żaczek-Zakrzewska
Contact Person Email
biuro@pryzmat-okulistyka.pl
Site Name
Gabinet Okulistyczny Prof Edward Wylegala
Department Name
not applicable
Contact Person Name
Adam Wylęgała
Contact Person Email
cmwylegala@gmail.com
Site Name
Lensclinic Sp. z o.o.
Department Name
not applicable
Contact Person Name
Katarzyna Michalska-Małecka
Contact Person Email
biuro@lensclinic.pl
Site Name
Lensclinic Sp. z o.o.
Department Name
not applicable
Contact Person Name
Katarzyna Michalska-Małecka
Contact Person Email
biuro@lensclinic.pl
Site Name
Gabinet Okulistyczny Jerzy Mackiewicz
Department Name
not applicable
Contact Person Name
Jerzy Mackiewicz
Site Name
Oftalmika Sp. z o.o.
Department Name
not applicable
Contact Person Name
Jakub Kałużny
Contact Person Email
magda.d.marzec@oftalmika.pl
Site Name
Pryzmat Sp. z o.o.
Department Name
not applicable
Contact Person Name
Karolina Żaczek-Zakrzewska
Contact Person Email
biuro@pryzmat-okulistyka.pl
Site Name
Centrum Diagnostyki I Mikrochirurgii Oka Lens Sp. z o.o.
Department Name
not applicable
Contact Person Name
Dominik Zalewski
Contact Person Email
badaniaklinicznelens@gmail.com
Site Name
Klinika Okulistyczna Jasne Blonia Sp. z o.o.
Department Name
not applicable
Contact Person Name
Zofia Nawrocka
Contact Person Email
jasneblonia@interia.pl
Site Name
Reoptis Sp. z o.o.
Department Name
not applicable
Contact Person Name
Andrzej Dmitriew
Contact Person Email
malwina.czekalska@reoptis.pl
Site Name
Centrum Medyczne Dietla 19 Sp. z o.o.
Department Name
not applicable
Contact Person Name
Piotr Oleksy
Contact Person Email
rejestracja@dietla19.pl

Spain

Earliest CTIS Part Ii Submission Date
01-12-2023
Latest Decision Or Authorization Date
09-02-2026
Processing Time Days
801
Number Of Sites
6
Number Of Participants
16

Sites

Site Name
Clinica Universidad De Navarra
Department Name
Ophtalmology
Contact Person Name
Alfredo García Layana
Contact Person Email
aglayana@unav.es
Site Name
Clinica De Oftalmologia De Cordoba S.L.
Department Name
Ophtalmology
Contact Person Name
Juan Manuel Cubero Parra
Contact Person Email
jmcubero@hospitalarruzafa.com
Site Name
Bellvitge University Hospital
Department Name
Ophtalmology
Contact Person Name
Luis Arias Barquet
Contact Person Email
luisariasbarquet@gmail.com
Site Name
Oftalmologia Vistahermosa S.L.
Department Name
Ophtalmology
Contact Person Name
Roberto Gallego Pinazo
Contact Person Email
robertogallegopinazo@gmail.com
Site Name
Complexo Hospitalario Universitario De Santiago
Department Name
Medical Retina and Ocular Diabetes Unit
Contact Person Name
Maximino Abraldes López-Veiga
Contact Person Email
maxiabraldes@gmail.com
Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Ophthalmology
Contact Person Name
José María Ruiz Moreno
Contact Person Email
josemaria.ruiz@uclm.es

Sponsor

Primary sponsor

Full Name
F. Hoffmann-La Roche AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
Drugdev Inc.
Responsibilities
Global CRO

Third parties

  • {"country":"United States","full_name":"Optymedge LLC","duties_or_roles":"Other Third Party Duty","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"1","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Technologies LLC","duties_or_roles":"6","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Other Third Party Duty","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Germany","full_name":"Steinbeis Forschungszentrum Grade Reading Center","duties_or_roles":"Other Third Party Duty","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services S.a.r.l.","duties_or_roles":"4","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Drugdev Inc.","duties_or_roles":"Global CRO","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
FARICIMAB
Active Substance
FARICIMAB
Modality
Bispecific antibody
Routes Of Administration
Intravitreal
Route
Intravitreal
Authorisation Status
Not authorised/Investigational (no marketing authorisation number provided)
Maximum Dose
0.5 mg (max daily as per product entry); max total amount listed 6 mg
Investigational Product Name
Lucentis 10 mg/ml solution for injection
Active Substance
RANIBIZUMAB
Modality
Monoclonal antibody
Routes Of Administration
Intravitreal
Route
Intravitreal
Authorisation Status
Marketing authorisation: EU/1/06/374/004
Maximum Dose
6 mg (max daily amount as listed in product entry)

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