Clinical trial • Phase I • Haematology
Clinical trial in Familial polycythemia (EPO gene mutation)
Phase I trial for Familial polycythemia (EPO gene mutation). open-label, none/not specified-controlled. 4 participants.
Overview
- Trial Therapeutic Area
- Haematology
- Trial Disease
- Familial polycythemia (EPO gene mutation)
- Trial Stage
- Phase I
Key dates
- Initial CTIS Submission Date
- 30-04-2025
- First CTIS Authorization Date
- 08-07-2025
Trial design
open-label, none/not specified-controlled Phase I trial across 2 sites in France.
- Open Label
- Yes
- Comparator
- None/Not specified
- Target Sample Size
- 4
Eligibility
Recruits 4 No vulnerable population selected; consent or assent handling not described..
- Vulnerable Population
- No vulnerable population selected; consent or assent handling not described.
Recruitment
- Planned Sample Size
- 4
- Recruitment Window Months
- 19
Geography
- Total Number Of Sites
- 2
- Total Number Of Participants
- 4
France
- Earliest CTIS Part Ii Submission Date
- 16-06-2025
- Latest Decision Or Authorization Date
- 08-07-2025
- Processing Time Days
- 22
- Number Of Sites
- 2
- Number Of Participants
- 4
Sites
- Site Name
- Centre Hospitalier de Macon
- Department Name
- Médecine Interne
- Principal Investigator Name
- Thibault MAILLET
- Principal Investigator Email
- thmaillet@ch-macon.fr
- Contact Person Name
- Thibault MAILLET
- Contact Person Email
- thmaillet@ch-macon.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Hématologie
- Principal Investigator Name
- Sabine BRECHIGNAC
- Principal Investigator Email
- Sabine.brechignac@aphp.fr
- Contact Person Name
- Sabine BRECHIGNAC
- Contact Person Email
- Sabine.brechignac@aphp.fr
Sponsor
Primary sponsor
- Full Name
- Centre Hospitalier Universitaire De Dijon
- Organisation Type
- Hospital/Clinic/Other health care facility
- Country Of Registered Address
- France
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