Clinical trial • Phase II • Haematology

GOLCADOMIDE for Follicular lymphoma (advanced stage)

Phase II trial of GOLCADOMIDE for Follicular lymphoma (advanced stage).

Overview

Trial Therapeutic Area
Haematology
Trial Disease
Follicular lymphoma (advanced stage)
Trial Stage
Phase II
Drug Modality
Small molecule|Monoclonal antibody|Peptide/protein/enzyme

Key dates

Initial CTIS Submission Date
31-05-2024
First CTIS Authorization Date
24-09-2024

Trial design

Randomised, open-label, comparator arms include: rituximab (iv; listed max daily dose 375 mg/m2 where provided) as comparator agent; chemotherapy comparators include bendamustine (iv; listed max daily dose 90 mg/m2), cyclophosphamide (iv; listed max daily dose 750 mg/m2), doxorubicin (iv; listed max daily dose 50 mg/m2), vincristine sulfate (iv; listed max daily dose 2 mg), and corticosteroids prednisone/prednisolone/betamethasone (oral/iv; listed max daily dose 100 mg). golcadomide is the investigational oral agent (test product) given in combination with rituximab in the experimental arm.-controlled Phase II trial in France, Germany, Italy and others.

Randomised
Yes
Open Label
Yes
Comparator
Comparator arms include: Rituximab (IV; listed max daily dose 375 mg/m2 where provided) as comparator agent; Chemotherapy comparators include Bendamustine (IV; listed max daily dose 90 mg/m2), Cyclophosphamide (IV; listed max daily dose 750 mg/m2), Doxorubicin (IV; listed max daily dose 50 mg/m2), Vincristine sulfate (IV; listed max daily dose 2 mg), and corticosteroids Prednisone/Prednisolone/Betamethasone (oral/IV; listed max daily dose 100 mg). Golcadomide is the investigational oral agent (test product) given in combination with rituximab in the experimental arm.
Single Multiple Or Escalation Dose Combined
Yes
Target Sample Size
113
Trial Duration For Participant
336

Eligibility

Recruits 113 No vulnerable populations selected (isVulnerablePopulationSelected: false). Participants are adults (>18); informed consent obtained from participants. No assent or special minor-consent procedures are mentioned..

Vulnerable Population
No vulnerable populations selected (isVulnerablePopulationSelected: false). Participants are adults (>18); informed consent obtained from participants. No assent or special minor-consent procedures are mentioned.

Inclusion criteria

  • {"criterion_text":"- Participants over the age of 18"}
  • {"criterion_text":"- Participants meeting all inclusion criteria regarding disease characteristics, laboratory values and reproductive capacity status would be considered eligible."}

Exclusion criteria

  • {"criterion_text":"- Medical conditions or physical and laboratory test results incompatible with participation in the trial, such as significant medical disease, active infection, laboratory abnormality, incapacitating psychiatric illness"}
  • {"criterion_text":"- Other lymphoma subtypes"}
  • {"criterion_text":"- Specific allergies or adverse reactions to certain types of medication"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- To evaluate if the patient´s condition improves using CMR. This means that at different times during the treatment, such as 6 months or 12 months after the start of treatment, the person's disease has completely responded to the treatment.","definition_or_measurement_approach":"CMR (Complete Metabolic Response) assessed at specified time points (examples given: 6 months and 12 months after start of treatment); defined as absence of detectable disease on clinical/metabolic tests as described in the main objective."}

Secondary endpoints

  • {"endpoint_text":"- To evaluate any negative side effects or adverse events (AE), which means an occurrence that has a negative impact on the health or well-being of a participant. This includes any new side effects that start after the treatment begins, which we call \"Treatment-Emergent Adverse Events\" (TEAEs).","definition_or_measurement_approach":"Collection and evaluation of adverse events (AEs) including Treatment-Emergent Adverse Events (TEAEs) during treatment."}
  • {"endpoint_text":"- To evaluate all AE, including TEAE and laboratory test as well as CMR data collected during the treatment of the Golcadomide and rituximab combination.","definition_or_measurement_approach":"Comprehensive safety assessment including AEs, TEAEs, laboratory tests and CMR data during Golcadomide+rituximab treatment."}
  • {"endpoint_text":"- To evaluate the overall response rate (ORR), the percentage of participants whose cancer shrinks or disappears.","definition_or_measurement_approach":"ORR measured as percentage of participants with tumour shrinkage or disappearance based on response assessments."}
  • {"endpoint_text":"- To evaluate PFS, the time from when we start the treatment until the disease gets worse or the patient passes away.","definition_or_measurement_approach":"Progression-Free Survival (PFS) measured as time from treatment start to disease progression or death."}
  • {"endpoint_text":"- To evaluate OS, which is the time from when we start the treatment until the patient passes away.","definition_or_measurement_approach":"Overall Survival (OS) measured as time from treatment start to death from any cause."}
  • {"endpoint_text":"- To evaluate all AE, including TEAE and laboratory test as well as CMR, ORR, PFS and OS data collected during the treatment of the rituximab and chemotherapy combination.","definition_or_measurement_approach":"Comprehensive evaluation of safety (AEs/TEAEs/labs) and efficacy endpoints (CMR, ORR, PFS, OS) for rituximab+chemotherapy arm."}

Recruitment

Planned Sample Size
113
Recruitment Window Months
49
Consent Approach
Informed consent obtained from adult participants (study includes participants >18). Country-specific subject information and informed consent forms are provided (documents available in French, German, Italian, Spanish, Polish). Pregnancy-specific information/ICFs and pregnancy prevention materials are included in the documentation; consent is participant-provided (no assent/minor consent procedures are described).

Geography

Total Number Of Sites
17
Total Number Of Participants
113

France

Earliest CTIS Part Ii Submission Date
06-09-2024
Latest Decision Or Authorization Date
14-08-2025
Processing Time Days
342
Number Of Sites
4
Number Of Participants
8

Sites

Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Hematology
Principal Investigator Name
Franck MORSCHHAUSER
Principal Investigator Email
franck.morchhauser@chru-lille.fr
Contact Person Name
Franck MORSCHHAUSER
Site Name
Institut Curie
Department Name
Hematology
Principal Investigator Name
Clementine SARKOZY
Principal Investigator Email
clementine.sarkozy@curie.fr
Contact Person Name
Clementine SARKOZY
Contact Person Email
clementine.sarkozy@curie.fr
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Haematology and Cell Therapy Department
Principal Investigator Name
Stephanie GUIDEZ
Principal Investigator Email
Stephanie.guidez@chu-poitiers.fr
Contact Person Name
Stephanie GUIDEZ
Site Name
Hopital Saint Louis
Department Name
Hematology
Principal Investigator Name
Catherine THIEBLEMONT
Principal Investigator Email
catherine.thieblemont@aphp.fr
Contact Person Name
Catherine THIEBLEMONT
Contact Person Email
catherine.thieblemont@aphp.fr

Germany

Earliest CTIS Part Ii Submission Date
23-08-2024
Latest Decision Or Authorization Date
13-08-2025
Processing Time Days
355
Number Of Sites
3
Number Of Participants
5

Sites

Site Name
Barmherzige Brueder gemeinnuetzige Krankenhaus GmbH
Department Name
Innere Medizin, Haematologie
Principal Investigator Name
Bernhard Heilmeier
Contact Person Name
Bernhard Heilmeier
Site Name
Gemeinschaftspraxis Haematologie Onkologie
Department Name
Haemato- Onkologie
Principal Investigator Name
Thomas Ilmer
Principal Investigator Email
buero@onkologie-dresden.net
Contact Person Name
Thomas Ilmer
Contact Person Email
buero@onkologie-dresden.net
Site Name
Klinikum Chemnitz gGmbH
Department Name
Klinik f. Innere Medizin III
Principal Investigator Name
Mathias Haenel
Principal Investigator Email
m.haenel@skc.de
Contact Person Name
Mathias Haenel
Contact Person Email
m.haenel@skc.de

Italy

Earliest CTIS Part Ii Submission Date
03-09-2024
Latest Decision Or Authorization Date
12-08-2025
Processing Time Days
343
Number Of Sites
4
Number Of Participants
6

Sites

Site Name
Humanitas Mirasole S.p.A.
Department Name
UO Oncologia medica e Ematologia
Principal Investigator Name
Armando Santoro
Principal Investigator Email
armando.santoro@cancercenter.humanitas.it
Contact Person Name
Armando Santoro
Site Name
Azienda Ospedaliera Policlinico Universitario Tor Vergata
Department Name
Ematologia e oncologia
Principal Investigator Name
Maria Christina Cox
Principal Investigator Email
mariacristina.cox@ptvonline.it
Contact Person Name
Maria Christina Cox
Contact Person Email
mariacristina.cox@ptvonline.it
Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
UOC Ematologia
Principal Investigator Name
Pier Luigi Zinzani
Principal Investigator Email
pierluigi.zinzani@unibo.it
Contact Person Name
Pier Luigi Zinzani
Contact Person Email
pierluigi.zinzani@unibo.it
Site Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale
Department Name
SC Ematologia Oncologia
Principal Investigator Name
Antonio Pinto
Principal Investigator Email
a.pinto@istitutotumori.a.it
Contact Person Name
Antonio Pinto
Contact Person Email
a.pinto@istitutotumori.a.it

Poland

Earliest CTIS Part Ii Submission Date
27-08-2024
Latest Decision Or Authorization Date
18-08-2025
Processing Time Days
356
Number Of Sites
3
Number Of Participants
10

Sites

Site Name
Lux Med Onkologia Sp. z o.o.
Department Name
Oddział Hematoonkologii
Principal Investigator Name
Joanna Barankiewicz
Principal Investigator Email
joanna.barankiewicz@luxmed.pl
Contact Person Name
Joanna Barankiewicz
Contact Person Email
joanna.barankiewicz@luxmed.pl
Site Name
Szpital Uniwersytecki Nr 2 Im Dr Jana Biziela W Bydgoszczy
Department Name
Klinika Hematologii
Principal Investigator Name
Jaroslaw Czyz
Principal Investigator Email
jczyz@onet.pl
Contact Person Name
Jaroslaw Czyz
Contact Person Email
jczyz@onet.pl
Site Name
Aidport Sp. z o.o.
Principal Investigator Name
Michal Kwiatek
Principal Investigator Email
michal.kwiatek@aidport.pl
Contact Person Name
Michal Kwiatek
Contact Person Email
michal.kwiatek@aidport.pl

Spain

Earliest CTIS Part Ii Submission Date
28-08-2024
Latest Decision Or Authorization Date
08-10-2025
Processing Time Days
406
Number Of Sites
3
Number Of Participants
8

Sites

Site Name
Hospital Universitario Fundacion Jimenez Diaz
Department Name
Hematology
Principal Investigator Name
Sergio Ramos
Principal Investigator Email
sergio.ramos@quironsalud.com
Contact Person Name
Sergio Ramos
Contact Person Email
sergio.ramos@quironsalud.com
Site Name
Hospital Universitario Dr Peset Aleixandre
Department Name
Hematology
Principal Investigator Name
Eva María Donato Martín
Principal Investigator Email
donato_eva@gva.es
Contact Person Name
Eva María Donato Martín
Contact Person Email
donato_eva@gva.es
Site Name
University Hospital Son Espases
Department Name
Hematology
Principal Investigator Name
Antonio Gutierrez Garcia
Principal Investigator Email
antoniom.gutierrez@ssib.es
Contact Person Name
Antonio Gutierrez Garcia
Contact Person Email
antoniom.gutierrez@ssib.es

Sponsor

Primary sponsor

Full Name
Celgene Corp.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Yprime LLC
Responsibilities
Subject number assignment, treatment arm assignment, drug supply assignment
Name
Accenture Solutions Private Limited
Responsibilities
Embarc operations
Name
Accenture Services Pvt. Ltd.
Responsibilities
Pharmacovigilance duties: Medical review and Cases Data Entry
Name
Signant Health Global LLC
Responsibilities
PRO/COA

Third parties

  • {"country":"Germany","full_name":"Azenta Germany GmbH","duties_or_roles":"Sample storage","organisation_type":"Pharmaceutical company"}
  • {"country":"India","full_name":"Syngene International Limited","duties_or_roles":"T-cell phenotyping","organisation_type":"Pharmaceutical company"}
  • {"country":"Singapore","full_name":"Labcorp Development (Asia) Pte Ltd","duties_or_roles":"Central Lab","organisation_type":"Pharmaceutical company"}
  • {"country":"Japan","full_name":"Labcorp Development Japan K.K.","duties_or_roles":"Central Lab, Sample mgmt, Kit building, Storage and distribution of samples to other vendors","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Yprime LLC","duties_or_roles":"Subject number assignment, treatment arm assignment, drug supply assignment","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"India","full_name":"Accenture Solutions Private Limited","duties_or_roles":"Embarc operations","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Signant Health Global LLC","duties_or_roles":"PRO/COA","organisation_type":"Pharmaceutical company"}
  • {"country":"India","full_name":"Accenture Services Pvt. Ltd.","duties_or_roles":"Pharmacovigilance duties: Medical review and Cases Data Entry","organisation_type":"SME"}
  • {"country":"Belgium","full_name":"Cerba Research","duties_or_roles":"Routine clinical pathology testing, Clinical chemistry, Clinical haematology, Clinical microbiology, Histopathology","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"Routine clinical pathology testing, Clinical chemistry, Clinical haematology, Clinical microbiology, Tumor blocks/slides storage, PGX spl, spl storage for vendors, IHC, Legacy LabCorp Central Lab","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"Routine clinical pathology testing, Clinical chemistry, Clinical haematology, Clinical microbiology, IHC Biomarker expression analysis (PD-L1), other APH","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Golcadomide
Active Substance
GOLCADOMIDE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Marketed (prodAuthStatus: 1)
Dose Levels
Two dose levels planned (described in objectives as "two doses level").
Maximum Dose
Max daily dose listed 0.4 mg; max total dose listed 67.2 mg
Combination Treatment
Yes

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