Clinical trial • Phase III • Haematology

DEXAMETHASONE for Multiple myeloma

Phase III trial of DEXAMETHASONE for Multiple myeloma.

Overview

Trial Therapeutic Area
Haematology
Trial Disease
Multiple myeloma
Trial Stage
Phase III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
01-05-2024
First CTIS Authorization Date
23-07-2024

Trial design

Randomised, open-label, standard of care chemotherapy (investigator pre-selected icaria schema: isatuximab + pomalidomide + dexamethasone or ikema schema: isatuximab + carfilzomib + dexamethasone) with continuous dexamethasone until progression ("dexamethasone arm", arm a) versus the same soc chemotherapy with dexamethasone discontinued from the 3rd cycle (after 8 weeks) ("dexamethasone-free arm", arm b). doses and schedules not specified in the provided text.-controlled Phase III trial across 46 sites in France.

Randomised
Yes
Open Label
Yes
Comparator
Standard of care chemotherapy (investigator pre-selected ICARIA schema: isatuximab + pomalidomide + dexamethasone OR IKEMA schema: isatuximab + carfilzomib + dexamethasone) with continuous dexamethasone until progression ("dexamethasone arm", arm A) versus the same SOC chemotherapy with dexamethasone discontinued from the 3rd cycle (after 8 weeks) ("dexamethasone-free arm", arm B). Doses and schedules not specified in the provided text.
Target Sample Size
334
Trial Duration For Participant
730

Stratification factors

  • Choice of treatment schema (ICARIA vs IKEMA) performed before randomisation for stratification

Eligibility

Recruits 334 No vulnerable populations selected. Trial enrols adult patients (≥18 years). Participants must provide signed informed consent (see ICF documents). Inability to give written informed consent is an exclusion criterion. No assent/child consent procedures are described..

Pregnancy Exclusion
Pregnancy or absence of effective contraceptive method for women of childbearing potential
Vulnerable Population
No vulnerable populations selected. Trial enrols adult patients (≥18 years). Participants must provide signed informed consent (see ICF documents). Inability to give written informed consent is an exclusion criterion. No assent/child consent procedures are described.

Inclusion criteria

  • {"criterion_text":"- Adult patients (≥18 years old)\n- Documented MM in relapse according to standard criteria.\n- All patients must have received between 1 to 3 prior therapies for MM (a prior therapy is defined as 2 or more cycles of therapy given as a MM treatment plan\n- Eligible for one of the following antibody-based approved combinations (see 2.6 for details on EMEA authorization): (1) ICARIA schema: isatuximab, pomalidomide and dexamethasone. (2) IKEMA schema: isatuximab, carfilzomib and dexamethasone\n- Subject must have achieved a response (PR or better) to the prior regimen.\n- ECOG Performance Status score of 0, 1, or 2.\n- For subjects experiencing toxicities resulting from previous therapy (including peripheral neuropathy), the toxicities must have been resolved or stabilized.\n- Signed informed consent"}

Exclusion criteria

  • {"criterion_text":"- Contraindications to investigational medicinal products or auxiliary medicinal product\n- Evidence of refractoriness or intolerance to anti-CD38 monoclonal antibodies or if the patient received an anti-CD38 within the last 6 months.\n- Previous treatment according to the ICARIA schema with pomalidomide orIKEMA schema with carfilzomib\n- Allogenic hematopoietic cell transplant (HCT, regardless of timing).\n- Planned to undergo an HCT prior to progression of disease ie, these patients should not be enrolled in order to reduce disease burden prior to transplant.\n- History of malignancy (other than MM) within 3 years before the date of randomization (exceptions are squamous and basal cell carcinomas of the skin, carcinoma in situ of the cervix, or malignancy that in the opinion of the Investigator is considered cured with minimal risk of recurrence within 3 years).\n- Known MM meningeal Involvement.\n- Plasma cell leukemia (>2.0 × 109/L circulating plasma cells by standard differential) or Waldenström’s macroglobulinemia or POEMS syndrome (polyneuropathy, organomegaly, endocrinopathy, monoclonal protein, and skin changes) or amyloidosis.\n- Any concurrent medical condition or disease (e.g., active systemic infection) that is likely to interfere with study procedures or results, or that, in the opinion, of the Investigator would constitute a hazard by participating in this study.\n- Uncontrolled chronic obstructive pulmonary disease (COPD)\n- Clinically significant cardiac disease.\n- Seropositive for hepatitis B with positive PCR\n- Seropositive for human immunodeficiency virus (HIV) or hepatitis C.\n- Creatinine clearance ≤30 mL/min\n- Pregnancy or absence of effective contraceptive method for women of childbearing potential\n- Lactation\n- Participation to another interventional clinical trial except with the agreement of the coordinating investigator.\n- Inability to give written informed consent"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- the ORR after six cycles of salvage therapy, defined as the proportion of subjects who achieve complete response (CR) or partial response (PR) according to the IMWG criteria, following salvage therapy.","definition_or_measurement_approach":"Overall response rate (ORR) after six cycles of salvage therapy measured as the proportion of subjects achieving CR or PR according to the International Myeloma Working Group (IMWG) criteria."}

Secondary endpoints

  • {"endpoint_text":"- Best ORR, defined as the proportion of subjects who achieve CR or PR according to the IMWG criteria, at any time point following salvage therapy.\n- Time to progression (TTP)\n- Progression-free survival (PFS) defined as the duration from the date of randomization to either progressive disease, according to the IMWG criteria, or death, at 2 years after randomization.\n- OS defined as the duration from the date of randomization to death, at 2 years after randomization.\n- Incidence of adverse events (AE) within the 2 years after randomization.\n- Quality of Life (QoL) within the 2 years after randomization.","definition_or_measurement_approach":"Best ORR: proportion achieving CR or PR by IMWG criteria at any time post-salvage; TTP: time from randomization to progression; PFS: time from randomization to progression per IMWG or death (assessed at 2 years); OS: time from randomization to death (assessed at 2 years); Incidence of AEs: collected within 2 years after randomization; QoL: assessed within 2 years after randomization (specific instruments not described here)."}

Recruitment

Planned Sample Size
334
Recruitment Window Months
46
Consent Approach
Adult participants must provide signed written informed consent. Subject Information Sheet and Informed Consent Form documents (L1_SIS and L1_SIS-ICF adult/majeur) are listed for publication. Inability to give written informed consent is an exclusion criterion. No specific languages or assent procedures are described in the available data.

Geography

Total Number Of Sites
46
Total Number Of Participants
334

France

Earliest CTIS Part Ii Submission Date
12-06-2024
Latest Decision Or Authorization Date
17-11-2025
Processing Time Days
523
Number Of Sites
46
Number Of Participants
334

Sites

Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
HEMATOLOGIE CLINIQUE
Principal Investigator Name
VINCENT Laure
Principal Investigator Email
l-vincent@chu-montpellier.fr
Contact Person Name
VINCENT Laure
Contact Person Email
l-vincent@chu-montpellier.fr
Site Name
Chorale Du Centre Hospitalier De Lens
Department Name
Service Hématologie
Principal Investigator Name
Daniela ROBU
Principal Investigator Email
drobu@ch-lens.fr
Contact Person Name
Daniela ROBU
Contact Person Email
drobu@ch-lens.fr
Site Name
Centre Hospitalier Du Pays D Aix Centre Hospitalier Intercommunal Aix-Pertuis
Department Name
ONCO HEMATOLOGIE MEDECINE INTERNE
Principal Investigator Name
CHAIB Abdelaziz
Principal Investigator Email
achaib@ch-aix.fr
Contact Person Name
CHAIB Abdelaziz
Contact Person Email
achaib@ch-aix.fr
Site Name
Groupe Hospitalier Du Havre
Department Name
Service Hématologie
Principal Investigator Name
Pierre LEBRETON
Principal Investigator Email
pierre.lebreton@ch-havre.fr
Contact Person Name
Pierre LEBRETON
Contact Person Email
pierre.lebreton@ch-havre.fr
Site Name
Centre Hospitalier Universitaire Grenoble Alpes
Department Name
HEMATOLOGIE
Principal Investigator Name
MARIETTE Clara
Principal Investigator Email
CMariette@chu-grenoble.fr
Contact Person Name
MARIETTE Clara
Contact Person Email
CMariette@chu-grenoble.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Service des maladies du sang
Principal Investigator Name
MANIER Salomon
Principal Investigator Email
Salomon.manier@chu-lille.fr
Contact Person Name
MANIER Salomon
Contact Person Email
Salomon.manier@chu-lille.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Service Hématologie clinique
Principal Investigator Name
TOUZEAU Cyrille
Principal Investigator Email
cyrille.touzeau@chu-nantes.fr
Contact Person Name
TOUZEAU Cyrille
Contact Person Email
cyrille.touzeau@chu-nantes.fr
Site Name
Centre Hospitalier Departemental Vendee
Department Name
HEMATOLOGIE
Principal Investigator Name
AGBETSIVI Komivi 02 51 44 61 73
Principal Investigator Email
komivi.agbetsivi@ght85.fr
Contact Person Name
AGBETSIVI Komivi 02 51 44 61 73
Contact Person Email
komivi.agbetsivi@ght85.fr
Site Name
Assistance Publique Hopitaux De Paris (Creteil Cedex)
Department Name
HEMATOLOGIE
Principal Investigator Name
BELHADJ KARIM
Principal Investigator Email
karim.belhadj@hmn.aphp.fr
Contact Person Name
BELHADJ KARIM
Contact Person Email
karim.belhadj@hmn.aphp.fr
Site Name
Centre Hospitalier Groupe Hospitalier De La Rochelle Re Aunis
Department Name
hematologie
Principal Investigator Name
ROUL Christophe
Principal Investigator Email
christophe.roul@ght-atlantique17.fr
Contact Person Name
ROUL Christophe
Site Name
Institut De Cancerologie De Bourgogne
Department Name
Service Hématologie
Principal Investigator Name
Lafon Ingrid
Principal Investigator Email
ilafon@icb-cancer.fr
Contact Person Name
Lafon Ingrid
Contact Person Email
ilafon@icb-cancer.fr
Site Name
Centre Hospitalier Universitaire Reims
Department Name
Service Hématologie clinique
Principal Investigator Name
GODET Sophie
Principal Investigator Email
sophie.godet@chu-reims.fr
Contact Person Name
GODET Sophie
Contact Person Email
sophie.godet@chu-reims.fr
Site Name
Centre Hospitalier William Morey
Department Name
HEMATOLOGIE ONCOLOGIE
Principal Investigator Name
KENNEL Céline
Principal Investigator Email
celine.kennel@ch-chalon71.fr
Contact Person Name
KENNEL Céline
Contact Person Email
celine.kennel@ch-chalon71.fr
Site Name
Centre Hospitalier De Versailles
Department Name
Service Hématologie
Principal Investigator Name
RIGAUDEAU Sophie
Principal Investigator Email
srigaudeau@ght78sud.fr
Contact Person Name
RIGAUDEAU Sophie
Contact Person Email
srigaudeau@ght78sud.fr
Site Name
Institut Bergonie
Department Name
Service Hématologie
Principal Investigator Name
SCHMITT Anna
Principal Investigator Email
a.schmitt@bordeaux.unicancer.fr
Contact Person Name
SCHMITT Anna
Site Name
Centre Hospitalier Metropole Savoie
Department Name
Service Hématologie
Principal Investigator Name
DONY Arthur
Principal Investigator Email
arthur.dony@ch-metropole-savoie.fr
Contact Person Name
DONY Arthur
Site Name
Assistance Publique Hopitaux De Paris (Paris Cedex 15)
Department Name
Service Hématologie adultes
Principal Investigator Name
Frenzel Laurent
Principal Investigator Email
laurent.frenzel@aphp.fr
Contact Person Name
Frenzel Laurent
Contact Person Email
laurent.frenzel@aphp.fr
Site Name
University Hospital Of Clermont-Ferrand
Department Name
Service de thérapie cellulaire et d’hématologie clinique
Principal Investigator Name
Carolyne CROIZIER
Principal Investigator Email
ccroizier@chu-clermontferrand.fr
Contact Person Name
Carolyne CROIZIER
Site Name
Groupement Des Hopitaux De L'Institut Catholique De Lille
Department Name
HEMATOLOGIE
Principal Investigator Name
BOURGEOIS-PETIT Emmanuelle
Principal Investigator Email
bourgeois.emmanuelle@ghicl.net
Contact Person Name
BOURGEOIS-PETIT Emmanuelle
Contact Person Email
bourgeois.emmanuelle@ghicl.net
Site Name
Assistance Publique Hopitaux De Paris (Bobigny Cedex)
Department Name
Service Hématologie
Principal Investigator Name
BRAUN Thorsten
Principal Investigator Email
Thorsten.braun@aphp.fr
Contact Person Name
BRAUN Thorsten
Contact Person Email
Thorsten.braun@aphp.fr
Site Name
Centre Hospitalier De Perigueux
Department Name
hematologie
Principal Investigator Name
CLAMETTES Claire
Principal Investigator Email
claire.clamettes@ch-perigueux.fr
Contact Person Name
CLAMETTES Claire
Site Name
Direction Centrale Du Service De Sante Des Armees
Department Name
HEMATOLOGIE
Principal Investigator Name
MAILLOT Jean
Principal Investigator Email
jean.maillot@intradef.gouv.fr
Contact Person Name
MAILLOT Jean
Contact Person Email
jean.maillot@intradef.gouv.fr
Site Name
Groupe Hospitalier Bretagne Sud
Department Name
Service Médecine Hématologie – VIH
Principal Investigator Name
Claire BREAL
Principal Investigator Email
c.breal@ghbs.bzh
Contact Person Name
Claire BREAL
Contact Person Email
c.breal@ghbs.bzh
Site Name
Centre Hospitalier Universitaire De Saint Etienne
Department Name
HEMATOLOGIE
Principal Investigator Name
SAPET Manon
Principal Investigator Email
manon.sapet@chu-st-etienne.fr
Contact Person Name
SAPET Manon
Contact Person Email
manon.sapet@chu-st-etienne.fr
Site Name
L'Hopital Prive Du Confluent
Department Name
HEMATOLOGIE
Principal Investigator Name
DELAUNAY Jacques
Principal Investigator Email
jacques.delaunay@groupeconfluent.fr
Contact Person Name
DELAUNAY Jacques
Site Name
Centre Hospitalier Annecy Genevois
Department Name
HEMATOLOGIE
Principal Investigator Name
ORSINI-PIOCELLE Dr Frédérique
Principal Investigator Email
forsinipiocelle@ch-annecygenevois.fr
Contact Person Name
ORSINI-PIOCELLE Dr Frédérique
Site Name
Hopital Saint Louis
Department Name
Immuno-Hématologie
Principal Investigator Name
HAREL Stéphanie
Principal Investigator Email
stephanie.harel@aphp.fr
Contact Person Name
HAREL Stéphanie
Contact Person Email
stephanie.harel@aphp.fr
Site Name
Centre Hospitalier D Avignon
Department Name
ONCO HEMATOLOGIE
Principal Investigator Name
CHEBREK Safia
Principal Investigator Email
chebrek.safia@ch-avignon.fr
Contact Person Name
CHEBREK Safia
Contact Person Email
chebrek.safia@ch-avignon.fr
Site Name
Centre Hospitalier Universitaire De Caen Normandie
Department Name
Service Hématologie
Principal Investigator Name
MACRO Margaret
Principal Investigator Email
macro-m@chu-caen.fr
Contact Person Name
MACRO Margaret
Contact Person Email
macro-m@chu-caen.fr
Site Name
L’Hopital Alexandra Lepeve
Department Name
Service Hématologie
Principal Investigator Name
Hélène Demarquette
Principal Investigator Email
helene.demarquette@ch-dunkerque.fr
Contact Person Name
Hélène Demarquette
Site Name
Centre Hospital Region Metz Thionville
Department Name
Hematologie
Principal Investigator Name
DORVAUX Véronique
Principal Investigator Email
v.dorvaux@chr-metz-thionville.fr
Contact Person Name
DORVAUX Véronique
Site Name
Centre Hospitalier De Troyes
Department Name
Service Hématologie
Principal Investigator Name
Alberto Santagostino
Principal Investigator Email
alberto.santagostino@hcs-sante.fr
Contact Person Name
Alberto Santagostino
Site Name
Les Hopitaux De Chartres
Department Name
ONCOLOGIE HEMATOLOGIE
Principal Investigator Name
DE LABARTHE Adrienne
Principal Investigator Email
adelabarthe@ch-chartres.fr
Contact Person Name
DE LABARTHE Adrienne
Contact Person Email
adelabarthe@ch-chartres.fr
Site Name
CH Argenteuil
Department Name
Service Hématologie
Principal Investigator Name
CHAOUI Driss
Principal Investigator Email
driss.chaoui@ch-argenteuil.fr
Contact Person Name
CHAOUI Driss
Contact Person Email
driss.chaoui@ch-argenteuil.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Service Hématologie et thérapie cellulaire
Principal Investigator Name
CHALOPIN Thomas
Principal Investigator Email
t.chalopin@chu-tours.fr
Contact Person Name
CHALOPIN Thomas
Contact Person Email
t.chalopin@chu-tours.fr
Site Name
Centre Henri Becquerel
Department Name
HEMATOLOGIE
Principal Investigator Name
LENAIN Pascal
Principal Investigator Email
pascal.lenain@chb.unicancer.fr
Contact Person Name
LENAIN Pascal
Contact Person Email
pascal.lenain@chb.unicancer.fr
Site Name
Clinique Du Parc
Department Name
Service Hématologie
Principal Investigator Name
Alexandre PAYSSOT
Principal Investigator Email
alexandre.payssot.hematoparc@outlook.fr
Contact Person Name
Alexandre PAYSSOT
Site Name
Centre Hospitalier Blois Simone Veil
Department Name
Service Oncologie-Hématologie
Principal Investigator Name
EL YAMANI Abderrazak
Principal Investigator Email
elyamaa@ch-blois.fr
Contact Person Name
EL YAMANI Abderrazak
Contact Person Email
elyamaa@ch-blois.fr
Site Name
Centre Hospitalier D'Abbeville
Department Name
Service Médecine Interne
Principal Investigator Name
LEDUC Isabelle
Principal Investigator Email
leduc.isabelle@ch-abbeville.fr
Contact Person Name
LEDUC Isabelle
Contact Person Email
leduc.isabelle@ch-abbeville.fr
Site Name
Centre Hospitalier Bretagne Atlantique
Department Name
HEMATOLOGIE
Principal Investigator Name
CHEREL Brieuc
Principal Investigator Email
Brieuc.cherel@ch-bretagne-atlantique.fr
Contact Person Name
CHEREL Brieuc
Site Name
Centre Hospitalier De Saint-Quentin
Department Name
HEMATOLOGIE
Principal Investigator Name
GARIDI Reda
Principal Investigator Email
R.GARIDI@ch-stquentin.fr
Contact Person Name
GARIDI Reda
Contact Person Email
R.GARIDI@ch-stquentin.fr
Site Name
Hopital Saint Antoine
Department Name
hematologie
Principal Investigator Name
MALARD Florent
Principal Investigator Email
florent.malard@aphp.fr
Contact Person Name
MALARD Florent
Contact Person Email
florent.malard@aphp.fr
Site Name
CHRU De Nancy
Department Name
Service Hématologie
Principal Investigator Name
JACQUET Caroline
Principal Investigator Email
c.jacquet@chru-nancy.fr
Contact Person Name
JACQUET Caroline
Contact Person Email
c.jacquet@chru-nancy.fr
Site Name
Hopital Prive Sevigne
Department Name
HEMATOLOGIE
Principal Investigator Name
BAREAU Benoît
Principal Investigator Email
benoit.bareau@gmail.com
Contact Person Name
BAREAU Benoît
Contact Person Email
benoit.bareau@gmail.com
Site Name
Centre Hospitalier De Niort
Department Name
HEMATOLOGIE
Principal Investigator Name
OLIVIER Gaelle
Principal Investigator Email
Gaelle.OLIVIER@ch-niort.fr
Contact Person Name
OLIVIER Gaelle
Contact Person Email
Gaelle.OLIVIER@ch-niort.fr
Site Name
Centre Hospitalier Intercommunal Compiegne Noyon
Department Name
Service Hématologie
Principal Investigator Name
AGBETIAFA Kossi Claude
Principal Investigator Email
k.agbetiafa@ch-compiegnenoyon.fr
Contact Person Name
AGBETIAFA Kossi Claude

Sponsor

Primary sponsor

Full Name
Assistance Publique Hopitaux De Paris
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
France

Investigational products

Investigational Product Name
DEXAMETHASONE (TABLET)
Active Substance
DEXAMETHASONE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
40 mg (max daily dose)
Investigational Product Name
DEXAMETHASONE (SOLUTION FOR INJECTION)
Active Substance
DEXAMETHASONE
Modality
Small molecule
Routes Of Administration
INTRAMUSCULAR AND INTRAVENOUS
Route
INTRAMUSCULAR AND INTRAVENOUS
Maximum Dose
40 mg (max daily dose)
Investigational Product Name
DEXAMETHASONE (ORAL SOLUTION)
Active Substance
DEXAMETHASONE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
40 mg (max daily dose)
Combination Treatment
Yes

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