Clinical trial • Phase II • Infectious Disease

CEF A ZOLIN for Acute osteomyelitis

Phase II trial of CEF A ZOLIN for Acute osteomyelitis.

Overview

Trial Therapeutic Area
Infectious Disease
Trial Disease
Acute osteomyelitis
Trial Stage
Phase II
Drug Modality
Small molecule
Paediatric Trial
Yes

Key dates

Initial CTIS Submission Date
15-10-2024
First CTIS Authorization Date
15-11-2024

Trial design

Randomised, open-label, standard strategy with conventional hospitalization and intravenous antibiotic therapy (hospitalization + iv antibiotics) — comparator described as hospitalization with iv antibiotic therapy; specific drug choice/dose/schedule not specified in the available data.-controlled Phase II trial across 34 sites in France.

Randomised
Yes
Open Label
Yes
Comparator
Standard strategy with conventional hospitalization and intravenous antibiotic therapy (hospitalization + IV antibiotics) — comparator described as hospitalization with IV antibiotic therapy; specific drug choice/dose/schedule not specified in the available data.
Target Sample Size
320
Trial Duration For Participant
180

Eligibility

Recruits 320 paediatric patients.

Vulnerable Population
Children aged 1–4 years are included; isVulnerablePopulationSelected = true. Specific consent/assent procedures are not detailed in the provided data; a Subject Information and Informed Consent Form document is listed (L1_SIS and ICF-AP) but its contents (who provides consent, assent requirements, languages) are not provided.

Inclusion criteria

  • {"criterion_text":"- Children ≥ 1 year old and ≤4 years old;"}
  • {"criterion_text":"- First episode of acute osteomyelitis suspected on clinical grounds (acute functional impotence (<15 days) most often associated with fever) and confirmed in the first days of treatment by bone scintigraphy or MRI"}
  • {"criterion_text":"- Absence of sepsis (absence of hemodynamic disorders, respiratory disorders, impaired consciousness)"}
  • {"criterion_text":"- And absence of subperiosteal abscess or associated arthritis or deep vein thrombosis"}
  • {"criterion_text":"- And absence of scarlatiniform rash"}
  • {"criterion_text":"- And CRP < 50 mg/ml"}
  • {"criterion_text":"- And normal initial bone x-ray (or thickening of soft parts)."}

Exclusion criteria

  • {"criterion_text":"- Infections ostéo-articulaires multifocales"}
  • {"criterion_text":"- Sickle cell patients, immunosuppressed"}
  • {"criterion_text":"- Antibiotic treatment in progress or within 48 hours before the emergency room consultation"}
  • {"criterion_text":"- Severe allergy to beta-lactamines"}
  • {"criterion_text":"- Digestive disorders"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Complete recovery without relapse at 6 months defined by the absence of clinical signs of osteomyelitis at 6 months AND the absence of secondary septic complications (septic arthritis, perioste abscess) before the end of antibiotic therapy AND the absence of relapse or rehospitalization for osteomyelitis in relation to the initial infection.","definition_or_measurement_approach":"Defined as absence of clinical signs of osteomyelitis at 6 months, absence of secondary septic complications (septic arthritis, periosteal abscess) before end of antibiotic therapy, and absence of relapse or rehospitalization for osteomyelitis related to the initial infection."}

Recruitment

Planned Sample Size
320
Recruitment Window Months
54
Consent Approach
Not specified in the available data. A Subject Information and Informed Consent Form document is listed (L1_SIS and ICF-AP), but the content (who provides consent, age-specific documents, languages, assent) is not provided. Given the population (children 1–4 years) consent would be expected from parent/legal guardian, but this is not explicitly detailed in the provided record.

Geography

Total Number Of Sites
34
Total Number Of Participants
320

France

Earliest CTIS Part Ii Submission Date
07-11-2024
Latest Decision Or Authorization Date
09-04-2025
Processing Time Days
153
Number Of Sites
34
Number Of Participants
320

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Pédiatrie
Principal Investigator Name
Romain BASMACI
Principal Investigator Email
romain.basmaci@aphp.fr
Contact Person Name
Romain BASMACI
Contact Person Email
romain.basmaci@aphp.fr
Site Name
Hopital NOVO
Department Name
Pédiatrie
Principal Investigator Name
Jean-Louis Ceolin
Principal Investigator Email
jean-louis.ceolin@ght-novo.fr
Contact Person Name
Jean-Louis Ceolin
Contact Person Email
jean-louis.ceolin@ght-novo.fr
Site Name
Grand Hopital De L Est Francilien
Department Name
Pédiatrie
Principal Investigator Name
Placide AGBO
Principal Investigator Email
kagbokpati@ghef.fr
Contact Person Name
Placide AGBO
Contact Person Email
kagbokpati@ghef.fr
Site Name
Centre Hospitalier De Versailles
Department Name
Pédiatrie
Principal Investigator Name
Véronique HENTGEN
Principal Investigator Email
vhentgen@ch-versailles.fr
Contact Person Name
Véronique HENTGEN
Contact Person Email
vhentgen@ch-versailles.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Orthopédie
Principal Investigator Name
Faustine MONGET
Principal Investigator Email
faustine.mon@gmail.com
Contact Person Name
Faustine MONGET
Contact Person Email
faustine.mon@gmail.com
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Orthopédie
Principal Investigator Name
Franck FITOUSSI
Principal Investigator Email
franck.fitoussi@aphp.fr
Contact Person Name
Franck FITOUSSI
Contact Person Email
franck.fitoussi@aphp.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Pédiatrie
Principal Investigator Name
François DUBOS
Principal Investigator Email
francois.dubos@chru-lille.fr
Contact Person Name
François DUBOS
Contact Person Email
francois.dubos@chru-lille.fr
Site Name
Centre Hospitalier Intercommunal Creteil
Department Name
Pédiatrie
Principal Investigator Name
Sandra BISCARDI
Principal Investigator Email
sandra.biscardi@chicreteil.fr
Contact Person Name
Sandra BISCARDI
Contact Person Email
sandra.biscardi@chicreteil.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Orthopédie
Principal Investigator Name
Jean-Charles Auregan
Principal Investigator Email
jean-charles.auregan@aphp.fr
Contact Person Name
Jean-Charles Auregan
Contact Person Email
jean-charles.auregan@aphp.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Orthopédie
Principal Investigator Name
Thierry Odent
Principal Investigator Email
L.AGOSTINI@chu-tours.fr
Contact Person Name
Thierry Odent
Contact Person Email
L.AGOSTINI@chu-tours.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Orthopédie
Principal Investigator Name
Antoine CHALOPIN
Principal Investigator Email
Antoine.CHALOPIN@chu-nantes.fr
Contact Person Name
Antoine CHALOPIN
Contact Person Email
Antoine.CHALOPIN@chu-nantes.fr
Site Name
Centre Hospitalier Intercommunal Creteil
Department Name
Orthopédie
Principal Investigator Name
Jamil Amhis
Principal Investigator Email
Jamil.Amhis@chicreteil.fr
Contact Person Name
Jamil Amhis
Contact Person Email
Jamil.Amhis@chicreteil.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Pédiatrie
Principal Investigator Name
Vincent GAJDOS
Principal Investigator Email
vincent.gajdos@aphp.fr
Contact Person Name
Vincent GAJDOS
Contact Person Email
vincent.gajdos@aphp.fr
Site Name
Fondation Lenval Nice
Department Name
Orthopédie
Principal Investigator Name
Virginie RAMPAL
Contact Person Name
Virginie RAMPAL
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Pédiatrie
Principal Investigator Name
Mathie LORROT
Principal Investigator Email
mathie.lorrot@aphp.fr
Contact Person Name
Mathie LORROT
Contact Person Email
mathie.lorrot@aphp.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Pédiatrie
Principal Investigator Name
Camille BREHIN
Principal Investigator Email
brehin.c@chu-toulouse.fr
Contact Person Name
Camille BREHIN
Contact Person Email
brehin.c@chu-toulouse.fr
Site Name
Grand Hopital De L Est Francilien
Department Name
Pédiatrie
Principal Investigator Name
Caroline MASSEROT
Principal Investigator Email
cmasserot@ghef.fr
Contact Person Name
Caroline MASSEROT
Contact Person Email
cmasserot@ghef.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Urgences
Principal Investigator Name
Laetitia Agostini
Principal Investigator Email
L.AGOSTINI@chu-tours.fr
Contact Person Name
Laetitia Agostini
Contact Person Email
L.AGOSTINI@chu-tours.fr
Site Name
Fondation Lenval Nice
Department Name
Pédiatrie
Principal Investigator Name
Hervé HAAS
Principal Investigator Email
herve.haas@free.fr
Contact Person Name
Hervé HAAS
Contact Person Email
herve.haas@free.fr
Site Name
Hospices Civils De Lyon
Department Name
Orthopédie
Principal Investigator Name
Antoine JOSSE
Principal Investigator Email
antoine.josse@chu-lyon.fr
Contact Person Name
Antoine JOSSE
Contact Person Email
antoine.josse@chu-lyon.fr
Site Name
Hospices Civils De Lyon
Department Name
Pédiatrie
Principal Investigator Name
Yves GILLET
Principal Investigator Email
yves.gillet@chu-lyon.fr
Contact Person Name
Yves GILLET
Contact Person Email
yves.gillet@chu-lyon.fr
Site Name
Centre Hospitalier Sud Francilien
Department Name
Rhumatologie Pédiatrique
Principal Investigator Name
Glory DINGULU
Principal Investigator Email
glory.dingulu@chsf.fr
Contact Person Name
Glory DINGULU
Contact Person Email
glory.dingulu@chsf.fr
Site Name
Centre Hospitalier Universitaire De Saint Etienne
Department Name
Urgences
Principal Investigator Name
Aymeric Cantais
Principal Investigator Email
Aymeric.Cantais@chu-st-etienne.fr
Contact Person Name
Aymeric Cantais
Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Urgences
Principal Investigator Name
Marion FAVIER
Principal Investigator Email
marion.favier@chu-bordeaux.fr
Contact Person Name
Marion FAVIER
Contact Person Email
marion.favier@chu-bordeaux.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Rhumatologie Pédiatrique
Principal Investigator Name
Caroline GALEOTTI
Principal Investigator Email
caroline.galeotti@aphp.fr
Contact Person Name
Caroline GALEOTTI
Contact Person Email
caroline.galeotti@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Pédiatrie
Principal Investigator Name
Melusine Kiener
Principal Investigator Email
melusine.kiener@aphp.fr
Contact Person Name
Melusine Kiener
Contact Person Email
melusine.kiener@aphp.fr
Site Name
Centre Hospitalier Universitaire De Saint Etienne
Department Name
Orthopédie
Principal Investigator Name
Elie HADDAD
Principal Investigator Email
Elie.HADDAD@chu-st-etienne.fr
Contact Person Name
Elie HADDAD
Contact Person Email
Elie.Haddad@chu-st-etienne.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Pédiatrie
Principal Investigator Name
Grégoire BENOIST
Principal Investigator Email
gregoire.benoist@aphp.fr
Contact Person Name
Grégoire BENOIST
Contact Person Email
gregoire.benoist@aphp.fr
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Pédiatrie
Principal Investigator Name
Eric JEZIORSKI
Principal Investigator Email
e-jeziorski@chu-montpellier.fr
Contact Person Name
Eric JEZIORSKI
Contact Person Email
e-jeziorski@chu-montpellier.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Pédiatrie
Principal Investigator Name
Elise LAUNAY
Principal Investigator Email
elise.launay@chu-nantes.fr
Contact Person Name
Elise LAUNAY
Contact Person Email
elise.launay@chu-nantes.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Pédiatrie
Principal Investigator Name
Zoha Maakaroun Vermesse
Principal Investigator Email
Z.MAAKAROUN-VERMESSE@chu-tours.fr
Contact Person Name
Zoha Maakaroun Vermesse
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Orthopédie
Principal Investigator Name
Jérôme COTTALORDA
Principal Investigator Email
j-cottalorda@chu-montpellier.fr
Contact Person Name
Jérôme COTTALORDA
Site Name
Centre Hospitalier Sud Essonne-Dourdan-Etampes
Department Name
Pédiatrie
Principal Investigator Name
Cédric TAHIRI
Principal Investigator Email
ctahiri@ch-sudessonne.fr
Contact Person Name
Cédric TAHIRI
Contact Person Email
ctahiri@ch-sudessonne.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Pédiatrie
Principal Investigator Name
Elsa Foucaud
Principal Investigator Email
elsa.foucaud@aphp.fr
Contact Person Name
Elsa Foucaud
Contact Person Email
elsa.foucaud@aphp.fr

Sponsor

Primary sponsor

Full Name
Assistance Publique Hopitaux De Paris
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
France

Investigational products

Investigational Product Name
CEFAZOLIN
Active Substance
CEF A ZOLIN
Modality
Small molecule
Routes Of Administration
INJECTION
Route
INJECTION
Maximum Dose
150 mg/kg
Investigational Product Name
CLOXACILLIN
Active Substance
CLOXACILLIN
Modality
Small molecule
Routes Of Administration
INJECTION
Route
INJECTION
Maximum Dose
150 mg/kg
Investigational Product Name
CLAVULANIC ACID
Active Substance
CLAVULANIC ACID
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
10 mg/kg
Investigational Product Name
AMOXICILLIN (oral suspension)
Active Substance
AMOXICILLIN
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
80 mg/kg
Investigational Product Name
AMOXICILLIN (injection)
Active Substance
AMOXICILLIN
Modality
Small molecule
Routes Of Administration
INJECTION
Route
INJECTION
Maximum Dose
150 mg/kg
Combination Treatment
Yes

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