Clinical trial • Phase III • Gastroenterology

ALLOGENEIC FAECAL MICROBIOTA, POOLED for Ulcerative colitis

Phase III trial of ALLOGENEIC FAECAL MICROBIOTA, POOLED for Ulcerative colitis.

Overview

Trial Therapeutic Area
Gastroenterology
Trial Disease
Ulcerative colitis
Trial Stage
Phase III
Drug Modality
Other

Key dates

Initial CTIS Submission Date
14-10-2024
First CTIS Authorization Date
08-11-2024

Trial design

Randomised, arms: fecal microbiome (fm) (test product: allogeneic faecal microbiota, pooled; capsules for oral use; max daily amount 6000 µl, max total amount 360 ml, max treatment period 12 months), fecal microbiome filtrate (fmf) (test product: allogeneic faecal microbiota, pooled; capsules for oral use; max daily amount 6000 µl, max total amount 360 ml, max treatment period 12 months) versus placebo, unauthorised capsule, hard for oral use. auxiliary antibiotics listed in trial (vancomycin, metronidazole) but dosing/schedule not specified in the provided trial summary.-controlled Phase III trial across 21 sites in Germany.

Randomised
Yes
Comparator
Arms: Fecal microbiome (FM) (test product: allogeneic faecal microbiota, pooled; capsules for oral use; max daily amount 6000 µl, max total amount 360 ml, max treatment period 12 months), Fecal Microbiome Filtrate (FMF) (test product: allogeneic faecal microbiota, pooled; capsules for oral use; max daily amount 6000 µl, max total amount 360 ml, max treatment period 12 months) versus Placebo, unauthorised capsule, hard for oral use. Auxiliary antibiotics listed in trial (vancomycin, metronidazole) but dosing/schedule not specified in the provided trial summary.
Target Sample Size
129
Trial Duration For Participant
365

Eligibility

Recruits 129 Vulnerable population not selected. Participants must be able to understand study procedures and provide written consent (inclusion criteria: written consent; ability to understand study procedures). Participants are adults (age between 18 and 75 years); no assent process described..

Pregnancy Exclusion
• potentially childbearing patient: negative pregnancy test and use of a highly effective contraceptive method
Vulnerable Population
Vulnerable population not selected. Participants must be able to understand study procedures and provide written consent (inclusion criteria: written consent; ability to understand study procedures). Participants are adults (age between 18 and 75 years); no assent process described.

Inclusion criteria

  • {"criterion_text":"- •\tAge between 18 and 75 years"}
  • {"criterion_text":"- •\twritten consent"}
  • {"criterion_text":"- •\tprior endoscopic confirmation of colitis ulcerosa (first diagnosis of at least 6 months, active disease: mayo score between 4-10 points at screening, documented endoscopic minimum disease extent of 15 cm from the anal verge (mayo endoskopic subscore >1)"}
  • {"criterion_text":"- •\tFailure of conventional therapy or treatment with biologicals and/or small molecules"}
  • {"criterion_text":"- •\tprevious medical therapy: -oral 5-ASA compounds (5-ASA) (stable dose for 4 weeks before randomisation) OR -Azathioprine, 6-MP or MTX (stable dose for 8 weeks before randomisation) OR -oral steroid therapy: (prednisone (≤ 20 mg/day) or budesonide (≤ 9 mg/day)) (stable dose for 2 weeks before randomisation) OR -topical therapy (foams, clysms) with mesalazine or budesonide (stable dose for 2 weeks before randomisation)"}
  • {"criterion_text":"- •\tprevious vaccination against SARS-CoV-2 or previous SARS-CoV-2 infection or positive serology"}
  • {"criterion_text":"- •\tAbility to understand study procedures and willingness to meet requirements associated with participation (e. g. endoscopy, intake antibiotics)"}
  • {"criterion_text":"- •\tpotentially childbearing patient: negative pregnancy test and use of a highly effective contraceptive method"}

Exclusion criteria

  • {"criterion_text":"- •\tCrohn´s disease, indeterminate colitis or ulcerative proctitis (< 15 cm ab ano)"}
  • {"criterion_text":"- •\tlack of immunity to SARS-CoV-2"}
  • {"criterion_text":"- •\tPrevious treatment with TNF-, IL12/IL23-, IL23- or integrin-antibodies (8 weeks before randomisation)"}
  • {"criterion_text":"- •\tTreatment with calcineurin inhibitors (4 weeks before randomization)"}
  • {"criterion_text":"- •\tTreatment with JAK inhibitors (e.g., tofacitinib, filgotinib, or upadacitinib) (4 weeks before randomization)"}
  • {"criterion_text":"- •\tTreatment with S1P receptor modulator (e. g. ozanimod, etrasimod) (4 weeks before randomization)"}
  • {"criterion_text":"- •\tSystemic antibiotic treatment (8 weeks before randomization)"}
  • {"criterion_text":"- •\tKnown intolerance to metronidazole or vancomycin"}
  • {"criterion_text":"- •\tParticipation in a clinical trial (3 months before randomization)"}
  • {"criterion_text":"- •\tPrevious FMT or FMFT, previous participation in this study (screening allowed)"}
  • {"criterion_text":"- •\tUse of probiotics in tablet, capsule, or powder form, or appropriate drinking yogurts (or similar) (2 weeks before randomization)"}
  • {"criterion_text":"- •\tAcute abdomen or other clinical emergencies (toxic megacolon, fulminant gastrointestinal hemorrhage, ileus, perforation, etc.)"}
  • {"criterion_text":"- •\tFailure to ensure frozen storage of investigational products: no possibility to store capsules at ≤ -10°C, planned longer absence (12 weeks after randomization)"}
  • {"criterion_text":"- •\tAddictive or other medical conditions or circumstances that do not allow the subject to appreciate the nature, significance, scope, and possible consequences of the clinical trial"}
  • {"criterion_text":"- •\tIndications that the patient would be unlikely to comply with the protocol (e.g., unwillingness to cooperate - compliance questionable)"}
  • {"criterion_text":"- •\tPrevious operations on the colon: colectomy, partial colon resections"}
  • {"criterion_text":"- •\tcurrent gastrointestinal infections (e. g. Clostridium difficile infection, CMV infection) until randomisation"}
  • {"criterion_text":"- •\tCongenital or acquired immunodeficiency"}
  • {"criterion_text":"- •\tsevere comorbidity (e.g. insulin-dependent diabetes mellitus, decompensated liver cirrhosis, primary sclerosing cholangitis, renal impairment > grade 2)"}
  • {"criterion_text":"- •\tdiagnosis of a malignoma in the last 3 years"}
  • {"criterion_text":"- •\trefusal of endoscopies with video documentation"}
  • {"criterion_text":"- •\tNo specific therapy for ulcerative colitis to date"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- clinical remission at week 12 post transfer defined by Mayo score ≤ 2 and any subcore ≤ 1, missing values to week 12 are considered as no remission","definition_or_measurement_approach":"Defined by Mayo score ≤ 2 and any subcore ≤ 1; missing values to week 12 are considered as no remission."}

Secondary endpoints

  • {"endpoint_text":"- steroid-free clinical remission","definition_or_measurement_approach":"Steroid-free clinical remission (no additional definition provided)."}
  • {"endpoint_text":"- Mayo score","definition_or_measurement_approach":"Measured using the Mayo score."}
  • {"endpoint_text":"- endoscopic remission","definition_or_measurement_approach":"Endoscopic remission (no additional definition provided)."}
  • {"endpoint_text":"- clinical response","definition_or_measurement_approach":"Clinical response (no additional definition provided)."}
  • {"endpoint_text":"- mucosal infammation (fecal calprotectin)","definition_or_measurement_approach":"Measured by fecal calprotectin."}
  • {"endpoint_text":"- histological mucosal inflammation (Nancy index)","definition_or_measurement_approach":"Measured using the Nancy histology index."}
  • {"endpoint_text":"- quality of life","definition_or_measurement_approach":"Quality of life (no specific instrument defined in provided data)."}
  • {"endpoint_text":"- microbiome and virome analysis","definition_or_measurement_approach":"Microbiome and virome analyses (methods not specified in provided data)."}
  • {"endpoint_text":"- safety","definition_or_measurement_approach":"Safety (no further definition provided)."}

Recruitment

Registry Or Advocacy Recruitment
Yes
Planned Sample Size
129
Recruitment Window Months
51
Consent Approach
Written informed consent required from participants (inclusion criterion: written consent). Participants must be aged 18-75. Subject information and informed consent form documents are listed among trial documents (L1 files). A German translation of some materials/criteria is present.

Geography

Total Number Of Sites
21
Total Number Of Participants
129

Germany

Earliest CTIS Part Ii Submission Date
23-10-2024
Latest Decision Or Authorization Date
12-01-2026
Processing Time Days
446
Number Of Sites
21
Number Of Participants
129

Sites

Site Name
Universitaetsklinikum Ulm AöR
Department Name
Klinik für Innere Medizin I
Principal Investigator Name
Jochen Klaus
Principal Investigator Email
jochen.klaus@uniklinik-ulm.de
Contact Person Name
Jochen Klaus
Contact Person Email
jochen.klaus@uniklinik-ulm.de
Site Name
Universitaetsklinikum Erlangen AöR
Department Name
Medizinische Klinik 1
Principal Investigator Name
Raja Atreya
Principal Investigator Email
Raja.Atreya@uk-erlangen.de
Contact Person Name
Raja Atreya
Contact Person Email
Raja.Atreya@uk-erlangen.de
Site Name
Otto Von Guericke Universitaet Magdeburg
Department Name
Zentrum für Innere Medizin
Principal Investigator Name
Ulrike von Arnim
Principal Investigator Email
ulrike.vonarnim@med.ovgu.de
Contact Person Name
Ulrike von Arnim
Contact Person Email
ulrike.vonarnim@med.ovgu.de
Site Name
Universitaetsklinikum Jena KöR
Department Name
Klinik für Innere Medizin IV
Principal Investigator Name
Andreas Stallmach
Principal Investigator Email
andreas.stallmach@med.uni-jena.de
Contact Person Name
Andreas Stallmach
Site Name
Sozialstiftung Bamberg
Department Name
Klinik für Integrative Medizin und Naturheilkunde
Principal Investigator Name
Jost Langhorst
Principal Investigator Email
FIGN@sozialstiftung-bamberg.de
Contact Person Name
Jost Langhorst
Contact Person Email
FIGN@sozialstiftung-bamberg.de
Site Name
Klinikum Fulda gAG
Department Name
Medizinische Klinik II
Principal Investigator Name
Carsten Schmidt
Principal Investigator Email
Carsten.Schmidt@klinikum-fulda.de
Contact Person Name
Carsten Schmidt
Site Name
St. Marien Und St. Annastiftskrankenhaus
Department Name
Klinik für Innere Medizin
Principal Investigator Name
Tanja Kühbacher
Principal Investigator Email
studienabteilung@st-marienkrankenhaus.de
Contact Person Name
Tanja Kühbacher
Site Name
Internistische Gemeinschaftspraxis für Verdauungs- und Stoffwechselerkrankungen (IGVS)
Department Name
Gesellschaft für Klinische Studien
Principal Investigator Name
Niels Teich
Principal Investigator Email
teich@igvs.de
Contact Person Name
Niels Teich
Contact Person Email
teich@igvs.de
Site Name
Medical Center - University Of Freiburg
Department Name
Klinik für Innere Medizin II
Principal Investigator Name
Peter Hasselblatt
Principal Investigator Email
peter.hasselblatt@uniklinik-freiburg.de
Contact Person Name
Peter Hasselblatt
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
Klinik für Gastroenterologie, Infektiologie und Rheumatologie
Principal Investigator Name
Britta Siegmund
Principal Investigator Email
britta.siegmund@charite.de
Contact Person Name
Britta Siegmund
Contact Person Email
britta.siegmund@charite.de
Site Name
Agaplesion Frankfurter Diakonie Kliniken gGmbH
Department Name
Medizinische Klinik I
Principal Investigator Name
Axel Dignaß
Principal Investigator Email
axel.dignass@agaplesion.de
Contact Person Name
Axel Dignaß
Contact Person Email
axel.dignass@agaplesion.de
Site Name
Universitaetsklinikum Essen AöR
Department Name
Medizinisches Zentrum I
Principal Investigator Name
Claudia Veltkamp
Principal Investigator Email
Claudia.Veltkamp@uk-essen.de
Contact Person Name
Claudia Veltkamp
Contact Person Email
Claudia.Veltkamp@uk-essen.de
Site Name
Gemeinschaftskrankenhaus Havelhoehe gGmbH
Department Name
Gastroenterologie/Diabetologie/Ernährungsmedizin
Principal Investigator Name
Markus Wispler
Principal Investigator Email
Markus.Wispler@havelhoehe.de
Contact Person Name
Markus Wispler
Contact Person Email
Markus.Wispler@havelhoehe.de
Site Name
University Medical Center Hamburg-Eppendorf
Department Name
Medizinische Klinik I
Principal Investigator Name
Thorben Fründt
Principal Investigator Email
t.fruendt@uke.de
Contact Person Name
Thorben Fründt
Contact Person Email
t.fruendt@uke.de
Site Name
Staedtisches Klinikum Lueneburg gGmbH
Department Name
Innere Medizin
Principal Investigator Name
Christian Maaser
Principal Investigator Email
christian.maaser@klinikum-lueneburg.de
Contact Person Name
Christian Maaser
Site Name
DRK Kliniken Berlin
Department Name
Klinik für Innere Medizin
Principal Investigator Name
Andreas Sturm
Principal Investigator Email
a.sturm@drk-kliniken-berlin.de
Contact Person Name
Andreas Sturm
Contact Person Email
a.sturm@drk-kliniken-berlin.de
Site Name
Universitaetsklinikum Carl Gustav Carus Dresden an der Technischen Universitaet Dresden AöR
Department Name
Medizinische Klinik und Poliklinik I
Principal Investigator Name
Renate Schmelz
Principal Investigator Email
schmelz.studien@ukdd.de
Contact Person Name
Renate Schmelz
Contact Person Email
schmelz.studien@ukdd.de
Site Name
Krankenhaus Waldfriede e.V.
Department Name
Innere Abteilung
Principal Investigator Name
Carsten Büning
Principal Investigator Email
C.Buening@waldfriede.de
Contact Person Name
Carsten Büning
Contact Person Email
C.Buening@waldfriede.de
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Klinik für Innere Medizin
Principal Investigator Name
Stefan Schreiber
Principal Investigator Email
s.schreiber@ikmb.uni-kiel.de
Contact Person Name
Stefan Schreiber
Contact Person Email
s.schreiber@ikmb.uni-kiel.de
Site Name
Martin-Luther-Universitaet Halle-Wittenberg
Department Name
Universitätsklinik und Poliklinik für Innere Medizin I
Principal Investigator Name
Jens Walldorf
Principal Investigator Email
jens.walldorf@uk-halle.de
Contact Person Name
Jens Walldorf
Contact Person Email
jens.walldorf@uk-halle.de
Site Name
Klinikum der Universitaet Muenchen AöR
Department Name
Medizinische Klinik und Poliklinik II
Principal Investigator Name
Helga Török
Principal Investigator Email
helga.toeroek@med.uni-muenchen.de
Contact Person Name
Helga Török

Sponsor

Primary sponsor

Full Name
Friedrich-Schiller-Universitaet Jena
Organisation Type
Educational Institution
Country Of Registered Address
Germany

Investigational products

Investigational Product Name
Fecal microbiome (FM)
Active Substance
ALLOGENEIC FAECAL MICROBIOTA, POOLED
Modality
Other
Routes Of Administration
ORAL USE
Route
Oral
Authorisation Status
Authorised
Maximum Dose
6000 µl per day; max total 360 ml
Investigational Product Name
Fecal Microbiome Filtrate (FMF)
Active Substance
ALLOGENEIC FAECAL MICROBIOTA, POOLED
Modality
Other
Routes Of Administration
ORAL USE
Route
Oral
Authorisation Status
Authorised
Maximum Dose
6000 µl per day; max total 360 ml
Investigational Product Name
Placebo, unauthorised capsule, hard for oral use
Modality
Other
Authorisation Status
Unauthorised

Related trials

Other published trials that may interest you.