Clinical trial • Phase III • Endocrinology|Rare Disease

AG-181 for Phenylketonuria

Phase III trial of AG-181 for Phenylketonuria. 10 participants.

Overview

Trial Therapeutic Area
Endocrinology|Rare Disease
Trial Disease
Phenylketonuria
Trial Stage
Phase III

Key dates

Initial CTIS Submission Date
28-11-2025
First CTIS Authorization Date
03-04-2026

Recruitment

Recruitment Window Months
22

Geography

Total Number Of Sites
2
Total Number Of Participants
10

Poland

Earliest CTIS Part Ii Submission Date
26-02-2026
Latest Decision Or Authorization Date
03-04-2026
Processing Time Days
36
Number Of Sites
2
Number Of Participants
10

Sites

Site Name
Centrum Wsparcia Badań Klinicznych Pomorskiego Uniwersytetu Medycznego w Szczecinie
Principal Investigator Name
Maria Giżewska
Principal Investigator Email
maria.gizewska@pum.edu.pl
Contact Person Name
Maria Giżewska
Contact Person Email
maria.gizewska@pum.edu.pl
Site Name
Uniwersyteckie Centrum Kliniczne
Principal Investigator Name
Joanna Jagłowska
Principal Investigator Email
jjaglowska@uck.gda.p
Contact Person Name
Joanna Jagłowska
Contact Person Email
jjaglowska@uck.gda.p

Sponsor

Primary sponsor

Full Name
Agios Pharmaceuticals Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Investigational products

Investigational Product Name
AG-181

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