Clinical trials

  • Pyridoxal phosphate for Pyridox(am)ine 5'-phosphate oxidase (PNPO) deficiency | Seizures associated with PNPO deficiency
  • Safinamide for Parkinson's disease with motor fluctuations
  • Risankizumab for Psoriatic arthritis | Crohn's disease | Plaque psoriasis | Ulcerative colitis
  • 2-[4-[4-(aminomethyl)-1-oxo-2h-phthalazin-6-yl]-2-methylpyrazol-3-yl]-4-chloro-6-cyclopropyloxy-3-fluorobenzonitrile for Metastatic non-small cell lung cancer
  • A-dopamine for Parkinson's disease
  • Donepezil hydrochloride for Acne vulgaris
  • RITLECITINIB for Vitiligo
  • PEMBROLIZUMAB for Urothelial carcinoma
  • GD2IL18CART for Neuroblastoma | Osteosarcoma | Ewing sarcoma | Advanced breast cancer
  • IPN60300 for Advanced or metastatic solid tumours | Malignant solid tumour
  • ENLICITIDE CHLORIDE for Hyperlipidemia
  • DEUCRICTIBANT for Acquired angioedema due to C1 inhibitor deficiency