Clinical trials

  • Cytisinicline for Nicotine dependence
  • Tildrakizumab for Lyell syndrome (toxic epidermal necrolysis) - ocular sequelae
  • PREDNISONE for Fabry disease
  • RNA (nucleic acid complex) (synonym: ALN-6400) for Hereditary haemorrhagic telangiectasia (HHT)
  • TRONTINEMAB for Alzheimer's disease | Mild cognitive impairment
  • PIRTOBRUTINIB for Chronic lymphocytic leukemia
  • IOHEXOL for Abdominal aortic aneurysm
  • Acetylsalicylic acid for Colorectal adenomas | Lynch syndrome
  • Adeno-associated viral vector serotype 9 expressing codon-optimized human GBA gene for Parkinson's disease with GBA1 mutation
  • FLUOROURACIL for Rectal adenocarcinoma | Locally advanced rectal cancer
  • Oxytocin for Autism spectrum disorder | Intellectual disability
  • ORX750 for Narcolepsy | Idiopathic hypersomnia