Clinical trials

  • Darolutamide for Prostate cancer (intermediate unfavorable risk)
  • VOXVOGANAN for COVID-19 | COVID-like illness
  • PEGUNIGALSIDASE ALFA for Fabry disease
  • KK8123 for X-linked hypophosphatemia
  • NEMTABRUTINIB for Small lymphocytic lymphoma (SLL) | Chronic lymphocytic leukemia (CLL)
  • HUMANISED IGG1 MONOCLONAL ANTIBODY AGAINST HUMAN LATENT MYOSTATIN for Facioscapulohumeral muscular dystrophy
  • (3S)-3-[6-[4-[[1-[4-[(1R,2S)-6-HYDROXY-2-PHENYL-1,2,3,4-TETRAHYDRONAPHTHALEN-1-YL]PHENYL]PIPERIDIN-4-YL]METHYL]PIPERAZIN-1-YL]-3-OXO-1H-ISOINDOL-2-YL]PIPERIDINE-2,6-DIONE for Advanced breast cancer | Metastatic breast cancer
  • NEMTABRUTINIB for Chronic lymphocytic leukemia | Small lymphocytic lymphoma
  • bidridistrogene xeboparvovec for Limb-girdle muscular dystrophy (LGMD2E/R4) | β-sarcoglycanopathy
  • DEXAMETHASONE for Solid tumors
  • OBINUTUZUMAB for Granulomatosis with polyangiitis (Wegener's)|PR3-ANCA positive granulomatosis with polyangiitis
  • Atezolizumab for Gastrointestinal stromal tumor (GIST) | Unresectable GIST | Metastatic GIST | Locally advanced GIST