Clinical trials

  • PEGTIBATINASE for Classical homocystinuria (cystathionine beta-synthase deficiency)
  • LUSPATERCEPT for Myelodysplastic syndrome|Lower-risk myelodysplastic syndrome
  • MIGLUSTAT for Late-onset Pompe disease
  • Dapagliflozin; Zibotentan for Chronic kidney disease with high proteinuria | IgA nephropathy (biopsy-confirmed subgroup)
  • BIMEKIZUMAB for Juvenile idiopathic arthritis | Enthesitis-related arthritis (including juvenile-onset ankylosing spondylitis) | Juvenile psoriatic arthritis
  • Clinical trial in Metastatic colorectal cancer
  • GIREDESTRANT for Endometrial cancer | Endometrial cancer stage I
  • GUSELKUMAB for Ulcerative colitis | Moderately to severely active ulcerative colitis
  • Clinical trial in Healthy volunteers
  • Bezafibrate for Primary biliary cholangitis
  • RO7502175 for Locally advanced or metastatic solid tumours
  • JNJ-77242113 for Moderate to severe plaque psoriasis|Plaque psoriasis