Clinical trials

  • ZICLUMERAN; SINGLE GUIDE RNA TARGETING THE HUMAN TTR GENE for Hereditary transthyretin amyloidosis with polyneuropathy (ATTRv-PN) | Transthyretin amyloidosis-related cardiomyopathy (ATTR-CM)
  • TERN-701 for Chronic Myeloid Leukemia
  • 4-[3-(cyanomethyl)-3-(3',5'-dimethyl-1H,1'H-[4,4'-bipyrazol]-1-yl)azetidin-1-yl]-2,5-difluoro-N-[(2S)-1,1,1-trifluoropropan-2-yl]benzamide for Hidradenitis suppurativa
  • Valemetostat tosylate for Peripheral T-cell lymphoma | Adult T-cell leukaemia/lymphoma (ATL)
  • AAA802 for PSMA-positive metastatic hormone-sensitive prostate cancer | PSMA-positive metastatic castration-resistant prostate cancer
  • CLOSTRIDIUM BOTULINUM, NEUROTOXIN SEROTYPE A/B for Upper limb spasticity (post-stroke) | Upper limb spasticity (post-traumatic brain injury)
  • VAFIDEMSTAT for Schizophrenia
  • VALINE, ALANINE, ARGININE, HISTIDINE, ISOLEUCINE, LEUCINE, METHIONINE, PHENYLALANINE, PROLINE, SERINE, TAURINE, THREONINE, TYROSINE, GLYCINE, OLIVE OIL, REFINED, SOYA-BEAN OIL REFINED, TRIGLYCERIDES, MEDIUM CHAIN, TRYPTOPHAN, POTASSIUM CHLORIDE, CALCIUM CHLORIDE DIHYDRATE, GLUCOSE MONOHYDRATE, MAGNESIUM SULFATE HEPTAHYDRATE, SODIUM ACETATE TRIHYDRATE, SODIUM GLYCEROPHOSPHATE, LYSINE ACETATE, ZINC SULPHATE HEPTAHYDRATE, FISH OIL, RICH IN OMEGA-3-ACIDS for Oesophagectomy
  • AMIODARONE HYDROCHLORIDE for Atrial fibrillation
  • PEMBROLIZUMAB for Inflammatory breast cancer|Breast cancer with lymphangitic spread to the chest wall
  • MOSAIC HBCOREAG for Chronic hepatitis B
  • PLATELET CONCENTRATE for Dry Eye Disease