Clinical trials

  • GOLIMUMAB for Peripheral spondyloarthritis
  • Etranacogene dezaparvovec for Hemophilia B (severe or moderately severe)
  • TRASTUZUMAB for HER2-positive locally advanced or metastatic breast cancer
  • RAPCABTAGENE AUTOLEUCEL for Systemic lupus erythematosus | Lupus nephritis
  • Triheptanoin for Long-chain fatty acid oxidation disorders (LC-FAOD)
  • BEPIROVIRSEN SODIUM for Chronic hepatitis B | HIV infection
  • N-(4-FLUOROPHENYL)-N-(4-((7-METHOXY-6-(METHYLCARBAMOYL)QUINOLIN-4-YL)OXY)PHENYL)CYCLOPROPANE-1,1-DICARBOXAMIDE for Clear cell renal cell carcinoma | Metastatic castration-resistant prostate cancer | Urothelial carcinoma | Non-clear cell renal cell carcinoma | Colorectal cancer | Hepatocellular carcinoma | Non-small cell lung cancer | Head and neck squamous cell carcinoma
  • REGN7075 for Non-small cell lung cancer
  • AXITINIB for Medulloblastoma | Ependymoma
  • Colecalciferol (Vitamin D3) for Metastatic pancreatic adenocarcinoma (previously untreated)
  • MELDONIUM for Heart failure with preserved ejection fraction
  • TEZACAFTOR, ELEXACAFTOR, IVACAFTOR for Cystic fibrosis