Clinical trials

  • Exagamglogene autotemcel for Sickle cell disease|Transfusion-dependent β-thalassemia
  • IOPAMIDOL for Peripheral arterial disease
  • HYDROXYCHLOROQUINE SULFATE for IgA nephropathy
  • Autologous bone marrow-derived mononuclear cells for Chronic limb-threatening ischemia | Diabetic foot ulcer
  • AUTOLOGOUS T-CELLS TRANSDUCED WITH LENTIVIRAL VECTOR ENCODING AN ANTI-SLAMF7 CD28/CD3-ZETA CHIMERIC ANTIGEN RECEPTOR for Multiple myeloma
  • NIFEDIPINE for Preterm premature rupture of membranes (PPROM)
  • ILOPROST TROMETAMOL for Infectious pulmonary endotheliopathy | Respiratory failure
  • DNTH103 for Generalized Myasthenia Gravis
  • resamirigene bilparvovec for X-linked myotubular myopathy (XLMTM)
  • Abatacept for IgG4-related disease
  • HUMAN IMMUNOGLOBULIN G1 CONSTANT REGION - HUMAN ECTODYSPLASIN-A1 RECEPTOR-BINDING DOMAIN FUSION PROTEIN for X-linked hypohidrotic ectodermal dysplasia (XLHED)
  • 18F-PSMA-1007 for Clinically significant prostate cancer