Clinical trial • Phase III • Oncology

ZANUBRUTINIB for B-cell malignancies

Phase III trial of ZANUBRUTINIB for B-cell malignancies. open-label, none/not specified-controlled. 444 participants.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
B-cell malignancies
Trial Stage
Phase III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
06-02-2024
First CTIS Authorization Date
07-03-2024

Trial design

open-label, none/not specified-controlled Phase III trial in Germany, Greece, Netherlands and others.

Open Label
Yes
Comparator
None/Not specified
Target Sample Size
444

Eligibility

Recruits 444 adults.

Pregnancy Exclusion
Pregnant or lactating woman

Inclusion criteria

  • {"criterion_text":"- As part of a BeiGene-sponsored parent study: a. Currently participating, or b. Participated recently\n- Intent to continue or start zanubrutinib treatment after occurrence of any of the following: a. At time of final analysis or study closure of the eligible BeiGene-sponsored parent study. b. At time of progressive disease (PD) after occurrence of either of the following: i. Patient was receiving zanubrutinib at the time of progressive disease (PD), and the investigator and patient agree it is in the patient's best interest to continue zanubrutinib (following discussion with the medical monitor or designee of the parent study and this study) *The following signs and symptoms may be indicators of non-clinically significant progression warranting continued use of zanubrutinib despite radiologic progression: absence of clinical symptoms and signs of disease progression (including clinically significant worsening of laboratory values), stable Eastern Cooperative Oncology Group Performance Scale (ECOG PS), absence of rapid progression of disease or of progressive tumor at critical anatomical sites that requires urgent alternative medical intervention. In these scenarios, investigators must inform patients that continuing treatment is not considered standard in the treatment of cancer but that in the opinion of the investigator, the patient will continue to benefit from zanubrutinib. ii. Patient was receiving a non-BTK inhibitor drug at the time of PD, and the investigator and patient agree that the patient may clinically benefit from zanubrutinib treatment (following discussion with the medical monitor or designee of the parent study and this study) c. At an alternative timepoint for an alternative reason not described in Inclusion Criteria 2a and 2b (following discussion with the medical monitor or designee)\n- In the opinion of the investigator, the patient will continue to benefit from, and tolerate zanubrutinib a. Patient who is currently on zanubrutinib treatment: Does not meet any criteria for zanubrutinib hold or permanent discontinuation"}

Exclusion criteria

  • {"criterion_text":"- Permanently discontinued from zanubrutinib treatment in the BeiGene-sponsored parent study due to unacceptable toxicity, noncompliance with study procedures, or withdrawal of consent\n- Uncontrolled active systemic infection or recent infection requiring parenteral anti-microbial therapy\n- Life-threatening illness, medical condition, or organ system dysfunction which, in the investigator's opinion, could compromise the patient's safety, interfere with the absorption or metabolism of zanubrutinib, or put the study outcomes at undue risk\n- Concomitant chemotherapy, targeted therapy, radiation therapy, antibody-based therapy, or any prohibited concomitant therapy outlined in the protocol\n- Pregnant or lactating woman\n- Inability to comply with study procedures\n- Concurrent participation in another therapeutic clinical study\n- History of progressive disease (PD) while receiving a BTK inhibitor (excluding zanubrutinib)\n- Vaccination with a live vaccine within 35 days prior to first dose of study drug"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- The primary endpoint of the study is safety as assessed by incidence of all TEAEs and SAEs.","definition_or_measurement_approach":"Safety assessed by incidence of all treatment-emergent adverse events (TEAEs) and serious adverse events (SAEs)."}

Secondary endpoints

  • {"endpoint_text":"- Progression-free Survival per investigator assessment","definition_or_measurement_approach":"Progression-free survival assessed by investigator evaluation (time from entry to disease progression or death as determined by investigator)."}
  • {"endpoint_text":"- Duration of Response per investigator assessment","definition_or_measurement_approach":"Duration of response assessed by investigator (time from first documented response to progression or death)."}
  • {"endpoint_text":"- Overall Survival","definition_or_measurement_approach":"Overall survival measured as time from entry/randomisation to death from any cause."}

Recruitment

Planned Sample Size
444
Recruitment Window Months
89

Geography

Total Number Of Sites
51
Total Number Of Participants
343

Germany

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
14
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
SRH Kliniken Landkreis Sigmaringen GmbH
Department Name
Innere Medizin | Hämatologie und Internistische Onkologie, Palliativmedizin
Contact Person Name
Gabriele Käfer
Contact Person Email
xxx@srh.de

Greece

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
23-04-2024
Processing Time Days
57
Number Of Sites
1
Number Of Participants
10

Sites

Site Name
Alexandra Hospital
Department Name
Plasma Cell Dyscrasias Unit, Department of Clinical Therapeutics
Contact Person Name
Athanasios-Meletios Dimopoulos
Contact Person Email
mdimop@med.uoa.gr

Netherlands

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
14
Number Of Sites
3
Number Of Participants
6

Sites

Site Name
Universitair Medisch Centrum Utrecht
Department Name
Hematology
Contact Person Name
Monique Minnema
Contact Person Email
m.c.minnema@umcutrecht.nl
Site Name
Amsterdam UMC Stichting
Department Name
Hematology
Contact Person Name
Marie José Kersten
Contact Person Email
m.j.kersten@amc.uva.nl
Site Name
Albert Schweitzer Ziekenhuis
Department Name
Hematology
Contact Person Name
Mark-David Levin
Contact Person Email
m-d.levin@asz.nl

France

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
21-03-2024
Processing Time Days
24
Number Of Sites
6
Number Of Participants
25

Sites

Site Name
Centre Hospitalier Departemental Vendee
Department Name
Onco-Hématologie
Contact Person Name
Bruno VILLEMAGNE
Contact Person Email
xxxxxx@xxxxxxx.fr
Site Name
Hopital Saint Louis
Department Name
Onco-Hématologie
Contact Person Name
Catherine THIEBLEMONT
Contact Person Email
xxxxxx@xxxxxxx.fr
Site Name
Centre Hospitalier Le Mans
Department Name
Hématologie
Contact Person Name
Kamel LARIBI
Contact Person Email
xxxxxx@xxxxxxx.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Hématologie et Thérapie Cellulaire
Contact Person Name
Caroline DARTIGEAS
Contact Person Email
xxxxxx@xxxxxxx.fr
Site Name
Institut Bergonie
Department Name
Hématologie
Contact Person Name
Fontanet BIJOU
Contact Person Email
xxxxxx@xxxxxxx.fr
Site Name
Hospices Civils De Lyon
Department Name
Hématologie Clinique
Contact Person Name
Emmanuelle FERRANT
Contact Person Email
xxxxxx@xxxxxxx.fr

Italy

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
14
Number Of Sites
10
Number Of Participants
39

Sites

Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
SC Oncologia Medica
Contact Person Name
Michela Ceccolini
Contact Person Email
michela.ceccolini@irst.emr.it
Site Name
Azienda Unita Sanitaria Locale Della Romagna
Department Name
UNITA DI EMATOLOGIA, DIPARTIMENTO DI EMATOLOGIA ED ONCOLOGIA
Contact Person Name
Monica Tani
Contact Person Email
monica.tani@auslromagna.it
Site Name
Azienda Ospedaliero-Universitaria Maggiore Della Carita
Department Name
S.C. Ematologia
Contact Person Name
Gloria Margiotta Casaluci
Contact Person Email
gloria.margiotta@med.uniupo.it
Site Name
Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
Department Name
Department of Molecular Biotechnology and Health Sciences
Contact Person Name
Federica Cavallo
Contact Person Email
f.cavallo@unito.it
Site Name
Azienda Ospedaliera Universitaria Di Modena
Department Name
S.C. Ematologia
Contact Person Name
Roberto Marasca
Contact Person Email
roberto.marasca@unimore.it
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
DIAGNOSTICA PER IMMAGINI, RADIOTERAPIA ONCOLOGICA ED EMATOLOGIA
Contact Person Name
Luca Laurenti
Contact Person Email
LUCA.LAURENTI@UNICATT.IT
Site Name
ASST Grande Ospedale Metropolitano Niguarda
Department Name
S.C. Ematologia
Contact Person Name
Anna Maria Frustaci
Site Name
Azienda Ospedaliera S Maria Di Terni
Department Name
Department of Medicine
Contact Person Name
Gaetano Vaudo
Contact Person Email
vaudogaetano@gmail.com
Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
Dip Malattie Oncologiche ed Ematologiche
Contact Person Name
Pier Luigi Zinzani
Contact Person Email
pierluigi.zinzani@unibo.it
Site Name
Azienda Sanitaria Universitaria Friuli Centrale
Department Name
SOC Clinica Ematologica
Contact Person Name
Jacopo Olivieri

Czechia

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
07-03-2024
Processing Time Days
10
Number Of Sites
6
Number Of Participants
43

Sites

Site Name
University Hospital Olomouc
Department Name
Hemato-onkologicka klinika
Contact Person Name
Peter Turcsanyi
Contact Person Email
peter.turcsanyi@fnol.cz
Site Name
Fakultni Nemocnice Ostrava
Department Name
Klinika hematoonkologie FNO a LF OU
Contact Person Name
Roman Hajek
Contact Person Email
roman.hajek@fno.cz
Site Name
Fakultni Nemocnice Kralovske Vinohrady
Department Name
Hematologicka klinika
Contact Person Name
Heidi Mocikova
Contact Person Email
Heidi.mocikova@fnkv.cz
Site Name
Vseobecna Fakultni Nemocnice V Praze
Department Name
I. Interni klinika – klinika hematologie
Contact Person Name
Marek Trneny
Contact Person Email
trneny@cesnet.cz
Site Name
Fakultni Nemocnice Brno
Department Name
Interni hematologicka a onkologicka klinika
Contact Person Name
Anna Panovska
Contact Person Email
panovska.anna@fnbrno.cz
Site Name
Fakultni Nemocnice Hradec Kralove
Department Name
IV. interni hematologicka klinika
Contact Person Name
David Belada
Contact Person Email
BeladaD@lfhk.cuni.cz

Sweden

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
07-03-2024
Processing Time Days
10
Number Of Sites
1
Number Of Participants
15

Sites

Site Name
Karolinska University Hospital
Department Name
Center for clinical cancer studies
Contact Person Name
Bjorn Wahlin
Contact Person Email
bjorn.wahlin@sll.se

Spain

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
14
Number Of Sites
12
Number Of Participants
40

Sites

Site Name
Institut Catala D'oncologia
Department Name
Hematology
Contact Person Name
Albert Oriol
Contact Person Email
aoriol@iconcologia.net
Site Name
Hospital Universitario De Toledo
Department Name
Hematology
Contact Person Name
Maria Isabel Gomez
Contact Person Email
mgroncero@telefonica.net
Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Hematology
Contact Person Name
Mario Arnao
Contact Person Email
arnao_mar@gva.es
Site Name
Hospital Universitari Vall D Hebron
Department Name
Hematology
Contact Person Name
Mercedes Gironella
Contact Person Email
mgironella@vhio.net
Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Hematology
Contact Person Name
Jose Antonio Garcia Vela
Contact Person Email
xxxx@xxx.xx
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Hematology
Contact Person Name
Jordi Lopez
Contact Person Email
JLopezPar@santpau.cat
Site Name
Hospital Universitario De Salamanca
Department Name
Hematology
Contact Person Name
Cristina de Ramon
Contact Person Email
cramon@saludcastillayleon.es
Site Name
Institut Catala D'oncologia (Girona)
Department Name
Hematology
Contact Person Name
Josep Maria Roncero
Contact Person Email
jroncero@iconcologia.net
Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Hematology
Contact Person Name
Javier Lopez
Contact Person Email
jlopezj.hrc@salud.madrid.org
Site Name
Institut Catala D'oncologia (L'hospitalet De Llobregat)
Department Name
Hematology
Contact Person Name
Ana Carla Oliveira
Contact Person Email
acoliveira@iconcologia.net
Site Name
Hospital Clinic De Barcelona
Department Name
Hematology
Contact Person Name
Pablo Javier Mozas
Contact Person Email
mozas@clinic.cat
Site Name
Institut Catala D'oncologia (Badalona)
Department Name
Hematology
Contact Person Name
Albert Oriol
Contact Person Email
aoriol@iconcologia.net

Poland

Earliest CTIS Part Ii Submission Date
26-02-2024
Latest Decision Or Authorization Date
12-03-2024
Processing Time Days
15
Number Of Sites
11
Number Of Participants
164

Sites

Site Name
Wojewodzkie Wielospecjalistyczne Centrum Onkologii I Traumatologii Im M.Kopernika W Lodzi
Department Name
Oddział Hematologii Ogólnej i Chorób Wewnętrznych
Contact Person Name
Tadeusz ROBAK
Contact Person Email
x@x
Site Name
Centrum Onkologii Ziemi Lubelskiej Im. Sw. Jana Z Dukli
Department Name
-
Contact Person Name
Paweł KICIŃSKI
Contact Person Email
x@x
Site Name
Szpital Uniwersytecki Nr 2 Im Dr Jana Biziela W Bydgoszczy
Department Name
Klinika Hematologii
Contact Person Name
Marta SOBAS
Contact Person Email
x@x
Site Name
Interhem Katarzyna Mazgajska-Barczyk Marek Milewski Jaroslaw Piszcz Janusz Kloczko Piotr Radziwon Sp. j.
Department Name
InterHem Opieka Szpitalna
Contact Person Name
Jarosław PISZCZ
Contact Person Email
x@x
Site Name
Aidport Sp. z o.o.
Department Name
-
Contact Person Name
Maciej Kaźmierczak
Contact Person Email
rejestracja@aidport.pl
Site Name
Szpital Specjalistyczny W Brzozowie Podkarpacki Osrodek Onkologiczny Im.Ks.B.Markiewicza
Department Name
Oddział Hematologii Onkologicznej z Pododdziałem Transplantologii Klinicznej
Contact Person Name
Jacek KRZANOWSKI
Site Name
Samodzielny Publiczny Zaklad Opieki Zdrowotnej Zespol Szpitali Miejskich
Department Name
Oddział Kliniczny Hematologii i Profilaktyki Chorób Nowotworowych
Contact Person Name
Aleksandra MELISZ
Contact Person Email
x@x
Site Name
Copernicus Podmiot Leczniczy Sp. z o.o.
Department Name
Oddział Onkologii Klinicznej/Chemioterapii
Contact Person Name
Hanna Ciepłuch
Contact Person Email
XX@XX
Site Name
Pratia S.A.
Department Name
-
Contact Person Name
Wojciech Jurczak
Contact Person Email
XX@XX
Site Name
Uniwersyteckie Centrum Kliniczne
Department Name
Klinika Hematologii i Transplantologii
Contact Person Name
Andrzej Mital
Contact Person Email
XX@XX
Site Name
Additional listed Polish sites

Sponsor

Primary sponsor

Full Name
BeOne Medicines AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
PRA Hellas CRO A.E.
Responsibilities
codes:1,2
Name
PPD (UK) Limited
Responsibilities
code:8
Name
IQVIA Limited
Responsibilities
code:12

Third parties

  • {"country":"United States","full_name":"Scout Clinical","duties_or_roles":"Patient engagement","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"Greece","full_name":"PRA Hellas CRO A.E.","duties_or_roles":"codes:1,2","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"PPD (UK) Limited","duties_or_roles":"code:8","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"Biomarkers sample storage","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Medidata Solutions International Limited","duties_or_roles":"code:7","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"code:12","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Zanubrutinib
Active Substance
ZANUBRUTINIB
Modality
Small molecule
Routes Of Administration
ORAL
Route
Oral
Authorisation Status
Authorised
Starting Dose
320 mg once daily or 160 mg twice daily (total daily dose 320 mg); for patients with prior zanubrutinib treatment, equivalent to the last dose level received in the BeiGene-sponsored parent study.
Dose Levels
320 mg once daily; 160 mg twice daily (total 320 mg/day)
Frequency
Once daily or twice daily (for 160 mg BID)
Maximum Dose
320 mg daily
Combination Treatment
Yes

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