Clinical trial • Phase II • Cardiology

TX000045 for Pulmonary hypertension | Heart failure with preserved ejection fraction (HFpEF)

Phase II trial of TX000045 for Pulmonary hypertension | Heart failure with preserved ejection fraction (HFpEF).

Overview

Trial Therapeutic Area
Cardiology
Trial Disease
Pulmonary hypertension | Heart failure with preserved ejection fraction (HFpEF)
Trial Stage
Phase II
Drug Modality
Peptide/protein/enzyme

Key dates

Initial CTIS Submission Date
02-08-2024
First CTIS Authorization Date
28-11-2024

Trial design

Randomised, placebo (sterile isotonic solution) administered as the comparator arm (placebo described as 'sterile isotonic solution'). dose/schedule for comparator not specified.-controlled Phase II trial in Poland, Belgium, Austria and others.

Randomised
Yes
Comparator
Placebo (sterile isotonic solution) administered as the comparator arm (placebo described as 'sterile isotonic solution'). Dose/schedule for comparator not specified.
Target Sample Size
54
Trial Duration For Participant
168

Eligibility

Recruits 54 Mentally or legally incapacitated individuals are excluded per criterion: "26. Is mentally or legally incapacitated, has significant emotional problems at the time of the study, or has a history of significant psychiatric disorders at the discretion of the investigator". Only adults aged 18–83 are eligible (no paediatric participants); informed consent is obtained from adult participants. No paediatric assent procedures are specified..

Pregnancy Exclusion
"20. Is pregnant or breastfeeding"
Vulnerable Population
Mentally or legally incapacitated individuals are excluded per criterion: "26. Is mentally or legally incapacitated, has significant emotional problems at the time of the study, or has a history of significant psychiatric disorders at the discretion of the investigator". Only adults aged 18–83 are eligible (no paediatric participants); informed consent is obtained from adult participants. No paediatric assent procedures are specified.

Inclusion criteria

  • {"criterion_text":"- 1. Is a male or female of non–childbearing potential between the ages of 18 and 83 years."}
  • {"criterion_text":"- 2. Has a diagnosis of PH-HFpEF based on ALL the following criteria: a) The baseline echocardiogram, performed during screening, demonstrates the following: left ventricular ejection fraction (LVEF) >40%, tricuspid regurgitation gradient peak >36 mm Hg, and SPAP >41 mm Hg."}
  • {"criterion_text":"- 3. Has NYHA functional class II-III heart failure"}
  • {"criterion_text":"- 4. Has 6MWT distance ≥100 m and ≤450 m, repeated during screening."}
  • {"criterion_text":"- 5. If the participant is receiving chronic medication for the treatment of heart failure, including diuretics, or any other cardiovascular condition (including systemic hypertension), the dose must be stable for ≥30 days before start of screening."}

Exclusion criteria

  • {"criterion_text":"- 1. Has a confirmed diagnosis of PH in WHO Group 1 (pulmonary arterial hypertension), WHO Group 3 (PH associated with significant lung disease), WHO Group 4 (PH associated with chronic thromboembolic disease), or WHO Group 5"}
  • {"criterion_text":"- 2. Was hospitalized for any indication within 7 days before the start of screening"}
  • {"criterion_text":"- 20. Is pregnant or breastfeeding"}
  • {"criterion_text":"- 22. Has a history of active malignancy within 5 years before the start of screening, except for fully excised or treated basal cell carcinoma, cervical carcinoma in situ, or squamous cell carcinomas of the skin"}
  • {"criterion_text":"- 23. Has a history of drug or alcohol abuse"}
  • {"criterion_text":"- 24. Was dosed in any clinical research study evaluating another investigational drug (including biologics) or therapy"}
  • {"criterion_text":"- 25. Has significant orthopedic or arthritic disease that limits the ability to complete a 6MWT"}
  • {"criterion_text":"- 26. Is mentally or legally incapacitated, has significant emotional problems at the time of the study, or has a history of significant psychiatric disorders at the discretion of the investigator"}
  • {"criterion_text":"- 27. Has a history of any illness that, in the opinion of the investigator, poses additional risk to the participant"}
  • {"criterion_text":"- 3. Received IV vasoactive therapies inotropes"}
  • {"criterion_text":"- 5. Initiated a new exercise program within 90 days before the start of screening or plans to initiate such a program during the study (patients who are stable in the maintenance phase of a program and who will continue for the duration of the study are eligible)"}
  • {"criterion_text":"- Has documented significant lung disease"}
  • {"criterion_text":"- 6. Has a body mass index (BMI) <18 kg/m2 or >50 kg/m2"}
  • {"criterion_text":"- 7. Was previously administered TX000045, relaxin, or a relaxin fusion protein"}
  • {"criterion_text":"- 8. Received a small molecule RXFP1 agonist within 30 days before the start of screening"}
  • {"criterion_text":"- 11. Has cardiovascular comorbidities"}
  • {"criterion_text":"- Has chronic liver disease (other than congestive hepatopathy), active hepatitis B infection (positive hepatitis B surface antigen and positive hepatitis B core antibodies), or hepatitis C infection (positive hepatitis C antibodies) at the screening visit. In patients with isolated positive hepatitis B core antibodies, a hepatitis B DNA test will be performed. If positive, the participant will be excluded from the study due to active hepatitis B."}
  • {"criterion_text":"- 14. Has HIV infection or HIV seropositivity at the screening visit"}
  • {"criterion_text":"- 15. Has an active tuberculosis infection"}
  • {"criterion_text":"- 16. Has any of the following clinical laboratory values during screening: a) Serum alanine aminotransferase or aspartate aminotransferase levels >3× the upper limit of normal (ULN) or total bilirubin >3× ULN b) Estimated glomerular filtration rate (eGFR) <30 mL/min/1.73m2 (CKD EPI [Chronic Kidney Disease Epidemiology Collaboration] equation) or required renal replacement therapy (eg, ultrafiltration or dialysis) within 90 days before the start of screening c) HbA1c (glycosylated hemoglobin) >9% d) Platelet count <50,000/mm3 e) Hemoglobin <10.0g/dL"}
  • {"criterion_text":"- 17. Has a history of severe allergic or anaphylactic reaction or hypersensitivity to recombinant proteins or excipients in the investigational product"}
  • {"criterion_text":"- 18. Had major surgery within 60 days before the start of screening."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Mean change from baseline to Week 24 in PVR as measured by right heart catheterization (RHC) in participants with baseline PVR ≥3 Wood units who received TX000045 compared with those who received placebo","definition_or_measurement_approach":"PVR measured by right heart catheterization (RHC); endpoint is mean change from baseline to Week 24 in participants with baseline PVR ≥3 Wood units comparing TX000045 vs placebo."}
  • {"endpoint_text":"- In participants who received TX000045 compared with placebo, describe: • Incidence of adverse events (AEs), adverse events of special interest (AESIs), and serious adverse events (SAEs) • Incidence of clinically significant changes from baseline in laboratory assessments, 12-lead electrocardiogram (ECG), vital sign assessments, and physical examinations","definition_or_measurement_approach":"Safety endpoints reported as incidence counts/rates: AEs, AESIs, SAEs, and clinically significant changes in laboratory assessments, 12-lead ECG, vital signs, and physical examinations."}

Secondary endpoints

  • {"endpoint_text":"- Mean change from baseline to Week 24 in PVR as measured by right heart catheterization (RHC) in participants with baseline PVR ≥3 Wood units who received TX000045 compared with those who received placebo","definition_or_measurement_approach":"Same measurement as primary: PVR measured by RHC; mean change baseline to Week 24 comparing TX000045 vs placebo."}

Recruitment

Digital Remote Recruitment
Yes
Planned Sample Size
54
Recruitment Window Months
31
Consent Approach
Informed consent is obtained from adult participants (eligible ages 18–83). Subject information and ICF main adult documents are provided (L1 SIS and ICF Main Adult) and pregnancy-partner information documents are available where applicable. Consent materials and subject information are available in multiple languages (examples in the document list: English, Polish, Spanish, German, Bulgarian, Romanian, Portuguese, Latvian and others). No paediatric assent procedures are specified.

Methods

  • Digital ads – recruitment materials referenced as 'Digital Ads' (K2 documents).
  • Referral letters – 'Referral letter screened and randomized patient' and 'Referral letter randomized patient' materials available in multiple languages.
  • Patient-facing printed materials – patient study guide, patient study brochure, patient fact cards, patient study poster (K2 materials).
  • Informed Consent Flipbook – used as recruitment/support material.
  • Patient emergency/alert card and participant-facing materials (L2).
  • Referral fee/payment per randomized or screened-and-randomized patient (country-specific documents referenced).

Geography

Total Number Of Sites
32
Total Number Of Participants
201

Poland

Earliest CTIS Part Ii Submission Date
25-10-2024
Latest Decision Or Authorization Date
02-12-2024
Processing Time Days
38
Number Of Sites
6
Number Of Participants
25

Sites

Site Name
Uniwersytecki Szpital Kliniczny Nr 4 W Lublinie
Department Name
Klinika Kardiologii
Contact Person Name
Michał Tomaszewski
Contact Person Email
szpital@spsk4.lublin.pl
Site Name
Narodowy Instytut Kardiologii Stefana Kardynala Wyszynskiego Panstwowy Instytut Badawczy
Department Name
Klinika Wad Wrodzonych Serca
Principal Investigator Email
miroslaw.kowalski@ikard.pl
Contact Person Name
Mirosław Kowalski
Contact Person Email
miroslaw.kowalski@ikard.pl
Site Name
Wojewodzki Specjalistyczny Szpital Im Dr Wl Bieganskiego
Department Name
Oddział Kardiologiczny
Principal Investigator Email
radoslaw.krecki@scanmed.pl
Contact Person Name
Radosław Kręcki
Contact Person Email
radoslaw.krecki@scanmed.pl
Site Name
Krakowski Szpital Specjalistyczny Im. Sw. Jana Pawla II
Department Name
Oddział Kliniczny Chorób Serca i Naczyń z Pododdziałem Intensywnego Nadzoru Kardiologicznego
Principal Investigator Email
sekr_kard@szpitaljp2.krakow.pl
Contact Person Name
Grzegorz Kopeć
Contact Person Email
sekr_kard@szpitaljp2.krakow.pl
Site Name
Uniwersytecki Szpital Kliniczny W Bialymstoku
Department Name
Klinika Kardiologii i Chorób Wewnętrznych z OINK
Principal Investigator Email
kardio@uskwb.pl
Contact Person Name
Karol Kamiński
Contact Person Email
kardio@uskwb.pl
Site Name
Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu
Department Name
Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego we Wrocławiu
Principal Investigator Email
dr.piotr.gajewski@gmail.com
Contact Person Name
Piotr Gajewski
Contact Person Email
dr.piotr.gajewski@gmail.com

Belgium

Earliest CTIS Part Ii Submission Date
12-02-2025
Latest Decision Or Authorization Date
05-03-2025
Processing Time Days
21
Number Of Sites
2
Number Of Participants
10

Sites

Site Name
Ziekenhuis Oost Limburg
Department Name
Cardiology
Contact Person Name
Pieter Martens
Contact Person Email
pieter.martens2@zol.be
Site Name
Hopital Erasme
Department Name
Cardiology
Principal Investigator Email
celine.dewachter@hubruxelles.be
Contact Person Name
Céline Dewachter

Austria

Earliest CTIS Part Ii Submission Date
20-11-2025
Latest Decision Or Authorization Date
08-12-2025
Processing Time Days
18
Number Of Sites
1
Number Of Participants
10

Sites

Site Name
Klinik Favoriten 5. Medizinische Abteilung mit Kardiologie
Department Name
Kardiologie
Principal Investigator Name
Diana Bonderman
Principal Investigator Email
diana.bonderman@meduniwien.ac.at
Contact Person Name
Diana Bonderman

Romania

Earliest CTIS Part Ii Submission Date
26-11-2024
Latest Decision Or Authorization Date
19-02-2025
Processing Time Days
85
Number Of Sites
3
Number Of Participants
20

Sites

Site Name
Spitalul Clinic Judetean De Urgenta Targu Mures
Department Name
Cardiology
Principal Investigator Email
theodora.benedek@umfst.ro
Contact Person Name
Theodora Mariana Nicoleta Benedek
Contact Person Email
theodora.benedek@umfst.ro
Site Name
Spitalul Clinic Judetean De Urgenta Craiova
Department Name
Cardiology
Principal Investigator Name
Octavian Istratoaie
Principal Investigator Email
info@scju.ro
Contact Person Name
Octavian Istratoaie
Contact Person Email
info@scju.ro
Site Name
Institutul De Urgenta Pentru Boli Cardiovasculare Prof. Dr. C. C. Iliescu
Department Name
Cardiology 3
Principal Investigator Email
cardiologie.fundeni@umfcd.ro
Contact Person Name
Bogdan Alexandru Popescu
Contact Person Email
cardiologie.fundeni@umfcd.ro

Germany

Earliest CTIS Part Ii Submission Date
14-10-2024
Latest Decision Or Authorization Date
28-11-2024
Processing Time Days
45
Number Of Sites
3
Number Of Participants
12

Sites

Site Name
University Medical Center Hamburg-Eppendorf
Department Name
Cardiology
Principal Investigator Name
Christina Magnussen
Principal Investigator Email
c.magnussen@uke.de
Contact Person Name
Christina Magnussen
Contact Person Email
c.magnussen@uke.de
Site Name
Universitätsmedizin der Johannes Gutenberg Universität Mainz
Department Name
Zentrum für Kardiologie
Principal Investigator Email
kai_helge.schmidt@unimedizin-mainz.de
Contact Person Name
Kai Helge Schmidt
Site Name
Sana-Klinikum Remscheid GmbH
Department Name
Medizinische Klinik I Kardiologie, Angiologie, Pneumologie, Nephrologie, Intensivmedizin
Principal Investigator Name
Burkhard Sievers
Principal Investigator Email
burkhard.sievers@sana.de
Contact Person Name
Burkhard Sievers
Contact Person Email
burkhard.sievers@sana.de

Spain

Earliest CTIS Part Ii Submission Date
12-11-2024
Latest Decision Or Authorization Date
28-11-2024
Processing Time Days
16
Number Of Sites
9
Number Of Participants
24

Sites

Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Advanced Heart Faulire Unit
Principal Investigator Name
Susana Del Prado
Principal Investigator Email
docsusana10@gmail.com
Contact Person Name
Susana Del Prado
Contact Person Email
docsusana10@gmail.com
Site Name
Hospital Universitari Vall D Hebron
Department Name
Cardiology
Principal Investigator Name
Eduardo Ródenas Alesina
Principal Investigator Email
eduard.rodenas@valldhebron.cat
Contact Person Name
Eduardo Ródenas Alesina
Contact Person Email
eduard.rodenas@valldhebron.cat
Site Name
Hospital 9 De Octubre S.A.
Department Name
Cardiology
Principal Investigator Name
Ignacio Jose Sánchez Lázaro
Principal Investigator Email
ignacio.sanchez@vithas.es
Contact Person Name
Ignacio Jose Sánchez Lázaro
Contact Person Email
ignacio.sanchez@vithas.es
Site Name
Complexo Hospitalario Universitario De Santiago
Department Name
Cardiology
Principal Investigator Name
María Álvarez Barredo
Principal Investigator Email
mariaalvarezba@hotmail.com
Contact Person Name
María Álvarez Barredo
Contact Person Email
mariaalvarezba@hotmail.com
Site Name
Hospital Universitario De Toledo
Department Name
Pulmonary Hypertension Unit
Principal Investigator Name
María Lázaro Salvador
Principal Investigator Email
maria.lasal@gmail.com
Contact Person Name
María Lázaro Salvador
Contact Person Email
maria.lasal@gmail.com
Site Name
Hospital Costa Del Sol
Department Name
Cardiology
Principal Investigator Name
Rafael Bravo Marqués
Principal Investigator Email
rafabravomarques@gmail.com
Contact Person Name
Rafael Bravo Marqués
Contact Person Email
rafabravomarques@gmail.com
Site Name
Hospital Clinico Universitario De Valencia
Department Name
Cardiology
Principal Investigator Name
Julio Núñez
Principal Investigator Email
yulnunez@gmail.com
Contact Person Name
Julio Núñez
Contact Person Email
yulnunez@gmail.com
Site Name
Hospital 9 De Octubre S.A.
Department Name
Cardiology
Principal Investigator Name
Ignacio José Sánchez Lázaro
Principal Investigator Email
ignacio.sanchez@vithas.es
Contact Person Name
Ignacio José Sánchez Lázaro
Contact Person Email
ignacio.sanchez@vithas.es
Site Name
Hospital 9 De Octubre S.A.
Department Name
Cardiology
Contact Person Name
Ignacio José Sánchez Lázaro
Contact Person Email
ignacio.sanchez@vithas.es

Bulgaria

Earliest CTIS Part Ii Submission Date
18-11-2024
Latest Decision Or Authorization Date
28-11-2024
Processing Time Days
10
Number Of Sites
4
Number Of Participants
40

Sites

Site Name
University Multiprofile Hospital For Active Treatment Dr. Georgi Stranski EAD
Department Name
Clinic of Cardiology
Principal Investigator Name
Snezhanka Tisheva- Gospodinova
Principal Investigator Email
doctisheva@abv.bg
Contact Person Name
Snezhanka Tisheva- Gospodinova
Contact Person Email
doctisheva@abv.bg
Site Name
University Hospital St. Anna
Department Name
Clinic of Internal Diseases
Principal Investigator Name
Dimitar Raev
Principal Investigator Email
draevbg56@yahoo.com
Contact Person Name
Dimitar Raev
Contact Person Email
draevbg56@yahoo.com
Site Name
Acibadem City Clinic University Multiprofile Hospital For Active Treatment EOOD
Department Name
First Clinic of Cardiology
Principal Investigator Name
Ivo Petrov
Principal Investigator Email
petrovivo@hotmail.com
Contact Person Name
Ivo Petrov
Contact Person Email
petrovivo@hotmail.com
Site Name
University Multiprofile Hospital For Active Treatment Saint Georgi EAD
Department Name
Interventional Cardiology Department
Principal Investigator Name
Krasimir Dzhinsov
Principal Investigator Email
dr.krasimir.djinsov@gmail.com
Contact Person Name
Krasimir Dzhinsov
Contact Person Email
dr.krasimir.djinsov@gmail.com

Latvia

Earliest CTIS Part Ii Submission Date
14-03-2025
Latest Decision Or Authorization Date
20-03-2025
Processing Time Days
6
Number Of Sites
1
Number Of Participants
30

Sites

Site Name
Pauls Stradins Clinical University Hospital
Department Name
Cardiology
Principal Investigator Name
Andris Skride
Principal Investigator Email
info@healthtravellatvia.lv
Contact Person Name
Andris Skride
Contact Person Email
info@healthtravellatvia.lv

Portugal

Earliest CTIS Part Ii Submission Date
17-09-2025
Latest Decision Or Authorization Date
04-11-2025
Processing Time Days
48
Number Of Sites
3
Number Of Participants
30

Sites

Site Name
Unidade Local De Saude De Almada-Seixal E.P.E.
Department Name
Cardiology
Principal Investigator Name
Filipa Ferreira
Principal Investigator Email
filipa.ferreira@hgo.min-saude.pt
Contact Person Name
Filipa Ferreira
Site Name
Hospital De Santa Maria E.P.E.
Department Name
Cardiology
Principal Investigator Name
Rui Plácido
Principal Investigator Email
rui.placido@chln.min-saude.pt
Contact Person Name
Rui Plácido
Contact Person Email
rui.placido@chln.min-saude.pt
Site Name
Unidade Local De Saude De Santo Antonio E.P.E.
Department Name
Cardiology
Principal Investigator Name
Mário Santos
Contact Person Name
Mário Santos

Sponsor

Primary sponsor

Full Name
Tectonic Therapeutic Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Novotech Clinical Research (Cyprus) Limited
Responsibilities
Regulatory and clinical operations support (sponsorDuties codes: 1,10,11,12,5,6,8); contact Europe.regulatory@novotech-cro.com
Name
Sonic Clinical Trials Pty Limited
Responsibilities
Laboratory/clinical testing support (sponsorDuties: code 5); contact JThai@sonicclinicaltrials.com
Name
Voiant LLC
Responsibilities
Clinical operations support (sponsorDuties: code 5); contact smarroquin@voiantclinical.com
Name
Bioclinica Inc.
Responsibilities
ECHO and laboratory support (sponsorDuties: ECHO, code 5); contact Aesha.Vyas@clario.com
Name
Innovative Trials Limited
Responsibilities
Patient facing materials; contact emma.coulthard@innovativetrials.co.uk

Third parties

  • {"country":"Cyprus","full_name":"Novotech Clinical Research (Cyprus) Limited","duties_or_roles":"sponsorDuties codes: 1,10,11,12,5,6,8; contact email: Europe.regulatory@novotech-cro.com","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"sponsorDuties: code 15 (patients diary); contact email: kelie.taylor@clario.com","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Myonex Limited","duties_or_roles":"sponsorDuties codes: 14,5; contact email: DistributionUK@myonex.com","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Innovative Trials Limited","duties_or_roles":"sponsorDuties code 15 (Patient Facing Materials); contact email: emma.coulthard@innovativetrials.co.uk","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"sponsorDuties: code 15 (eCRF); contact email: helpdesk@mdsol.com","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"sponsorDuties: code 15 (IRT); contact email: helpdesk@mdsol.com","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Germany","full_name":"Myonex GmbH","duties_or_roles":"sponsorDuties: code 15 (Other - Storage of IMP, Distribution); contact email: sdittmann@myonex.com","organisation_type":"Pharmaceutical company"}
  • {"country":"Australia","full_name":"Sonic Clinical Trials Pty Limited","duties_or_roles":"sponsorDuties: code 5; contact email: JThai@sonicclinicaltrials.com","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Voiant LLC","duties_or_roles":"sponsorDuties: code 5; contact email: smarroquin@voiantclinical.com","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"The Doctors Laboratory Limited","duties_or_roles":"sponsorDuties: code 4; contact email: JThai@sonicclinicaltrials.com","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"sponsorDuties: code 15 (ECHO), code 5; contact email: Aesha.Vyas@clario.com","organisation_type":"Laboratory/Research/Testing facility"}

Investigational products

Investigational Product Name
TX000045
Active Substance
TX000045
Modality
Peptide/protein/enzyme
Routes Of Administration
SUBCUTANEOUS
Route
SUBCUTANEOUS
Authorisation Status
MIA number IMP12234/00001
Maximum Dose
300 mg (maxDailyDoseAmount: 300 mg)

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