Clinical trial • Phase III • Oncology

Tucatinib for HER2-positive breast cancer | Locally advanced breast cancer | Metastatic breast cancer

Phase III trial of Tucatinib for HER2-positive breast cancer | Locally advanced breast cancer | Metastatic breast cancer.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
HER2-positive breast cancer | Locally advanced breast cancer | Metastatic breast cancer
Trial Stage
Phase III
Drug Modality
Small molecule | ADC

Key dates

Initial CTIS Submission Date
17-06-2024
First CTIS Authorization Date
18-07-2024

Trial design

Randomised, control arm: placebo given po bid; t-dm1 3.6 mg/kg iv every 21 days. experimental arm: tucatinib 300 mg po bid; t-dm1 3.6 mg/kg iv every 21 days. Phase III trial across 36 sites in Sweden, Belgium, Spain and others.

Randomised
Yes
Comparator
Control arm: Placebo given PO BID; T-DM1 3.6 mg/kg IV every 21 days. Experimental arm: Tucatinib 300 mg PO BID; T-DM1 3.6 mg/kg IV every 21 days.
Target Sample Size
466

Eligibility

Recruits 466 Vulnerable population selected. Informed consent will be obtained using the provided Subject Information and Informed Consent Forms (L1_SIS and ICF) documents listed for each Member State. No detailed information on assent or specific consent-age handling is available in the provided record..

Vulnerable Population
Vulnerable population selected. Informed consent will be obtained using the provided Subject Information and Informed Consent Forms (L1_SIS and ICF) documents listed for each Member State. No detailed information on assent or specific consent-age handling is available in the provided record.

Inclusion criteria

  • {"criterion_text":"- Histologically confirmed HER2+ breast carcinoma as determined by a sponsor-designated central laboratory\n- History of prior treatment with a taxane and trastuzumab in any setting, separately or in combination\n- Have progression of unresectable locally advanced/metastatic breast cancer after last systemic therapy, or be intolerant of last systemic therapy\n- Measurable or non-measurable disease assessable by RECIST v1.1\n- ECOG performance status score of 0 or 1\n- CNS Inclusion - Based on screening contrast brain magnetic resonance imaging (MRI), participants must have at least one of the following: (a) No evidence of brain metastases (b) Untreated brain metastases not needing immediate local therapy (c) Previously treated brain metastases 1.\tBrain metastases previously treated with local therapy may either be stable since treatment or may have progressed since prior local CNS therapy, provided that there is no clinical indication for immediate re-treatment with local therapy 2.\tParticipants treated with CNS local therapy for newly identified lesions or previously treated and progressing lesions may be eligible to enroll if all of the following criteria are met: (i) Time since SRS is at least 7 days prior to first dose of study treatment, time since WBRT is at least 14 days prior to first dose, or time since surgical resection is at least 28 days. (ii) Other sites of evaluable disease are present 3.\tRelevant records of any CNS treatment must be available to allow for classification of target and non-target lesions"}

Exclusion criteria

  • {"criterion_text":"- Prior treatment with tucatinib, afatinib, trastuzumab deruxtecan (DS-8201a), or any other investigational anti-HER2, anti-EGFR, or HER2 TKI agent. Prior treatment with lapatinib or neratinib within 12 months of starting study treatment (except in cases where they were given for ≤21 days and was discontinued for reasons other than disease progression or severe toxicity). Prior treatment with pyrotinib for recurrent of mBC (except in cases where pyrotinib was given for ≤21 days and was discontinued for reasons other than disease progression or severe toxicity).\n- CNS Exclusion - Based on screening contrast brain magnetic resonance imaging (MRI), participants must not have any of the following: 1.\tAny untreated brain lesions >2 cm in size 2.\tOngoing use of corticosteroids for control of symptoms of brain metastases at a total daily dose of >2 mg of dexamethasone (or equivalent). 3.\tAny brain lesion thought to require immediate local therapy 4.\tKnown or concurrent leptomeningeal disease as documented by the investigator 5.\tPoorly controlled generalized or complex partial seizures"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- PFS per RECIST v1.1, as determined by investigator assessment","definition_or_measurement_approach":"Determined by investigator assessment per RECIST v1.1"}

Secondary endpoints

  • {"endpoint_text":"- OS\n- PFS.BM per RECIST v1.1, as determined by investigator assessment\n- ORR per RECIST v1.1, by investigator assessment\n- OS.BM","definition_or_measurement_approach":"OS: overall survival. PFS.BM and ORR: assessed by investigator per RECIST v1.1. OS.BM: overall survival in subjects with brain metastases at baseline."}

Recruitment

Planned Sample Size
466
Recruitment Window Months
74
Consent Approach
Informed consent obtained from subjects using country-specific Subject Information and Informed Consent Forms (L1_SIS and ICF) as listed in the documents (multiple country/language versions available: EN, FR, NL, IT, DE, DK, etc.). The record does not provide further details on assent or age-specific consent procedures.

Geography

Total Number Of Sites
36
Total Number Of Participants
101

Sweden

Latest Decision Or Authorization Date
22-07-2024
Number Of Sites
2
Number Of Participants
3

Sites

Site Name
Region Joenkoepings Laen
Department Name
Department of Oncology
Principal Investigator Name
Maria Ekholm
Principal Investigator Email
maria.ekholm@rjl.se
Contact Person Name
Maria Ekholm
Contact Person Email
maria.ekholm@rjl.se
Site Name
Sahlgrenska University Hospital-Vaestra Goetalandsregionen
Department Name
Institutionen For Kliniska Vetenskaper (Institute Of Clinical Sciences)
Principal Investigator Name
Barbro Linderholm
Principal Investigator Email
barbro.linderholm@oncology.gu.se
Contact Person Name
Barbro Linderholm

Belgium

Latest Decision Or Authorization Date
22-07-2024
Number Of Sites
6
Number Of Participants
16

Sites

Site Name
Centre Hospitalier Universitaire Dinant Godinne Sainte-Elisabeth-UCL-Namur
Department Name
Service d'oncologie
Principal Investigator Name
Donatienne Taylor
Principal Investigator Email
donatienne.taylor@uclouvain.be
Contact Person Name
Donatienne Taylor
Contact Person Email
donatienne.taylor@uclouvain.be
Site Name
Antwerp University Hospital
Department Name
Multidisciplinair Oncologisch Centrum Antwerpen
Principal Investigator Name
Konstantinos Papadimitriou
Principal Investigator Email
konstantinos.papadimitriou@uza.be
Contact Person Name
Konstantinos Papadimitriou
Site Name
Algemeen Ziekenhuis Groeninge
Department Name
Kankercentrum: medische oncologie
Principal Investigator Name
Laure Nuytemans
Principal Investigator Email
laure.nuytemans@azgroeninge.be
Contact Person Name
Laure Nuytemans
Contact Person Email
laure.nuytemans@azgroeninge.be
Site Name
Centre hospitalier universitaire de Liege
Department Name
Centre Multidisciplinaire d’Onocologie Médicale
Principal Investigator Name
Andree Rorive
Principal Investigator Email
andree.rorive@chuliege.be
Contact Person Name
Andree Rorive
Contact Person Email
andree.rorive@chuliege.be
Site Name
Institut Jules Bordet
Department Name
Medical oncology department
Principal Investigator Name
Andrea Gombos
Principal Investigator Email
andrea.gombos@bordet.be
Contact Person Name
Andrea Gombos
Contact Person Email
andrea.gombos@bordet.be
Site Name
UZ Leuven
Department Name
Algemene medische oncologie
Principal Investigator Name
Hans Wildiers
Principal Investigator Email
hans.wildiers@uzleuven.be
Contact Person Name
Hans Wildiers
Contact Person Email
hans.wildiers@uzleuven.be

Spain

Latest Decision Or Authorization Date
18-07-2024
Number Of Sites
8
Number Of Participants
25

Sites

Site Name
University Hospital Son Espases
Department Name
Servicio de Oncologia
Principal Investigator Name
Neus Ferrer Tur
Principal Investigator Email
nieves.ferrer@ssib.es
Contact Person Name
Neus Ferrer Tur
Contact Person Email
nieves.ferrer@ssib.es
Site Name
Hospital Clinico Universitario De Valencia
Department Name
Materno Infantil - Servicio Oncologia
Principal Investigator Name
Begona Bermejo
Principal Investigator Email
begobermejo@gmail.com
Contact Person Name
Begona Bermejo
Contact Person Email
begobermejo@gmail.com
Site Name
Hospital Universitari Vall D Hebron
Department Name
Head, Breast Cancer and Melanoma Unit
Principal Investigator Name
Cristina Saura Manich
Principal Investigator Email
csaura@vhio.net
Contact Person Name
Cristina Saura Manich
Contact Person Email
csaura@vhio.net
Site Name
Hospital Unviersitario Miguel Servet
Department Name
Medical Oncology
Principal Investigator Name
Antonio Anton Torres
Principal Investigator Email
aantont@gmail.com
Contact Person Name
Antonio Anton Torres
Contact Person Email
aantont@gmail.com
Site Name
Hospital Clinico San Carlos
Department Name
Servicio de Oncologia Medica
Principal Investigator Name
Jose Garcia Saenz
Principal Investigator Email
jgsaenz@salud.madrid.org
Contact Person Name
Jose Garcia Saenz
Contact Person Email
jgsaenz@salud.madrid.org
Site Name
Consorci Sanitari Integral
Department Name
Hospital Moises Broggi - Servicio Oncologia
Principal Investigator Name
Rafael Villanueva Vazquez
Principal Investigator Email
ravillanueva@iconcologia.net
Contact Person Name
Rafael Villanueva Vazquez
Contact Person Email
ravillanueva@iconcologia.net
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Servicio Oncologia
Principal Investigator Name
Manuel Ruiz Borrego
Principal Investigator Email
ruizsabater@gmail.com
Contact Person Name
Manuel Ruiz Borrego
Contact Person Email
ruizsabater@gmail.com
Site Name
Hospital Universitario Hm Sanchinarro
Department Name
Centro Integral Oncologico Clara Campal
Principal Investigator Name
Eva Ciruelos Gil
Principal Investigator Email
eva.ciruelos@gmail.com
Contact Person Name
Eva Ciruelos Gil
Contact Person Email
eva.ciruelos@gmail.com

Denmark

Latest Decision Or Authorization Date
21-07-2024
Number Of Sites
2
Number Of Participants
3

Sites

Site Name
Region Hovedstaden
Department Name
Deptartment of Oncology
Principal Investigator Name
Eva Harder Brix
Principal Investigator Email
eva.harder.brix@regionh.dk
Contact Person Name
Eva Harder Brix
Contact Person Email
eva.harder.brix@regionh.dk
Site Name
Lillebaelt Hospital
Department Name
Deptartment of Oncology
Principal Investigator Name
Else Iversen
Principal Investigator Email
else.iversen@rsyd.dk
Contact Person Name
Else Iversen
Contact Person Email
else.iversen@rsyd.dk

Germany

Latest Decision Or Authorization Date
22-07-2024
Number Of Sites
4
Number Of Participants
6

Sites

Site Name
Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
Department Name
III. Medizinische Klinik und Poliklinik - Haematologie und Medizinische Onkologie
Principal Investigator Name
Marcus Schmidt
Principal Investigator Email
marcus.schmidt@unimedizin-mainz.de
Contact Person Name
Marcus Schmidt
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Klinik fur Innere Medizin II, Hamatologie und internistische Onkologie
Principal Investigator Name
Marion Van Mackelenbergh
Principal Investigator Email
marion.vanmackelenbergh@uksh.de
Contact Person Name
Marion Van Mackelenbergh
Site Name
Institut Fuer Versorgungsforschung In Der Onkologie GbR
Department Name
InVO- Institut fur Versorgungsforschung in der Onkologie GbR
Principal Investigator Name
Rudolf Weide
Principal Investigator Email
weide@invo-koblenz.de
Contact Person Name
Rudolf Weide
Contact Person Email
weide@invo-koblenz.de
Site Name
Klinikum rechts der Isar der TU Muenchen AöR
Department Name
Klinik und Poliklinik für Frauenheilkunde
Principal Investigator Name
Franziska Kotzur
Principal Investigator Email
franziska.kotzur@mri.tum.de
Contact Person Name
Franziska Kotzur
Contact Person Email
franziska.kotzur@mri.tum.de

Italy

Latest Decision Or Authorization Date
05-08-2024
Number Of Sites
1
Number Of Participants
5

Sites

Site Name
Istituto Europeo Di Oncologia S.r.l.
Department Name
Divisione di Senologia Medica
Principal Investigator Name
Marco Colleoni
Principal Investigator Email
marco.colleoni@ieo.it
Contact Person Name
Marco Colleoni
Contact Person Email
marco.colleoni@ieo.it

Netherlands

Latest Decision Or Authorization Date
05-08-2024
Number Of Sites
3
Number Of Participants
4

Sites

Site Name
Amphia Hospital
Department Name
Oncology Center: Breast Cancer
Principal Investigator Name
Joan Heijns
Principal Investigator Email
JHeijns@amphia.nl
Contact Person Name
Joan Heijns
Contact Person Email
JHeijns@amphia.nl
Site Name
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Department Name
Internal Oncology
Principal Investigator Name
Agnes Jager
Principal Investigator Email
a.jager@erasmusmc.nl
Contact Person Name
Agnes Jager
Contact Person Email
a.jager@erasmusmc.nl
Site Name
Het Nederlands Kanker Instituut-Antoni van Leeuwenhoek Ziekenhuis Stichting
Department Name
Department of Medical
Principal Investigator Name
Gabe Sonke
Principal Investigator Email
g.sonke@nki.nl
Contact Person Name
Gabe Sonke
Contact Person Email
g.sonke@nki.nl

France

Latest Decision Or Authorization Date
13-08-2024
Number Of Sites
10
Number Of Participants
39

Sites

Site Name
Oncopole Claudius Regaud
Department Name
Oncologie Medicale
Principal Investigator Name
Mony Ung
Principal Investigator Email
ung.mony@iuct-oncopole.fr
Contact Person Name
Mony Ung
Contact Person Email
ung.mony@iuct-oncopole.fr
Site Name
Centre Francois Baclesse
Department Name
Service Oncologie
Principal Investigator Name
George Emile
Principal Investigator Email
g.emile@baclesse.unicancer.fr
Contact Person Name
George Emile
Contact Person Email
g.emile@baclesse.unicancer.fr
Site Name
Institut Curie
Department Name
Oncologie Medicale
Principal Investigator Name
Delphine Loirat
Principal Investigator Email
delphine.loirat@curie.fr
Contact Person Name
Delphine Loirat
Contact Person Email
delphine.loirat@curie.fr
Site Name
Clinique Victor Hugo
Department Name
Oncologie Medicale
Principal Investigator Name
Alice Delafoy
Principal Investigator Email
essaisdelafoy@ilcgroupe.fr
Contact Person Name
Alice Delafoy
Contact Person Email
essaisdelafoy@ilcgroupe.fr
Site Name
CHU Besancon
Department Name
Service Oncologie
Principal Investigator Name
Elsa Curtit
Principal Investigator Email
elsa.curtit@univ-fcomte.fr
Contact Person Name
Elsa Curtit
Contact Person Email
elsa.curtit@univ-fcomte.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Hematologie et Therapie Cellulaire
Principal Investigator Name
Marie-Agnes By
Principal Investigator Email
ma.by@chu-tours.fr
Contact Person Name
Marie-Agnes By
Contact Person Email
ma.by@chu-tours.fr
Site Name
Centre Leon Berard
Department Name
Cancerologie Medicale
Principal Investigator Name
Thomas Bachelot
Principal Investigator Email
thomas.bachelot@lyon.unicancer.fr
Contact Person Name
Thomas Bachelot
Site Name
Centr Georges Francois Leclerc
Department Name
Departement d'Oncologie Medicale
Principal Investigator Name
Isabelle Desmoulins
Principal Investigator Email
IDesmoulins@cgfl.fr
Contact Person Name
Isabelle Desmoulins
Contact Person Email
IDesmoulins@cgfl.fr
Site Name
Institut Paoli Calmettes
Department Name
Service Oncologie
Principal Investigator Name
Frederic Viret
Principal Investigator Email
viretf@ipc.unicancer.fr
Contact Person Name
Frederic Viret
Contact Person Email
viretf@ipc.unicancer.fr
Site Name
Centre Regional Lutte Contre Le Cancer
Department Name
Oncologie Medicale
Principal Investigator Name
Thierry Petit
Principal Investigator Email
t.petit@icans.eu
Contact Person Name
Thierry Petit
Contact Person Email
t.petit@icans.eu

Sponsor

Primary sponsor

Full Name
Seagen Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Parexel International (IRL) Limited
Responsibilities
Monitoring, Medical monitoring and Pharmacovigilance
Name
Icon Clinical Research Limited
Responsibilities
Sample management (receipt, shipment and storage)
Name
Icon Laboratory Services Inc.
Responsibilities
Central lab (kit build, sample management, storage and collection of local lab data)
Name
Clario
Responsibilities
Medical image analysis/ review - Primary/surrogate endpoint test

Third parties

  • {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"Monitoring, Medical monitoring and Pharmacovigilance; (contact: ichin.chung@parexel.com)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Scout Clinical","duties_or_roles":"Subject reimbursement; (contact: abiola.ojuade@scoutclinical.com)","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"France","full_name":"Novasco","duties_or_roles":"Subject Reimbursement; (contact: c.maudet@novasco.fr)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Subject Reimbursement; (contact: samantha.moyer@greenphire.com)","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Suvoda LLC","duties_or_roles":"IVRS – treatment randomisation; (contact: ssannicolas@suvoda.com)","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"Data platform/vendor (sponsor duty code listed); (contact: rachel.johnson@3ds.com)","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Clario","duties_or_roles":"Medical image analysis/ review - X-ray, MRI, ultrasound, etc.; (contact: jahnavi.vyas@clario.com)","organisation_type":"Health care"}
  • {"country":"United States","full_name":"Icon Laboratory Services Inc.","duties_or_roles":"Central lab (Kit build, sample management, storage and collection of local lab data); (contact: Benjamin.Haibach@iconplc.com)","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"Sample management (receipt, shipment and storage); (contact: Charl.Schoeman@iconplc.com)","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
TUKYSA 150 mg film-coated tablets
Active Substance
Tucatinib
Modality
Small molecule
Routes Of Administration
ORAL
Route
oral
Authorisation Status
Marketing authorisation (EU) PRD8771193 / EU/1/20/1526/002
Starting Dose
300 mg PO BID (trial experimental arm)
Dose Levels
150 mg (available tablet strength); trial dosing uses 300 mg PO BID (two 150 mg tablets BID)
Frequency
BID
Maximum Dose
600 mg/day (product maxDailyDoseAmount 600 mg)
Investigational Product Name
TUKYSA 50 mg film-coated tablets
Active Substance
Tucatinib
Modality
Small molecule
Routes Of Administration
ORAL
Route
oral
Authorisation Status
Marketing authorisation (EU) PRD8771172 / EU/1/20/1526/001
Starting Dose
300 mg PO BID (trial experimental arm)
Dose Levels
50 mg (available tablet strength); trial dosing uses 300 mg PO BID
Frequency
BID
Maximum Dose
600 mg/day
Investigational Product Name
Kadcyla 160 mg powder for concentrate for solution for infusion.
Active Substance
Trastuzumab emtansine (T-DM1)
Modality
ADC
Routes Of Administration
INTRAVENOUS INFUSION
Route
intravenous infusion
Authorisation Status
Marketing authorisation (EU) PRD974895 / EU/1/13/885/002
Starting Dose
3.6 mg/kg IV every 21 days (per arm description)
Dose Levels
3.6 mg/kg IV q21 days
Frequency
Every 21 days
Maximum Dose
3.6 mg/kg per administration
Investigational Product Name
Tucatinib 50mg placebo tablets / Tucatinib 150mg placebo tablets
Active Substance
N/A (placebo)
Modality
Other
Starting Dose
Placebo given PO BID in control arm
Dose Levels
Placebo matching 50 mg and 150 mg tablet forms
Frequency
BID
Combination Treatment
Yes

Related trials

Other published trials that may interest you.