Clinical trial • Phase III • Oncology

TRASTUZUMAB DERUXTECAN for HER2-positive metastatic breast cancer | Metastatic breast cancer

Phase III trial of TRASTUZUMAB DERUXTECAN for HER2-positive metastatic breast cancer | Metastatic breast cancer.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
HER2-positive metastatic breast cancer | Metastatic breast cancer
Trial Stage
Phase III
Drug Modality
ADC

Key dates

Initial CTIS Submission Date
26-03-2024
First CTIS Authorization Date
23-05-2024

Trial design

Randomised, open-label, test: ds-8201a (trastuzumab deruxtecan) — intravenous infusion; maximum total dose amount listed 5.4 mg/kg. comparator: ado-trastuzumab emtansine (t-dm1) (kadcyla 100 mg powder for concentrate for solution for infusion) — intravenous infusion; maximum total dose amount listed 3.6 mg/kg.-controlled Phase III trial in Belgium, France, Italy and others.

Randomised
Yes
Open Label
Yes
Comparator
Test: DS-8201a (trastuzumab deruxtecan) — intravenous infusion; maximum total dose amount listed 5.4 mg/Kg. Comparator: ado-trastuzumab emtansine (T-DM1) (Kadcyla 100 mg powder for concentrate for solution for infusion) — intravenous infusion; maximum total dose amount listed 3.6 mg/Kg.
Target Sample Size
177

Eligibility

Recruits 177 Vulnerable population selected. Study enrols adults ≥18 years; "Please follow local regulatory requirements if the legal age of consent for study participation is >18 y old." No specific assent procedures for minors are described in the available documents..

Pregnancy Exclusion
Female subjects of reproductive/childbearing potential must agree to use a highly effective form of contraception or avoid intercourse during and upon completion of the study and for at least 7 mo after the last dose of trastuzumab deruxtecan and 7 mo after the last dose of T-DM1. Male subjects must agree to inform all potential female partners that they are participating in a clinical trial of a drug that may cause birth defects. Male subjects must also agree to either avoid intercourse or that they and/or any female partners of reproductive / childbearing potential will use a highly effective form of contraception during and upon completion of the study and for at least 4.5 mo after the last dose of trastuzumab deruxtecan or 4 mo after the last dose of T-DM1.
Vulnerable Population
Vulnerable population selected. Study enrols adults ≥18 years; "Please follow local regulatory requirements if the legal age of consent for study participation is >18 y old." No specific assent procedures for minors are described in the available documents.

Inclusion criteria

  • {"criterion_text":"- Adults ≥18 years old. (Please follow local regulatory requirements if the legal age of consent for study participation is >18 y old.)\n- Pathologically documented breast cancer that:\n- - is unresectable or metastatic\n- - has confirmed HER2 positive expression as determined according to American Society of Clinical Oncology – College of American Pathologists guidelines evaluated at a central laboratory.\n- - was previously treated with trastuzumab and taxane in the advanced/metastatic setting or progressed within 6 mo after neoadjuvant or adjuvant treatment involving a regimen including trastuzumab and taxane.\n- Documented radiologic progression (during or after most recent treatment or within 6 mo after completing adjuvant therapy).\n- Subjects must be HER2 positive as confirmed by central laboratory assessment of most recent tumor tissue sample available.\n- Female subjects of reproductive/childbearing potential must agree to use a highly effective form of contraception or avoid intercourse during and upon completion of the study and for at least 7 mo after the last dose of trastuzumab deruxtecan and 7 mo after the last dose of T-DM1. Male subjects must agree to inform all potential female partners that they are participating in a clinical trial of a drug that may cause birth defects. Male subjects must also agree to either avoid intercourse or that they and/or any female partners of reproductive / childbearing potential will use a highly effective form of contraception during and upon completion of the study and for at least 4.5 mo after the last dose of trastuzumab deruxtecan or 4 mo after the last dose of T-DM1.\n- Adequate renal function, defined as:\n- - Creatinine clearance ≥ 30 mL/min, as calculated using the Cockcroft-Gault equation\n- Adequate hepatic function, defined as:\n- - Total bilirubin ≤ 1.5 × upper limit of normal (ULN) if no liver metastases or < 3 × ULN in the presence of documented Gilbert's Syndrome (unconjugated hyperbilirubinemia) or liver metastases at baseline and\n- - Aspartate aminotransferase (AST)/alanine aminotransferase (ALT) ≤5 × ULN."}

Exclusion criteria

  • {"criterion_text":"- Prior treatment with an anti-HER2 ADC (such as T-DM1) in the metastatic setting. Prior treatment in the adjuvant/neo-adjuvant setting would be allowed if progression of disease did not occur within 12 mo of end of adjuvant therapy.\n- Uncontrolled or significant cardiovascular disease, including any of the following:\n- - History of myocardial infarction within 6 mo before randomization\n- - History of symptomatic congestive heart failure (New York Heart Association Class II to IV)\n- - Troponin levels consistent with myocardial infarction as defined according to the manufacturer within 28 d prior to randomization\n- - Corrected QT interval prolongation to > 470 ms (females) or > 450 ms (male) based on average of Screening triplicate 12 lead electrocardiogram (ECG)\n- - Left ventricular ejection fraction (LVEF) < 50% within 28 d prior to randomization\n- Has a history of (noninfectious) interstitial lung disease (ILD)/pneumonitis that required steroids, has current ILD/pneumonitis, or where suspected ILD/pneumonitis cannot be ruled out by imaging at Screening.\n- Spinal cord compression or clinically active central nervous system (CNS) metastases, defined as untreated and symptomatic, or requiring therapy with corticosteroids or anticonvulsants to control associated symptoms.\n- - Subjects with clinically inactive brain metastases may be included in the study.\n- - Subjects with treated brain metastases that are no longer symptomatic and who require no treatment with corticosteroids or anticonvulsants may be included in the study if they have recovered from the acute toxic effect of radiotherapy. A minimum of 2 weeks must have elapsed between the end of whole brain radiotherapy and study enrollment.\n- Prior participation in a study involving an antibody drug conjugate (ADC) produced by Daiichi Sankyo."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- The primary efficacy endpoint is PFS as determined by blinded independent central review (BICR).","definition_or_measurement_approach":"PFS measured as determined by blinded independent central review (BICR)."}

Secondary endpoints

  • {"endpoint_text":"- The key secondary efficacy endpoint is OS.","definition_or_measurement_approach":"Overall survival (OS)."}

Other endpoints

  • {"endpoint_text":"- To evaluate efficacy of trastuzumab deruxtecan compared to T-DM1 on: Confirmed objective response rate (ORR);\n- To evaluate efficacy of trastuzumab deruxtecan compared to T-DM1 on: Duration of response (DoR);\n- To further determine PK of trastuzumab deruxtecan;\n- To further evaluate safety of trastuzumab deruxtecan compared to TDM1;\n- To evaluate Health Economic and Outcomes Research (HEOR) endpoints for trastuzumab deruxtecan compared to T-DM1.","definition_or_measurement_approach":"ORR and DoR as efficacy measures (confirmed objective response rate; duration of response). PK assessed by pharmacokinetic sampling and analysis. Safety assessed by adverse event reporting and laboratory monitoring. HEOR endpoints assessed per health economic/outcomes measures. (Descriptions are from secondary objectives; detailed measurement methods not provided in the available data.)"}

Recruitment

Planned Sample Size
177
Recruitment Window Months
87
Consent Approach
Informed consent provided by adult participants (≥18 years); follow local regulatory requirements if legal age of consent is >18. Informed consent forms and patient information documents available in multiple language versions (documents list includes English, French, Spanish, Italian and regional BE-FR/BE-NL versions). No specific remote consent or assent procedures for minors are described in the available documents.

Geography

Total Number Of Sites
36
Total Number Of Participants
63

Belgium

Earliest CTIS Part Ii Submission Date
02-02-2024
Latest Decision Or Authorization Date
11-03-2025
Processing Time Days
403
Number Of Sites
4
Number Of Participants
5

Sites

Site Name
Institut Jules Bordet
Department Name
Oncology
Contact Person Name
Andrea Gombos
Contact Person Email
andrea.gombos@hubruxelles.be
Site Name
UZ Leuven
Department Name
Oncology
Contact Person Name
Hans Wildiers
Contact Person Email
hans.wildiers@uzleuven.be
Site Name
Antwerp University Hospital
Department Name
Oncology
Contact Person Name
Selvilay Altintas
Contact Person Email
sevilay.altintas@uza.be
Site Name
UZ Brussel
Department Name
Oncology
Contact Person Name
Christel Fontaire
Contact Person Email
christel.fontaine@uzbrussel.be

France

Earliest CTIS Part Ii Submission Date
02-02-2024
Latest Decision Or Authorization Date
14-03-2025
Processing Time Days
406
Number Of Sites
11
Number Of Participants
23

Sites

Site Name
Institut Curie
Department Name
Medical Oncology
Contact Person Name
Jean-Yves Pierga
Contact Person Email
jean-yves.pierga@curie.fr
Site Name
Institut Regional Du Cancer De Montpellier
Department Name
Medical Oncology Service
Contact Person Name
William Jacot
Contact Person Email
William.Jacot@icm.unicancer.fr
Site Name
Institut Curie
Department Name
Medical Oncology department
Contact Person Name
Jean-Yves Pierga
Contact Person Email
jean-yves.pierga@curie.fr
Site Name
Institut De Cancerologie De L Ouest
Department Name
Medical Oncology Service
Contact Person Name
Jean-Sebastien Frenel
Site Name
Clinique Victor Hugo
Department Name
Onco-radiotherapy
Contact Person Name
Sophie Roche
Contact Person Email
essaisroche@ilcgroupe.fr
Site Name
Institut Sainte Catherine
Department Name
Oncology
Contact Person Name
Julien Grenier
Contact Person Email
j.grenier@isc84.org
Site Name
Centre Leon Berard
Department Name
Medical Oncology department
Contact Person Name
Thomas Bachelot
Site Name
Centre Francois Baclesse
Department Name
Gynecological pathologies
Contact Person Name
Christelle Levy
Contact Person Email
c.levy@baclesse.unicancer.fr
Site Name
Hopital Tenon
Department Name
Medical Oncology department
Contact Person Name
Joseph Gligorov
Contact Person Email
joseph.gligorov@aphp.fr
Site Name
Centre Hospitalier Regional De Marseille
Department Name
Multidisciplinary Oncology and Therapeutic Innovations Department
Contact Person Name
Marjorie Baciuchka-Palmaro
Contact Person Email
marjorie.baciuchka@ap-hm.fr
Site Name
Institut Gustave Roussy
Department Name
Medical Oncology
Contact Person Name
Fabrice André
Contact Person Email
fabrice.andre@gustaveroussy.fr

Italy

Earliest CTIS Part Ii Submission Date
02-02-2024
Latest Decision Or Authorization Date
13-03-2025
Processing Time Days
405
Number Of Sites
9
Number Of Participants
19

Sites

Site Name
Ospedale San Raffaele S.r.l.
Department Name
Oncology
Contact Person Name
Giampaolo Bianchini
Contact Person Email
bianchini.giampaolo@hsr.it
Site Name
Azienda Socio Sanitaria Territoriale Papa Giovanni XXIII
Department Name
Oncology
Contact Person Name
Elena Rota Caremoli
Contact Person Email
ecrota@hpg23.it
Site Name
Azienda Ospedaliero Universitaria Di Modena
Department Name
Oncology
Contact Person Name
Federico Piacentini
Contact Person Email
federico.piacentini@unimore.it
Site Name
Azienda Ospedaliero Universitaria Parma
Department Name
Oncology
Contact Person Name
Daniela Boggiani
Contact Person Email
boggiani@ao.pr.it
Site Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale
Department Name
Oncology
Contact Person Name
Michelino De Laurentiis
Contact Person Email
delauren@breastunit.org
Site Name
Humanitas Research Hospital
Department Name
Oncology and Hematology
Contact Person Name
Armando Santoro
Site Name
Centro Di Riferimento Oncologico Di Aviano
Department Name
Oncology
Contact Person Name
Fabio Puglisi
Contact Person Email
fabio.puglisi@cro.it
Site Name
Fondazione IRCCS San Gerardo Dei Tintori
Department Name
Oncology
Contact Person Name
Marina Elena Cazzaniga
Site Name
IRCCS Centro di Riferimento Oncologico (other listed site)
Department Name
Oncology

Spain

Earliest CTIS Part Ii Submission Date
02-02-2024
Latest Decision Or Authorization Date
11-03-2025
Processing Time Days
403
Number Of Sites
12
Number Of Participants
16

Sites

Site Name
Hospital Quironsalud Barcelona
Department Name
Oncology
Contact Person Name
Fabricio Racca Bussano
Contact Person Email
fracca@nextoncology.eu
Site Name
Institut Catala D'oncologia
Department Name
Oncology
Contact Person Name
Juan Miguel Gil Gil
Contact Person Email
mgilgil@iconcologia.net
Site Name
Hospital Universitari Vall D Hebron
Department Name
Oncology
Contact Person Name
Cristina Saura Manich
Contact Person Email
cristina.saura@vallhebron.cat
Site Name
Hospital Clinico San Carlos
Department Name
Oncology
Contact Person Name
Jose Angel Garcia Saenz
Contact Person Email
jgsaenz@salud.madrid.org
Site Name
Hospital Universitario De Canarias
Department Name
Oncology
Contact Person Name
Josefina Cruz Jurado
Contact Person Email
jcruzjurado@gmail.com
Site Name
Hospital Universitario 12 De Octubre
Department Name
Oncology
Contact Person Name
Eva Ciruelos Gil
Contact Person Email
eva.ciruelos@gmail.com
Site Name
Hospital Universitario Virgen De La Macarena
Department Name
Oncology
Contact Person Name
Esteban Nogales Fernández
Contact Person Email
esteban.nogales@gmail.com
Site Name
Hospital Clinic De Barcelona
Department Name
Oncology
Contact Person Name
Aleix Prat
Contact Person Email
alprat@clinic.cat
Site Name
Hospital Universitario De Badajoz
Department Name
Oncology
Contact Person Name
Marta González Cordero
Contact Person Email
martagcordero@gmail.com
Site Name
Hospital General Universitario Gregorio Maranon
Department Name
Oncology
Contact Person Name
Sara Lopez-Tarruella Cobo
Contact Person Email
sltc21@hotmail.com
Site Name
Complexo Hospitalario Universitario A Coruna
Department Name
Oncology
Contact Person Name
Silvia Antolin Novoa
Contact Person Email
silvia.antolin.novoa@sergas.es
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Oncology
Contact Person Name
Francisco Javier Salvador Bofill
Contact Person Email
jsalvad2002@yahoo.es

Sponsor

Primary sponsor

Full Name
Daiichi Sankyo Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Icon Laboratory Services Inc.
Responsibilities
Manage local lab reports for safety labs
Name
PPD Development L.P.
Name
IQVIA Limited
Name
Fortrea Inc.
Name
Guardant Health Inc.
Name
Labcorp Central Laboratory Services SARL
Name
Labcorp Central Laboratory Services LP
Name
Almac Clinical Technologies LLC
Name
Azenta US Inc.
Responsibilities
Long-term storage of biosamples

Third parties

  • {"country":"United States","full_name":"Icon Laboratory Services Inc.","duties_or_roles":"Manage local lab reports for safety labs","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Fortrea Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Guardant Health Inc.","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"PPD Development L.P.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Technologies LLC","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Azenta US Inc.","duties_or_roles":"Long-term storage of biosamples","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
DS-8201a
Active Substance
TRASTUZUMAB DERUXTECAN
Modality
ADC
Routes Of Administration
INTRAVENIOUS INFUSION
Route
INTRAVENIOUS INFUSION
Maximum Dose
5.4 mg/Kg
Investigational Product Name
Kadcyla (ado-trastuzumab emtansine, T-DM1)
Active Substance
TRASTUZUMAB EMTANSINE
Modality
ADC
Routes Of Administration
INTRAVENIOUS INFUSION
Route
INTRAVENIOUS INFUSION
Authorisation Status
Authorised (EU marketing authorisation EU/1/13/885/001)
Maximum Dose
3.6 mg/Kg

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