Clinical trial • Phase II • Respiratory

TOZORAKIMAB for Asthma

Phase II trial of TOZORAKIMAB for Asthma.

Overview

Trial Therapeutic Area
Respiratory
Trial Disease
Asthma
Trial Stage
Phase II
Drug Modality
Monoclonal antibody | Small molecule

Key dates

Initial CTIS Submission Date
23-01-2025
First CTIS Authorization Date
03-04-2025

Trial design

Randomised, placebo arm (placebo arm: patients will receive placebo). background therapy: participants remain on medium-to-high dose ics in combination with laba (per gina 2024); no active comparator dose/schedule stated for investigational product.-controlled Phase II trial across 30 sites in France, Italy, Greece and others.

Randomised
Yes
Comparator
Placebo arm (Placebo Arm: Patients will receive placebo). Background therapy: participants remain on medium-to-high dose ICS in combination with LABA (per GINA 2024); no active comparator dose/schedule stated for investigational product.
Single Multiple Or Escalation Dose Combined
Yes
Target Sample Size
470
Trial Duration For Participant
448

Eligibility

Recruits 470 isVulnerablePopulationSelected is true. Informed consent: "Provision of signed and dated written informed consent prior to any study-specific procedures." Participants are adults (18-75) so assent for minors is not applicable. Optional genetic research requires separate signed consent. Subject information and ICF documents (including versions for pregnant partners and optional genomic consent) are provided for participating countries..

Pregnancy Exclusion
10. Women of Child Bearing Potential (WOCBP) must have a negative serum pregnancy test at the Screening Visit and a negative urine pregnancy test prior to randomisation.
Vulnerable Population
isVulnerablePopulationSelected is true. Informed consent: "Provision of signed and dated written informed consent prior to any study-specific procedures." Participants are adults (18-75) so assent for minors is not applicable. Optional genetic research requires separate signed consent. Subject information and ICF documents (including versions for pregnant partners and optional genomic consent) are provided for participating countries.

Inclusion criteria

  • {"criterion_text":"- 1. Provision of signed and dated written informed consent prior to any study-specific procedures."}
  • {"criterion_text":"- 10. Women of Child Bearing Potential (WOCBP) must have a negative serum pregnancy test at the Screening Visit and a negative urine pregnancy test prior to randomisation."}
  • {"criterion_text":"- 11. Contraceptive use by males and females should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies."}
  • {"criterion_text":"- 2. Optional: Provision of signed and dated written Optional Genetic Research Information informed consent before the sample collection or optional genetic research that supports the Genomic Initiative."}
  • {"criterion_text":"- 3. Adults aged 18-75, inclusive when signing the informed consent at Visit 1."}
  • {"criterion_text":"- 4. Documented physician-diagnosis of asthma for at least 12 months prior to V1."}
  • {"criterion_text":"- 5. Treated with medium or high dose ICS (as per GINA 2024 report) in combination with LABA."}
  • {"criterion_text":"- 6. Demonstration of uncontrolled asthma through ACQ-6 score ≥ 1.5 at screening and randomisation."}
  • {"criterion_text":"- 7. Pre-bronchodilator FEV1 ≥ 40% to ≤ 90% of predicted normal at both screening and randomisation."}
  • {"criterion_text":"- 8. Documented exacerbation history in the last 12 months before screening and biomarker requirements of: (a) 2 severe exacerbations OR (b) 1 severe exacerbation and: (i) Eosinophils ≥ 150 cells/μl at screening or (ii) FeNo ≥ 25 ppb at screening and randomisation (Visits 1 and 2)"}
  • {"criterion_text":"- 9. Participants need to demonstrate a ≥70% compliance for Asthma Daily Diary."}

Exclusion criteria

  • {"criterion_text":"- 1. Completed treatment for respiratory infection with antibiotics in the 4 weeks prior to Visit 1."}
  • {"criterion_text":"- 2. Clinically significant pulmonary disease other than asthma."}
  • {"criterion_text":"- 3. Current smokers, former smokers with >10 pack-years history, or former smokers who stopped smoking <6 months before Visit 1."}
  • {"criterion_text":"- 4. Clinically significant aortic stenosis or pulmonary arterial hypertension."}
  • {"criterion_text":"- 5. Active tuberculosis, hepatitis, HIV, or current diagnosis of cancer or immune complex disease."}
  • {"criterion_text":"- 6. Unstable cardiovascular disorders."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Annualised rate of severe asthma exacerbations.","definition_or_measurement_approach":""}

Secondary endpoints

  • {"endpoint_text":"- 1. Annualised rate of severe asthma exacerbations (in participants with uncontrolled moderate-to-severe asthma and baseline eosinophils <300 cells/μL and history of ≥2 exacerbations within 12 months prior to screening).","definition_or_measurement_approach":"Annualised rate in the specified subgroup (baseline eosinophils <300 cells/μL and history of ≥2 exacerbations in prior 12 months)."}
  • {"endpoint_text":"- 2. Time-to-first severe asthma exacerbation.","definition_or_measurement_approach":"Time-to-event analysis measuring time from randomisation to first severe asthma exacerbation."}
  • {"endpoint_text":"- 3. Change from baseline in pre-bronchodilator forced expiratory volume in 1 second (FEV1) over weeks 20-26.","definition_or_measurement_approach":"Change from baseline in pre-bronchodilator FEV1 measured during weeks 20-26."}
  • {"endpoint_text":"- 4. Change from baseline in post-bronchodilator FEV1 at week 26.","definition_or_measurement_approach":"Change from baseline in post-bronchodilator FEV1 measured at week 26."}
  • {"endpoint_text":"- 5. Change from baseline in ACQ-6 at week 26.","definition_or_measurement_approach":"Change from baseline in ACQ-6 score measured at week 26."}
  • {"endpoint_text":"- 6. Change from baseline in AQLQ(S)+12 at week 26.","definition_or_measurement_approach":"Change from baseline in AQLQ(S)+12 score measured at week 26."}
  • {"endpoint_text":"- 7. Trough serum concentrations of tozorakimab over 52 weeks treatment period.","definition_or_measurement_approach":"Trough (pre-dose) serum concentration measurements of tozorakimab collected over the 52-week treatment period."}
  • {"endpoint_text":"- 8. Anti-drug antibody (ADA) prevalence, incidence, and titre.","definition_or_measurement_approach":"Assessment of ADA prevalence, incidence and titre from immunogenicity assays."}

Recruitment

Planned Sample Size
470
Recruitment Window Months
35
Consent Approach
Adults (18-75) provide signed and dated written informed consent prior to any study-specific procedures. Separate optional consent is required for optional genetic/genomic research. Subject information and informed consent forms (L1 SIS and ICF) are provided in multiple country-specific versions/languages (documents listed for ES, GR, HU, FR and other localised versions). Pregnant partner information is available as a separate ICF document.

Methods

  • K1_Recruitment arrangements (documented recruitment arrangements uploaded per country)
  • K2_Recruitment material_Poster (study posters for recruitment)
  • K3_Recruitment material_PrimayCare_Spain (primary care recruitment material for Spain)
  • JLC recruitment materials / information to EC (country-specific recruitment packages listed in documents)

Geography

Total Number Of Sites
30
Total Number Of Participants
70

France

Earliest CTIS Part Ii Submission Date
28-03-2025
Latest Decision Or Authorization Date
14-01-2026
Processing Time Days
292
Number Of Sites
7
Number Of Participants
12

Sites

Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
Service de Pneumologie
Contact Person Name
Raphael Le Mao
Contact Person Email
raphael.lemao@chu-brest.fr
Site Name
Centre Hospitalier Regional De Marseille
Department Name
Clinique des Bronches Allergie et Sommeil -CHU Nord
Contact Person Name
Marion Gouitaa
Contact Person Email
marion.gouitaa@ap-hm.fr
Site Name
Centre Hospitalier Intercommunal Creteil
Department Name
Pneumologie
Contact Person Name
Amel Boudjemaa
Contact Person Email
amel.boudjemaa@chicreteil.fr
Site Name
Hospital Foch
Department Name
Department of pneumology
Contact Person Name
Colas Tcherakian
Contact Person Email
c.tcherakian@hopital-foch.com
Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Clinical investigation of pulmonary center
Contact Person Name
Pierre Olivier Girodet
Site Name
Hopital De La Croix-Rousse
Department Name
Service de Pneumologie
Contact Person Name
Gilles Devouassoux
Contact Person Email
gilles.devouassoux@chu-lyon.fr
Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
Service de Pneumologie
Contact Person Name
Naji Khayat

Italy

Earliest CTIS Part Ii Submission Date
06-03-2025
Latest Decision Or Authorization Date
19-01-2026
Processing Time Days
319
Number Of Sites
4
Number Of Participants
8

Sites

Site Name
IRCCS Ospedale Policlinico San Martino
Department Name
Respiratory System Diseases and Allergy
Contact Person Name
Fulvio Braido
Contact Person Email
fulvio.braido@unige.it
Site Name
Azienda Ospedaliero-Universitaria Policlinico G. Rodolico-San Marco Di Catania
Department Name
UOC Pneumology
Contact Person Name
Claudia Crimi
Contact Person Email
claudia.crimi@unict.it
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
UOSD allergology
Contact Person Name
Cristiano Caruso
Site Name
Azienda Ospedaliero Universitaria Ospedali Riuniti
Department Name
S.C. Malattie Apparato Respiratorio Universitaria
Contact Person Name
Giulia Scioscia
Contact Person Email
giulia.scioscia@unifg.it

Greece

Earliest CTIS Part Ii Submission Date
24-03-2025
Latest Decision Or Authorization Date
14-01-2026
Processing Time Days
296
Number Of Sites
6
Number Of Participants
16

Sites

Site Name
Athens Medical Center S.A.
Department Name
Department of Sleep Apnea Study Pulmonology Laboratory
Contact Person Name
Dimosthenis Papapetrou
Contact Person Email
dimospapapetroudsa@hotmail.com
Site Name
General University Hospital Of Patras
Department Name
Department of Respiratory Medicine
Contact Person Name
Argyrios Tzouvelekis
Contact Person Email
argyris.tzouvelekis@gmail.com
Site Name
Athens Naval Hospital
Department Name
Pulmonary Clinic
Contact Person Name
Nikolaos Zias
Contact Person Email
nikoszias@gmail.com
Site Name
University General Hospital Of Ioannina
Department Name
Respiratory Clinic
Contact Person Name
Konstantinos Kostikas
Contact Person Email
ktkostikas@gmail.com
Site Name
Thermi Clinic S.A.
Department Name
Internal Medicine Dpt
Contact Person Name
Stavros Tryfon
Contact Person Email
stavrostryfon@yahoo.gr
Site Name
Geniko Nosokomeio Thessalonikis George Papanikolaou
Department Name
University Pulmonary Clinic
Contact Person Name
Konstantinos Porpodis
Contact Person Email
kporpodis@yahoo.gr

Spain

Earliest CTIS Part Ii Submission Date
19-03-2025
Latest Decision Or Authorization Date
19-01-2026
Processing Time Days
306
Number Of Sites
6
Number Of Participants
14

Sites

Site Name
Hospital Universitari Vall D Hebron
Department Name
Neumology
Contact Person Name
Iñigo Ojanguren Arranz
Contact Person Email
inigo.ojanguren@vallhebron.cat
Site Name
Hospital Del Mar
Department Name
Neumology
Contact Person Name
Maria Pilar Ausin Herrero
Contact Person Email
mpausin@parcdesalutmar.cat
Site Name
Hospital Universitario Virgen De La Victoria
Department Name
Neumology
Contact Person Name
Jose Luis Velasco Garrido
Contact Person Email
jlvelascogarrido@hotmail.com
Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Neumology
Contact Person Name
Juan Luis Garcia Rivero
Contact Person Email
jgarcianml@gmail.com
Site Name
Hospital Universitario Dr Peset Aleixandre
Department Name
Neumology
Contact Person Name
Eva Martinez Moragon
Contact Person Email
evamartinezmoragon@gmail.com
Site Name
Hospital Universitario 12 De Octubre
Department Name
Alergology
Contact Person Name
Ismael Garcia Moguel
Contact Person Email
ismaelgmoguel@gmail.com

Hungary

Earliest CTIS Part Ii Submission Date
10-03-2025
Latest Decision Or Authorization Date
16-01-2026
Processing Time Days
312
Number Of Sites
7
Number Of Participants
20

Sites

Site Name
Obudai Egeszseguegyi Centrum Kft.
Contact Person Name
Zsófia Ajtay
Contact Person Email
zsofia.ajtay@oec.hu
Site Name
Balassagyarmati Dr. Kenessey Albert Korhaz Rendelointezet
Department Name
Pulmonológia Krónikus Osztály
Contact Person Name
Magdolna Póczi
Contact Person Email
magdolnapoczi@gmail.com
Site Name
Infer-Med Kft.
Contact Person Name
Márta Papp
Contact Person Email
drpappm@gmail.com
Site Name
University Of Debrecen
Department Name
Tüdőgyógyászati Klinika
Contact Person Name
Ildikó Kissné Horváth
Contact Person Email
horvath.ildiko@med.unideb.hu
Site Name
Orszagos Koranyi Pulmonologiai Intezet
Department Name
Asthma Ambulancia
Contact Person Name
Zsuzsanna Csoma
Contact Person Email
csoma@koranyi.hu
Site Name
Reformatus Pulmonologiai Centrum
Contact Person Name
Edit Dulka
Contact Person Email
dulkaedit@gmail.com
Site Name
Erzsebet Gondozohaz Kft.
Contact Person Name
János Mucsi
Contact Person Email
mucsitrial@gmail.com

Sponsor

Primary sponsor

Full Name
AstraZeneca AB
Organisation Type
Pharmaceutical company
Country Of Registered Address
Sweden

Investigational products

Investigational Product Name
Tozorakimab
Active Substance
TOZORAKIMAB
Modality
Monoclonal antibody
Routes Of Administration
SUBCUTANEOUS INJECTION
Route
SUBCUTANEOUS INJECTION
Investigational Product Name
Tozorakimab-placebo
Modality
Other
Combination Treatment
Yes

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