Clinical trial • Phase III • Ophthalmology|Neurology|Cardiology

TENECTEPLASE for Central retinal artery occlusion

Phase III trial of TENECTEPLASE for Central retinal artery occlusion.

Overview

Trial Therapeutic Area
Ophthalmology|Neurology|Cardiology
Trial Disease
Central retinal artery occlusion
Trial Stage
Phase III
Drug Modality
Peptide/protein/enzyme|Small molecule

Key dates

Initial CTIS Submission Date
27-09-2024
First CTIS Authorization Date
31-10-2024

Trial design

Randomised, albyl-e 75 mg enterotabletter (acetylsalicylic acid) oral (comparator arm described as asa + placebo; product listed as albyl-e 75 mg enterotabletter). dosing schedule not specified in the summary.-controlled Phase III trial in Belgium, Denmark, Finland and others.

Randomised
Yes
Comparator
Albyl-E 75 mg enterotabletter (acetylsalicylic acid) oral (comparator arm described as ASA + placebo; product listed as Albyl-E 75 mg enterotabletter). Dosing schedule not specified in the summary.
Target Sample Size
76
Trial Duration For Participant
30

Eligibility

Recruits 76 No vulnerable populations selected. Only adults (Age ≥18). Informed written consent required from each patient. Subject information and informed consent forms for adults are provided (including a Dutch version). No assent procedures described..

Pregnancy Exclusion
Pregnancy (if suspicion of pregnancy s-hCG or u-hCG must be negative).
Vulnerable Population
No vulnerable populations selected. Only adults (Age ≥18). Informed written consent required from each patient. Subject information and informed consent forms for adults are provided (including a Dutch version). No assent procedures described.

Inclusion criteria

  • {"criterion_text":"- 1.\tNon-arteritic central retinal artery occlusion with ≥ 1.0 logMAR best-corrected visual acuity and symptoms lasting less than 4.5 hours.\n- 2.\tAbility to administer the Investigator Medicinal Product (IMP) within 4.5 hours of symptom onset.\n- 3.\tAge ≥18 years.\n- 4.\tInformed written consent of the patient.\n- 5.\tA woman of childbearing potential (WOCBP) must confirm that in her opinion, she cannot be pregnant, OR if there is a possibility that she is pregnant, a negative pregnancy test must be confirmed before any IMP is given."}

Exclusion criteria

  • {"criterion_text":"- 1.\tNo other active intervention targeting CRAO.\n- 2.\tBranch retinal artery occlusion, cilioretinal artery supplying the macula, combined arterial-venous occlusion, proliferative diabetic retinopathy, elevated intraocular pressure (> 30 mmHg) or clinical suspicion of ophthalmic artery occlusion (e.g. choroidal nonperfusion, absence of cherry red spot, no light perception).\n- 3.\tSystemic diseases; severe general diseases, systemic arterial hypertension (blood pressure >185/110 mmHg (2)), despite medical therapy, or clinical suspicion of acute systemic inflammation.\n- 4.\tPresence of intracranial haemorrhage on brain MRI/CT.\n- 5.\tMedical history: heart attack within the last 6 weeks, intracerebral bleeding or neurosurgical operation within the last 4 weeks, therapy with anticoagulation, allergic reaction to contrast agent, hemorrhagic diathesis, aneurysms, inflammatory vascular diseases (eg, giant cell arteritis, granulomatosis with polyangitis), endocarditis, or gastric ulcer.\n- 6.\tNo willingness and ability of the patient to participate in all follow-up examinations.\n- 7.\tPregnancy (if suspicion of pregnancy s-hCG or u-hCG must be negative).\n- 8.\tAllergy or intolerance to any ingredients of IMP (including placebo) or gentamicin or acetylsalicylic acid.\n- 9.\tOther conditions / circumstances likely to lead to poor treatment adherence (eg, history of poor compliance, alcohol or drug dependency, no fixed abode).\n- 10.\tSignificant bleeding disorder either at present or within the past 6 months.\n- 11.\tEffective oral anticoagulant treatment, eg, warfarin sodium (INR >1.3).\n- 12.\tEffective anticoagulant treatment with heparin or low molecular weight heparin the last 48 hours.\n- 13.\tAny history of central nervous system damage (ie, neoplasm, aneurysm, intracranial or spinal surgery).\n- 14.\tKnown hemorrhagic diathesis.\n- 15.\tMajor surgery, biopsy of a parenchymal organ, or significant trauma within the past 2 months (this includes any trauma associated with acute myocardial infarction).\n- 16.\tRecent non-compressible vessel puncture within 2 weeks.\n- 17.\tRecent trauma to the head or cranium.\n- 18.\tProlonged cardiopulmonary resuscitation (>2 minutes) within the past 2 weeks.\n- 19.\tAcute pericarditis and/or subacute bacterial endocarditis.\n- 20.\tAcute pancreatitis.\n- 21.\tSevere hepatic dysfunction, including hepatic failure, cirrhosis, portal hypertension (oesophageal varices) and active hepatitis.\n- 22.\tActive peptic ulceration.\n- 23.\tArterial aneurysm and known arterial/venous malformation.\n- 24.\tNeoplasm with increased bleeding risk.\n- 25.\tAny known history of hemorrhagic stroke or stroke of unknown origin.\n- 26.\tKnown history of ischemic stroke or transient ischemic attack in the preceding 3 months.\n- 27.\tDementia."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Primary endpoint: Proportion of patients with ≤ 0.7 logMAR best-corrected visual acuity in the affected eye at 30 (±5) days after treatment, representing an improvement in best-corrected visual acuity of at least 0.3 logMAR (intention-to-treat (ITT) analysis).","definition_or_measurement_approach":"Proportion of patients with ≤ 0.7 logMAR best-corrected visual acuity in the affected eye measured at 30 (±5) days after treatment; improvement defined as at least 0.3 logMAR; analysed as intention-to-treat (ITT)."}

Recruitment

Planned Sample Size
76
Recruitment Window Months
63
Consent Approach
Informed written consent required from each patient (adults only, Age ≥18). Subject information and informed consent forms for adults are available (L1_SIS and ICF adults documents listed, including a Dutch version). No assent for minors described.

Geography

Total Number Of Sites
18
Total Number Of Participants
76

Belgium

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
04-11-2024
Processing Time Days
11
Number Of Sites
1
Number Of Participants
8

Sites

Site Name
UZ Leuven
Department Name
neurology
Principal Investigator Name
Robin Lemmens
Principal Investigator Email
robin.lemmens@uzleuven.be
Contact Person Name
Robin Lemmens
Contact Person Email
robin.lemmens@uzleuven.be

Denmark

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
04-11-2024
Processing Time Days
11
Number Of Sites
3
Number Of Participants
19

Sites

Site Name
Aarhus Universitet
Department Name
Neurology
Principal Investigator Name
Claus Ziegler Simonsen
Principal Investigator Email
clausimo@rm.dk
Contact Person Name
Claus Ziegler Simonsen
Contact Person Email
clausimo@rm.dk
Site Name
Rigshospitalet
Department Name
Neurology
Principal Investigator Name
Thomas Clement Truelsen
Principal Investigator Email
thomas.clement.truelsen@regionh.dk
Contact Person Name
Thomas Clement Truelsen
Site Name
Copenhagen University Hospital
Department Name
Neurology
Principal Investigator Name
Louisa Marguerite Christensen
Principal Investigator Email
louisa.marguerite.christensen@regionh.dk
Contact Person Name
Louisa Marguerite Christensen

Finland

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
01-11-2024
Processing Time Days
8
Number Of Sites
2
Number Of Participants
13

Sites

Site Name
HUS-Yhtymae
Department Name
Neurology
Principal Investigator Name
Petra Ijäs
Principal Investigator Email
Petra.Ijas@hus.fi
Contact Person Name
Petra Ijäs
Contact Person Email
Petra.Ijas@hus.fi
Site Name
Turku University Hospital
Department Name
Neurology
Principal Investigator Name
Pauli Ylikotila
Principal Investigator Email
Pauli.ylikotila@tyks.fi
Contact Person Name
Pauli Ylikotila
Contact Person Email
Pauli.ylikotila@tyks.fi

Ireland

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
31-10-2024
Processing Time Days
7
Number Of Sites
1
Number Of Participants
3

Sites

Site Name
Mater Misericordiae University Hospital
Department Name
Neurology
Principal Investigator Name
Sean Murphy
Principal Investigator Email
seanmurphy@mater.ie
Contact Person Name
Sean Murphy
Contact Person Email
seanmurphy@mater.ie

Sweden

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
31-10-2024
Processing Time Days
7
Number Of Sites
2
Number Of Participants
4

Sites

Site Name
Region Vaesternorrland
Department Name
Neurology
Principal Investigator Name
Fredrik Björck
Principal Investigator Email
fredrik.bjork@rvn.se
Contact Person Name
Fredrik Björck
Contact Person Email
fredrik.bjork@rvn.se
Site Name
Karolinska Institutet
Department Name
Neurology
Principal Investigator Name
Michael Mazya
Principal Investigator Email
michael.mazya@regionstockholm.se
Contact Person Name
Michael Mazya

Norway

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
05-11-2024
Processing Time Days
12
Number Of Sites
9
Number Of Participants
29

Sites

Site Name
Sykehuset Telemark HF
Department Name
Neurology
Principal Investigator Name
Vetle Nilsen Malmberg
Principal Investigator Email
vetmal@sthf.no
Contact Person Name
Vetle Nilsen Malmberg
Contact Person Email
vetmal@sthf.no
Site Name
St. Olavs Hospital HF
Department Name
Neurology
Principal Investigator Name
Hanne Ellekjær
Principal Investigator Email
hanne.ellekjar@ntnu.no
Contact Person Name
Hanne Ellekjær
Contact Person Email
hanne.ellekjar@ntnu.no
Site Name
Helse Stavanger HF
Department Name
Neurology
Principal Investigator Name
Martin Kurz
Principal Investigator Email
friedrich.martin.wilhelm.kurz@sus.no
Contact Person Name
Martin Kurz
Site Name
Helse Bergen HF
Department Name
Neurology
Principal Investigator Name
Andrej Khanevski
Principal Investigator Email
andrej.netland.khanevski@helse-bergen.no
Contact Person Name
Andrej Khanevski
Site Name
Sykehuset Innlandet HF
Department Name
Neurology
Principal Investigator Name
Anette Huuse Farmen
Principal Investigator Email
anette.huuse.farmen@sykehuset-innlandet.no
Contact Person Name
Anette Huuse Farmen
Site Name
Vestre Viken HF
Department Name
Neurology
Principal Investigator Name
Kristin Evensen
Principal Investigator Email
SBEVEK@vestreviken.no
Contact Person Name
Kristin Evensen
Contact Person Email
SBEVEK@vestreviken.no
Site Name
Sykehuset I Vestfold HF
Department Name
Neurology
Principal Investigator Name
Håvard Lisether
Principal Investigator Email
haalis@siv.no
Contact Person Name
Håvard Lisether
Contact Person Email
haalis@siv.no
Site Name
Oslo University Hospital HF
Department Name
Neurology
Principal Investigator Name
Anne Hege Aamodt
Principal Investigator Email
anhaam@ous-hf.no
Contact Person Name
Anne Hege Aamodt
Contact Person Email
anhaam@ous-hf.no
Site Name
Sykehuset Oestfold HF Kalnes
Department Name
Ophthalmology
Principal Investigator Name
Oddbjørn Bjordal
Principal Investigator Email
oddbjorn.bjordal@so-hf.no
Contact Person Name
Oddbjørn Bjordal
Contact Person Email
oddbjorn.bjordal@so-hf.no

Sponsor

Primary sponsor

Full Name
Oslo University Hospital HF
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
Norway

Third parties

  • {"country":"Denmark","full_name":"Aarhus Universitet","duties_or_roles":"[{\"id\":421516,\"code\":\"1\"}]","organisation_type":"Educational Institution"}
  • {"country":"Denmark","full_name":"Rigshospitalet","duties_or_roles":"[{\"id\":421515,\"code\":\"1\"}]","organisation_type":"Hospital/Clinic/Other health care facility"}

Investigational products

Investigational Product Name
TENECTEPLASE
Active Substance
TENECTEPLASE
Modality
Peptide/protein/enzyme
Routes Of Administration
INTRAVENOUS INJECTION
Route
INTRAVENOUS INJECTION
Authorisation Status
2
Starting Dose
0.25 mg/kg
Dose Levels
0.25 mg/kg
Maximum Dose
25 mg
Investigational Product Name
Albyl-E 75 mg enterotabletter
Active Substance
ACETYLSALICYLIC ACID
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
2
Starting Dose
75 mg
Dose Levels
75 mg (product listed as 75 mg enterotabletter); max daily dose reported 300 mg
Maximum Dose
300 mg
Investigational Product Name
Sodium Chloride Fresenius Kabi Italia 0.9 % Solution for infusion
Active Substance
SODIUM CHLORIDE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Authorisation Status
2
Maximum Dose
25 mg
Investigational Product Name
encapsulated tablets of inactive substance
Modality
Other

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