Clinical trial • Phase I/II • Oncology
Temozolomide for Neuroblastoma (relapsed, high-risk)
Phase I/II trial of Temozolomide for Neuroblastoma (relapsed, high-risk).
Overview
- Trial Therapeutic Area
- Oncology
- Trial Disease
- Neuroblastoma (relapsed, high-risk)
- Trial Stage
- Phase I/II
- Drug Modality
- Small molecule|Monoclonal antibody
- Paediatric Trial
- Yes
- Orphan Drug
- Yes
Key dates
- Initial CTIS Submission Date
- 08-04-2025
- First CTIS Authorization Date
- 28-07-2025
Trial design
Randomised, current best available treatment / standard of care (not further specified in provided data)-controlled, adaptive Phase I/II trial in Spain, Netherlands, Austria and others.
- Randomised
- Yes
- Comparator
- Current best available treatment / standard of care (not further specified in provided data)
- Adaptive
- True, multi-arm multi-stage platform design with Tier 1 randomised comparison and Tier 2 dose-escalation and dose-expansion/confirmation cohorts
- Single Multiple Or Escalation Dose Combined
- Yes
- Target Sample Size
- 52
Eligibility
Recruits 52 paediatric patients.
- Pregnancy Exclusion
- Pregnant or lactating participant
- Vulnerable Population
- Includes paediatric participants (age ≥1 year) and adolescents; consent must be signed by participant, parent or guardian. Age-specific informed consent and assent materials are provided (multiple assent and ICF documents listed for age groups such as 5-9, 8-11, 10-13, 12-15, 15-17, 16+, parent/guardian ICFs) in multiple country/language versions.
Inclusion criteria
- {"criterion_text":"- Disease specific: Histologically proven neuroblastoma as per International Neuroblastoma Staging System (INSS) definition"}
- {"criterion_text":"- Performance and organ function: Liver function (within 72 hours prior to randomisation) - Absence of clinically significant signs of liver dysfunction. AST or ALT ≤ 3.0 ULN and total bilirubin ≤ 1.5 ULN. In patients with liver metastases, AST or ALT ≤ 5 ULN and total bilirubin ≤ 2.5 ULN is allowed"}
- {"criterion_text":"- Performance and organ function: Coagulation - Participants must not have an active uncontrolled coagulopathy. Anticoagulation is permitted as long as the INR or APTT is within therapeutic limits (according to the medical standard of the institution) and the participant has been on a stable dose of anticoagulants for at least two weeks at the time of study enrolment."}
- {"criterion_text":"- Performance and organ function: Blood pressure below 95th centile for age and sex. Participants ≥18 years of age should have a blood pressure ≤150/90 mmHg (within 72 hours prior to randomisation). Use of antihypertensive medication is permitted."}
- {"criterion_text":"- Tier 2 Specific Inclusion Criteria: More than one relapse event or ineligible for Tier 1. NB - The following previous treatments are allowed provided that the principal investigator expects a favourable benefit/risk assessment (e.g. patients could derive potential benefit from the Tier 2 combination): bevacizumab, any anti-GD2 antibody given with chemotherapy (‘chemo-immunotherapy’) and previous treatment with temozolomide with irinotecan"}
- {"criterion_text":"- Disease Specific: High risk relapsed neuroblastoma (relapsed or progressed after being defined as High Risk at any time following diagnosis or progressed/relapsed as high-risk neuroblastoma)"}
- {"criterion_text":"- Disease Specific: Measurable disease by cross sectional imaging or evaluable disease (uptake on MIBG scan with or without bone marrow histology), as per INRC [2, 3]. Participants with only bone marrow detectable disease (bone marrow aspirate or trephine) are NOT eligible for the study"}
- {"criterion_text":"- General: Age ≥1 year"}
- {"criterion_text":"- General: Signed informed consent from participant, parent or guardian"}
- {"criterion_text":"- Performance and organ function: Performance Status - Lansky (for patients ≤12 years of age) or Karnofsky (for those >12) ≥ 50%, (Participants who are unable to walk because of paralysis, but who are able to sit upright unassisted in a wheelchair, will be considered ambulatory for the purpose of assessing performance score)"}
- {"criterion_text":"- Performance and organ function: Life expectancy of ≥12 weeks"}
- {"criterion_text":"- Performance and organ function: Bone marrow function (within 72 hours prior to randomisation) - Platelets ≥ 50 x 109/L (unsupported for 72 hours), ANC ≥ 0.50 x 109/L (no G-CSF support for 72 hours) and Haemoglobin > 8 g/dL (transfusions allowed)"}
- {"criterion_text":"- Performance and organ function: Renal function (within 72 hours prior to randomisation) - Absence of clinically significant proteinuria (either early morning urine dipstick ≤ 2+) or if dipstick urinalysis shows > 2+ proteinuria, protein: creatinine (Pr/Cr) ratio must be < 0.5 or a 24 hour protein excretion must be < 0.5g and Serum creatinine ≤ 1.5 ULN for age, if higher, a measured GFR (radioisotope or 24 hour urine calculated creatinine clearance) must be ≥ 60 ml/min/1.73 m2"}
Exclusion criteria
- {"criterion_text":"- Known contraindication or hypersensitivity to: Any study drug or component of the formulation, Chinese hamster ovary products or other recombinant human or humanised antibodies and Participants with mild previous hypersensitivity reactions to anti-GD2 antibodies may be included, but those with severe (or G4) hypersensitivity reactions to anti-GD2 antibodies will be excluded."}
- {"criterion_text":"- Bleeding metastases (participants with CNS metastases can be enrolled as long as the metastases are not bleeding). At least 6 months from any ≥ G3 haemoptysis or pulmonary haemorrhage"}
- {"criterion_text":"- Use of enzyme inducing anticonvulsants within 72hr of start of trial treatment"}
- {"criterion_text":"- Conditions that increase the risk of bevacizumab-related toxicities: History or evidence of inherited bleeding diathesis or significant coagulopathy at risk of bleeding (i.e. in the absence of therapeutic anticoagulation), History of abdominal fistula, gastrointestinal perforation, intra-abdominal abscess or active gastrointestinal bleeding within 6 months prior to study enrolment and Current chronic intestinal inflammatory disease/bowel obstruction"}
- {"criterion_text":"- Intolerance to galactose and fructose, lactase deficiency, and/or defect of absorption of galactose and fructose"}
- {"criterion_text":"- Males or females of reproductive potential may not participate unless they agree to use a highly effective method of birth control, i.e. with a failure rate of less than 1% per year, (e.g. implants, injectables, combined oral contraceptives, IUDs, sexual abstinence or vasectomised partner), for the duration of study therapy and for up to 6 months after the last dose of trial drugs. A negative urine or serum pregnancy test must be obtained within 72 hours prior to dosing in females who are post-menarche."}
- {"criterion_text":"- Pregnant or lactating participant"}
- {"criterion_text":"- Live or live-attenuated vaccines given within previous 28 days prior to study enrolment"}
- {"criterion_text":"- Any uncontrolled medical condition that poses an additional risk to the participant"}
- {"criterion_text":"- Tier 1 Specific Exclusion Criteria: More than one relapse event after the start of high risk neuroblastoma therapy"}
- {"criterion_text":"- Tier 1 Specific Exclusion Criteria: Previous treatments that are not allowed - Bevacizumab for relapsed neuroblastoma. Patients who have received BIT for refractory disease are not excluded, providing no progression of disease during this treatment occurred and Treatment with any anti-GD2 antibody given with chemotherapy (‘chemo-immunotherapy’) for treatment of relapsed neuroblastoma. Prior treatment with chemo-immunotherapy for refractory disease is allowed, provided no disease progression during this therapy."}
- {"criterion_text":"- Clinically significant neurological toxicity, uncontrolled seizures or objective peripheral neuropathy (> grade 2). (Unresolved neurological deficits from previous spinal cord compression or surgeries are acceptable). Participants with previous ≥ Grade 3 motor neurotoxicity secondary to anti-GD2 are excluded, even if recovered."}
- {"criterion_text":"- Prior severe arterial thrombo-embolic events (e.g. cardiac ischemia, cerebral vascular accident, peripheral arterial thrombosis) or any ongoing arterial thrombo-embolic events"}
- {"criterion_text":"- A history of (noninfectious) pneumonitis requiring steroids, or current pneumonitis."}
- {"criterion_text":"- Patients that are allergic to all therapies for Pnemocystis jirovecii pneumonia and can thus not receive prophylaxis for PJP."}
- {"criterion_text":"- Uncontrolled infection"}
- {"criterion_text":"- Inadequate recovery from prior surgery with ongoing ≥ Grade 3 surgical complications. Grade ≥ 2 wound dehiscence."}
- {"criterion_text":"- Recent surgical procedures (at start of trial treatment). Patient can be randomised up to 48hr prior to these periods being completed provided that trial treatment only starts after complying with all of them: Core biopsies within previous 24hr, Open excisional biopsies within previous 48hr, Major surgery within previous 2 weeks, Bone marrow aspirates/trephines, within previous 48hr and Tunnelled central line insertion within previous 48hr"}
- {"criterion_text":"- Washout from prior treatments (at start of trial treatment): Chemotherapy within previous 2 weeks (1 week for oral metronomic chemotherapy regimens), Any anti-GD2 therapy within previous 2 weeks, Craniospinal radiotherapy or MIBG therapy within previous 6 weeks, Radiotherapy to the tumour bed within previous 2 weeks (no washout for palliative radiotherapy), Myeloablative therapy with haematopoietic stem cell rescue (autologous stem cell transplant) within previous 8 weeks, Allogeneic stem cell transplant within previous 12 weeks (with absence of active ≥ G2 acute GVHD) and 14 days or 5 half-lives (whichever occurs later) from last administration of an IMP in an IMP-trial"}
Endpoints
Primary endpoints
- {"endpoint_text":"- Progression-Free Survival time (as per INRC 2017) – for Tier 1 (randomised comparison)","definition_or_measurement_approach":"Progression-Free Survival measured as per INRC 2017 criteria for Tier 1 randomised comparison."}
- {"endpoint_text":"- Definition of a safe and tolerable combination regimen – for Tier 2 (dose expansion-confirmation cohorts)","definition_or_measurement_approach":"Safety and tolerability assessed in dose expansion/confirmation cohorts (Tier 2) to define a safe/tolerable combination regimen."}
Secondary endpoints
- {"endpoint_text":"- Best objective response (complete and partial response) as per INRC 2017 during trial treatment (12 cycles)","definition_or_measurement_approach":"Objective responses (complete, partial) assessed using INRC 2017 criteria during up to 12 cycles of trial treatment."}
- {"endpoint_text":"- Clinical benefit (complete, partial and minor response and stable disease) as per INRC 2017.","definition_or_measurement_approach":"Clinical benefit determined per INRC 2017 including complete, partial, minor responses and stable disease."}
- {"endpoint_text":"- Time response to progression (for responders)","definition_or_measurement_approach":"Time from response to documented progression for responders."}
- {"endpoint_text":"- Overall Survival time","definition_or_measurement_approach":"Overall survival measured from randomisation/enrolment to death from any cause."}
- {"endpoint_text":"- Quality of life measured by Peds-QL questionnaires","definition_or_measurement_approach":"Quality of life assessed using Peds-QL questionnaires."}
- {"endpoint_text":"- Incidence and Severity of AEs","definition_or_measurement_approach":"Adverse events collected and graded to assess incidence and severity."}
Recruitment
- Planned Sample Size
- 52
- Recruitment Window Months
- 84
- Consent Approach
- Signed informed consent from participant, parent or guardian required. Age-specific consent/assent materials are provided (assent forms and ICFs for age groups such as 5-9, 8-11, 10-13, 12-15, 15-17, 16+, parent/guardian ICFs). Documents available in multiple country/language versions (examples in Spanish, Dutch, French, German, English (EN-GB), Swedish, Norwegian, Italian and country-specific versions listed in trial documents).
Geography
- Total Number Of Sites
- 49
- Total Number Of Participants
- 102
Spain
- Earliest CTIS Part Ii Submission Date
- 02-07-2025
- Latest Decision Or Authorization Date
- 29-07-2025
- Processing Time Days
- 27
- Number Of Sites
- 6
- Number Of Participants
- 18
Sites
- Site Name
- University Hospital Virgen Del Rocio S.L.
- Department Name
- Pediatric Oncology
- Contact Person Name
- Mercedes Llempen
- Contact Person Email
- mercedesl.llempen.sspa@juntadeandalucia.es
- Site Name
- Hospital Universitario La Paz
- Department Name
- Pediatric hematology-oncology and stem cell transplant
- Contact Person Name
- Pedro Rubio
- Contact Person Email
- pedro.rubio@salud.madrid.org
- Site Name
- Hospital Universitario Y Politecnico La Fe
- Department Name
- Pediatric Oncology Unit
- Contact Person Name
- Adela Cañete
- Contact Person Email
- canyete_ade@gva.es
- Site Name
- Hospital Universitario De Cruces
- Department Name
- Pediatric Oncology and Hematology Section
- Contact Person Name
- Ricardo López Almara
- Contact Person Email
- ricardo.lopezalmaraz@osakidetza.eus
- Site Name
- Hospital Universitari Vall D Hebron
- Department Name
- Paediatric Oncology and Hematology Unit
- Contact Person Name
- Lucas Moreno
- Contact Person Email
- lucas.moreno@vallhebron.cat
- Site Name
- Hospital Infantil Universitario Nino Jesus
- Department Name
- Paediatric Haemato - Oncology Service
- Contact Person Name
- Alba Rubio
- Contact Person Email
- alba.rubio@salud.madrid.org
Netherlands
- Earliest CTIS Part Ii Submission Date
- 04-07-2025
- Latest Decision Or Authorization Date
- 30-07-2025
- Processing Time Days
- 26
- Number Of Sites
- 1
- Number Of Participants
- 10
Sites
- Site Name
- Princess Maxima Center Utrecht
- Department Name
- Paediatric Oncology
- Contact Person Name
- Natasha Van Eijkelenburg
- Contact Person Email
- n.k.a.vaneijkelenburg@prinsesmaximacentrum.nl
Austria
- Earliest CTIS Part Ii Submission Date
- 19-06-2025
- Latest Decision Or Authorization Date
- 04-08-2025
- Processing Time Days
- 46
- Number Of Sites
- 4
- Number Of Participants
- 3
Sites
- Site Name
- Gemeinnuetzige Salzburger Landeskliniken Betriebsgesellschaft mbH
- Department Name
- Pediatric Hematology and Oncology
- Contact Person Name
- Neil Jones
- Contact Person Email
- n.jones@salk.at
- Site Name
- Johannes Kepler University Linz
- Contact Person Name
- Barbara Winkler
- Contact Person Email
- barbara.winkler@kepleruniklinikum.at
- Site Name
- Medizinische Universitaet Innsbruck
- Contact Person Name
- Roman Crazzolara
- Contact Person Email
- roman.crazzolara@i-med.ac.at
- Site Name
- St. Anna Kinderspital GmbH
- Department Name
- Pediatric Hematology and Oncology
- Contact Person Name
- Heidrun Boztug
- Contact Person Email
- heidrun.boztug@stanna.at
Belgium
- Earliest CTIS Part Ii Submission Date
- 08-07-2025
- Latest Decision Or Authorization Date
- 28-07-2025
- Processing Time Days
- 20
- Number Of Sites
- 5
- Number Of Participants
- 5
Sites
- Site Name
- Association Hospitaliere De Bruxelles Hopital Universitaire Des Enfants Reine Fabiola
- Department Name
- Department of Pediatric Hemato-Oncology
- Contact Person Name
- Safiatou Diallo
- Contact Person Email
- Safiatou.diallo@hubruxelles.be
- Site Name
- Cliniques Universitaires Saint-Luc
- Department Name
- Department of Pediatric Hemato-Oncology
- Contact Person Name
- Bénédicte Brichard
- Contact Person Email
- benedicte.brichard@saintluc.uclouvain.be
- Site Name
- Universitair Ziekenhuis Antwerpen
- Department Name
- Department of Pediatric Hemato-Oncology
- Contact Person Name
- Jaques Van Heerden
- Contact Person Email
- jaques.vanheerden@uza.be
- Site Name
- Universitair Ziekenhuis Gent
- Department Name
- Department of Paediatric Haemato-oncology
- Contact Person Name
- Bram De Wilde
- Contact Person Email
- Bram.dewilde@uzgent.be
- Site Name
- UZ Leuven
- Department Name
- Department of Pediatric Hemato-Oncology
- Contact Person Name
- Marleen Renard
- Contact Person Email
- marleen.renard@uzleuven.be
Denmark
- Earliest CTIS Part Ii Submission Date
- 09-07-2025
- Latest Decision Or Authorization Date
- 28-07-2025
- Processing Time Days
- 19
- Number Of Sites
- 1
- Number Of Participants
- 4
Sites
- Site Name
- Rigshospitalet
- Department Name
- Department of Paediatric and Adolescent Medicine
- Contact Person Name
- Karsten Nysom
- Contact Person Email
- Karsten.nysom@regionh.dk
France
- Earliest CTIS Part Ii Submission Date
- 23-07-2025
- Latest Decision Or Authorization Date
- 29-07-2025
- Processing Time Days
- 6
- Number Of Sites
- 11
- Number Of Participants
- 25
Sites
- Site Name
- Gustave Roussy
- Department Name
- Departement de Cancerologie de L’enfant et de L’adolescent
- Contact Person Name
- Pablo Berlanga
- Contact Person Email
- PABLO.BERLANGA@gustaveroussy.fr
- Site Name
- Institut Curie
- Department Name
- Pédiatrie
- Contact Person Name
- Gudrun Schleiermacher
- Contact Person Email
- Gudrun.schleiermacher@curie.fr
- Site Name
- Centre Leon Berard
- Department Name
- Pediatric Oncology
- Contact Person Name
- Benoit Dumont
- Contact Person Email
- benoit.dumont@ihope.fr
- Site Name
- University Of Bordeaux
- Department Name
- Hémato Onco Ped
- Contact Person Name
- Julie Tandonnet
- Contact Person Email
- julie.tandonnet@chu-bordeaux.fr
- Site Name
- ASSISTANCE PUBLIQUE DES HOPITAUX DE MARSEILLE
- Contact Person Name
- Carole Coze
- Contact Person Email
- carole.coze@ap-hm.fr
- Site Name
- CHRU De Nancy
- Department Name
- Service d’onco-hematologie pediatrique
- Contact Person Name
- Ludovic Mansuy
- Contact Person Email
- lu.mansuy@chru-nancy.fr
- Site Name
- CHU Nantes - HME-Department onco-hematology pédiatric
- Contact Person Name
- Estelle Thebaud
- Contact Person Email
- Estelle.THEBAUD@chu-nantes.fr
- Site Name
- Hopital Des Enfants
- Department Name
- Hematologie, immunologie et oncologie pédiatrique
- Contact Person Name
- Marion Gambart
- Contact Person Email
- gambart.m@chu-toulouse.fr
- Site Name
- Trousseau Hospital
- Department Name
- Hémato-immuno-oncologie
- Contact Person Name
- Hélène Boutroux
- Contact Person Email
- helene.boutroux@aphp.fr
- Site Name
- Centre Oscar Lambret
- Department Name
- Pediatric Oncology
- Contact Person Name
- Anne Sophie Defachelles Thomassin
- Contact Person Email
- AS-Defachelles@o-lambret.fr
- Site Name
- Les Hopitaux Universitaires De Strasbourg
- Department Name
- Onco-hematologie-pediatrique
- Contact Person Name
- Sarah Jannier
- Contact Person Email
- Sarah.jannier@chru-strasbourg.fr
Germany
- Earliest CTIS Part Ii Submission Date
- 20-06-2025
- Latest Decision Or Authorization Date
- 29-07-2025
- Processing Time Days
- 39
- Number Of Sites
- 11
- Number Of Participants
- 24
Sites
- Site Name
- Universitätsklinikum Augsburg Schwäbisches Kinderkrebszentrum Kinderkrebsforschungszentrum Stenglins
- Department Name
- Universitätsklinikum Augsburg
- Contact Person Name
- Simone Storck
- Contact Person Email
- simone.storck@uk-augsburg.de
- Site Name
- Universitätsklinikum Köln Klinik und Poliklinik für Kinder- und Jugendmedizin Pädiatrische Onkologie
- Department Name
- Pädiatrische Onkologie und Hämatologie
- Contact Person Name
- Thorsten Simon
- Contact Person Email
- Thorsten.Simon@uk-koeln.de
- Site Name
- Universitätsmedizin der Johannes-Gutenberg-Universität Mainz
- Department Name
- Klinik und Poliklinik für Kinder- und Jugendmedizin, Pädiatrische Onkologie,
- Contact Person Name
- arthur Wingerter
- Contact Person Email
- arthur.wingerter@unimedizin-mainz.de
- Site Name
- Universitätsklinikum Münster Klinik für Kinder- und Jugendmedizin, Pediatric Hematology/Oncology
- Department Name
- Pediatric Hematology/Oncology
- Contact Person Name
- Birgit Fröhlich
- Contact Person Email
- birgit.froehlich@ukmuenster.de
- Site Name
- Universitätsklinikum Essen
- Department Name
- Universitätsklinikum Essen
- Contact Person Name
- Uta Dirksen
- Contact Person Email
- uta.dirksen@uk-essen.de
- Site Name
- Ludwig Maximilian Universität München
- Department Name
- Ludwig Maximilian Universität München
- Contact Person Name
- Irene Schmid
- Contact Person Email
- irene.schmid@med.uni-muenchen.de
- Site Name
- Universitaetsklinikum Regensburg AöR
- Department Name
- Pädiatric Hematology/Oncology Pädriatische Hematologie/Onkologie
- Contact Person Name
- Selim Corbacioglu
- Contact Person Email
- selim.corbacioglu@ukr.de
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- Pediatric Oncology and Hematology
- Contact Person Name
- Hedwig Deubzer
- Contact Person Email
- hedwig.deubzer@charite.de
- Site Name
- Universitätsmedizin Greifswald Klinik und Poliklinik für Kinder- und Jugendmedizin, Pädiatrische Häm
- Department Name
- Pädiatrische Hämatologie und Onkologie
- Contact Person Name
- holger Lode
- Contact Person Email
- holger.lode@med.uni-greifswald.de
- Site Name
- Universitätsklinikum Hamburg-Eppendorf Poliklinik für Pädiatrische Hämatologie und Onkologie
- Department Name
- Universitätsklinikum Hamburg-Eppendorf,
- Contact Person Name
- Uwe Kordes
- Contact Person Email
- u.kordes@uke.de
- Site Name
- Universitätsklinikum Tübingen Klinik für Kinder- und Jugendmedizin
- Department Name
- Hämatologie und Onkologie
- Contact Person Name
- Tim Flaadt
- Contact Person Email
- tim.flaadt@med.uni-tuebingen.de
Sweden
- Earliest CTIS Part Ii Submission Date
- 17-06-2025
- Latest Decision Or Authorization Date
- 01-08-2025
- Processing Time Days
- 44
- Number Of Sites
- 2
- Number Of Participants
- 4
Sites
- Site Name
- Queen Silvia Childrens Hospital - Sahlgrenska University Hospital - Vaestra Goetalandsregionen
- Department Name
- Child Oncologist
- Contact Person Name
- Torben Ek
- Contact Person Email
- Torben.ek@vgregion.se
- Site Name
- Astrid Lindgren Children´s Hospital, Karolinska University Hospital
- Department Name
- Child Oncologist
- Contact Person Name
- Kleopatra Georgantzi
- Contact Person Email
- kleopatra.georgantzi@regionstockholm.se
Norway
- Earliest CTIS Part Ii Submission Date
- 10-07-2025
- Latest Decision Or Authorization Date
- 29-07-2025
- Processing Time Days
- 19
- Number Of Sites
- 1
- Number Of Participants
- 2
Sites
- Site Name
- Oslo University Hospital HF
- Department Name
- Department of Pediatric Hematology and Oncology
- Contact Person Name
- Aina Ulvmoen
- Contact Person Email
- ainulv@ous-hf.no
Italy
- Earliest CTIS Part Ii Submission Date
- 07-07-2025
- Latest Decision Or Authorization Date
- 30-07-2025
- Processing Time Days
- 23
- Number Of Sites
- 7
- Number Of Participants
- 7
Sites
- Site Name
- Ospedale Pediatrico Bambino Gesu
- Department Name
- Clinical Oncohematology and Cell Therapy Studies
- Contact Person Name
- Franco Locatelli
- Contact Person Email
- franco.locatelli@opbg.net
- Site Name
- Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
- Department Name
- Aou Città Della Salute e Della Scienza di Torino
- Contact Person Name
- Franca Fagioli
- Contact Person Email
- fagioli@pediatria.unito.it
- Site Name
- Azienda Ospedaliera di Padova
- Department Name
- UOC Oncoematologia Pediatrica
- Contact Person Name
- Elisabetta Viscardi
- Contact Person Email
- elisabetta.viscardi@unipd.it
- Site Name
- Azienda Ospedaliera Universitaria Meyer IRCCS
- Department Name
- Oncology and Hematology Department
- Contact Person Name
- Annalisa Tondo
- Contact Person Email
- annalisa.tondo@meyer.it
- Site Name
- Fondazione IRCCS Istituto Nazionale Dei Tumori
- Department Name
- S.C. Pediatria Oncologica
- Contact Person Name
- Roberto Luksch
- Contact Person Email
- roberto.luksch@istitutotumori.mi.it
- Site Name
- IRCCS Istituto Giannina Gaslini
- Department Name
- Dipartimento Emato-Oncologia
- Contact Person Name
- Carla Manzitti
- Contact Person Email
- carlamanzitti@gaslini.org
- Site Name
- Azienda Ospedaliera di Padova (additional entry present in list)
Sponsor
Primary sponsor
- Full Name
- The University Of Birmingham
- Organisation Type
- Educational Institution
- Country Of Registered Address
- United Kingdom
Contract research organisations
- Name
- Julius Clinical International B.V.
- Responsibilities
- sponsorDuties codes: 1
- Name
- Viedoc Technologies AB
- Responsibilities
- sponsorDuties codes: 7 (electronic data capture)
Third parties
- {"country":"Belgium","full_name":"European Society for Paediatric Oncology","duties_or_roles":"code:4","organisation_type":"Health care"}
- {"country":"Denmark","full_name":"Frederiksberg Hospital","duties_or_roles":"code:1","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"France","full_name":"Mapi Research Trust","duties_or_roles":"code:15 (Quality of Life PedsQL)","organisation_type":"Pharmaceutical company"}
- {"country":"Italy","full_name":"Consorzio Per Valutazioni Biologiche E Farmacologiche","duties_or_roles":"code:1","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Recordati Pharmaceuticals Limited","duties_or_roles":"code:14","organisation_type":"Pharmaceutical company"}
- {"country":"France","full_name":"Orphelia Pharma","duties_or_roles":"code:14","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Newcastle University","duties_or_roles":"code:4","organisation_type":"Educational Institution"}
- {"country":"Sweden","full_name":"Viedoc Technologies AB","duties_or_roles":"code:7","organisation_type":"Non-Pharmaceutical company"}
- {"country":"Netherlands","full_name":"Julius Clinical International B.V.","duties_or_roles":"code:1","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"St James's University Hospital","duties_or_roles":"code:4","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"Sweden","full_name":"ApoEx NKS","duties_or_roles":"code:14","organisation_type":"Health care"}
Investigational products
- Investigational Product Name
- TEMOZOLOMIDE
- Active Substance
- Temozolomide
- Modality
- Small molecule
- Routes Of Administration
- ORAL USE
- Route
- Oral
- Investigational Product Name
- BEVACIZUMAB
- Active Substance
- Bevacizumab
- Modality
- Monoclonal antibody
- Routes Of Administration
- INTRAVENOUS
- Route
- Intravenous
- Investigational Product Name
- IRINOTECAN
- Active Substance
- Irinotecan
- Modality
- Small molecule
- Routes Of Administration
- INTRAVENOUS USE
- Route
- Intravenous
- Investigational Product Name
- TOPOTECAN
- Active Substance
- Topotecan
- Modality
- Small molecule
- Routes Of Administration
- INTRAVENOUS USE
- Route
- Intravenous
- Investigational Product Name
- Qarziba 4.5 mg/mL concentrate for solution for infusion
- Active Substance
- Dinutuximab beta
- Modality
- Monoclonal antibody
- Routes Of Administration
- INTRAVENOUS USE
- Route
- Intravenous
- Authorisation Status
- Authorised (marketing authorisation EU/1/17/1191/001)
- Investigational Product Name
- Kimozo 40 mg/ml, suspension buvable
- Active Substance
- Temozolomide
- Modality
- Small molecule
- Routes Of Administration
- ORAL USE
- Route
- Oral
- Authorisation Status
- Authorised (marketing authorisation number 34009 589 035 7 1, authorisation country FR)
- Orphan Designation
- Yes
- Combination Treatment
- Yes
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