Clinical trial • Phase III • Oncology

SACITUZUMAB TIRUMOTECAN for Urothelial carcinoma | Bladder cancer

Phase III trial of SACITUZUMAB TIRUMOTECAN for Urothelial carcinoma | Bladder cancer.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Urothelial carcinoma | Bladder cancer
Trial Stage
Phase III
Drug Modality
ADC | Monoclonal antibody | Small molecule

Key dates

Initial CTIS Submission Date
09-12-2025
First CTIS Authorization Date
20-04-2026

Trial design

Randomised, open-label, investigator's choice non-platinum chemotherapy: paclitaxel (up to 175 mg/m2, intravenous infusion), docetaxel (up to 75 mg/m2, intravenous infusion), vinflunine (up to 320 mg/m2, intravenous infusion) — schedule not specified in provided data.-controlled Phase III trial in Belgium, France, Germany and others.

Randomised
Yes
Open Label
Yes
Comparator
Investigator's choice non-platinum chemotherapy: Paclitaxel (up to 175 mg/m2, intravenous infusion), Docetaxel (up to 75 mg/m2, intravenous infusion), Vinflunine (up to 320 mg/m2, intravenous infusion) — schedule not specified in provided data.
Target Sample Size
274

Eligibility

Recruits 274 No vulnerable population selected. Standard informed consent from adult participants; no assent or paediatric consent procedures described..

Vulnerable Population
No vulnerable population selected. Standard informed consent from adult participants; no assent or paediatric consent procedures described.

Inclusion criteria

  • {"criterion_text":"- Has histologically documented locally advanced/metastatic urothelial cancer. Locally advanced disease must not be amenable to resection or radiation with curative intent per investigator assessment.\n- If human immunodeficiency virus (HIV) positive, has well-controlled HIV on antiretroviral therapy (ART).\n- If hepatitis B surface antigen (HBsAg) positive, has received hepatitis B virus (HBV) antiviral therapy for at least 4 weeks and has undetectable HBV viral load.\n- If history of hepatitis C virus (HCV) infection, has undetectable HCV viral load.\n- Has adequate organ function.\n- Has measurable disease per Response Evaluation Criteria In Solid Tumors Version 1.1 (RECIST 1.1) as assessed by the investigator.\n- Has received treatment with anti-programmed cell death [ligand] 1 (anti-PD-[L]1) therapy, platinum-based chemotherapy, and enfortumab vedotin (EV).\n- Prior therapy with disitamab vedotin (DV) is allowed but will not meet the requirement for prior treatment with EV, except in China, where participants may have received DV instead of EV before study entry.\n- Has received a maximum of 3 prior lines of therapy.\n- Has experienced radiographic disease progression on or after the immediate prior line of therapy before study entry.\n- Has Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 assessed within 7 days of randomization.\n- Is eligible to receive at least one of the control arm nonplatinum chemotherapy options (paclitaxel, docetaxel, or vinflunine).\n- Is able to provide archival tumor tissue sample or newly obtained biopsy of a tumor lesion not previously irradiated."}

Exclusion criteria

  • {"criterion_text":"- Has history of documented severe dry eye syndrome, severe Meibomian gland disease and/or blepharitis, or severe corneal disease that prevents/delays corneal healing.\n- Has received prior chemotherapy for urothelial cancer with any of the study therapies in the control arm (paclitaxel, docetaxel, and vinflunine).\n- Has received an investigational agent or has used an investigational device within 4 weeks prior to study intervention administration.\n- Has a diagnosis of immunodeficiency or is receiving chronic systemic steroid therapy or any other form of immunosuppressive therapy within 7 days prior to the first dose of study intervention.\n- Has a known additional malignancy that is progressing or has required active treatment within the past 3 years.\n- Has a current or past history of central nervous system (CNS) metastases and/or carcinomatous meningitis.\n- Has an active infection requiring systemic therapy other than those permitted per protocol.\n- Has a history of stem cell/solid organ transplant.\n- Has not adequately recovered from major surgery, or has ongoing surgical complications.\n- Has uncontrolled, significant cardiovascular disease or cerebrovascular disease.\n- Has a history of (noninfectious) pneumonitis/interstitial lung disease that required steroids or has current pneumonitis/interstitial lung disease.\n- HIV-infected participants with a history of Kaposi’s sarcoma and/or Multicentric Castleman’s Disease.\n- Has received prior systemic anticancer therapy within 4 weeks or 5 half-lives (whichever is shorter) and has not recovered to grade ≤ 1 or baseline from adverse event (AE) associated with anticancer therapy.\n- Has received prior therapy with trophoblast cell-surface antigen 2 (TROP2)-targeted antibody drug conjugate (ADC).\n- Has received prior therapy with a topoisomerase 1 inhibitor-containing ADC.\n- Has completed prior external radiotherapy within 6 weeks or stereotactic radiotherapy within 4 weeks of start of study intervention, or has radiation related toxicities, requiring corticosteroids.\n- Has received a live or live-attenuated vaccine within 30 days before the first dose of study intervention. Administration of killed vaccines is allowed."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Overall Survival (OS)","definition_or_measurement_approach":""}

Secondary endpoints

  • {"endpoint_text":"- Progression-Free Survival (PFS)","definition_or_measurement_approach":"Per RECIST 1.1 as assessed by investigator (as stated in secondary objectives)."}
  • {"endpoint_text":"- Objective Response Rate (ORR)","definition_or_measurement_approach":"Per RECIST 1.1 as assessed by investigator."}
  • {"endpoint_text":"- Duration of Response (DOR)","definition_or_measurement_approach":"Per RECIST 1.1 as assessed by investigator."}
  • {"endpoint_text":"- Number of Participants Who Experience an Adverse Event (AE)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Number of Participants Who Discontinue Study Treatment Due to an AE","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Change From Baseline in European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire-Core 30 (EORTC QLQ-C30) Global Health Status/Quality of Life (Items 29 and 30) Combined Score","definition_or_measurement_approach":"Change from baseline in specified EORTC QLQ-C30 combined score (items 29 and 30)."}
  • {"endpoint_text":"- Change From Baseline in EORTC QLQ-C30 Physical Functioning (Items 1-5) Combined Score","definition_or_measurement_approach":"Change from baseline in specified EORTC QLQ-C30 physical functioning combined score (items 1-5)."}
  • {"endpoint_text":"- Change From Baseline in EORTC QLQ-C30 Role Functioning (Items 6 and 7) Combined Score","definition_or_measurement_approach":"Change from baseline in specified EORTC QLQ-C30 role functioning combined score (items 6 and 7)."}
  • {"endpoint_text":"- Change From Baseline in EORTC QLQ-C30 Fatigue (Items 10, 12, and 18) Combined Score","definition_or_measurement_approach":"Change from baseline in specified EORTC QLQ-C30 fatigue combined score (items 10, 12, 18)."}
  • {"endpoint_text":"- Change From Baseline in EORTC QLQ-C30 Nausea/Vomiting (Items 14 and 15) Combined Score","definition_or_measurement_approach":"Change from baseline in specified EORTC QLQ-C30 nausea/vomiting combined score (items 14 and 15)."}
  • {"endpoint_text":"- Change From Baseline in EORTC QLQ-C30 Diarrhea (Item 17) Score","definition_or_measurement_approach":"Change from baseline in specified EORTC QLQ-C30 diarrhea score (item 17)."}

Recruitment

Planned Sample Size
274
Recruitment Window Months
47
Consent Approach
Informed consent obtained from participants using country-specific main consent forms. Main consent documents are provided in country-specific languages (examples in dossier: English, French, Dutch, German, Greek, Italian, Spanish, Swedish). No assent or paediatric consent procedures are described.

Geography

Total Number Of Sites
59
Total Number Of Participants
265

Belgium

Earliest CTIS Part Ii Submission Date
19-03-2026
Latest Decision Or Authorization Date
20-04-2026
Processing Time Days
32
Number Of Sites
4
Number Of Participants
20

Sites

Site Name
CHC MontLegia
Department Name
Oncology
Contact Person Name
Lyonel Herman
Contact Person Email
lyonel.herman@chc.be
Site Name
Az Maria Middelares Gent
Department Name
Oncology
Contact Person Name
Christof Vulsteke
Site Name
Cliniques Universitaires Saint-Luc
Department Name
Oncology
Contact Person Name
Emmanual Seront
Site Name
Universitair Ziekenhuis Gent
Department Name
Oncology
Contact Person Name
Sylvie Rottey
Contact Person Email
Sylvie.rottey@uzgent.be

France

Earliest CTIS Part Ii Submission Date
05-03-2026
Latest Decision Or Authorization Date
21-04-2026
Processing Time Days
47
Number Of Sites
14
Number Of Participants
80

Sites

Site Name
Centre Antoine Lacassagne
Department Name
Oncology
Contact Person Name
Delphine BORCHIELLINI
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Oncology and Cellular Therapy
Contact Person Name
Mathieu JAMELOT
Contact Person Email
mathieu.jamelot@aphp.fr
Site Name
Centre Hospitalier Universitaire Amiens Picardie
Department Name
Medical Oncology
Contact Person Name
Aline HOUESSINON
Contact Person Email
houessinon.aline@chu-amiens.fr
Site Name
Centre De Lutte Contre Le Cancer Eugene Marquis
Department Name
Oncology
Contact Person Name
Brigitte LAGUERRE
Contact Person Email
b.laguerre@rennes.unicancer.fr
Site Name
Centre Hospitalier Universitaire De Nimes
Department Name
Department of Medical Oncology
Contact Person Name
Nadine HOUEDE
Contact Person Email
nadine.houede@chu-nimes.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Oncology
Contact Person Name
Loïc JAFFRELOT
Contact Person Email
loic.jaffrelot@aphp.fr
Site Name
Centre Jean Perrin
Department Name
Oncology
Contact Person Name
Hakim MAHAMMEDI
Site Name
Centre Leon Berard
Department Name
Oncology
Contact Person Name
Aude FLECHON
Contact Person Email
aude.flechon@lyon.unicancer.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Oncology
Contact Person Name
Charlotte JOLY
Contact Person Email
charlotte.joly@aphp.fr
Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
Oncology
Contact Person Name
Benjamin AUBERGER
Contact Person Email
benjamin.auberger@chu-brest.fr
Site Name
Institut Gustave Roussy
Department Name
Oncology
Contact Person Name
Yohann LORIOT
Contact Person Email
yohann.loriot@gustaveroussy.fr
Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Oncology
Contact Person Name
Marine GROSS-GOUPIL
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Oncology
Contact Person Name
Constance THIBAUT
Contact Person Email
constance.thibault@aphp.fr
Site Name
Centr Georges Francois Leclerc
Department Name
Medical Oncology
Contact Person Name
Sylvain LADOIRE
Contact Person Email
sladoire@cgfl.fr

Germany

Earliest CTIS Part Ii Submission Date
12-03-2026
Latest Decision Or Authorization Date
25-04-2026
Processing Time Days
44
Number Of Sites
10
Number Of Participants
34

Sites

Site Name
St. Elisabeth Gruppe GmbH Katholische Kliniken Rhein-Ruhr
Department Name
Klinik für Urologie, Zentrum für Uro-Onkologie der Ruhr-Universität Bochum
Contact Person Name
Karl Tully
Contact Person Email
Karl.tully@elisabethgruppe.de
Site Name
University Medical Center Hamburg-Eppendorf
Department Name
Klinik für Onkologie, II. Medizinische Klinik und Poliklinik
Contact Person Name
Gunhild von Amsberg
Contact Person Email
g.von-amsberg@uke.de
Site Name
Universitaetsklinikum Duesseldorf AöR
Department Name
Klinik für Urologie
Contact Person Name
Günter Niegisch
Site Name
Universitaetsklinikum Heidelberg AöR
Department Name
Klinik f. Medizinische Onkologie
Contact Person Name
Stefanie Zschäbitz
Site Name
Universitaetsklinikum Regensburg AöR
Department Name
Klinik für Urologie
Contact Person Name
Marco Schnabel
Contact Person Email
mschnabel@csj.de
Site Name
Universitaetsklinikum Ulm AöR
Department Name
Klinik für Urologie und Kinderurologie
Contact Person Name
Friedemann Zengerling
Site Name
Klinikum Der Landeshauptstadt Stuttgart gKAöR
Department Name
Klinik für Urologie und Transplantationschirurgie
Contact Person Name
Jens Bedke
Contact Person Email
j.bedke@klinikum-stuttgart.de
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
Klinik für Urologie
Contact Person Name
Maria De Santis
Contact Person Email
maria.de-santis@charite.de
Site Name
Technische Universitaet Dresden
Department Name
AöR des Freistaates Sachsen, Klinik und Poliklinik für Urologie
Contact Person Name
Severine Banek
Contact Person Email
severine.banek@ukdd.de
Site Name
Universitaet Muenster
Department Name
Klinik für Urologie
Contact Person Name
Martin Bögemann
Contact Person Email
Uroonkologie@ukmuenster.de

Greece

Earliest CTIS Part Ii Submission Date
29-12-2025
Latest Decision Or Authorization Date
20-04-2026
Processing Time Days
112
Number Of Sites
5
Number Of Participants
20

Sites

Site Name
Athens Medical Center S.A.
Department Name
GU Department of Oncology
Contact Person Name
Marinos Tsiatas
Contact Person Email
tsiatas@hotmail.com
Site Name
General Oncological Hospital Of Kifissia Agioi Anargyroi
Department Name
Department of Medical Oncology
Contact Person Name
Roubini Zakopoulou
Contact Person Email
rzakopoul@gmail.com
Site Name
University General Hospital Attikon General Hospital Of West Attica H Agia Varvara
Department Name
2nd University Propaedeutic Pathology clinic
Contact Person Name
Aristotelis Bamias
Contact Person Email
abamias@med.uoa.gr
Site Name
Athens Medical Center S.A.
Department Name
4th Department of Medical Oncology
Contact Person Name
Ippokratis Korantzis
Contact Person Email
ippokratis.korantzis@gmail.com
Site Name
Metropolitan General Hospital Healthcare Facilities Operation And Management Single Member S.A.
Department Name
Oncologic Clinical Trials and Research Clinic
Contact Person Name
Evangelos Bournakis
Contact Person Email
vagimith@yahoo.com

Italy

Earliest CTIS Part Ii Submission Date
29-12-2025
Latest Decision Or Authorization Date
21-04-2026
Processing Time Days
113
Number Of Sites
9
Number Of Participants
32

Sites

Site Name
Humanitas Mirasole S.p.A.
Department Name
Oncologia Medica ed Ematologia
Contact Person Name
Paolo Zucali
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
Oncologia Medica
Contact Person Name
Roberto Iacovelli
Site Name
IRCCS Ospedale Policlinico San Martino
Department Name
Oncologia Medica 1
Contact Person Name
Giuseppe Fornarini
Site Name
Istituto Nazionale Dei Tumori
Department Name
Struttura Complessa Oncologia Medica 1
Contact Person Name
Valentina Guadalupi
Site Name
Azienda Unita' Sanitaria Locale Toscana Sud Est
Department Name
Oncologia Medica
Contact Person Name
Alketa Hamzaj
Site Name
Azienda Ospedaliera Di Rilievo Nazionale Antonio Cardarelli
Department Name
UOC Oncologia
Contact Person Name
Sarah Scagliarini
Site Name
Centro Ricerche Cliniche Di Verona S.r.l.
Department Name
Centro Ricerche Cliniche di Verona
Contact Person Name
Andrea Zivi
Contact Person Email
andrea.zivi@aovr.veneto.it
Site Name
Ospedale Generale Provinciale Di Macerata
Department Name
UOC Oncologia
Contact Person Name
Nicola Battelli
Site Name
Azienda Ospedaliero-Universitaria San Luigi Gonzaga
Department Name
S.C.D.U. Oncologia Medica
Contact Person Name
Consuelo Buttigliero
Contact Person Email
consuelo.buttigliero@unito.it

Spain

Earliest CTIS Part Ii Submission Date
26-03-2026
Latest Decision Or Authorization Date
24-04-2026
Processing Time Days
29
Number Of Sites
9
Number Of Participants
49

Sites

Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Oncología Médica
Contact Person Name
Pablo Gajate Borau
Contact Person Email
pgajateborau@gmail.com
Site Name
Hospital Clinico San Carlos
Department Name
Oncología Médica
Contact Person Name
Javier Puente Vázquez
Contact Person Email
javierpuente.hcsc@gmail.com
Site Name
Institut Catala D'oncologia
Department Name
Oncología Médica
Contact Person Name
Juan Martin Liberal
Contact Person Email
jmartinliberal@iconcologia.net
Site Name
Hospital Universitari Vall D Hebron
Department Name
Oncología Médica
Contact Person Name
Rafael Morales Barrera
Contact Person Email
rmorales@vhio.net
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Oncología Médica
Contact Person Name
Begoña Perez Valderrama
Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Oncología Médica
Contact Person Name
Ignacio Durán Martínez
Contact Person Email
ignacioduranmartinez@gmail.com
Site Name
Complejo Hospitalario Universitario Insular Materno Infantil
Department Name
Oncología Médica
Contact Person Name
Alfonso Gómez de Liaño Lista
Contact Person Email
agomlis@gobiernodecanarias.org
Site Name
Hospital Universitario 12 De Octubre
Department Name
Oncología Médica
Contact Person Name
Daniel Castellano Gauna
Contact Person Email
cdanicas@hotmail.com
Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Oncología Médica
Contact Person Name
Ignacio Durán Martínez
Contact Person Email
ignacioduranmartinez@gmail.com

Sweden

Earliest CTIS Part Ii Submission Date
19-03-2026
Latest Decision Or Authorization Date
20-04-2026
Processing Time Days
32
Number Of Sites
2
Number Of Participants
8

Sites

Site Name
Region Joenkoepings Laen
Department Name
Onkologkliniken
Contact Person Name
Dimitrios Papantoniou
Contact Person Email
dimitrios.papantoniou@rjl.se
Site Name
Karolinska University Hospital
Department Name
Urologisk Onkologi
Contact Person Name
Anders Ullen

Netherlands

Earliest CTIS Part Ii Submission Date
19-03-2026
Latest Decision Or Authorization Date
20-04-2026
Processing Time Days
32
Number Of Sites
6
Number Of Participants
22

Sites

Site Name
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Department Name
Interne Oncologie / Medical Oncology
Contact Person Name
Debbie Robbrecht
Contact Person Email
interne.oncologie@erasmusmc.nl
Site Name
Sint Antonius Ziekenhuis Stichting
Department Name
Interne geneeskunde, medische oncologie
Contact Person Name
Maartje Los
Site Name
Isala Klinieken Stichting
Department Name
Interne geneeskunde
Contact Person Name
Elianne De Boer
Contact Person Email
rioc@isala.nl
Site Name
Het Nederlands Kanker Instituut-Antoni van Leeuwenhoek Ziekenhuis Stichting
Department Name
Vakgroep Interne Geneeskunde
Contact Person Name
Michiel Van der Heijden
Contact Person Email
urologieinterne@nki.nl
Site Name
Stichting Elisabeth-TweeSteden Ziekenhuis
Department Name
Interne geneeskunde - Oncologie
Contact Person Name
Janneke Ham
Contact Person Email
trialbureau-onco@etz.nl
Site Name
Academisch Ziekenhuis Maastricht
Department Name
Medical Oncology
Contact Person Name
Thomas Kerkhofs

Sponsor

Primary sponsor

Full Name
Merck Sharp & Dohme LLC
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Signant Health Global LLC
Responsibilities
sponsorDuties codes: 7
Name
Parexel International Corp.
Responsibilities
EUB services (call center and medical services) (sponsorDuties code: 15)
Name
Iqvia Laboratories Limited
Responsibilities
sponsorDuties codes: 4
Name
Frontage Laboratories Inc.
Responsibilities
sponsorDuties codes: 4
Name
Bioclinica Inc.
Responsibilities
sponsorDuties codes: 4

Third parties

  • {"country":"United States","full_name":"Signant Health Global LLC","duties_or_roles":"sponsorDuties codes: 7","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Parexel International Corp.","duties_or_roles":"EUB services (call center and medical services) (sponsorDuties code: 15)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Signant Health Global LLC","duties_or_roles":"sponsorDuties codes: 3","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Iqvia Laboratories Limited","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Frontage Laboratories Inc.","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Ventana (Roche Tissue Diagnostics)","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Industry"}

Investigational products

Investigational Product Name
MK-2870
Active Substance
SACITUZUMAB TIRUMOTECAN
Modality
ADC | Monoclonal antibody
Routes Of Administration
INTRAVENOUS INFUSION
Route
Intravenous infusion
Authorisation Status
1
Maximum Dose
4 mg/kg
Investigational Product Name
DOCETAXEL
Active Substance
DOCETAXEL
Modality
Small molecule
Routes Of Administration
INTRAVENOUS INFUSION
Route
Intravenous infusion
Authorisation Status
2
Maximum Dose
75 mg/m2
Investigational Product Name
VINFLUNINE
Active Substance
VINFLUNINE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS INFUSION
Route
Intravenous infusion
Authorisation Status
2
Maximum Dose
320 mg/m2
Investigational Product Name
PACLITAXEL
Active Substance
PACLITAXEL
Modality
Small molecule
Routes Of Administration
INTRAVENOUS INFUSION
Route
Intravenous infusion
Authorisation Status
2
Maximum Dose
175 mg/m2

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