Clinical trial • Phase III • Oncology

SACITUZUMAB TIRUMOTECAN for Non-small cell lung cancer | Nonsquamous non-small cell lung cancer

Phase III trial of SACITUZUMAB TIRUMOTECAN for Non-small cell lung cancer | Nonsquamous non-small cell lung cancer.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Non-small cell lung cancer | Nonsquamous non-small cell lung cancer
Trial Stage
Phase III
Drug Modality
ADC | Small molecule

Key dates

Initial CTIS Submission Date
27-09-2023
First CTIS Authorization Date
06-02-2024

Trial design

Randomised, open-label, docetaxel (anhydrous docetaxel) iv; maximum indicated dose 75 mg/m2 (intravenous infusion) and pemetrexed iv; maximum indicated dose 500 mg/m2 (intravenous infusion). supportive/auxiliary medications listed (e.g., dexamethasone, antihistamines, h2-antagonists, paracetamol combinations) per trial documents.-controlled Phase III trial in Germany, Czechia, Greece and others.

Randomised
Yes
Open Label
Yes
Comparator
Docetaxel (anhydrous docetaxel) IV; maximum indicated dose 75 mg/m2 (intravenous infusion) and Pemetrexed IV; maximum indicated dose 500 mg/m2 (intravenous infusion). Supportive/auxiliary medications listed (e.g., dexamethasone, antihistamines, H2-antagonists, paracetamol combinations) per trial documents.
Biomarker Stratified
True, biomarker: EGFR mutation status (EGFR mutations vs other genomic alterations)
Target Sample Size
455

Eligibility

Recruits 455 The record indicates vulnerable population selection (isVulnerablePopulationSelected = true). Informed consent is documented via country-specific L1_ICF_Main consent documents (available for DEU, CZE, GRC, FRA, ITA, POL, ESP, etc.). Consent is provided by the adult participant (minimum age requirement: At least 18 years). No assent procedures for minors are described in the available material..

Vulnerable Population
The record indicates vulnerable population selection (isVulnerablePopulationSelected = true). Informed consent is documented via country-specific L1_ICF_Main consent documents (available for DEU, CZE, GRC, FRA, ITA, POL, ESP, etc.). Consent is provided by the adult participant (minimum age requirement: At least 18 years). No assent procedures for minors are described in the available material.

Inclusion criteria

  • {"criterion_text":"- Histologically- or cytologically-documented advanced (Stage III not eligible for resection or curative radiation) or metastatic non-squamous NSCLC with specific mutations\n- Have an ECOG performance status of 0 or 1 within 3 days before randomization\n- Documentation of locally assessed radiological disease progression while on or after last treatment based on Response Evaluation Criteria in Solid Tumors Version (RECIST) 1.1\n- Participants with genome mutations must have received 1 or 2 prior lines of epidermal growth factor receptor tyrosine kinase inhibitor (EGFR TKI), including a third generation TKI for participants with a T790M mutation; and 1 platinum-based therapy after progression on or after EGFR TKI\n- At least 18 years of age at the time of providing informed consent\n- Measurable disease per RECIST 1.1 as assessed by the local site investigator\n- Archival tumor tissue sample or newly obtained core, incisional, or excisional biopsy of a tumor lesion not previously irradiated has been provided\n- Participants who have AEs due to previous anticancer therapies must have recovered to Grade ≤1 or baseline\n- Participants who are hepatitis B surface antigen (HBsAg) positive are eligible if they have received HBV antiviral therapy for at least 4 weeks, and have undetectable HBV viral load prior to randomization\n- HIV-infected participants must have well controlled HIV on ART"}

Exclusion criteria

  • {"criterion_text":"- Has predominantly squamous cell histology NSCLC\n- Completed palliative radiotherapy within 7 days of the first dose. Participants must have recovered from all radiation-related toxicities and not require corticosteroids\n- Received radiation therapy to the lung that is >30 Gy within 6 months of the first dose of study intervention\n- Received prior treatment with a trophoblast cell-surface antigen 2 (TROP2)-targeted antibody-drug conjugate (ADC)\n- Received prior treatment with a topoisomerase I-containing ADC\n- Has received an investigational agent or has used an investigational device within 4 weeks prior to study intervention administration\n- Known additional malignancy that is progressing or has required active treatment within the past 3 years\n- Active infection requiring systemic therapy\n- History of noninfectious pneumonitis/ILD that required steroids or has current pneumonitis/ILD\n- Has known active central nervous system metastases and/or carcinomatous meningitis. Participants with previously treated brain metastases may participate provided they are clinically stable, radiologically stable for at least 4 weeks and do not require glucocorticoids for at least 14 days prior to randomization.\n- HIV-infected participants with a history of Kaposi’s sarcoma and/or Multicentric Castleman’s Disease\n- Has mixed tumor(s) with small cell elements\n- Concurrent active Hepatitis B (defined as HBsAg positive and/or detectable HBV DNA) and Hepatitis C virus (defined as anti-HCV Ab positive and detectable HCV RNA) infection\n- Has active inflammatory bowel disease requiring immunosuppressive medication or previous history of inflammatory bowel disease\n- Has Grade ≥2 peripheral neuropathy\n- Has history of documented severe dry eye syndrome, severe Meibomian gland disease and/or blepharitis, or corneal disease that prevents/delays corneal healing\n- Has uncontrolled, significant cardiovascular disease or cerebrovascular disease\n- Has an EGFR T790M mutation and has not received a third generation EGFR TKI (eg, osimertinib)\n- Received prior systemic anticancer therapy including investigational agents within 4 weeks or 5 half-lives (whichever is shorter) before randomization\n- Received a live or live-attenuated vaccine within 30 days before the first dose of study intervention"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Progression-free Survival (PFS) of Participants with NSCLC with Epidermal Growth Factor Receptor (EGFR) mutations","definition_or_measurement_approach":"PFS measured per RECIST 1.1 as assessed by blinded independent central review (BICR) (as specified in main objectives)."}
  • {"endpoint_text":"- Overall Survival (OS) of Participants with NSCLC with EGFR mutations","definition_or_measurement_approach":"Overall survival measured as time to death from any cause (OS); standard survival follow-up (definition not further specified in the available extract)."}

Secondary endpoints

  • {"endpoint_text":"- PFS of All Participants with NSCLC","definition_or_measurement_approach":"PFS per RECIST 1.1 as assessed by BICR in all participants with NSCLC."}
  • {"endpoint_text":"- OS of All Participants with NSCLC","definition_or_measurement_approach":"Overall survival (OS) in all participants with NSCLC (time to death)."}
  • {"endpoint_text":"- Objective Response Rate (ORR) of Participants with NSCLC with EGFR mutations","definition_or_measurement_approach":"ORR assessed per RECIST 1.1 based on BICR."}
  • {"endpoint_text":"- ORR of All Participants with NSCLC","definition_or_measurement_approach":"ORR per RECIST 1.1 (methodology: BICR for assessments as specified)."}
  • {"endpoint_text":"- Duration of Response (DOR) of All Participants with NSCLC","definition_or_measurement_approach":"DOR (definition not further specified in the extract)."}
  • {"endpoint_text":"- Change in Score from Baseline in Global Health Status/QoL Score (European Organisation for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire-Core 30 (QLQ-C30) items 29 and 30)","definition_or_measurement_approach":"Change from baseline in EORTC QLQ-C30 items 29 and 30 (global health status/QoL)."}
  • {"endpoint_text":"- Change in Score from Baseline in Dyspnea score (EORTC QLQ-C30 item 8)","definition_or_measurement_approach":"Change from baseline in EORTC QLQ-C30 item 8 (dyspnea)."}
  • {"endpoint_text":"- Change in Score from Baseline in Cough (EORTC Quality of Life Questionnaire-Lung Cancer 13 (QLQ-LC13) item 31)","definition_or_measurement_approach":"Change from baseline in EORTC QLQ-LC13 item 31 (cough)."}
  • {"endpoint_text":"- Change in Score from Baseline in Chest pain (EORTC QLQ-LC13 item 40)","definition_or_measurement_approach":"Change from baseline in EORTC QLQ-LC13 item 40 (chest pain)."}
  • {"endpoint_text":"- Time to Deterioration from Baseline in Global Health Status/QoL Score (EORTS QLQ-C30 items 29 and 30)","definition_or_measurement_approach":"Time to deterioration in EORTC QLQ-C30 items 29 and 30 (global health status/QoL)."}
  • {"endpoint_text":"- Time to Deterioration from Baseline in Dyspnea score (EORTC QLQ-C30 item 8)","definition_or_measurement_approach":"Time to deterioration in EORTC QLQ-C30 item 8 (dyspnea)."}
  • {"endpoint_text":"- Time to Deterioration from Baseline in Cough (EORTC Quality of Life Questionnaire-Lung Cancer 13 (QLQ-LC13) item 31)","definition_or_measurement_approach":"Time to deterioration in EORTC QLQ-LC13 item 31 (cough)."}
  • {"endpoint_text":"- Time to Deterioration from Baseline in Chest pain (EORTC QLQ-LC13 item 40)","definition_or_measurement_approach":"Time to deterioration in EORTC QLQ-LC13 item 40 (chest pain)."}
  • {"endpoint_text":"- Number of Participants Who Experience One or More Adverse Events (AEs)","definition_or_measurement_approach":"Count of participants experiencing ≥1 adverse event (AE); safety/tolerability monitoring (standard AE reporting)."}
  • {"endpoint_text":"- Number of Participants Who Discontinue Study Treatment Due to an Adverse Event (AE)","definition_or_measurement_approach":"Count of participants discontinuing study treatment due to AE (as reported in safety data)."}

Recruitment

Registry Or Advocacy Recruitment
True, Advocacy materials referenced (e.g., 'K2_Recruitment Doc Advocacy Card_DEU_DE_SM05_for pub' listed) — no specific registry or advocacy group name provided in the available extract.
Digital Remote Recruitment
True, digital/remote methods referenced via website materials (e.g., 'K2_Recruitment Doc Website_POL_PL'), ClinCard/ConneX travel/online patient card materials and other electronic patient information leaflets (documents listed for multiple countries).
Planned Sample Size
455
Recruitment Window Months
68
Consent Approach
Informed consent obtained from adult participants (minimum age ≥18). Country-specific main consent forms and information sheets (L1_ICF_Main consent documents) are available for DEU, CZE, GRC, FRA, ITA, POL, ESP and others; additional optional addenda and GDPR/data privacy documents are provided per country. No assent for minors is described.

Methods

  • Site-based recruitment via participating hospitals/clinics (site lists and contact persons provided for each country).
  • Use of recruitment materials (documented in K2 documents): patient brochures, patient visit guides, posters, master tissue brochures and invitation letters (country-specific K2_Recruitment Doc files for DEU, CZE, GRC, FRA, ITA, POL, ESP).
  • Use of central recruitment materials and procedures (K1_Recruitment Arrangements and IC Procedure documents, country-specific).
  • Digital recruitment/support materials: website presence (K2_Recruitment Doc Website_POL_PL), online ClinCard/ConneX travel/ClinCard materials (documents listed), and other electronic patient information templates.

Geography

Total Number Of Sites
41
Total Number Of Participants
107

Germany

Earliest CTIS Part Ii Submission Date
07-12-2023
Latest Decision Or Authorization Date
04-02-2026
Processing Time Days
790
Number Of Sites
6
Number Of Participants
15

Sites

Site Name
Technische Universitat Dresden
Department Name
Medizinische Fakultät Carl Gustav Carus Med. Klinik I
Contact Person Name
Felix Saalfeld
Site Name
KEM I Evang. Kliniken Essen-Mitte gGmbH
Department Name
Klinik für Innere Medizin IV
Contact Person Name
Sebastian Ertl
Contact Person Email
onkologie@kem-med.com
Site Name
Klinikum Chemnitz gGmbH
Department Name
Klinik für Innere Medizin IV
Contact Person Name
Stefan Hammerschmidt
Contact Person Email
s.hammerschmidt@skc.de
Site Name
Asklepios Kliniken Hamburg GmbH
Department Name
Klinik für Pneumologie
Contact Person Name
Claas Wesseler
Contact Person Email
c.wesseler@asklepios.com
Site Name
Universitaetsmedizin Goettingen
Department Name
Klinik für Hämatologie und Medizinische Onkologie
Contact Person Name
Tobias Overbeck
Site Name
Medical Center - University Of Freiburg
Department Name
Klinik für Innere Medizin I
Contact Person Name
Justyna Rawluk

Czechia

Earliest CTIS Part Ii Submission Date
13-10-2023
Latest Decision Or Authorization Date
04-02-2026
Processing Time Days
845
Number Of Sites
5
Number Of Participants
10

Sites

Site Name
Vseobecna Fakultni Nemocnice V Praze
Department Name
Onkologická klinika
Contact Person Name
Milada Zemanova
Contact Person Email
milada.zemanova@vfn.cz
Site Name
Fakultni Nemocnice Plzen
Department Name
Klinika pneumologie a ftizeologie
Contact Person Name
Martin Svatoň
Contact Person Email
SVATONM@fnplzen.cz
Site Name
Masarykuv Onkologicky Ustav
Department Name
Klinika komplexni onkologicke pece
Contact Person Name
Ondřej Bílek
Contact Person Email
bilek@mou.cz
Site Name
Nemocnice AGEL Ostrava-Vitkovice a.s.
Department Name
Plicni oddeleni
Contact Person Name
Jaromír Roubec
Contact Person Email
jaromir.roubec@vtn.agel.cz
Site Name
University Hospital Olomouc
Department Name
Klinika plicnich nemoci a tuberkulozy
Contact Person Name
Juraj Kultan
Contact Person Email
juraj.kultan@fnol.cz

Greece

Earliest CTIS Part Ii Submission Date
21-12-2023
Latest Decision Or Authorization Date
05-02-2026
Processing Time Days
777
Number Of Sites
6
Number Of Participants
18

Sites

Site Name
Henry Dunant Hospital Center
Department Name
D Oncology department
Contact Person Name
Ioannis Mountzios
Contact Person Email
gmountzios@gmail.com
Site Name
General Hospital Of Thessaloniki Papageorgiou
Department Name
Papageorgiou General Hospital of Thessaloniki Molecular Medicine Clinical Trials Department
Contact Person Name
Sofia Baka
Contact Person Email
bakasofia@hotmail.com
Site Name
Thoracic General Hospital Of Athens I Sotiria
Department Name
3rd Department of Internal Medicine and Laboratory - Oncology Unit
Contact Person Name
Konstantinos Syrigos
Contact Person Email
ksyrigos.trials@gmail.com
Site Name
University General Hospital Attikon General Hospital Of West Attica H Agia Varvara
Department Name
4th Department of Internal Medicine Hematology Oncology Unit, NKUA
Contact Person Name
Anna Koumarianou
Contact Person Email
akoumari@yahoo.es
Site Name
Areteio Hospital
Department Name
Oncology Unit, B' Surgery Department
Contact Person Name
Flora Zagouri
Contact Person Email
florazagouri@yahoo.co.uk
Site Name
Theageneio Cancer Hospital
Department Name
1st Department of Medical Oncology
Contact Person Name
Pavlos Papakotoulas
Contact Person Email
papakotoulas@gmail.com

France

Earliest CTIS Part Ii Submission Date
07-12-2023
Latest Decision Or Authorization Date
09-02-2026
Processing Time Days
795
Number Of Sites
5
Number Of Participants
15

Sites

Site Name
Centre Leon Berard
Department Name
Oncology
Contact Person Name
Maurice Perol
Site Name
Institut Bergonie
Department Name
Oncology
Contact Person Name
Sophie Cousin
Contact Person Email
s.cousin@bordeaux.unicancer.fr
Site Name
GIE Groupe hospitalier Paris Saint-Joseph/Vinci
Department Name
medical oncology departement
Contact Person Name
Carole Helissey
Contact Person Email
carole.helissey@gmail.com
Site Name
CHU De Rouen
Department Name
Pneumology, intensive care and thoracic oncology
Contact Person Name
Florian Guisier
Contact Person Email
florian.guisier@chu-rouen.fr
Site Name
Institut Curie
Department Name
Oncology
Contact Person Name
Catherine Daniel
Contact Person Email
catherine.daniel@curie.fr

Italy

Earliest CTIS Part Ii Submission Date
07-12-2023
Latest Decision Or Authorization Date
05-02-2026
Processing Time Days
791
Number Of Sites
5
Number Of Participants
15

Sites

Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
Oncologia Medica
Contact Person Name
Angelo Delmonte
Contact Person Email
angelo.delmonte@irst.emr.it
Site Name
I.F.O. Istituti Fisioterapici Ospitalieri
Department Name
Oncologia Medica 2
Contact Person Name
Federico Cappuzzo
Contact Person Email
federico.cappuzzo@ifo.it
Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
Struttura Complessa Oncologia Medica 1
Contact Person Name
Arsela Prelaj
Site Name
Humanitas Research Hospital
Department Name
Oncologia medica ed ematologia (Cancer Center)
Contact Person Name
Giovanna Finocchiaro
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
Oncologia Medica
Contact Person Name
Emilio Bria

Poland

Earliest CTIS Part Ii Submission Date
21-12-2023
Latest Decision Or Authorization Date
08-02-2026
Processing Time Days
780
Number Of Sites
7
Number Of Participants
18

Sites

Site Name
Uniwersytecki Szpital Kliniczny Nr 4 W Lublinie
Department Name
Centrum Innowacyjnych Terapii
Contact Person Name
Tomasz Jankowski
Contact Person Email
onkotorun@gmail.com
Site Name
Swietokrzyskie Centrum Onkologii Samodzielny Publiczny Zaklad Opieki Zdrowotnej W Kielcach
Department Name
Klinika Onkologii Klinicznej
Contact Person Name
Kinga Szydziak – Zwierzyńska
Site Name
Centrum Onkologii Im. Prof. Franciszka Lukaszczyka W Bydgoszczy
Department Name
Ambulatorium Chemioterapii
Contact Person Name
Bogdan Żurawski
Site Name
Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy (Gliwice)
Department Name
Oddzial w Gliwicach II Klinika Radioterapii i Chemioterapii
Contact Person Name
Adam Idasiak
Contact Person Email
CWBK@gliwie.nio.gv.pl
Site Name
INSTYTUT GRUŹLICY I CHORÓB PŁUC
Department Name
III Klinika Chorób Płuc i Onkologii
Contact Person Name
Mateusz Polaczek
Contact Person Email
bk3@igichp.edu.pl
Site Name
Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy (Warsaw)
Department Name
Klinika Nowotworow Pluca i Klatki Piersiowej
Contact Person Name
Dariusz Kowalski
Contact Person Email
dariusz.kowalski@nio.gov.pl
Site Name
Wojewodzki Szpital Im. Sw.Ojca Pio W Przemyslu
Department Name
Oddzial Onkologiczny z Pododdzialem Dziennej Chemioterapii
Contact Person Name
Kamil Kuć
Contact Person Email
kkuc@wszp.pl

Spain

Earliest CTIS Part Ii Submission Date
12-12-2023
Latest Decision Or Authorization Date
12-03-2026
Processing Time Days
821
Number Of Sites
7
Number Of Participants
16

Sites

Site Name
Hospital General Universitario Gregorio Maranon
Department Name
Medical Oncology
Contact Person Name
Antonio Calles
Site Name
Clinica Universidad De Navarra
Department Name
Medical Oncology
Contact Person Name
Gonzalo Fernández
Contact Person Email
gfernandezh@unav.es
Site Name
Complejo Hospitalario Universitario Insular Materno Infantil
Department Name
Medical Oncology
Contact Person Name
Delvys Rodríguez
Contact Person Email
drodabr@gobiernodecanarias.org
Site Name
Hospital Universitario Quironsalud Madrid
Department Name
Medical Oncology
Contact Person Name
Belén Rubio
Site Name
Hospital Universitari Vall D Hebron
Department Name
Medical Oncology
Contact Person Name
Enriqueta Felip
Contact Person Email
efelip@vhio.net
Site Name
Hospital Clinic De Barcelona
Department Name
Medical Oncology
Contact Person Name
Noemi Reguart
Contact Person Email
NREGUART@clinic.cat
Site Name
Hospital Universitario Regional De Malaga
Department Name
Medical Oncology
Contact Person Name
Manuel Cobo
Contact Person Email
manuelcobodols@yahoo.es

Sponsor

Primary sponsor

Full Name
Merck Sharp & Dohme LLC
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Eresearchtechnology Inc.
Responsibilities
sponsorDuties codes: 7
Name
Iqvia Laboratories Limited
Responsibilities
sponsorDuties codes: 4
Name
Signant Health Global Solutions Limited
Responsibilities
sponsorDuties codes: 3
Name
Bioclinica Inc.
Responsibilities
Central imaging (sponsorDuties code 15)
Name
Roche Diagnostics GmbH
Responsibilities
sponsorDuties codes: 4
Name
Parexel International Corp.
Responsibilities
EUB services (call center and medical services) (sponsorDuties code 15)
Name
Frontage Laboratories Inc.
Responsibilities
sponsorDuties codes: 4

Third parties

  • {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"sponsorDuties codes: 7","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Iqvia Laboratories Limited","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Signant Health Global Solutions Limited","duties_or_roles":"sponsorDuties codes: 3","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"sponsorDuties: 15; value: Central imaging","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Germany","full_name":"Roche Diagnostics GmbH","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Parexel International Corp.","duties_or_roles":"sponsorDuties: 15; value: EUB services (call center and medical services)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Frontage Laboratories Inc.","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
MK-2870
Active Substance
SACITUZUMAB TIRUMOTECAN
Modality
ADC
Routes Of Administration
INTRAVENOUS INFUSION
Route
INTRAVENOUS INFUSION
Authorisation Status
Investigational
Maximum Dose
4 mg/kg
Investigational Product Name
DOCETAXEL
Active Substance
ANHYDROUS DOCETAXEL
Modality
Small molecule
Routes Of Administration
INTRAVENOUS INFUSION
Route
INTRAVENOUS INFUSION
Maximum Dose
75 mg/m2
Investigational Product Name
PEMETREXED
Active Substance
PEMETREXED
Modality
Small molecule
Routes Of Administration
INTRAVENOUS INFUSION
Route
INTRAVENOUS INFUSION
Maximum Dose
500 mg/m2

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