Clinical trial • Phase I/II | Phase II • Oncology

RILVEGOSTOMIG for HER2-expressing gastric cancer | HER2-expressing gastroesophageal junction (GEJ) adenocarcinoma | HER2-expressing esophageal adenocarcinoma

Phase I/II | Phase II trial of RILVEGOSTOMIG for HER2-expressing gastric cancer | HER2-expressing gastroesophageal junction (GEJ) adenocarcinoma | HER2-ex…

Overview

Trial Therapeutic Area
Oncology
Trial Disease
HER2-expressing gastric cancer | HER2-expressing gastroesophageal junction (GEJ) adenocarcinoma | HER2-expressing esophageal adenocarcinoma
Trial Stage
Phase I/II | Phase II
Drug Modality
Monoclonal antibody | Bispecific antibody | ADC | Small molecule

Key dates

Initial CTIS Submission Date
25-09-2024
First CTIS Authorization Date
08-10-2024

Trial design

open-label, cisplatin; trastuzumab (comparator arms listed; dose and schedule not specified in provided data)-controlled, adaptive Phase I/II | Phase II trial in Germany, Italy, Spain and others.

Open Label
Yes
Comparator
Cisplatin; Trastuzumab (comparator arms listed; dose and schedule not specified in provided data)
Adaptive
True, Part 1 is a dose-escalation design to assess safety/tolerability and determine the recommended Phase 2 dose (RP2D) or the highest protocol-defined dose; adaptive elements include assessment of dose-limiting toxicities (DLTs) and escalation to define RP2D.
Biomarker Stratified
True, biomarker: HER2 — strata: HER2-positive (IHC 3+ or IHC 2+/ISH+) | HER2-low (IHC 2+/ISH-negative or IHC 1+)
Single Multiple Or Escalation Dose Combined
Yes
Target Sample Size
414

Eligibility

Recruits 414 Vulnerable population flag is selected in the registry. The protocol and provided documents include Subject Information Sheets and Informed Consent Forms for adult participants and specific ICFs for pregnant partners and optional genetic/future research. Participants must be ≥18 years and provide their own informed consent. No study-specific assent procedures for minors are provided in the available documents..

Vulnerable Population
Vulnerable population flag is selected in the registry. The protocol and provided documents include Subject Information Sheets and Informed Consent Forms for adult participants and specific ICFs for pregnant partners and optional genetic/future research. Participants must be ≥18 years and provide their own informed consent. No study-specific assent procedures for minors are provided in the available documents.

Inclusion criteria

  • {"criterion_text":"- 1. Male and female participants must be at least 18 years of age. Other age restrictions mayapply as per local regulations\n- 2. Disease Characteristics: a/Locally advanced, unresectable, or metastatic disease based on most recent imaging b/For Parts 1, 2, 3a and 4a, pathologically documented adenocarcinoma of the stomach/GEJ/esophagus, HER2-positive (IHC 3+ or IHC 2+/ISH+) based on local tissue testing results c/For Parts 3b, 4b and Part 5 pathologically documented adenocarcinoma of the stomach/GEJ/esophagus, HER2-low (IHC 2+/ISH-negative or IHC 1+) based on local tissue testing results\n- 3. For Part 1, progression on or after at least one prior trastuzumab-containing regimen For Part 2, 3, 4 and 5, previously untreated for unresectable or metastatic adenocarcinoma of the stomach/GEJ/ esophagus with HER2-positive (Part 2, Part 3 [Arm 3A] and Part 4[Arm 4A]) or HER2-low (Part 3 [Arm 3B] , Part 4 [Arm 4B] and Part 5) status.\n- 4. Has measurable target disease assessed by the Investigator based on RECIST version 1.1\n- 5. Has protocol-defined adequate bone marrow and organ function including cardiac, renal and hepatic function\n- 6. If of reproductive potential, agrees to use a highly effective form of contraception or avoid intercourse during and upon completion of the study and for at least 7 months for female and 6 months (all treatment arms except Arm 2B) or 4 months (Arm 2B) for male patients"}

Exclusion criteria

  • {"criterion_text":"- 1. Part 1 to 4: Active primary immunodeficiency, known human immunodeficiency virus (HIV) infection, active, chronic, or past hepatitis B infection, or hepatitis C infection. Part 5: Evidence of the following infections: Uncontrolled HIV infection, Active or uncontrolled hepatitis B (HBV) or hepatitis C (HCV) or active hepatitis A.\n- 2. Uncontrolled intercurrent illness.\n- 3. History of non-infectious pneumonitis/ILD, current ILD, or where suspected ILD that cannot be ruled out by imaging at screening.\n- 4. Lung-specific intercurrent clinically significant severe illnesses.\n- 5. Uncontrolled infection requiring intravenous (IV) antibiotics, antivirals, or antifungals.\n- 6. Pleural effusion, ascites or pericardial effusion that requires drainage, peritoneal shunt, or Cell-free and Concentrated Ascites Reinfusion Therapy (CART).\n- 7. Has spinal cord compression or clinically active central nervous system metastases.\n- 8. For Part 5: Any serious cardiac conditions, such as: Cardiomyopathy of any etiology or history of myocarditis, Heart failure, Uncontrolled hypertension, Unstable angina pectoris, Clinically significant coronary, carotid, or peripheral artery stenosis, Acute coronary syndrome/acute myocardial infarction etc."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Part 1: Occurrence of adverse events (AEs) and serious adverse events (SAEs), graded according to NCI CTCAE v5.0, dose-limiting toxicities (DLTs), and changes from baseline in laboratory parameters, vital signs, and electrocardiogram (ECG) results\n- Part 2, Part 3, Part 4 and Part 5: Endpoint assessed by Investigator per RECIST v1.1: Confirmed Objective Response Rate (ORR)","definition_or_measurement_approach":"Part 1: AEs/SAEs graded per NCI CTCAE v5.0; DLTs tracked; laboratory parameters, vital signs and ECG changes from baseline monitored. Part 2–5: Investigator-assessed confirmed Objective Response Rate (ORR) according to RECIST v1.1."}

Secondary endpoints

  • {"endpoint_text":"- Part 1: Endpoints assessed by Investigator per RECIST v1.1: Confirmed Objective ResponseRate (ORR), Disease control rate (DCR), Duration of response (DoR), Progression-freesurvival (PFS), Overall survival (OS)\n- Part 2, Part 3, Part 4 and Part 5: Endpoints assessed by Investigator per RECISIT v1.1: Diseasecontrol rate (DCR), Duration of response (DoR), Progression-free survival (PFS), Overallsurvival (OS)\n- Part 2, Part 3, Part 4 and Part 5: Occurrence of adverse events (AEs) and serious adverse events(SAEs), dose-limiting toxicities (DLTs) and changes from baseline in laboratory parameters, vital signs, body weight and electrocardiogram (ECG) results\n- Part 2, Part 3, Part 4 and Part 5: -Serum concentration of T-DXd, total anti-HER2 antibody, and MAAA-1181a in all arms; -Serum concentration of durvalumab in study arms including T-DXd in combination with durvalumab; -Serum concentrations of volrustomig and rilvegostomig in study arms including T-DXd incombination with volrustomig and T-DXd in combination with rilvegostomig,\n- -Presence of ADAs for T-DXd, durvalumab, volrustomig and rilvegostomig (in study arms including T-DXd and durvalumab T-DXd and volrustomig, and T-DXd and rilvegostomig, respectively) -Comparison of ORR, DCR, DoR, PFS, OS between participants using local HER2 test results and central HER2 test results from tumor samples with evaluable results","definition_or_measurement_approach":"Secondary endpoints are measured per RECIST v1.1 for tumor response metrics (ORR, DCR, DoR, PFS, OS). Safety endpoints use NCI CTCAE v5.0 grading. PK endpoints: serum concentrations of T-DXd, anti-HER2 antibody, MAAA-1181a, durvalumab, volrustomig, rilvegostomig. Immunogenicity: assessment of anti-drug antibodies (ADAs). Comparison analyses between local and central HER2 testing for response endpoints."}

Recruitment

Planned Sample Size
414
Recruitment Window Months
73
Consent Approach
Informed consent obtained from adult participants (minimum age 18). Subject Information Sheets and Informed Consent Forms are provided and available for country-specific use (documents available for DE, IT, ES, NL, PL and English versions). There are specific ICFs for pregnant partners and optional/genetic research; consent is provided by the participant. No assent procedures for minors are described in the available documents.

Methods

  • Use of recruitment arrangements documents and patient-facing materials (posters and pamphlets) — country-specific recruitment arrangements files provided (Germany, Italy, Spain, Netherlands, Poland).
  • Local site-based recruitment via participating hospitals/centres (contact details and responsible clinicians listed per site).

Geography

Total Number Of Sites
30
Total Number Of Participants
154

Germany

Earliest CTIS Part Ii Submission Date
05-04-2024
Latest Decision Or Authorization Date
09-10-2024
Processing Time Days
187
Number Of Sites
6
Number Of Participants
27

Sites

Site Name
Universitaetsklinikum Frankfurt AöR
Department Name
Schwerpunkt GI Onkologie Medizinische Klinik 1
Contact Person Name
Jörg Trojan
Contact Person Email
trojan@em.uni-frankfurt.de
Site Name
Krankenhaus Nordwest GmbH
Department Name
Institut für Klinisch-Onkologische Forschung (IKF),UCT-Frankfurt
Contact Person Name
Salah-Eddin Al-Batran
Contact Person Email
albatran@khnw.de
Site Name
Universitaet Leipzig
Department Name
Universitäres Krebszentrum Leipzig (UCCL)
Contact Person Name
Florian Lordick
Site Name
Universitaetsklinikum Mannheim GmbH
Department Name
Tagestherapiezentrum am ITM
Contact Person Name
Ralf-Dieter Hofheinz
Contact Person Email
ralf.hofheinz@umm.de
Site Name
Klinikum rechts der Isar der TU Muenchen AöR
Department Name
Klinik und Poliklinik für Innere Medizin III, Hämatologie
Contact Person Name
Sylvie Lorenzen
Contact Person Email
Sylvie.Lorenzen@mri.tum.de
Site Name
Haematologisch Onkologische Praxis Eppendorf
Contact Person Name
Alexander Stein
Contact Person Email
stein@hope-hamburg.de

Italy

Earliest CTIS Part Ii Submission Date
05-04-2024
Latest Decision Or Authorization Date
14-10-2024
Processing Time Days
192
Number Of Sites
7
Number Of Participants
41

Sites

Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
Medical Oncology
Contact Person Name
Gennaro Daniele
Site Name
Istituto Oncologico Veneto
Department Name
Medical Oncology
Contact Person Name
Sara Lonardi
Contact Person Email
sara.lonardi@iov.veneto.it
Site Name
ASST Grande Ospedale Metropolitano Niguarda
Department Name
Oncology
Contact Person Name
Salvatore Siena
Site Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale
Department Name
Medical Oncology
Contact Person Name
Adriano Gravina
Contact Person Email
a.gravina@istitutotumori.na.it
Site Name
Centro Ricerche Cliniche Di Verona S.r.l.
Department Name
Medical Oncology
Contact Person Name
Davide Melisi
Contact Person Email
davide.melisi@univr.it
Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
Gastroenterological Medical Oncology
Contact Person Name
Filippo Pietrantonio
Site Name
Centro Ricerche Cliniche Di Verona S.r.l. (duplicate entry in listing)
Department Name
Medical Oncology
Contact Person Name
Davide Melisi
Contact Person Email
davide.melisi@univr.it

Spain

Earliest CTIS Part Ii Submission Date
05-04-2024
Latest Decision Or Authorization Date
08-10-2024
Processing Time Days
186
Number Of Sites
6
Number Of Participants
19

Sites

Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Oncology
Contact Person Name
Maria Luisa Limon Miron
Contact Person Email
mluisalimon@gmail.com
Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Oncology
Contact Person Name
Sara Lonardi
Contact Person Email
sara.lonardi@iov.veneto.it
Site Name
Hospital Universitari Vall D Hebron
Department Name
Oncology
Contact Person Name
Daniel Alejandro Acosta Eyzaguirre
Contact Person Email
dacosta@vhio.net
Site Name
Hospital General Universitario Gregorio Maranon
Department Name
Oncology
Contact Person Name
Aitana Calvo Ferrandiz
Contact Person Email
aitanacalvo@hotmail.com
Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Oncology
Contact Person Name
Federico Longo Munoz
Contact Person Email
fedelongomunoz@hotmail.com
Site Name
Hospital Universitari Vall D Hebron (duplicate/other department)
Department Name
Oncology
Contact Person Name
Daniel Alejandro Acosta Eyzaguirre
Contact Person Email
dacosta@vhio.net

Netherlands

Earliest CTIS Part Ii Submission Date
05-04-2024
Latest Decision Or Authorization Date
09-10-2024
Processing Time Days
187
Number Of Sites
3
Number Of Participants
44

Sites

Site Name
Stichting Amsterdam UMC
Department Name
Medical Oncology
Contact Person Name
Hanneke van Laarhoven
Contact Person Email
h.vanlaarhoven@amsterdamumc.nl
Site Name
Het Nederlands Kanker Instituut-Antoni van Leeuwenhoek Ziekenhuis Stichting
Department Name
Internist Oncology
Contact Person Name
Neeltje Steeghs
Contact Person Email
n.steeghs@nki.nl
Site Name
Universitair Medisch Centrum Utrecht
Department Name
Inernist Oncology
Contact Person Name
Nadia Haj Mohammad
Contact Person Email
n.hajmohammad@umcutrecht.nl

Poland

Earliest CTIS Part Ii Submission Date
05-04-2024
Latest Decision Or Authorization Date
13-11-2024
Processing Time Days
222
Number Of Sites
8
Number Of Participants
23

Sites

Site Name
Szpital Wojewodzki Im. Mikolaja Kopernika W Koszalinie
Department Name
Oddział Onkologii Klinicznej z Pododdziałem Chemioterapii Jednodniowej
Contact Person Name
Mariusz Kwiatkowski
Contact Person Email
mariusz.kwiatkowski@swk.med.pl
Site Name
Specjalistyczny Szpital Onkologiczny Nu-Med Sp. z o.o.
Department Name
Oddzial Chemioterapii
Contact Person Name
Ewa Chmielowska
Contact Person Email
ewa.chmielowska@nu-med.pl
Site Name
Samodzielny Publiczny Zaklad Opieki Zdrowotnej Szpital Uniwersytecki W Krakowie
Department Name
Oddzial Kliniczny Onkologii
Contact Person Name
Piotr Wysocki
Contact Person Email
piotr.wysocki@uj.edu.pl
Site Name
Przychodnia Lekarska KOMED
Contact Person Name
Boguslawa Karaszewska
Contact Person Email
karasiowa@gmail.com
Site Name
Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy
Department Name
Klinika Onkologii i Radioterapii
Contact Person Name
Lucjan Wyrwicz
Contact Person Email
lucjanwyrwicz@gmail.com
Site Name
Opolskie Centrum Onkologii Im. Prof. Tadeusza Koszarowskiego W Opolu Samodzielny Publiczny Zaklad Opieki Zdrowotnej
Department Name
Oddzial Onkologii Klinicznej
Contact Person Name
Barbara Radecka
Contact Person Email
brad@onkologia.opole.pl
Site Name
Uniwersyteckie Centrum Kliniczne
Department Name
Osrodek Badan Klinicznych Wczesnych Faz Uniwersyteckiego Centrum Klinicznego w Gdansku
Contact Person Name
Anna Kowalczyk
Contact Person Email
akow@gumed.edu.pl
Site Name
Samodzielny Publiczny Zaklad Opieki Zdrowotnej Szpital Uniwersytecki W Krakowie (duplicate listing)
Department Name
Oddzial Kliniczny Onkologii
Contact Person Name
Piotr Wysocki
Contact Person Email
piotr.wysocki@uj.edu.pl

Sponsor

Primary sponsor

Full Name
AstraZeneca AB
Organisation Type
Pharmaceutical company
Country Of Registered Address
Sweden

Investigational products

Investigational Product Name
Rilvegostomig
Active Substance
RILVEGOSTOMIG
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Investigational Product Name
volrustomig
Active Substance
VOLRUSTOMIG
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Investigational Product Name
DS-8201a
Active Substance
TRASTUZUMAB DERUXTECAN
Modality
ADC
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Investigational Product Name
IMFINZI 50 mg/mL concentrate for solution for infusion.
Active Substance
DURVALUMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Marketing authorisation: EU/1/18/1322/001
Investigational Product Name
PEMBROLIZUMAB
Active Substance
PEMBROLIZUMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Investigational Product Name
OXALIPLATIN
Active Substance
OXALIPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Investigational Product Name
CAPECITABINE
Active Substance
CAPECITABINE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Investigational Product Name
CISPLATIN
Active Substance
CISPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Investigational Product Name
FLUOROURACIL
Active Substance
FLUOROURACIL
Modality
Small molecule
Routes Of Administration
SOLUTION FOR INJECTION OR INFUSION
Route
INTRAVENOUS
Investigational Product Name
TRASTUZUMAB
Active Substance
TRASTUZUMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Combination Treatment
Yes

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