Clinical trial • Phase III • Neurology
REMIBRUTINIB for Relapsing multiple sclerosis
Phase III trial of REMIBRUTINIB for Relapsing multiple sclerosis.
Overview
- Trial Therapeutic Area
- Neurology
- Trial Disease
- Relapsing multiple sclerosis
- Trial Stage
- Phase III
- Drug Modality
- Small molecule|Monoclonal antibody
Key dates
- Initial CTIS Submission Date
- 14-04-2025
- First CTIS Authorization Date
- 01-08-2025
Trial design
Randomised, open-label, ocrelizumab — comparator; treated according to routine clinical practice and at standard doses (commercially confidential information).-controlled Phase III trial in Belgium, Denmark, France and others.
- Randomised
- Yes
- Open Label
- Yes
- Comparator
- Ocrelizumab — comparator; treated according to routine clinical practice and at standard doses (Commercially confidential information).
- Target Sample Size
- 185
- Trial Duration For Participant
- 730
Eligibility
Recruits 185 adults.
- Pregnancy Exclusion
- Women of childbearing potential, defined as all women physiologically capable of becoming pregnant, unless they are using highly effective methods of contraception and do not donate eggs while taking study treatment and for (Commercially confidential information) after stopping ocrelizumab.
Inclusion criteria
- {"criterion_text":"-Signed informed consent obtained prior to any assessment performed (confirm at Screening Visit).\n-Male or female aged 40 (Commercially confidential information) at Screening.\n-Diagnosis of RMS according to the revised 2017 McDonald criteria at Screening.\n-EDSS score of (Commercially confidential information) at Screening and randomization.\n-Treated with ocrelizumab according to routine clinical practice and at standard doses (Commercially confidential information).\n-Neurologically stable within 30 days prior to Screening and randomization (including no MS relapse in this period).\n-Suitable to be switched to remibrutinib based on physician judgement or patient preference."}
Exclusion criteria
- {"criterion_text":"-Diagnosis of primary progressive multiple sclerosis (PPMS) according to the revised 2017 McDonald criteria at Screening.\n-Participants who have had a splenectomy.\n-Active clinically significant systemic bacterial, viral, parasitic or fungal infections in the judgement of the investigator prior to randomization (e.g. infections requiring hospitalization or i.v. antibiotics)\n-Active, chronic disease of the immune system (including stable disease treated with immune therapy, e.g. leflunomide, methotrexate) other than MS (e.g. rheumatoid arthritis, systemic lupus erythematosus, etc.) with the exception of well-controlled diabetes or thyroid disorder.\n-Participants with a known immunodeficiency syndrome (acquired immunodeficiency syndrome (AIDS), hereditary immune deficiency, or drug induced immune deficiency other than those caused by anti-CD20 therapy), or tested positive for human immunodeficiency virus (HIV) antibody, at Screening.\n-Participants at risk of developing or having reactivation of hepatitis: Positive results at Screening for serological markers for hepatitis (H) A, B, C, and E indicating acute or chronic infection: - anti-HA Immunoglobulin (Ig) M (IgM) - HB surface Antigen (HBs Ag) and/or anti-HBc IgM and/or HB virus deoxyribonucleic acid (DNA) - anti-HBc positive - anti-HC IgG (if positive IgG, HC Virus (HCV)-RNA Polymerase Chain Reaction (PCR) will be performed and if negative, participant can be randomized) - anti-HE IgM positive (regardless of IgG status)\n-Participants with any of the following abnormal hematology laboratory values at Screening: - Hemoglobin: (Commercially confidential information) - Platelets: (Commercially confidential information) - Absolute lymphocyte count (Commercially confidential information) - White blood cells: (Commercially confidential information) - Neutrophils: (Commercially confidential information) - (Commercially confidential information)\n-Resting QT interval corrected by Fridericia’s formula (QTcF) ≥ (Commercially confidential information) msec (male) or ≥ (Commercially confidential information) msec (female) at pre-treatment as per central ECG reading at Screening visit.\n-Use of exclusionary medication prior to Screening/randomization (as defined in the protocol).\n-Use of other investigational drugs within 5 half-lives of Screening; or within 30 days (e.g. small molecules); or until the expected pharmacodynamic effect has returned to baseline (e.g. biologics); whichever is longer; or longer if required by local regulations.\n-Significant (Commercially confidential information) at Screening.\n-Women of childbearing potential, defined as all women physiologically capable of becoming pregnant, unless they are using highly effective methods of contraception and do not donate eggs while taking study treatment and for (Commercially confidential information) after stopping ocrelizumab.\n-History of life-threatening infusion or injection reaction related to ocrelizumab, such as acute hypersensitivity or acute respiratory distress syndrome.\n-History of clinically significant CNS disease (e.g., stroke, traumatic brain or spinal injury, history or presence of myelopathy) or neurological disorders which may mimic MS at Screening.\n-Participants with history of confirmed progressive multifocal leukoencephalopathy (PML) or neurological symptoms consistent with PML prior to randomization."}
Endpoints
Primary endpoints
- {"endpoint_text":"-Annualized rate of new or enlarging T2 lesions (AR-NELT2) on MRI at Month 24 (relative to baseline MRI scan).","definition_or_measurement_approach":"AR-NELT2 measured on MRI at Month 24 relative to baseline MRI scan (annualized rate of new or enlarging T2 lesions)."}
Secondary endpoints
- {"endpoint_text":"-Participants with no evidence of disease activity-3 (NEDA-3), as assessed by absence of confirmed MS relapses, 6-month confirmed disability progression (6mCDP) and new/enlarging T2 lesions on MRI between baseline and Month 24.","definition_or_measurement_approach":"NEDA-3 defined as absence of confirmed MS relapses, absence of 6-month confirmed disability progression (6mCDP), and absence of new/enlarging T2 lesions on MRI between baseline and Month 24."}
- {"endpoint_text":"-Adverse events, laboratory data, vital signs, electrocardiograms (ECGs), (Commercially confidential information).","definition_or_measurement_approach":"Safety assessments including adverse events, laboratory tests, vital signs and ECG monitoring as recorded during the study (additional details marked commercially confidential)."}
- {"endpoint_text":"-Extension Part: Adverse events, laboratory data, vital signs, electrocardiogram (ECG), (Commercially confidential information).","definition_or_measurement_approach":"Extension part safety assessments including adverse events, laboratory data, vital signs and ECG (details commercially confidential)."}
- {"endpoint_text":"-Extension Part: - Annualized rate of new or enlarging T2 lesions on MRI - Participants with NEDA-3.","definition_or_measurement_approach":"Extension part efficacy endpoints: annualized rate of new or enlarging T2 lesions on MRI and proportion of participants meeting NEDA-3 in the extension period."}
Recruitment
- Planned Sample Size
- 185
- Recruitment Window Months
- 68
- Consent Approach
- Signed informed consent obtained prior to any assessment performed (confirm at Screening Visit). Adult informed consent forms available (multiple country-specific ICFs present in the submission). Separate data protection consent forms are provided. Country-specific ICFs and related documents (e.g. follow-up for pregnant participant) are listed for participating countries.
Geography
- Total Number Of Sites
- 62
- Total Number Of Participants
- 215
Belgium
- Earliest CTIS Part Ii Submission Date
- 10-07-2025
- Latest Decision Or Authorization Date
- 27-11-2025
- Processing Time Days
- 140
- Number Of Sites
- 2
- Number Of Participants
- 8
Sites
- Site Name
- Az St-Jan Brugge-Oostende A.V.
- Department Name
- #2001: Neurology
- Principal Investigator Name
- Melissa Cambron
- Principal Investigator Email
- melissa.cambron@azsintjan.be
- Contact Person Name
- Melissa Cambron
- Contact Person Email
- melissa.cambron@azsintjan.be
- Site Name
- Noorderhart
- Department Name
- #2002: Neurology
- Principal Investigator Name
- Cornelia Rogojan
- Principal Investigator Email
- Cornelia.rogojan@noorderhart.be
- Contact Person Name
- Cornelia Rogojan
- Contact Person Email
- Cornelia.rogojan@noorderhart.be
Denmark
- Earliest CTIS Part Ii Submission Date
- 14-07-2025
- Latest Decision Or Authorization Date
- 21-11-2025
- Processing Time Days
- 130
- Number Of Sites
- 2
- Number Of Participants
- 8
Sites
- Site Name
- Rigshospitalet
- Department Name
- #2012: Afdeling for Hjerne- og Nervesygdomme
- Principal Investigator Name
- Finn Sellebjerg
- Principal Investigator Email
- finn.sellebjerg@regionh.dk
- Contact Person Name
- Finn Sellebjerg
- Contact Person Email
- finn.sellebjerg@regionh.dk
- Site Name
- Region Midtjylland
- Department Name
- #2011: Neurologisk Forskning
- Principal Investigator Name
- Kristina Bacher Svendsen
- Principal Investigator Email
- krissven@rm.dk
- Contact Person Name
- Kristina Bacher Svendsen
- Contact Person Email
- krissven@rm.dk
France
- Earliest CTIS Part Ii Submission Date
- 20-06-2025
- Latest Decision Or Authorization Date
- 21-11-2025
- Processing Time Days
- 154
- Number Of Sites
- 13
- Number Of Participants
- 50
Sites
- Site Name
- Les Hopitaux Universitaires De Strasbourg
- Department Name
- #2107: Neurology
- Principal Investigator Name
- Jérôme DE SEZE
- Principal Investigator Email
- Jerome.deseze@chru-strasbourg.fr
- Contact Person Name
- Jérôme DE SEZE
- Contact Person Email
- Jerome.deseze@chru-strasbourg.fr
- Site Name
- Centre Hospitalier Universitaire De Poitiers
- Department Name
- #2105: Neurology
- Principal Investigator Name
- Amélie DOS SANTOS
- Principal Investigator Email
- Amelie.dos-santos@chu-poitiers.fr
- Contact Person Name
- Amélie DOS SANTOS
- Contact Person Email
- Amelie.dos-santos@chu-poitiers.fr
- Site Name
- Centre Hospitalier Regional De Marseille
- Department Name
- #2109: Neurology
- Principal Investigator Name
- Audrey RICO
- Principal Investigator Email
- Audrey.rico@ap-hm.fr
- Contact Person Name
- Audrey RICO
- Contact Person Email
- Audrey.rico@ap-hm.fr
- Site Name
- Groupement Des Hopitaux De L'Institut Catholique De Lille
- Department Name
- #2110: Neurology
- Principal Investigator Name
- Julien POUPART
- Principal Investigator Email
- Poupart.julien@ghicl.fr
- Contact Person Name
- Julien POUPART
- Contact Person Email
- Poupart.julien@ghicl.fr
- Site Name
- Centre Hospitalier Intercommunal De Poissy Saint Germain
- Department Name
- #2113: Neurology
- Principal Investigator Name
- Olivier HEINZLEF
- Principal Investigator Email
- Olivier.heinzlef@ght-yvelinesnord.fr
- Contact Person Name
- Olivier HEINZLEF
- Contact Person Email
- Olivier.heinzlef@ght-yvelinesnord.fr
- Site Name
- Centre Hospitalier Universitaire De Nice
- Department Name
- #2114: Neurology
- Principal Investigator Name
- Mikael COHEN
- Principal Investigator Email
- Cohen.m@chu-nices.fr
- Contact Person Name
- Mikael COHEN
- Contact Person Email
- Cohen.m@chu-nices.fr
- Site Name
- Centre Hospitalier Universitaire De Nimes
- Department Name
- #2112: Neurology
- Principal Investigator Name
- Eric THOUVENOT
- Principal Investigator Email
- Eric.thouvenot@chu-nimes.fr
- Contact Person Name
- Eric THOUVENOT
- Contact Person Email
- Eric.thouvenot@chu-nimes.fr
- Site Name
- Centre Hospitalier Universitaire De Toulouse
- Department Name
- #2111: Neurology
- Principal Investigator Name
- Jonathan CIRON
- Principal Investigator Email
- Ciron.j@chu-toulouse.fr
- Contact Person Name
- Jonathan CIRON
- Contact Person Email
- Ciron.j@chu-toulouse.fr
- Site Name
- CHU Gabriel-Montpied
- Department Name
- #2102: Neurology
- Principal Investigator Name
- Pierre CLAVELOU
- Principal Investigator Email
- Pclavelou@chu-clermontferrand.fr
- Contact Person Name
- Pierre CLAVELOU
- Contact Person Email
- Pclavelou@chu-clermontferrand.fr
- Site Name
- Centre Hospitalier Regional Universitaire De Tours
- Department Name
- #2108: Neurology
- Principal Investigator Name
- Inès DOGHRI
- Principal Investigator Email
- i.doghri@chu-tours.fr
- Contact Person Name
- Inès DOGHRI
- Contact Person Email
- i.doghri@chu-tours.fr
- Site Name
- CHU Besancon
- Department Name
- #2104: Neurology
- Principal Investigator Name
- Eric BERGER
- Principal Investigator Email
- Eberger@chu-besancon.fr
- Contact Person Name
- Eric BERGER
- Contact Person Email
- Eberger@chu-besancon.fr
- Site Name
- Fondation A De Rothschild
- Department Name
- #2103: Neurology
- Principal Investigator Name
- Januel EDOUARD
- Principal Investigator Email
- Edjanuel@for.paris
- Contact Person Name
- Januel EDOUARD
- Contact Person Email
- Edjanuel@for.paris
- Site Name
- Centre Hospitalier Universitaire De Bordeaux
- Department Name
- #2101: Neurology
- Principal Investigator Name
- Aurélie RUET
- Principal Investigator Email
- Aurelie.ruet@chu-bordeaux.fr
- Contact Person Name
- Aurélie RUET
- Contact Person Email
- Aurelie.ruet@chu-bordeaux.fr
Greece
- Earliest CTIS Part Ii Submission Date
- 19-05-2025
- Latest Decision Or Authorization Date
- 20-11-2025
- Processing Time Days
- 185
- Number Of Sites
- 3
- Number Of Participants
- 12
Sites
- Site Name
- General University Hospital Of Larissa
- Department Name
- #2302: Department of Neurology
- Principal Investigator Name
- Efthimios Dardiotis
- Principal Investigator Email
- ebsdar@gmail.com
- Contact Person Name
- Efthimios Dardiotis
- Contact Person Email
- ebsdar@gmail.com
- Site Name
- University General Hospital Attikon
- Department Name
- #2303: 2nd Department of Neurology
- Principal Investigator Name
- Sotirios Giannopoulos
- Principal Investigator Email
- sgiannop@uoi.gr
- Contact Person Name
- Sotirios Giannopoulos
- Contact Person Email
- sgiannop@uoi.gr
- Site Name
- St. Luke's Hospital S.A.
- Department Name
- #2301: Multiple Sclerosis Center (Department of Neurology)
- Principal Investigator Name
- Konstantinos Notas
- Principal Investigator Email
- konstantinos_notas@hotmail.com
- Contact Person Name
- Konstantinos Notas
- Contact Person Email
- konstantinos_notas@hotmail.com
Italy
- Earliest CTIS Part Ii Submission Date
- 08-07-2025
- Latest Decision Or Authorization Date
- 03-12-2025
- Processing Time Days
- 148
- Number Of Sites
- 7
- Number Of Participants
- 15
Sites
- Site Name
- IRCCS Ospedale Policlinico San Martino
- Department Name
- #2332: U.O. Clinica Neurologica
- Principal Investigator Name
- Matilde INGLESE
- Principal Investigator Email
- m.inglese@unige.it
- Contact Person Name
- Matilde INGLESE
- Contact Person Email
- m.inglese@unige.it
- Site Name
- Azienda Ospedaliero Universitaria Ospedali Riuniti
- Department Name
- #2334: Centro Sclerosi Multipla e Neuromielite Ottica S.C. Neurologia Universitaria
- Principal Investigator Name
- Emanuele D'AMICO
- Principal Investigator Email
- emanuele.damico@unifg.it
- Contact Person Name
- Emanuele D'AMICO
- Contact Person Email
- emanuele.damico@unifg.it
- Site Name
- Ospedale San Raffaele S.r.l.
- Department Name
- #2331: Divisione di neuroscienze - Dip. Neurologia - Pad. DIMER
- Principal Investigator Name
- Massimo FILIPPI
- Principal Investigator Email
- filippi.massimo@hsr.it
- Contact Person Name
- Massimo FILIPPI
- Contact Person Email
- filippi.massimo@hsr.it
- Site Name
- Azienda Socio Sanitaria Territoriale Papa Giovanni Xxiii
- Department Name
- #2335: Centro Sclerosi Multipla U.S.S. Neuroimmunologia
- Principal Investigator Name
- Sara LA GIOIA
- Principal Investigator Email
- slagioia@asst-pg23.it
- Contact Person Name
- Sara LA GIOIA
- Contact Person Email
- slagioia@asst-pg23.it
- Site Name
- Azienda Ospedaliera Policlinico Universitario Tor Vergata
- Department Name
- #2333: U.O.S.D. Centro di Riferimento Regionale per la Sclerosi Multipla
- Principal Investigator Name
- Girolama Alessandra MARFIA
- Principal Investigator Email
- marfia@uniroma2.it
- Contact Person Name
- Girolama Alessandra MARFIA
- Contact Person Email
- marfia@uniroma2.it
- Site Name
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Department Name
- #2340: U.O.S. Sclerosi Multipla U.O.C. Neurologia
- Principal Investigator Name
- Massimiliano MIRABELLA
- Principal Investigator Email
- massimiliano.mirabella@unicatt.it
- Contact Person Name
- Massimiliano MIRABELLA
- Contact Person Email
- massimiliano.mirabella@unicatt.it
- Site Name
- Fondazione Istituto Neurologico Nazionale Casimiro Mondino
- Department Name
- #2336: U.O.S.S. Sclerosi Multipla U.O.S.C. Neuroncologia e Neuroinfiammazione
- Principal Investigator Name
- Elena COLOMBO
- Principal Investigator Email
- elena.colombo@mondino.it
- Contact Person Name
- Elena COLOMBO
- Contact Person Email
- elena.colombo@mondino.it
Slovakia
- Earliest CTIS Part Ii Submission Date
- 13-06-2025
- Latest Decision Or Authorization Date
- 01-12-2025
- Processing Time Days
- 171
- Number Of Sites
- 2
- Number Of Participants
- 4
Sites
- Site Name
- University Hospital Bratislava
- Department Name
- #2381 Neurologická klinika SZU a UNB
- Principal Investigator Name
- Viera Hančinová
- Principal Investigator Email
- dr.hancinova@gmail.com
- Contact Person Name
- Viera Hančinová
- Contact Person Email
- dr.hancinova@gmail.com
- Site Name
- Fakultna Nemocnica Trnava
- Department Name
- #2382: Neurologická klinika FN Trnava a SZU
- Principal Investigator Name
- Georgi Krastev
- Principal Investigator Email
- georgi.krastev@fntt.sk
- Contact Person Name
- Georgi Krastev
- Contact Person Email
- georgi.krastev@fntt.sk
Spain
- Earliest CTIS Part Ii Submission Date
- 08-07-2025
- Latest Decision Or Authorization Date
- 18-02-2026
- Processing Time Days
- 225
- Number Of Sites
- 13
- Number Of Participants
- 52
Sites
- Site Name
- Hospital Universitario Dr Peset Aleixandre
- Department Name
- #2408: Neurología
- Principal Investigator Name
- Lamberto Landete Pascual
- Principal Investigator Email
- landete_lam@gva.es
- Contact Person Name
- Lamberto Landete Pascual
- Contact Person Email
- landete_lam@gva.es
- Site Name
- Hospital General Universitario Gregorio Maranon
- Department Name
- #2412: Neurología
- Principal Investigator Name
- María Luisa Martinez Gines
- Principal Investigator Email
- marisamgines@hotmail.com
- Contact Person Name
- María Luisa Martinez Gines
- Contact Person Email
- marisamgines@hotmail.com
- Site Name
- Hospital Universitario Virgen De La Macarena
- Department Name
- #2403: Neurología
- Principal Investigator Name
- Sara Eichau Madueno
- Principal Investigator Email
- saraeichau@gmail.com
- Contact Person Name
- Sara Eichau Madueno
- Contact Person Email
- saraeichau@gmail.com
- Site Name
- Hospital Universitari Vall D Hebron
- Department Name
- #2404: Neurología
- Principal Investigator Name
- Xavier Montalban Gairin
- Principal Investigator Email
- xavier.montalban@cem-cat.org
- Contact Person Name
- Xavier Montalban Gairin
- Contact Person Email
- xavier.montalban@cem-cat.org
- Site Name
- Hospital Universitario Ramon Y Cajal
- Department Name
- #2411: Neurología
- Principal Investigator Name
- Lucienne Costa-Frossard França
- Principal Investigator Email
- lucienne.costa@salud.madrid.org
- Contact Person Name
- Lucienne Costa-Frossard França
- Contact Person Email
- lucienne.costa@salud.madrid.org
- Site Name
- Hospital Universitario Puerta De Hierro De Majadahonda
- Department Name
- #2409: Neurología
- Principal Investigator Name
- Rosario Blasco Quilez
- Principal Investigator Email
- neimtrials.hpth@salud.madrid.org
- Contact Person Name
- Rosario Blasco Quilez
- Contact Person Email
- neimtrials.hpth@salud.madrid.org
- Site Name
- Hospital Universitario Reina Sofia
- Department Name
- #2407: Neurología
- Principal Investigator Name
- Eduardo Agüera Morales
- Principal Investigator Email
- doctoredu@gmail.com
- Contact Person Name
- Eduardo Agüera Morales
- Contact Person Email
- doctoredu@gmail.com
- Site Name
- University Clinical Hospital Virgen De La Arrixaca
- Department Name
- #2405: Neurología
- Principal Investigator Name
- Jose Meca Lallana
- Principal Investigator Email
- pmecal@gmail.com
- Contact Person Name
- Jose Meca Lallana
- Contact Person Email
- pmecal@gmail.com
- Site Name
- Hospital Universitario Fundacion Jimenez Diaz
- Department Name
- #2410: Neurología
- Principal Investigator Name
- Irene del Pilar Moreno Torres
- Principal Investigator Email
- irene.morenot@quironsalud.es
- Contact Person Name
- Irene del Pilar Moreno Torres
- Contact Person Email
- irene.morenot@quironsalud.es
- Site Name
- Hospital Clinico San Carlos
- Department Name
- #2401: Neurología
- Principal Investigator Name
- Celia Oreja-Guevara
- Principal Investigator Email
- orejacbn@gmail.com
- Contact Person Name
- Celia Oreja-Guevara
- Contact Person Email
- orejacbn@gmail.com
- Site Name
- Hospital Universitario Regional De Malaga
- Department Name
- #2406: Neurología
- Principal Investigator Name
- Ana María Alonso Torres
- Principal Investigator Email
- anam.alonso.ssp@juntadeandalucia.es
- Contact Person Name
- Ana María Alonso Torres
- Contact Person Email
- anam.alonso.ssp@juntadeandalucia.es
- Site Name
- Hospital Universitario Y Politecnico La Fe
- Department Name
- #2402: Neurología
- Principal Investigator Name
- Francisco Perez Miralles
- Principal Investigator Email
- perez_fca@gva.es
- Contact Person Name
- Francisco Perez Miralles
- Contact Person Email
- perez_fca@gva.es
- Site Name
- Hospital Santa Caterina Ias
- Department Name
- #2413: Neurología
- Principal Investigator Name
- Gary Ciceron Álvarez Bravo
- Principal Investigator Email
- galvarez@idibgi.org
- Contact Person Name
- Gary Ciceron Álvarez Bravo
- Contact Person Email
- galvarez@idibgi.org
Portugal
- Earliest CTIS Part Ii Submission Date
- 06-06-2025
- Latest Decision Or Authorization Date
- 24-02-2026
- Processing Time Days
- 263
- Number Of Sites
- 3
- Number Of Participants
- 9
Sites
- Site Name
- Unidade Local De Saude De Coimbra E.P.E.
- Department Name
- #2464: Serviço de Neurologia
- Principal Investigator Name
- Inês Correia
- Principal Investigator Email
- uid@ulscoimbra.min-saude.pt
- Contact Person Name
- Inês Correia
- Contact Person Email
- uid@ulscoimbra.min-saude.pt
- Site Name
- CCAB Centro Clinico Academico Braga Associacao
- Department Name
- #2462: Serviço de Neurologia
- Principal Investigator Name
- João Cerqueira
- Principal Investigator Email
- joao.cerqueira@ccabraga.org
- Contact Person Name
- João Cerqueira
- Contact Person Email
- joao.cerqueira@ccabraga.org
- Site Name
- Unidade Local De Saude De Sao Jose E.P.E.
- Department Name
- #2463: Serviço de Neurologia
- Principal Investigator Name
- João Sequeira
- Principal Investigator Email
- joao.sequeira@ulssjose.min-saude.pt
- Contact Person Name
- João Sequeira
- Contact Person Email
- joao.sequeira@ulssjose.min-saude.pt
Czechia
- Earliest CTIS Part Ii Submission Date
- 24-03-2026
- Latest Decision Or Authorization Date
- 17-04-2026
- Processing Time Days
- 24
- Number Of Sites
- 6
- Number Of Participants
- 30
Sites
- Site Name
- Nemocnice Pardubickeho kraje a.s.
- Department Name
- #2052: Neurologicka klinika, MS Centrum
- Principal Investigator Name
- Miroslav Mares
- Principal Investigator Email
- miroslav.mares@nempk.cz
- Contact Person Name
- Miroslav Mares
- Contact Person Email
- miroslav.mares@nempk.cz
- Site Name
- Fakultni Nemocnice U Sv Anny V Brne
- Department Name
- #2054: Neurologie MS centrum
- Principal Investigator Name
- Michal Dufek
- Principal Investigator Email
- michal.dufek@fnusa.cz
- Contact Person Name
- Michal Dufek
- Contact Person Email
- michal.dufek@fnusa.cz
- Site Name
- Fakultni Nemocnice Hradec Kralove
- Department Name
- #2051: Neurologicka klinika, MS centrum
- Principal Investigator Name
- Zbysek Pavelek
- Principal Investigator Email
- zbysekpavelek@email.cz
- Contact Person Name
- Zbysek Pavelek
- Contact Person Email
- zbysekpavelek@email.cz
- Site Name
- Fakultni Nemocnice Motol A Homolka
- Department Name
- #2056: Centrum pro diagnostiku a léčbu demyelinizačních onemocnění
- Principal Investigator Name
- Jana Libertinova
- Principal Investigator Email
- jana.libertinova@fnmotol.cz
- Contact Person Name
- Jana Libertinova
- Contact Person Email
- jana.libertinova@fnmotol.cz
- Site Name
- Nemocnice Jihlava prispevkova organizace
- Department Name
- #2053: Neurologicke oddeleni
- Principal Investigator Name
- Ondrej Skoda
- Principal Investigator Email
- skodao@nemji.cz
- Contact Person Name
- Ondrej Skoda
- Contact Person Email
- skodao@nemji.cz
- Site Name
- Fakultni Nemocnice Brno
- Department Name
- #2055: Neurologick klinika
- Principal Investigator Name
- Pavel Stourac
- Principal Investigator Email
- stourac.pavel@fnbrno.cz
- Contact Person Name
- Pavel Stourac
- Contact Person Email
- stourac.pavel@fnbrno.cz
Germany
- Earliest CTIS Part Ii Submission Date
- 18-03-2026
- Latest Decision Or Authorization Date
- 13-04-2026
- Processing Time Days
- 26
- Number Of Sites
- 11
- Number Of Participants
- 27
Sites
- Site Name
- Neuro Centrum Science GmbH
- Department Name
- #2207: Neurologie
- Principal Investigator Name
- Stefan Ries
- Principal Investigator Email
- s.ries@neuro-centrum-science.de
- Contact Person Name
- Stefan Ries
- Contact Person Email
- s.ries@neuro-centrum-science.de
- Site Name
- Universitaet Muenster
- Department Name
- #2204: Klinik fuer Neurologie
- Principal Investigator Name
- Luisa Klotz
- Principal Investigator Email
- Luisa.klotz@ukmuenster.de
- Contact Person Name
- Luisa Klotz
- Contact Person Email
- Luisa.klotz@ukmuenster.de
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- #2211: Klinik und Hochschulambulanz fuer Neurologie
- Principal Investigator Name
- Carolin Otto
- Principal Investigator Email
- carolin.otto@charite.de
- Contact Person Name
- Carolin Otto
- Contact Person Email
- carolin.otto@charite.de
- Site Name
- Universitaetsklinikum Ulm AöR
- Department Name
- #2209: Klinik für Neurologie
- Principal Investigator Name
- Makbule Senel
- Principal Investigator Email
- makbule.senel@uni-ulm.de
- Contact Person Name
- Makbule Senel
- Contact Person Email
- makbule.senel@uni-ulm.de
- Site Name
- Universitaetsklinikum Heidelberg AöR
- Department Name
- #2212: Neurologische Klinik
- Principal Investigator Name
- Klemens Ruprecht
- Principal Investigator Email
- klemens.ruprecht@med.uni-heidelberg.de
- Contact Person Name
- Klemens Ruprecht
- Contact Person Email
- klemens.ruprecht@med.uni-heidelberg.de
- Site Name
- Philipps-Universitaet Marburg
- Department Name
- #2213: Clinic for neurology
- Principal Investigator Name
- Clemens Warnke
- Principal Investigator Email
- clemens.warnke@uni-marburg.de
- Contact Person Name
- Clemens Warnke
- Contact Person Email
- clemens.warnke@uni-marburg.de
- Site Name
- NeuroPoint Gesellschaft fur vorbeugende Gesundheitspflege GmbH
- Department Name
- #2206: NeuroPoint
- Principal Investigator Name
- Daniela Rau
- Principal Investigator Email
- rau@neurologie-ulm.de
- Contact Person Name
- Daniela Rau
- Contact Person Email
- rau@neurologie-ulm.de
- Site Name
- Universitaetsklinikum Essen AöR
- Department Name
- #2205: Klinik für Neurologie
- Principal Investigator Name
- Refik Pul
- Principal Investigator Email
- Refik.pul@uk-essen.de
- Contact Person Name
- Refik Pul
- Contact Person Email
- Refik.pul@uk-essen.de
- Site Name
- Katholisches Klinikum Bochum gGmbH
- Department Name
- #2215: Klinik fuer Neurologie
- Principal Investigator Name
- Simon Faissner
- Principal Investigator Email
- Simon.faissner@ruhr-uni-bochum.de
- Contact Person Name
- Simon Faissner
- Contact Person Email
- Simon.faissner@ruhr-uni-bochum.de
- Site Name
- Universitaetsmedizin Greifswald KöR
- Department Name
- #2203: Klinik und Poliklinik für Neurologie
- Principal Investigator Name
- Matthias Grothe
- Principal Investigator Email
- matthias.grothe@med.uni-greifswald.de
- Contact Person Name
- Matthias Grothe
- Contact Person Email
- matthias.grothe@med.uni-greifswald.de
- Site Name
- Universitaetsklinikum Regensburg AöR
- Department Name
- #2201: Neurology
- Principal Investigator Name
- Klemens Angstwurm
- Principal Investigator Email
- Klemens.Angstwurm@medbo.de
- Contact Person Name
- Klemens Angstwurm
- Contact Person Email
- Klemens.Angstwurm@medbo.de
Sponsor
Primary sponsor
- Full Name
- Novartis Pharma AG
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- Switzerland
Contract research organisations
- Name
- IQVIA Limited
- Responsibilities
- Central trial services; ECG Machine provision, Central ECG Collection, Analysis, Reporting; other duties (codes: 1,15,3)
- Name
- Syneos Health Inc.
- Responsibilities
- Duties code 1
- Name
- Parexel International (IRL) Limited
- Responsibilities
- Duties code 12
- Name
- Icon Clinical Research Limited
- Responsibilities
- Duties code 1
Third parties
- {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Patient Travel and Reimbursement for site visits.","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"4","organisation_type":"Pharmaceutical company"}
- {"country":"France","full_name":"Creapharm Clinical Supplies","duties_or_roles":"14","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"1; ECG Machine provision, Central ECG Collection, Analysis, Reporting; 3","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"15; 7","organisation_type":"Pharmaceutical company"}
- {"country":"Switzerland","full_name":"Neurostatus-UHB AG","duties_or_roles":"13; EDSS Licensing","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"United States","full_name":"Syneos Health Inc.","duties_or_roles":"1","organisation_type":"Pharmaceutical company"}
- {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"12","organisation_type":"Pharmaceutical company"}
- {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"4","organisation_type":"Pharmaceutical company"}
- {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"1","organisation_type":"Pharmaceutical company"}
- {"country":"Canada","full_name":"Neurorx Research Inc.","duties_or_roles":"13; Central MRI Analysis","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Medical Equipment Supplies And Management Limited","duties_or_roles":"Ancillary Supplies","organisation_type":"Pharmaceutical company"}
Investigational products
- Investigational Product Name
- LOU064
- Active Substance
- REMIBRUTINIB
- Modality
- Small molecule
- Routes Of Administration
- ORAL USE
- Route
- ORAL USE
- Authorisation Status
- Investigational (prodAuthStatus:1)
- Investigational Product Name
- OCRELIZUMAB
- Active Substance
- OCRELIZUMAB
- Modality
- Monoclonal antibody
- Routes Of Administration
- SUBCUTANEOUS|INTRAVENOUS
- Route
- SUBCUTANEOUS/INTRAVENOUS
- Authorisation Status
- Authorised (prodAuthStatus:2)
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