Clinical trial • Phase III • Immunology|Dermatology
REMIBRUTINIB for Hidradenitis suppurativa (moderate to severe)
Phase III trial of REMIBRUTINIB for Hidradenitis suppurativa (moderate to severe).
Overview
- Trial Therapeutic Area
- Immunology|Dermatology
- Trial Disease
- Hidradenitis suppurativa (moderate to severe)
- Trial Stage
- Phase III
- Drug Modality
- Small molecule
- Paediatric Trial
- Yes
Key dates
- Initial CTIS Submission Date
- 22-01-2025
- First CTIS Authorization Date
- 12-05-2025
Trial design
Randomised, placebo (matching film-coated tablet) administered as double-dummy placebo-controlled arm; no active comparator specified. Phase III trial in Germany, Greece, Portugal and others.
- Randomised
- Yes
- Comparator
- Placebo (matching film-coated tablet) administered as double-dummy placebo-controlled arm; no active comparator specified.
- Target Sample Size
- 282
- Trial Duration For Participant
- 476
Eligibility
Recruits 282 paediatric patients.
- Vulnerable Population
- Adolescents are included (participants ≥12 to <18 years). For participants aged ≥ 12 to < 18 years: parent’s or legal guardian’s signed written informed consent and the child’s assent, if appropriate, must be obtained before any assessment is performed. If a participant reaches the age of consent (as per local law) during the study, they will also need to sign the corresponding study Informed Consent Form (ICF) at the next study visit.
Inclusion criteria
- {"criterion_text":"- Signed informed consent must be obtained prior to participation in the study. For participants aged ≥ 12 to < 18 years: parent’s or legal guardian’s signed written informed consent and child’s assent, if appropriate, must be obtained before any assessment is performed. Of note, if the participant reaches age of consent (age as per local law) during the study, they will also need to sign the corresponding study Informed Consent Form (ICF) at the next study visit.\n- Male and female participants ≥ 12 years of age at the time of signing of the informed consent forms.\n- Diagnosis of Hidradenitis Suppurativa (HS) based on clinical history and physical examination for at least 6 months prior to the Baseline visit.\n- Participants with moderate to severe HS at baseline defined as: •\tA total of at least 5 AN, i.e. abscesses and/or inflammatory nodules AND •\tInflammatory lesions should affect at least 2 distinct anatomic areas (e.g., left and right axillae)"}
Exclusion criteria
- {"criterion_text":"- Presence of more than 20 fistulae/tunnels (both draining and non-draining) in total at baseline.\n- History of hypersensitivity to any of the study drug constituents.\n- Known or suspected infectious disease that is active, chronic or recurrent which precludes the participant from participating in the trial as per investigator's assessment. These infectious diseases include and are not limited to opportunistic infections (e.g., tuberculosis, atypical mycobacterioses, listeriosis or aspergillosis) and/or known or suspected Human Immunodeficiency Virus (HIV) infection. Should it be required by local regulations and/or considered appropriate by the investigator, an HIV test can be performed to confirm eligibility.\n- History of live attenuated vaccine administration within 6 weeks prior to randomization or requirement to receive these vaccinations at any time while on study treatment\n- Major surgery within 8 weeks prior to screening or planned surgery for the duration of the study.\n- Any active skin disease or conditions that may interfere with the assessment of HS.\n- Previous exposure to remibrutinib or other BTK inhibitors.\n- Use of other investigational drugs within 5 half-lives, or within 30 days (for small molecules) prior to randomization, or until the pharmacodynamic effect has returned to baseline (for biologics), whichever is longer.\n- Significant bleeding risk or coagulation disorders\n- History of gastrointestinal bleeding.\n- Requirement for anti-platelet (except for acetylsalicylic acid up to 100 mg/d or clopidogrel up to 75 mg/d) or anti-coagulant medication.\n- History or current hepatic disease.\n- Evidence of clinically significant cardiovascular, neurological, psychiatric, pulmonary, renal, hepatic, endocrine, metabolic, hematological disorders, gastrointestinal disease or immunodeficiency that, in the Investigator's opinion, would compromise the safety of the participant, interfere with the interpretation of the study results or otherwise preclude participation or protocol adherence of the participant."}
Endpoints
Primary endpoints
- {"endpoint_text":"- Achievement of HiSCR50 at Week 16. HiSCR50 is defined as at least a 50% decrease in Abscess and Inflammatory Nodule (AN) count with no increase in the number of abscesses and in the number of draining tunnels/fistulae compared to baseline.","definition_or_measurement_approach":"HiSCR50 is defined as at least a 50% decrease in Abscess and Inflammatory Nodule (AN) count with no increase in the number of abscesses and in the number of draining tunnels/fistulae compared to baseline; measured at Week 16."}
Secondary endpoints
- {"endpoint_text":"- Achievement of AN50 at Week 16. AN50 is defined as at least a 50% decrease in Abscess and Inflammatory Nodule (AN) count compared to baseline","definition_or_measurement_approach":"AN50: at least a 50% decrease in Abscess and Inflammatory Nodule (AN) count compared to baseline; measured at Week 16."}
- {"endpoint_text":"- Percentage change from baseline in IHS4 at Week 16","definition_or_measurement_approach":"Percent change from baseline in IHS4 score at Week 16."}
- {"endpoint_text":"- Achievement of HiSCR75 at Week 16. HiSCR75 is defined as at least a 75% decrease in Abscess and Inflammatory Nodule (AN) count with no increase in the number of abscesses and in the number of draining tunnels/fistulae compared to baseline.","definition_or_measurement_approach":"HiSCR75: at least a 75% decrease in AN count with no increase in abscesses or draining tunnels/fistulae compared to baseline; measured at Week 16."}
- {"endpoint_text":"- Flaring up to Week 16. Flare is defined as at least a 25% increase in AN count with a minimum increase of 2 AN relative to baseline.","definition_or_measurement_approach":"Flare: ≥25% increase in AN count with minimum increase of 2 AN relative to baseline; assessed up to Week 16."}
- {"endpoint_text":"- Achievement of HiSCR50 at Week 8.","definition_or_measurement_approach":"HiSCR50 at Week 8 defined as for primary endpoint but measured at Week 8."}
- {"endpoint_text":"- Achievement of HiSCR90 at Week 16. HiSCR90 is defined as at least a 90% decrease in Abscess and Inflammatory Nodule (AN) count with no increase in the number of abscesses and in the number of draining tunnels/fistulae compared to baseline.","definition_or_measurement_approach":"HiSCR90: ≥90% decrease in AN count with no increase in abscesses or draining tunnels/fistulae vs baseline; measured at Week 16."}
- {"endpoint_text":"- Achievement of NRS30 at Week 16, among participants with baseline NRS ≥ 3 (pooled data from studies CLOU064J12301 and CLOU064J12302). NRS30 is defined as at least a 30% reduction and at least 2-unit reduction from baseline in Patient's Global Assessment of Skin Pain - at worst over the past 7 days","definition_or_measurement_approach":"NRS30: ≥30% and ≥2-unit reduction from baseline in Patient's Global Assessment of Skin Pain (worst over past 7 days); assessed at Week 16 among participants with baseline NRS≥3."}
- {"endpoint_text":"- Occurrence of treatment emergent adverse events and serious adverse events during the study","definition_or_measurement_approach":"Recording and reporting of treatment-emergent adverse events (TEAEs) and serious adverse events (SAEs) during the study period."}
Recruitment
- Planned Sample Size
- 282
- Recruitment Window Months
- 31
- Consent Approach
- Adults provide signed informed consent. For participants aged ≥12 to <18 years, parent/legal guardian signed written informed consent and child assent (if appropriate) must be obtained before any assessments. If a participant reaches the legal age of consent during the study, they must sign the study ICF at the next visit. Age-specific ICFs and assent/parent/guardian forms are provided (documents available in country-specific languages and English).
Methods
- Recruitment advertisements (K2_Advertisements and K1_Recruitment Arrangements documents listed for multiple countries).
- Third-party patient recruitment via vendors listed in sponsor third parties (e.g., Subject Well Inc. listed with duty 'Patient Recrtuitment').
- Patient convenience and support services via vendors (e.g., Greenphire LLC listed with duty 'Patient Convenience').
Geography
- Total Number Of Sites
- 60
- Total Number Of Participants
- 205
Germany
- Earliest CTIS Part Ii Submission Date
- 16-04-2025
- Latest Decision Or Authorization Date
- 13-04-2026
- Processing Time Days
- 362
- Number Of Sites
- 17
- Number Of Participants
- 75
Sites
- Site Name
- Hautaerzte Zentrum Hannover
- Department Name
- 3116: Practice
- Principal Investigator Name
- Florian Schenck
- Principal Investigator Email
- schenck@hautaerzte-zentrum.de
- Contact Person Name
- Florian Schenck
- Contact Person Email
- schenck@hautaerzte-zentrum.de
- Site Name
- Praxis Dr. med. Abdou Zarzour
- Department Name
- 3113: Practice
- Principal Investigator Name
- Abdou Zarzour
- Principal Investigator Email
- Zarzour@gmx.de
- Contact Person Name
- Abdou Zarzour
- Contact Person Email
- Zarzour@gmx.de
- Site Name
- Universitaetsklinikum Schleswig-Holstein AöR
- Department Name
- 3107: Psoriasis-Zentrum-Kiel Klinik für Dermatologie, Venerologie und Allergologie
- Principal Investigator Name
- Sascha Gerdes
- Principal Investigator Email
- Sascha.Gerdes@uksh.de
- Contact Person Name
- Sascha Gerdes
- Contact Person Email
- Sascha.Gerdes@uksh.de
- Site Name
- Universitaetsklinikum Erlangen AöR
- Department Name
- 3105: Hautklinik
- Principal Investigator Name
- Lukas Sollfrank
- Principal Investigator Email
- Lukas.sollfrank@uk-erlangen.de
- Contact Person Name
- Lukas Sollfrank
- Contact Person Email
- Lukas.sollfrank@uk-erlangen.de
- Site Name
- ISA Interdisciplinary Study Association GmbH
- Department Name
- 3110
- Principal Investigator Name
- Margrit Simon
- Principal Investigator Email
- msimon@isa-research.de
- Contact Person Name
- Margrit Simon
- Contact Person Email
- msimon@isa-research.de
- Site Name
- Katholisches Klinikum Bochum gGmbH
- Department Name
- 3109: Klinik fuer Dermatologie, Venerologie und Allergologie
- Principal Investigator Name
- Falk Bechara
- Principal Investigator Email
- Falk.bechara@klinikum-bochum.de
- Contact Person Name
- Falk Bechara
- Contact Person Email
- Falk.bechara@klinikum-bochum.de
- Site Name
- Universitaet Muenster
- Department Name
- 3108: Klinik für Hautkrankheiten
- Principal Investigator Name
- Nina Magnolo
- Principal Investigator Email
- Nina.Magnolo@ukmuenster.de
- Contact Person Name
- Nina Magnolo
- Contact Person Email
- Nina.Magnolo@ukmuenster.de
- Site Name
- Beldio Research GmbH
- Department Name
- 3119: Beldio Research GmbH
- Principal Investigator Name
- Nicolai Treiber
- Principal Investigator Email
- Treiber@beldio.com
- Contact Person Name
- Nicolai Treiber
- Contact Person Email
- Treiber@beldio.com
- Site Name
- Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
- Department Name
- 3101: Hautklinik u Poliklinik d Universitaetsmedizin Mainz/ Clinical Research Center
- Principal Investigator Name
- Petra Staubach-Renz
- Principal Investigator Email
- petra.staubach@unimedizin-mainz.de
- Contact Person Name
- Petra Staubach-Renz
- Contact Person Email
- petra.staubach@unimedizin-mainz.de
- Site Name
- Studienzentrum Dr. med. Beate Schwarz
- Department Name
- 3103: Practice
- Principal Investigator Name
- Beate Schwarz
- Principal Investigator Email
- beate@hautarzt-langenau.de
- Contact Person Name
- Beate Schwarz
- Contact Person Email
- beate@hautarzt-langenau.de
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- 3102: Klinik für Dermatologie, Venerologie und Allergologie Psoriasis Studienzentrum
- Principal Investigator Name
- Sonja Molin
- Principal Investigator Email
- sonja-christine.molin@charite.de
- Contact Person Name
- Sonja Molin
- Contact Person Email
- sonja-christine.molin@charite.de
- Site Name
- Elbe Kliniken Stade-Buxtehude Elbe Klinikum Buxtehude gGmbH
- Department Name
- 3120: Klinik für Dermatologie
- Principal Investigator Name
- Andreas Karl Kleinheinz
- Principal Investigator Email
- Andreas.Kleinheinz@elbekliniken.de
- Contact Person Name
- Andreas Karl Kleinheinz
- Contact Person Email
- Andreas.Kleinheinz@elbekliniken.de
- Site Name
- Eurofins bioskin GmbH
- Department Name
- 3115
- Principal Investigator Name
- Swarna Ekanayake-Bohlig
- Principal Investigator Email
- Swarna.Ekanayake@cpt.eurofinseu.com
- Contact Person Name
- Swarna Ekanayake-Bohlig
- Contact Person Email
- Swarna.Ekanayake@cpt.eurofinseu.com
- Site Name
- Universitaetsklinikum Carl Gustav Carus Dresden an der Technischen Universitaet Dresden AöR
- Department Name
- 3118: Klinik fuer Dermatologie
- Principal Investigator Name
- Roland Aschoff
- Principal Investigator Email
- Roland.Aschoff@uniklinikum-dresden.de
- Contact Person Name
- Roland Aschoff
- Contact Person Email
- Roland.Aschoff@uniklinikum-dresden.de
- Site Name
- Universitaetsklinikum Bonn AöR
- Department Name
- 3114: Klinik für Dermatologie und Allergologie
- Principal Investigator Name
- Jörg Wenzel
- Principal Investigator Email
- joerg.wenzel@ukbonn.de
- Contact Person Name
- Jörg Wenzel
- Contact Person Email
- joerg.wenzel@ukbonn.de
- Site Name
- Universitaetsklinikum Aachen AöR
- Department Name
- 3117: Klinik für Dermatologie und Allergologie
- Principal Investigator Name
- Amir Yazdi
- Principal Investigator Email
- Ayazdi@ukaachen.de
- Contact Person Name
- Amir Yazdi
- Contact Person Email
- Ayazdi@ukaachen.de
- Site Name
- Klinikum Darmstadt GmbH
- Department Name
- 3106: Dermatology
- Principal Investigator Name
- Mana Zur Brügge
- Principal Investigator Email
- Mana.zur-bruegge@mail.klinikum-darmstadt.de
- Contact Person Name
- Mana Zur Brügge
- Contact Person Email
- Mana.zur-bruegge@mail.klinikum-darmstadt.de
Greece
- Earliest CTIS Part Ii Submission Date
- 04-02-2025
- Latest Decision Or Authorization Date
- 17-04-2026
- Processing Time Days
- 437
- Number Of Sites
- 3
- Number Of Participants
- 9
Sites
- Site Name
- Ippokratio General Hospital Of Thessaloniki
- Department Name
- 3152: 1st Dermatology and Venereology Department
- Principal Investigator Name
- Eleni Sotiriou
- Principal Investigator Email
- elenasotiriou@yahoo.gr
- Contact Person Name
- Eleni Sotiriou
- Contact Person Email
- elenasotiriou@yahoo.gr
- Site Name
- University General Hospital Of Heraklion
- Department Name
- 3153: Department of Dermatology
- Principal Investigator Name
- Konstantinos Krasagakis
- Principal Investigator Email
- krasagak@med.uoc.gr
- Contact Person Name
- Konstantinos Krasagakis
- Contact Person Email
- krasagak@med.uoc.gr
- Site Name
- University General Hospital Attikon
- Department Name
- 3151: 4th Department of Internal Medicine
- Principal Investigator Name
- Evangelos Giamarellos Bourboulis
- Principal Investigator Email
- egiamarel@med.uoa.gr
- Contact Person Name
- Evangelos Giamarellos Bourboulis
- Contact Person Email
- egiamarel@med.uoa.gr
Portugal
- Earliest CTIS Part Ii Submission Date
- 21-04-2025
- Latest Decision Or Authorization Date
- 14-04-2026
- Processing Time Days
- 358
- Number Of Sites
- 6
- Number Of Participants
- 19
Sites
- Site Name
- Unidade Local De Saude De Coimbra E.P.E.
- Department Name
- 3305: Serviço de Dermatologia
- Principal Investigator Name
- Ricardo Vieira
- Principal Investigator Email
- 6817@ulscoimbra.min-saude.pt
- Contact Person Name
- Ricardo Vieira
- Contact Person Email
- 6817@ulscoimbra.min-saude.pt
- Site Name
- CCAB Centro Clinico Academico Braga Associacao
- Department Name
- 3301: Serviço de Dermatologia
- Principal Investigator Name
- Celeste Brito
- Principal Investigator Email
- celeste.brito@hb.min-saude.pt
- Contact Person Name
- Celeste Brito
- Contact Person Email
- celeste.brito@hb.min-saude.pt
- Site Name
- Unidade Local De Saude De Almada-Seixal E.P.E.
- Department Name
- 3306: Serviço de Dermatologia
- Principal Investigator Name
- Rita Figueiredo Pimenta
- Principal Investigator Email
- rita.pimenta@hgo.min-saude.pt
- Contact Person Name
- Rita Figueiredo Pimenta
- Contact Person Email
- rita.pimenta@hgo.min-saude.pt
- Site Name
- Unidade Local De Saude De Sao Jose E.P.E.
- Department Name
- 3303: Serviço de Dermatologia
- Principal Investigator Name
- Joana Cabete
- Principal Investigator Email
- Joana.cabete@ulssjose.min-saude.pt
- Contact Person Name
- Joana Cabete
- Contact Person Email
- Joana.cabete@ulssjose.min-saude.pt
- Site Name
- Unidade Local De Saude De Santo Antonio E.P.E.
- Department Name
- 3304: Serviço de Dermatologia
- Principal Investigator Name
- Inês Lobo
- Principal Investigator Email
- u08253@chporto.min-saude.pt
- Contact Person Name
- Inês Lobo
- Contact Person Email
- u08253@chporto.min-saude.pt
- Site Name
- Hospital Cuf Descobertas S.A.
- Department Name
- 3302: Serviço de Dermatologia
- Principal Investigator Name
- Pedro Mendes Bastos
- Principal Investigator Email
- pedro.mm.bastos@cuf.pt
- Contact Person Name
- Pedro Mendes Bastos
- Contact Person Email
- pedro.mm.bastos@cuf.pt
Bulgaria
- Earliest CTIS Part Ii Submission Date
- 16-04-2025
- Latest Decision Or Authorization Date
- 20-04-2026
- Processing Time Days
- 369
- Number Of Sites
- 4
- Number Of Participants
- 10
Sites
- Site Name
- ASMC IPSMC Skin And Venereal Diseases
- Department Name
- 3001
- Principal Investigator Name
- Ivan Botev
- Principal Investigator Email
- botev2@yahoo.com
- Contact Person Name
- Ivan Botev
- Contact Person Email
- botev2@yahoo.com
- Site Name
- Medical Center Kordis OOD
- Department Name
- 3003
- Principal Investigator Name
- Dimitar Gospodinov
- Principal Investigator Email
- dkg@abv.bg
- Contact Person Name
- Dimitar Gospodinov
- Contact Person Email
- dkg@abv.bg
- Site Name
- Acibadem City Clinic Tokuda University Hospital EAD
- Department Name
- 3004: Clinic of Dermatology and Venereology disease
- Principal Investigator Name
- Ivan Bogdanov
- Principal Investigator Email
- iv.bogdanov@gmail.com
- Contact Person Name
- Ivan Bogdanov
- Contact Person Email
- iv.bogdanov@gmail.com
- Site Name
- Umbal - Prof. D-R Stoyan Kirkovich AD
- Department Name
- 3002: Dermatology and Venereology clinic
- Principal Investigator Name
- Evgenia Hristakieva
- Principal Investigator Email
- ehristakieva@gmail.com
- Contact Person Name
- Evgenia Hristakieva
- Contact Person Email
- ehristakieva@gmail.com
Spain
- Earliest CTIS Part Ii Submission Date
- 16-04-2025
- Latest Decision Or Authorization Date
- 20-04-2026
- Processing Time Days
- 369
- Number Of Sites
- 10
- Number Of Participants
- 39
Sites
- Site Name
- Hospital Universitario De Fuenlabrada
- Department Name
- 3451: Servicio Dermatología
- Principal Investigator Name
- Alberto Romero Maté
- Principal Investigator Email
- romerom@salud.madrid.org
- Contact Person Name
- Alberto Romero Maté
- Contact Person Email
- romerom@salud.madrid.org
- Site Name
- Hospital Universitario Dr Peset Aleixandre
- Department Name
- 3452: Servicio Dermatología
- Principal Investigator Name
- Almudena Mateu Puchades
- Principal Investigator Email
- mateu_alm@gva.es
- Contact Person Name
- Almudena Mateu Puchades
- Contact Person Email
- mateu_alm@gva.es
- Site Name
- Hospital General Universitario De Valencia
- Department Name
- 3460: Servicio Dermatología
- Principal Investigator Name
- José María Ortiz Salvador
- Principal Investigator Email
- ortiz_jossal@gva.es
- Contact Person Name
- José María Ortiz Salvador
- Contact Person Email
- ortiz_jossal@gva.es
- Site Name
- Hospital Universitario Puerta Del Mar
- Department Name
- 3455: Servicio Dermatología
- Principal Investigator Name
- David Jimenez Gallo
- Principal Investigator Email
- david.jimenez.gallo.sspa@juntadeandalucia.es
- Contact Person Name
- David Jimenez Gallo
- Contact Person Email
- david.jimenez.gallo.sspa@juntadeandalucia.es
- Site Name
- Hospital Universitario La Paz
- Department Name
- 3459: Servicio Dermatología
- Principal Investigator Name
- Pedro Herranz Pinto
- Principal Investigator Email
- pedro.herranz@salud.madrid.org
- Contact Person Name
- Pedro Herranz Pinto
- Contact Person Email
- pedro.herranz@salud.madrid.org
- Site Name
- Parc Tauli Hospital Universitari
- Department Name
- 3458: Servicio Dermatología
- Principal Investigator Name
- Patricia Garbayo Salmons
- Principal Investigator Email
- pgarbayo.parctauli@gmail.com
- Contact Person Name
- Patricia Garbayo Salmons
- Contact Person Email
- pgarbayo.parctauli@gmail.com
- Site Name
- Hospital General Universitario Gregorio Maranon
- Department Name
- 3454: Servicio Dermatología
- Principal Investigator Name
- Cristina Ciudad Blanco
- Principal Investigator Email
- cristina.ciudad@salud.madrid.org
- Contact Person Name
- Cristina Ciudad Blanco
- Contact Person Email
- cristina.ciudad@salud.madrid.org
- Site Name
- Hospital Germans Trias I Pujol
- Department Name
- 3457: Servicio Dermatología
- Principal Investigator Name
- Julio Bassas Vila
- Principal Investigator Email
- jbassas@igtp.cat
- Contact Person Name
- Julio Bassas Vila
- Contact Person Email
- jbassas@igtp.cat
- Site Name
- Hospital Del Mar
- Department Name
- 3456: Servicio Dermatología
- Principal Investigator Name
- Gemma Martín Ezquerra
- Principal Investigator Email
- GMartin@parcdesalutmar.cat
- Contact Person Name
- Gemma Martín Ezquerra
- Contact Person Email
- GMartin@parcdesalutmar.cat
- Site Name
- Hospital De Manises
- Department Name
- 3453: Servicio Dermatología
- Principal Investigator Name
- Antonio Martorell Calatayud
- Principal Investigator Email
- antmarto@hotmail.com
- Contact Person Name
- Antonio Martorell Calatayud
- Contact Person Email
- antmarto@hotmail.com
Poland
- Earliest CTIS Part Ii Submission Date
- 11-04-2025
- Latest Decision Or Authorization Date
- 20-04-2026
- Processing Time Days
- 374
- Number Of Sites
- 3
- Number Of Participants
- 14
Sites
- Site Name
- Dermoklinika Centrum Medyczne s.c. M. Kierstan, J. Narbutt, A. Lesiak
- Department Name
- 3252
- Principal Investigator Name
- Joanna Narbutt
- Principal Investigator Email
- joanna.narbutt@onet.pl
- Contact Person Name
- Joanna Narbutt
- Contact Person Email
- joanna.narbutt@onet.pl
- Site Name
- Uniwersyteckie Centrum Kliniczne
- Department Name
- 3251: Klinika Dermatologii, Wenerologii i Alergologii
- Principal Investigator Name
- Roman Nowicki
- Principal Investigator Email
- nowicki@gumed.edu.pl
- Contact Person Name
- Roman Nowicki
- Contact Person Email
- nowicki@gumed.edu.pl
- Site Name
- Szpital Uniwersytecki Nr 1 Im. Dr. A. Jurasza W Bydgoszczy
- Department Name
- 3253: Klinika Dermatologii, Chorób Przenoszonych Drogą Płciową i Immunodermatologii
- Principal Investigator Name
- Luiza Marek-Jozefowicz
- Principal Investigator Email
- lui06@interia.pl
- Contact Person Name
- Luiza Marek-Jozefowicz
- Contact Person Email
- lui06@interia.pl
Italy
- Earliest CTIS Part Ii Submission Date
- 04-02-2025
- Latest Decision Or Authorization Date
- 20-04-2026
- Processing Time Days
- 440
- Number Of Sites
- 11
- Number Of Participants
- 22
Sites
- Site Name
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Department Name
- 3201: U.O.C. Dermatologia
- Principal Investigator Name
- Ketty Peris
- Principal Investigator Email
- ketty.peris@unicatt.it
- Contact Person Name
- Ketty Peris
- Contact Person Email
- ketty.peris@unicatt.it
- Site Name
- Azienda Ospedaliero-Universitaria Policlinico G. Rodolico-San Marco Di Catania
- Department Name
- 3210: U.O.C. Clinica Dermatologica
- Principal Investigator Name
- Giuseppe Micali
- Principal Investigator Email
- gmicalitrial@gmail.com
- Contact Person Name
- Giuseppe Micali
- Contact Person Email
- gmicalitrial@gmail.com
- Site Name
- Azienda Ospedaliero Universitaria Di Modena
- Department Name
- 3202: S.C. Dermatologia
- Principal Investigator Name
- Cristina Magnoni
- Principal Investigator Email
- cristina.magnoni@unimore.it
- Contact Person Name
- Cristina Magnoni
- Contact Person Email
- cristina.magnoni@unimore.it
- Site Name
- University Hospital Of Ferrara
- Department Name
- 3209: U.O. di Dermatologia
- Principal Investigator Name
- Alessandro Borghi
- Principal Investigator Email
- brglsn1@unife.it
- Contact Person Name
- Alessandro Borghi
- Contact Person Email
- brglsn1@unife.it
- Site Name
- Azienda USL Toscana Centro
- Department Name
- 3206: U.O. Dermatologia II
- Principal Investigator Name
- Francesca Prignano
- Principal Investigator Email
- francesca.prignano@unifi.it
- Contact Person Name
- Francesca Prignano
- Contact Person Email
- francesca.prignano@unifi.it
- Site Name
- Azienda Ospedaliero Universitaria Pisana
- Department Name
- 3207: U.O.C. Dermatologia
- Principal Investigator Name
- Marco Romanelli
- Principal Investigator Email
- m.romanelli@med.unipi.it
- Contact Person Name
- Marco Romanelli
- Contact Person Email
- m.romanelli@med.unipi.it
- Site Name
- Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
- Department Name
- 3205: U.O. Dermatologia
- Principal Investigator Name
- Marina Venturini
- Principal Investigator Email
- marina.venturini@unibs.it
- Contact Person Name
- Marina Venturini
- Contact Person Email
- marina.venturini@unibs.it
- Site Name
- Humanitas Mirasole S.p.A.
- Department Name
- 3212: U.O. Dermatologia e Venereologia
- Principal Investigator Name
- Mario Valenti
- Principal Investigator Email
- mario.valenti@hunimed.eu
- Contact Person Name
- Mario Valenti
- Contact Person Email
- mario.valenti@hunimed.eu
- Site Name
- Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
- Department Name
- 3204: S.C. Dermatologia
- Principal Investigator Name
- Angelo Valerio Marzano
- Principal Investigator Email
- angelo.marzano@unimi.it
- Contact Person Name
- Angelo Valerio Marzano
- Contact Person Email
- angelo.marzano@unimi.it
- Site Name
- Azienda Ospedaliero Universitaria Delle Marche
- Department Name
- 3213: SOD Clinica di Dermatologia
- Principal Investigator Name
- Elisa Molinelli
- Principal Investigator Email
- elisa.molinelli@ospedaliriuniti.marche.it
- Contact Person Name
- Elisa Molinelli
- Contact Person Email
- elisa.molinelli@ospedaliriuniti.marche.it
- Site Name
- Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
- Department Name
- 3211: Osp. Dermatologico San Lazzaro
- Principal Investigator Name
- Simone Ribero
- Principal Investigator Email
- simone.ribero@unito.it
- Contact Person Name
- Simone Ribero
- Contact Person Email
- simone.ribero@unito.it
Slovakia
- Earliest CTIS Part Ii Submission Date
- 16-04-2025
- Latest Decision Or Authorization Date
- 20-04-2026
- Processing Time Days
- 369
- Number Of Sites
- 4
- Number Of Participants
- 13
Sites
- Site Name
- Cliniq s.r.o.
- Department Name
- 3353: Dermatovenerologická ambulancia
- Principal Investigator Name
- Barbora Ondrak
- Principal Investigator Email
- ondrak@polibez.sk
- Contact Person Name
- Barbora Ondrak
- Contact Person Email
- ondrak@polibez.sk
- Site Name
- University Hospital Bratislava
- Department Name
- 3355: Dermatovenerologická klinika
- Principal Investigator Name
- Martina Part
- Principal Investigator Email
- martina.part@icloud.com
- Contact Person Name
- Martina Part
- Contact Person Email
- martina.part@icloud.com
- Site Name
- Fakultna Nemocnica Trnava
- Department Name
- 3351: Dermatovenerologické oddelenie
- Principal Investigator Name
- Peter Kozub
- Principal Investigator Email
- peter.kozub.derm@gmail.com
- Contact Person Name
- Peter Kozub
- Contact Person Email
- peter.kozub.derm@gmail.com
- Site Name
- Medikard s.r.o.
- Department Name
- 3354: Kožná ambulancia Youderm
- Principal Investigator Name
- Tomáš Uhrin
- Principal Investigator Email
- tomasuhrin404@gmail.com
- Contact Person Name
- Tomáš Uhrin
- Contact Person Email
- tomasuhrin404@gmail.com
Denmark
- Earliest CTIS Part Ii Submission Date
- 07-05-2025
- Latest Decision Or Authorization Date
- 06-05-2026
- Processing Time Days
- 364
- Number Of Sites
- 2
- Number Of Participants
- 4
Sites
- Site Name
- Region Sjaelland
- Department Name
- 3053: Dermatologisk afdeling
- Principal Investigator Name
- Peter Theut Riis
- Principal Investigator Email
- pmik@regionsjaelland.dk
- Contact Person Name
- Peter Theut Riis
- Contact Person Email
- pmik@regionsjaelland.dk
- Site Name
- Region Hovedstaden
- Department Name
- 3051: Dermatologisk-Venerologisk Afdeling og videncenter for sårheling D/S
- Principal Investigator Name
- Simon Francis Thomsen
- Principal Investigator Email
- simon.francis.thomsen.02@regionh.dk
- Contact Person Name
- Simon Francis Thomsen
- Contact Person Email
- simon.francis.thomsen.02@regionh.dk
Sponsor
Primary sponsor
- Full Name
- Novartis Pharma AG
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- Switzerland
Contract research organisations
- Name
- IQVIA Limited
- Responsibilities
- sponsorDuties codes: 1; contact eu_clinical_trials_information@iqvia.com
- Name
- Parexel International (IRL) Limited
- Responsibilities
- sponsorDuties codes: 12
- Name
- Icon Clinical Research Limited
- Responsibilities
- sponsorDuties codes: 1
- Name
- PRA Hellas CRO A.E.
- Responsibilities
- sponsorDuties codes: 1
- Name
- Syneos Health Inc.
- Responsibilities
- sponsorDuties codes: 1
Third parties
- {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"sponsorDuties codes: 1 (contact eu_clinical_trials_information@iqvia.com)","organisation_type":"Pharmaceutical company"}
- {"country":"France","full_name":"Kayentis","duties_or_roles":"PRO management, PRO licensing and translations, data collection via tablet","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"Subject Well Inc.","duties_or_roles":"Patient Recrtuitment","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"Italy","full_name":"Opis S.r.l.","duties_or_roles":"TMF archive","organisation_type":"Pharmaceutical company"}
- {"country":"China","full_name":"Q Squared Solutions (Beijing) Co. Ltd.","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
- {"country":"Germany","full_name":"Labor Dr. Spranger","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"sponsorDuties codes: 12","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"sponsorDuties codes: 1 (duplicate entry)","organisation_type":"Pharmaceutical company"}
- {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"sponsorDuties codes: 1","organisation_type":"Pharmaceutical company"}
- {"country":"France","full_name":"SGS France","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
- {"country":"Greece","full_name":"PRA Hellas CRO A.E.","duties_or_roles":"sponsorDuties codes: 1","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Iqvia Laboratories Limited","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Patient Convenience","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"RWS Life Sciences Inc.","duties_or_roles":"PRO formatting and translations and Trial Feedback Questionnaire","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Syneos Health Inc.","duties_or_roles":"sponsorDuties codes: 1","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Canfield Scientific Inc.","duties_or_roles":"Photography","organisation_type":"Pharmaceutical company"}
- {"country":"Bulgaria","full_name":"S & D Pharma Logistics BG EOOD","duties_or_roles":"Storage and destruction of IMPD.","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"Central ECG reading","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"sponsorDuties codes: 7","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Medical Equipment Supplies And Management Limited","duties_or_roles":"Freezer and cooler bag supplies","organisation_type":"Pharmaceutical company"}
Investigational products
- Investigational Product Name
- LOU064
- Active Substance
- REMIBRUTINIB
- Modality
- Small molecule
- Routes Of Administration
- ORAL
- Route
- ORAL
- Authorisation Status
- prodAuthStatus: 1
- Investigational Product Name
- Placebo to Remibrutinib (LOU064) 0 mg matching 00 mg film-coated tablet
- Modality
- Other
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