Clinical trial • Phase I • Dermatology|Immunology

RAY121 for Immune-mediated necrotizing myopathy | Antiphospholipid syndrome | Behçet’s syndrome | Bullous pemphigoid | Dermatomyositis | Immune thrombocytopenia

Phase I trial of RAY121 for Immune-mediated necrotizing myopathy | Antiphospholipid syndrome | Behçet’s syndrome | Bullous pemphigoid | Dermatomyositis |…

Overview

Trial Therapeutic Area
Dermatology|Immunology
Trial Disease
Immune-mediated necrotizing myopathy | Antiphospholipid syndrome | Behçet’s syndrome | Bullous pemphigoid | Dermatomyositis | Immune thrombocytopenia
Trial Stage
Phase I

Key dates

Initial CTIS Submission Date
07-10-2024
First CTIS Authorization Date
11-02-2025

Trial design

open-label Phase I trial in Austria, Romania, France and others.

Open Label
Yes
Target Sample Size
66

Recruitment

Planned Sample Size
66
Recruitment Window Months
21

Geography

Total Number Of Sites
43
Total Number Of Participants
78

Austria

Earliest CTIS Part Ii Submission Date
28-01-2025
Latest Decision Or Authorization Date
17-02-2025
Processing Time Days
20
Number Of Sites
1
Number Of Participants
4

Sites

Site Name
Medical University Of Vienna
Department Name
Department of Clinical Pharmacology
Principal Investigator Name
Bernd Jilma
Principal Investigator Email
bernd.jilma@meduniwien.ac.at
Contact Person Name
Bernd Jilma
Contact Person Email
bernd.jilma@meduniwien.ac.at

Romania

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
14-02-2025
Processing Time Days
113
Number Of Sites
2
Number Of Participants
7

Sites

Site Name
Arensia Clinics S.R.L.
Department Name
Internal Medicine
Principal Investigator Name
Mihai Abobului
Principal Investigator Email
mihai.abobului.ext@arensia-em.com
Contact Person Name
Mihai Abobului
Site Name
Institute Of Oncology Prof. Dr. Ion Chiricuta Cluj-Napoca
Department Name
Internal Medicine
Principal Investigator Name
Ionut-Ciprian Tomuleasa
Principal Investigator Email
ciprian.tomuleasa.ext@arensia-em.com
Contact Person Name
Ionut-Ciprian Tomuleasa

France

Earliest CTIS Part Ii Submission Date
15-11-2024
Latest Decision Or Authorization Date
12-02-2025
Processing Time Days
89
Number Of Sites
2
Number Of Participants
10

Sites

Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Rheumatology
Principal Investigator Name
Christian Jorgensen
Principal Investigator Email
c-jorgensen@chu-montpellier.fr
Contact Person Name
Christian Jorgensen
Contact Person Email
c-jorgensen@chu-montpellier.fr
Site Name
Hopitaux Universitaires Pitie Salpetriere
Department Name
Internal Medicine and Clinical Immunology
Principal Investigator Name
David Saadoun
Principal Investigator Email
david.saadoun@aphp.fr
Contact Person Name
David Saadoun
Contact Person Email
david.saadoun@aphp.fr

Spain

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
27-03-2025
Processing Time Days
154
Number Of Sites
9
Number Of Participants
10

Sites

Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Hematology
Principal Investigator Name
Santiago Bonanad Boix
Principal Investigator Email
bonanad_san@gva.es
Contact Person Name
Santiago Bonanad Boix
Contact Person Email
bonanad_san@gva.es
Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Rheumatology
Principal Investigator Name
Francisco Javier Bachiller Corral
Principal Investigator Email
javierbachiller@gmail.com
Contact Person Name
Francisco Javier Bachiller Corral
Contact Person Email
javierbachiller@gmail.com
Site Name
Hospital Universitario 12 De Octubre
Department Name
Rheumatology
Principal Investigator Name
Patricia Carreira Delgado
Principal Investigator Email
carreira@h12o.es
Contact Person Name
Patricia Carreira Delgado
Contact Person Email
carreira@h12o.es
Site Name
Clinica Universidad De Navarra
Department Name
Hematology
Principal Investigator Name
Carlos Grande Garcia
Principal Investigator Email
cgrandeg@unav.es
Contact Person Name
Carlos Grande Garcia
Contact Person Email
cgrandeg@unav.es
Site Name
Hospital Universitari Vall D Hebron
Department Name
Hematology
Principal Investigator Name
David Valcarcel Ferreiras
Principal Investigator Email
dvalcarcelct@vhio.net
Contact Person Name
David Valcarcel Ferreiras
Contact Person Email
dvalcarcelct@vhio.net
Site Name
Hospital Universitario Reina Sofia
Department Name
Rheumatology
Principal Investigator Name
Alejandro Escudero Contreras
Principal Investigator Email
alexcudero@hotmail.com
Contact Person Name
Alejandro Escudero Contreras
Contact Person Email
alexcudero@hotmail.com
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Hematology
Principal Investigator Name
Maria Eva Mingot Castellano
Principal Investigator Email
mariae.mingot.sspa@juntadeandalucia.es
Contact Person Name
Maria Eva Mingot Castellano
Site Name
Hospital Universitari Vall D Hebron
Department Name
Internal Medicine
Principal Investigator Name
Jose Pardos Gea
Principal Investigator Email
jose.pardos@vallhebron.cat
Contact Person Name
Jose Pardos Gea
Contact Person Email
jose.pardos@vallhebron.cat
Site Name
Clinica Universidad De Navarra
Department Name
Hematology
Principal Investigator Name
Carlos Grande Garcia
Principal Investigator Email
cgrandeg@unav.es
Contact Person Name
Carlos Grande Garcia
Contact Person Email
cgrandeg@unav.es

Italy

Earliest CTIS Part Ii Submission Date
13-12-2024
Latest Decision Or Authorization Date
12-02-2025
Processing Time Days
61
Number Of Sites
3
Number Of Participants
2

Sites

Site Name
Ospedale San Giovanni Bosco
Department Name
SCdU Nefrologia e Dialisi
Principal Investigator Name
Savino Sciascia
Principal Investigator Email
savino.sciascia@unito.it
Contact Person Name
Savino Sciascia
Contact Person Email
savino.sciascia@unito.it
Site Name
Humanitas Mirasole S.p.A.
Department Name
Dermatology
Principal Investigator Name
Antonio Costanzo
Principal Investigator Email
antonio.costanzo@hunimed.eu
Contact Person Name
Antonio Costanzo
Contact Person Email
antonio.costanzo@hunimed.eu
Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
Oncologia ed Ematologia Clinica e Sperimentale
Principal Investigator Name
Alessandro Lucchesi
Principal Investigator Email
alessandro.lucchesi@irst.emr.it
Contact Person Name
Alessandro Lucchesi

Poland

Earliest CTIS Part Ii Submission Date
14-01-2025
Latest Decision Or Authorization Date
17-02-2025
Processing Time Days
34
Number Of Sites
1
Number Of Participants
4

Sites

Site Name
Narodowy Instytut Geriatrii Reumatologii I Rehabilitacji Im Prof. Dr Hab. Med. Eleonory Reicher
Department Name
Centrum Wsparcia Badań Klinicznych
Principal Investigator Name
Małgorzata Wisłowska
Principal Investigator Email
malgorzata.wislowska@spartanska.pl
Contact Person Name
Małgorzata Wisłowska

Czechia

Earliest CTIS Part Ii Submission Date
16-01-2025
Latest Decision Or Authorization Date
12-02-2025
Processing Time Days
27
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Fakultni Nemocnice Kralovske Vinohrady
Department Name
Dermatovenerologická klinika
Principal Investigator Name
Petr Arenberger
Principal Investigator Email
avemedica@email.cz
Contact Person Name
Petr Arenberger
Contact Person Email
avemedica@email.cz

Bulgaria

Earliest CTIS Part Ii Submission Date
24-10-2024
Latest Decision Or Authorization Date
12-02-2025
Processing Time Days
111
Number Of Sites
3
Number Of Participants
6

Sites

Site Name
Specialized Hospital For Active Treatment Of Hematological Diseases EAD
Department Name
Clinic of Clinical Hematology
Principal Investigator Name
Tanya Yankova
Principal Investigator Email
t.yankova@hematology.bg
Contact Person Name
Tanya Yankova
Contact Person Email
t.yankova@hematology.bg
Site Name
Umbal - Prof. D-R Stoyan Kirkovich AD
Department Name
Department of Clinical Hematology
Principal Investigator Name
Mariya Todorova
Principal Investigator Email
dr.maria.dtodorova@gmail.com
Contact Person Name
Mariya Todorova
Contact Person Email
dr.maria.dtodorova@gmail.com
Site Name
University Multiprofile Hospital For Active Treatment St. Ivan Rilski EAD
Department Name
Clinic of Rheumatology
Principal Investigator Name
Vladimira Boyazhieva
Principal Investigator Email
vladimira.boyazhieva@gmail.com
Contact Person Name
Vladimira Boyazhieva
Contact Person Email
vladimira.boyazhieva@gmail.com

Croatia

Earliest CTIS Part Ii Submission Date
13-01-2025
Latest Decision Or Authorization Date
25-02-2025
Processing Time Days
43
Number Of Sites
6
Number Of Participants
6

Sites

Site Name
Specijalna Bolnica Medico
Department Name
Hematology
Principal Investigator Name
Toni Valkovic
Principal Investigator Email
medico@medico.hr
Contact Person Name
Toni Valkovic
Contact Person Email
medico@medico.hr
Site Name
Specijalna Bolnica Medico
Department Name
Clinical pharmacology
Principal Investigator Name
Andrej Belančić
Principal Investigator Email
a.belancic93@gmail.com
Contact Person Name
Andrej Belančić
Contact Person Email
a.belancic93@gmail.com
Site Name
Specijalna Bolnica Medico
Department Name
Dermatology and Venerology
Principal Investigator Name
Sandra Peternel
Principal Investigator Email
sandra.peternel@medico.hr
Contact Person Name
Sandra Peternel
Contact Person Email
sandra.peternel@medico.hr
Site Name
Klinicki bolnicki centar Sestre milosrdnice
Department Name
Dermatovenerology
Principal Investigator Name
Iva Blajić
Principal Investigator Email
ivablajic@hotmail.com
Contact Person Name
Iva Blajić
Contact Person Email
ivablajic@hotmail.com
Site Name
KBC Zagreb
Department Name
Immunodermatology
Principal Investigator Name
Branka Marinović
Principal Investigator Email
branka.marinovic@kbc-zagreb.hr
Contact Person Name
Branka Marinović
Contact Person Email
branka.marinovic@kbc-zagreb.hr
Site Name
Specijalna Bolnica Medico
Department Name
Rheumatology
Principal Investigator Name
Marija Rogoznica Pavlović
Principal Investigator Email
marija.rogoznica@gmail.com
Contact Person Name
Marija Rogoznica Pavlović
Contact Person Email
marija.rogoznica@gmail.com

Hungary

Earliest CTIS Part Ii Submission Date
06-12-2024
Latest Decision Or Authorization Date
13-02-2025
Processing Time Days
69
Number Of Sites
2
Number Of Participants
7

Sites

Site Name
University Of Szeged
Department Name
Szent-Györgyi Albert Klinikai Központ, Klinikai Farmakológiai Központ Fázis I. Vizsgálóhely
Principal Investigator Name
Róbert Takács
Principal Investigator Email
takacs.robert@med.u-szeged.hu
Contact Person Name
Róbert Takács
Contact Person Email
takacs.robert@med.u-szeged.hu
Site Name
Semmelweis University
Department Name
Belgyógyászati és Onkológiai Klinika
Principal Investigator Name
István Takács
Principal Investigator Email
takacs.istvan@semmelweis.hu
Contact Person Name
István Takács
Contact Person Email
takacs.istvan@semmelweis.hu

Netherlands

Earliest CTIS Part Ii Submission Date
30-01-2025
Latest Decision Or Authorization Date
14-02-2025
Processing Time Days
15
Number Of Sites
2
Number Of Participants
6

Sites

Site Name
Universitair Medisch Centrum Utrecht
Department Name
Haematology
Principal Investigator Name
Ward Van Beers
Principal Investigator Email
E.J.vanBeers-3@umcutrecht.nl
Contact Person Name
Ward Van Beers
Contact Person Email
E.J.vanBeers-3@umcutrecht.nl
Site Name
Universitair Medisch Centrum Groningen
Department Name
Dermatology
Principal Investigator Name
Joost Meijer
Principal Investigator Email
j.m.meijer@umcg.nl
Contact Person Name
Joost Meijer
Contact Person Email
j.m.meijer@umcg.nl

Germany

Earliest CTIS Part Ii Submission Date
23-01-2025
Latest Decision Or Authorization Date
19-03-2025
Processing Time Days
55
Number Of Sites
6
Number Of Participants
9

Sites

Site Name
Universitaetsmedizin Goettingen
Department Name
Klinik für Neurologie
Principal Investigator Name
Jana Zschüntzsch
Principal Investigator Email
j.zschuentzsch@med.uni-goettingen
Contact Person Name
Jana Zschüntzsch
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Institut für Entzündungsmedizin
Principal Investigator Name
Diamant Thaci
Principal Investigator Email
diamant.thaci@uksh.de
Contact Person Name
Diamant Thaci
Contact Person Email
diamant.thaci@uksh.de
Site Name
Technische Universitaet Dresden
Department Name
Klinik und Poliklinik für Dermatologie
Principal Investigator Name
Susanne Abraham
Principal Investigator Email
susanne.abraham@ukdd.de
Contact Person Name
Susanne Abraham
Contact Person Email
susanne.abraham@ukdd.de
Site Name
Immanuel Klinik Ruedersdorf
Department Name
Neurologie
Principal Investigator Name
Jens Schmidt
Principal Investigator Email
jens.schmidt@mhb-fontane.de
Contact Person Name
Jens Schmidt
Contact Person Email
jens.schmidt@mhb-fontane.de
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Hautklinik
Principal Investigator Name
Matthias Hahn
Principal Investigator Email
matthias.hahn@med.uni-tuebingen.de
Contact Person Name
Matthias Hahn
Site Name
Universitaetsklinikum Erlangen AöR
Department Name
Hautklinik
Principal Investigator Name
Michael Sticherling
Principal Investigator Email
michael.sticherling@uk-erlangen.de
Contact Person Name
Michael Sticherling

Portugal

Earliest CTIS Part Ii Submission Date
22-01-2025
Latest Decision Or Authorization Date
11-02-2025
Processing Time Days
20
Number Of Sites
2
Number Of Participants
3

Sites

Site Name
Unidade Local De Saude De Gaia/Espinho E.P.E.
Department Name
Rheumatology
Principal Investigator Name
Taciana Videira
Principal Investigator Email
taciana.videira@ulsge.min-saude.pt
Contact Person Name
Taciana Videira
Site Name
CCAB Centro Clinico Academico Braga Associacao
Department Name
Rheumatology
Principal Investigator Name
Joana Sousa Neves
Principal Investigator Email
joana.neves@hb.min-saude.pt
Contact Person Name
Joana Sousa Neves
Contact Person Email
joana.neves@hb.min-saude.pt

Norway

Earliest CTIS Part Ii Submission Date
21-01-2025
Latest Decision Or Authorization Date
13-02-2025
Processing Time Days
23
Number Of Sites
3
Number Of Participants
2

Sites

Site Name
Helse Stavanger HF
Department Name
Rheumatology
Principal Investigator Name
Jens Vikse
Principal Investigator Email
jens.vikse@sus.no
Contact Person Name
Jens Vikse
Contact Person Email
jens.vikse@sus.no
Site Name
Sykehuset Oestfold HF Kalnes
Department Name
Hematology
Principal Investigator Name
Eirik Tjønnfjord
Principal Investigator Email
eirik.tjonnfjord@so-hf.no
Contact Person Name
Eirik Tjønnfjord
Contact Person Email
eirik.tjonnfjord@so-hf.no
Site Name
Sorlandet Sykehus HF
Department Name
Rheumatology
Principal Investigator Name
Katarzyna Weronika Losinska
Principal Investigator Email
katarzyna.weronika.losinska@sshf.no
Contact Person Name
Katarzyna Weronika Losinska

Sponsor

Primary sponsor

Full Name
Chugai Pharmaceutical Co. Ltd.
Organisation Type
Pharmaceutical company
Country Of Registered Address
Japan

Investigational products

Investigational Product Name
RAY121

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