Clinical trial • Phase III • Infectious Disease

RASBURICASE for Sepsis

Phase III trial of RASBURICASE for Sepsis.

Overview

Trial Therapeutic Area
Infectious Disease
Trial Disease
Sepsis
Trial Stage
Phase III
Drug Modality
Peptide/protein/enzyme

Key dates

Initial CTIS Submission Date
01-08-2025
First CTIS Authorization Date
24-11-2025

Trial design

Randomised, control arm: 50 ml of a sodium chloride (0.9%) single intravenous infusion associated with standard of care (placebo control). experimental arm: fasturtec (rasburicase 1.5 mg/ml) 7.5 mg, reconstituted and diluted in 50 ml sodium chloride (0.9%), single intravenous infusion over 30 minutes, associated with standard of care. Phase III trial across 8 sites in France.

Randomised
Yes
Comparator
Control arm: 50 ml of a sodium chloride (0.9%) single intravenous infusion associated with standard of care (placebo control). Experimental arm: Fasturtec (Rasburicase 1.5 mg/ml) 7.5 mg, reconstituted and diluted in 50 ml sodium chloride (0.9%), single intravenous infusion over 30 minutes, associated with standard of care.
Target Sample Size
240
Trial Duration For Participant
90

Eligibility

Recruits 240 Vulnerable population selected. Informed consent form required ("Informed consent form signed" as inclusion). Subject information sheets and informed consent forms are provided for patients and for 'proche' (relative/legal representative), indicating proxy/representative consent procedures may be used. Trial restricted to adults (≥18), so no assent procedures for minors..

Pregnancy Exclusion
Pregnant or breastfeeding woman
Vulnerable Population
Vulnerable population selected. Informed consent form required ("Informed consent form signed" as inclusion). Subject information sheets and informed consent forms are provided for patients and for 'proche' (relative/legal representative), indicating proxy/representative consent procedures may be used. Trial restricted to adults (≥18), so no assent procedures for minors.

Inclusion criteria

  • {"criterion_text":"- Patients ≥18 years old\n- Diagnosis of sepsis (presumed or known infection and increase in SOFA score ≥ 2), included within 48 hours of diagnosis.\n- Uricémia ≥ 200 µmol/L\n- Rapid diagnostic test strip for G6PD deficiency negative\n- Patient affiliated with a social security scheme\n- Informed consent form signed\n- Woman of childbearing age using effective contraception throughout the treatment and for 1 month after the end of the treatment.\n- Hospitalised in intensive care unit"}

Exclusion criteria

  • {"criterion_text":"- Minor\n- Surgery involving the kidneys or urinary tract in the last 3 months\n- Life expectancy less than 6 months\n- Pregnant or breastfeeding woman\n- Chronic kidney failure on hemodialysis\n- AKI with need for dialysis treatment estimated within 12 hours\n- Known hypersensitivity to Rasburicase, or to any of the excipients,\n- Pre-existing condition or situation at risk of lysis syndrome\n- Known G6PD deficiency or suggestive family history\n- Other metabolic disorders known to cause hemolytic anemia\n- Chronic treatment with a urate-lowering agent\n- Enrolled in another\n- Sepsis due to urinary obstruction"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Worsening of renal function defined by at least one of the following:  The onset of acute kidney injury (AKI) within 7 days of inclusion.  Non-improvement or progression of the stage of AKI according to KDIGO criteria on the 7th day after inclusion","definition_or_measurement_approach":"Worsening defined as either onset of AKI within 7 days of inclusion or non-improvement/progression of AKI stage according to KDIGO criteria assessed at day 7 after inclusion."}

Secondary endpoints

  • {"endpoint_text":"- Death rate at D28 and D90","definition_or_measurement_approach":"Mortality assessed at day 28 and day 90."}
  • {"endpoint_text":"- The maximum SOFA score during the first 7 days","definition_or_measurement_approach":"Maximum Sequential Organ Failure Assessment (SOFA) score recorded during the first 7 days."}
  • {"endpoint_text":"- The evolution of renal aggression markers (N-GAL, Pro-enkephalin, IL-18) in blood and urine at D0, D3, and D7","definition_or_measurement_approach":"Serial measurement of plasma and urinary markers (N-GAL, Pro-enkephalin, IL-18) at baseline (D0), D3 and D7."}
  • {"endpoint_text":"- The evolution of the leukocyte rate, pro- and anti-inflammatory cytokines (TNFα, IL-1, 6, 8, 10) at D1, D3, and D7","definition_or_measurement_approach":"Serial measurement of leukocyte count and cytokines (TNFα, IL-1, IL-6, IL-8, IL-10) at D1, D3 and D7."}

Recruitment

Planned Sample Size
240
Recruitment Window Months
39
Consent Approach
Informed consent form signed is required from the participant. Trial includes adults only (≥18). Subject information sheets and informed consent forms exist for patient and for 'proche' (relative/legal representative), indicating procedures for proxy/representative consent; continuation ('poursuite') versions and a non-opposition document for treatment/data are available. Languages not specified in the available data.

Geography

Total Number Of Sites
8
Total Number Of Participants
240

France

Earliest CTIS Part Ii Submission Date
08-08-2025
Latest Decision Or Authorization Date
24-11-2025
Processing Time Days
108
Number Of Sites
8
Number Of Participants
240

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Réanimation des grands brulés
Principal Investigator Name
François Depret
Principal Investigator Email
francois.depret@aphp.fr
Contact Person Name
François Depret
Contact Person Email
francois.depret@aphp.fr
Site Name
Ramsay Generale De Sante
Department Name
Anesthésie réanimation
Principal Investigator Name
Matthieu Jamme
Principal Investigator Email
mat.jamme@gmail.com
Contact Person Name
Matthieu Jamme
Contact Person Email
mat.jamme@gmail.com
Site Name
Centre Hospitalier Victor Dupouy
Department Name
Anesthésie réanimation
Principal Investigator Name
Gaetan Plantefeve
Principal Investigator Email
gaetan.plantefeve@ch-argenteuil.fr
Contact Person Name
Gaetan Plantefeve
Site Name
Assistance Publique Hopitaux De Paris
Department Name
ANESTHESIE REANIMATION CHIRURGICALE SMUR
Principal Investigator Name
Benjamin Chousterman
Principal Investigator Email
benjamin.chouterman@aphp.fr
Contact Person Name
Benjamin Chousterman
Contact Person Email
benjamin.chouterman@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Reanimation medico-chirurgicale
Principal Investigator Name
Adrien Picod
Principal Investigator Email
adrien.picod@aphp.fr
Contact Person Name
Adrien Picod
Contact Person Email
adrien.picod@aphp.fr
Site Name
Ramsay Generale De Sante
Department Name
Anesthésie Réanimation
Principal Investigator Name
Riad Chelha
Principal Investigator Email
r.chelha@free.fr
Contact Person Name
Riad Chelha
Contact Person Email
r.chelha@free.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
REANIMATION DE CHIRURGIE CARDIO-VASCULAIRE
Principal Investigator Name
Nicolas Mongardon
Principal Investigator Email
nicolas.mongardon@aphp.fr
Contact Person Name
Nicolas Mongardon
Contact Person Email
nicolas.mongardon@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Réanimation médicale
Principal Investigator Name
Bruno Megarbane
Principal Investigator Email
bruno.megarbane@aphp.fr
Contact Person Name
Bruno Megarbane
Contact Person Email
bruno.megarbane@aphp.fr

Sponsor

Primary sponsor

Full Name
Assistance Publique Hopitaux De Paris
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
France

Investigational products

Investigational Product Name
Fasturtec 1.5 mg/ml powder and solvent for concentrate for solution for infusion.
Active Substance
RASBURICASE
Modality
Peptide/protein/enzyme
Routes Of Administration
Intravenous
Route
Intravenous
Authorisation Status
Authorised (EU/1/00/170/002)
Starting Dose
7.5 mg
Dose Levels
7.5 mg
Frequency
Single intravenous infusion (30 minutes)
Maximum Dose
7.5 mg
Investigational Product Name
Placebo de fasturtec
Modality
Other
Routes Of Administration
Intravenous
Route
Intravenous
Starting Dose
50 ml sodium chloride (0.9%)
Frequency
Single intravenous infusion

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