Clinical trial • Phase II • Oncology

RALUDOTATUG DERUXTECAN for Advanced/metastatic solid tumors | Endometrial cancer | Cervical cancer | Ovarian cancer | Urothelial carcinoma | Clear cell renal cell carcinoma

Phase II trial of RALUDOTATUG DERUXTECAN for Advanced/metastatic solid tumors | Endometrial cancer | Cervical cancer | Ovarian cancer | Urothelial carcino…

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Advanced/metastatic solid tumors | Endometrial cancer | Cervical cancer | Ovarian cancer | Urothelial carcinoma | Clear cell renal cell carcinoma
Trial Stage
Phase II
Drug Modality
ADC|Monoclonal antibody

Key dates

Initial CTIS Submission Date
26-11-2024
First CTIS Authorization Date
24-03-2025

Trial design

open-label, none/not specified-controlled Phase II trial in Belgium, Denmark, Spain and others.

Open Label
Yes
Comparator
None/Not specified
Target Sample Size
127

Eligibility

Recruits 127 Vulnerable population selected. Participants are adults (≥18 years) and consent is obtained from participants; local regulatory requirements apply if legal age of consent is >18. Participant information and consent forms (including pregnancy-specific ICFs) are available in multiple languages (English, French, Dutch, Italian, Spanish). No specific assent procedures for minors are provided (minors are not eligible)..

Vulnerable Population
Vulnerable population selected. Participants are adults (≥18 years) and consent is obtained from participants; local regulatory requirements apply if legal age of consent is >18. Participant information and consent forms (including pregnancy-specific ICFs) are available in multiple languages (English, French, Dutch, Italian, Spanish). No specific assent procedures for minors are provided (minors are not eligible).

Inclusion criteria

  • {"criterion_text":"- Adults ≥18 years of age on the day of signing the ICF. Follow local regulatory requirements if the legal age of consent for trial participation is >18 years old.\n- Additional inclusion criterion for the ccRCC cohort a. Pathologically or cytologically documented unresectable or metastatic ccRCC that was previously treated with no more than 3 prior systemic regimens for locally advanced or metastatic RCC, including both a PD-(L)1 checkpoint inhibitor and a VEGF-TKI in sequence or in combination.\n- Participants must have at least 1 lesion, not previously irradiated, amenable to biopsy, and must consent to provide a pre-treatment biopsy from a primary and/or metastatic lesion.\n- Has at least 1 measurable lesion according to RECIST version 1.1 per investigator assessment.\n- Participants must have progressed radiologically on or after their most recent line of systemic therapy.\n- Eastern Cooperative Oncology Group (ECOG) performance status (PS) of 0 or 1.\n- Additional inclusion criteria for endometrial cancer cohort a. Pathologically or cytologically documented endometrial cancer (carcinoma of any histological subtype or carcinosarcoma), irrespective of MSI or mismatch repair status. b. Documented disease progression after having received ≥1 line of therapy (no more than 3), including PBC-containing systemic treatment and an anti-PD-1 therapy containing regimen (combined or sequential) in the advanced/metastatic setting.\n- Additional inclusion criteria for cervical cancer cohort a. Pathologically or cytologically documented recurrent or persistent squamous, adenosquamous, or adenocarcinoma of the uterine cervix. b. Disease progression after having received ≥1 prior line of therapy that includes systemic therapy in the advanced or metastatic setting.\n- Additional inclusion criterion for non-HGSOC cohort a. Pathologically or cytologically documented unresectable or metastatic CCOC, lowgrade endometrioid, low-grade serous, or mucinous OVC that was previously treated with at least 1 prior line of therapy.\n- Additional inclusion criteria for urothelial cancer cohort a. Pathologically or cytologically documented unresectable or metastatic urothelial carcinoma of the bladder, renal pelvis, ureter, or urethra. Histological variants are allowed if urothelial histology is predominant. b. Relapsed or progressed after treatment with ≥1 prior line of therapy (maximum of 3) that contains anti-PD-(L)1 therapy in the perioperative or metastatic setting."}

Exclusion criteria

  • {"criterion_text":"- Clinically active brain metastases, spinal cord compression, or leptomeningeal carcinomatosis.\n- Evidence of ongoing uncontrolled systemic bacterial, fungal, or viral infection.\n- Has active or uncontrolled HIV, HBV or HCV infection.\n- Any of the following within the past 6 months prior to enrollment: cerebrovascular accident, transient ischemic attack, or other arterial thromboembolic event.\n- Uncontrolled or significant cardiovascular disease as specified in the protocol.\n- Has a history of (noninfectious) ILD/pneumonitis that required corticosteroids, has current ILD/pneumonitis, or where suspected ILD/pneumonitis cannot be ruled out by imaging at screening.\n- Clinically severe pulmonary compromise\n- Chronic steroid treatment (>10 mg/day) with exceptions as noted in the protocol.\n- History of other active malignancy within 3 years prior to enrollment, with the exception of those with a negligible risk of metastasis or death (eg, 5-year OS rate >90%) and treated with expected curative outcome .\n- Unresolved toxicities from previous anticancer therapy, defined as toxicities (other than alopecia) not yet resolved to NCI-CTCAE Version 5.0, Grade ≤1 or baseline.\n- Prior exposure to other CDH6-targeted agents or an ADC that consists of an exatecan derivative that is a topoisomerase I inhibitor (eg, trastuzumab deruxtecan, datopotamab deruxtecan)."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- For all cohorts except ccRCC: ORR is defined as the proportion of participants with a BOR of confirmed CR or confirmed PR according to RECIST version 1.1 criteria.For ccRCC cohort only: DCR is defined as the proportion of participants who achieved a BOR of confirmed CR, confirmed PR, or stable disease (maintained for ≥5 weeks) according to RECIST version 1.1. Incidence of TEAEs, SAEs, AESIs","definition_or_measurement_approach":"ORR (all cohorts except ccRCC): proportion with best overall response (BOR) of confirmed complete response (CR) or confirmed partial response (PR) per RECIST v1.1 (investigator assessment). DCR (ccRCC cohort): proportion with BOR of confirmed CR, confirmed PR, or stable disease maintained for ≥5 weeks per RECIST v1.1. Safety endpoints measured as incidence of TEAEs, SAEs, AESIs."}

Recruitment

Digital Remote Recruitment
Yes
Planned Sample Size
127
Recruitment Window Months
29
Consent Approach
Informed consent is provided by participants (adults ≥18 years). The protocol states: 'Adults ≥18 years of age on the day of signing the ICF. Follow local regulatory requirements if the legal age of consent for trial participation is >18 years old.' Subject information and consent forms are available in multiple languages (English, French, Dutch, Italian, Spanish) and include specific pregnancy information forms and pregnancy ICFs; no assent procedures for minors are provided as minors are not eligible.

Methods

  • Doctor-to-Patient letter (K2) distributed by treating physicians; country-specific versions available (e.g. BE, DK, ES, IT, FR).
  • Physician Referral Letter (K2) to enable physician-to-physician referrals.
  • Recruitment and consent procedure documents (K1) provided to sites to standardise site-level recruitment and consent.
  • Site engagement platform (Teckro Limited) used for site engagement and communications.
  • Patient contact by email (L2_Patient Emails) — patient-facing electronic communications materials available (country-specific).

Geography

Total Number Of Sites
30
Total Number Of Participants
73

Belgium

Earliest CTIS Part Ii Submission Date
25-02-2025
Latest Decision Or Authorization Date
29-08-2025
Processing Time Days
185
Number Of Sites
3
Number Of Participants
7

Sites

Site Name
UZ Leuven
Department Name
Gynecological Oncology
Principal Investigator Name
Toon Van Gorp
Principal Investigator Email
toon.vangorp@uzleuven.be
Contact Person Name
Toon Van Gorp
Contact Person Email
toon.vangorp@uzleuven.be
Site Name
Ziekenhuis Aan De Stroom
Department Name
Medical Oncology
Principal Investigator Name
Thomas van Cann
Principal Investigator Email
thomas.vancann@zas.be
Contact Person Name
Thomas van Cann
Contact Person Email
thomas.vancann@zas.be
Site Name
Institut Jules Bordet
Department Name
Medical Oncology
Principal Investigator Name
Laura Polastro
Principal Investigator Email
laura.polastro@hubruxelles.be
Contact Person Name
Laura Polastro
Contact Person Email
laura.polastro@hubruxelles.be

Denmark

Earliest CTIS Part Ii Submission Date
28-02-2025
Latest Decision Or Authorization Date
29-08-2025
Processing Time Days
182
Number Of Sites
2
Number Of Participants
5

Sites

Site Name
Region Hovedstaden
Department Name
Oncology
Principal Investigator Name
Rikke Løvendahl Eefsen
Principal Investigator Email
rikke.helene.loevendahl.eefsen@regionh.dk
Contact Person Name
Rikke Løvendahl Eefsen
Site Name
Rigshospitalet
Department Name
Oncology
Principal Investigator Name
Kristoffer Staal Rohrberg
Principal Investigator Email
Kristoffer.Staal.Rohrberg@regionh.dk
Contact Person Name
Kristoffer Staal Rohrberg

Spain

Earliest CTIS Part Ii Submission Date
10-03-2025
Latest Decision Or Authorization Date
05-11-2025
Processing Time Days
240
Number Of Sites
8
Number Of Participants
19

Sites

Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Oncology
Principal Investigator Name
Georgia Anguera Palacios
Principal Investigator Email
ganguera@santpau.cat
Contact Person Name
Georgia Anguera Palacios
Contact Person Email
ganguera@santpau.cat
Site Name
Hospital Universitario 12 De Octubre
Department Name
Oncology
Principal Investigator Name
Daniel Castellano Gauna
Principal Investigator Email
cdanicas@gmail.com
Contact Person Name
Daniel Castellano Gauna
Contact Person Email
cdanicas@gmail.com
Site Name
MD Anderson Cancer Center
Department Name
Oncology
Principal Investigator Name
Enrique Grande Pulido
Principal Investigator Email
egrande@mdanderson.es
Contact Person Name
Enrique Grande Pulido
Contact Person Email
egrande@mdanderson.es
Site Name
Complexo Hospitalario Universitario A Coruna
Department Name
Oncology
Principal Investigator Name
Maria Quindos Varela
Principal Investigator Email
maria.quindos.varela@sergas.es
Contact Person Name
Maria Quindos Varela
Contact Person Email
maria.quindos.varela@sergas.es
Site Name
Clinica Universidad De Navarra
Department Name
Oncology
Principal Investigator Name
Antonio Gonzalez Martin
Principal Investigator Email
agonzalezma@unav.es
Contact Person Name
Antonio Gonzalez Martin
Contact Person Email
agonzalezma@unav.es
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Oncology
Principal Investigator Name
Begoña Pérez Valderrama
Principal Investigator Email
bpvalderrama@gmail.com
Contact Person Name
Begoña Pérez Valderrama
Contact Person Email
bpvalderrama@gmail.com
Site Name
Hospital Universitario Virgen De La Victoria
Department Name
Oncology
Principal Investigator Name
Maria Jose Bermejo Perez
Principal Investigator Email
cheberpe@gmail.com
Contact Person Name
Maria Jose Bermejo Perez
Contact Person Email
cheberpe@gmail.com
Site Name
Hospital Universitari Vall D Hebron
Department Name
Oncology
Principal Investigator Name
Elena Garralda Cabanas
Principal Investigator Email
egarralda@vhio.net
Contact Person Name
Elena Garralda Cabanas
Contact Person Email
egarralda@vhio.net

Italy

Earliest CTIS Part Ii Submission Date
31-10-2024
Latest Decision Or Authorization Date
08-01-2026
Processing Time Days
434
Number Of Sites
8
Number Of Participants
21

Sites

Site Name
Ospedale San Raffaele S.r.l.
Department Name
Medical Oncology
Principal Investigator Name
Andrea Necchi
Principal Investigator Email
necchi.andrea@hsr.it
Contact Person Name
Andrea Necchi
Contact Person Email
necchi.andrea@hsr.it
Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
Medical Oncology
Principal Investigator Name
Emilio Giunta
Principal Investigator Email
emilio.giunta@irst.emr.it
Contact Person Name
Emilio Giunta
Contact Person Email
emilio.giunta@irst.emr.it
Site Name
Azienda Ospedaliera Universitaria Federico II Di Napoli
Department Name
Medical Oncology
Principal Investigator Name
Luigi Formisano
Principal Investigator Email
luigi.formisano1@unina.it
Contact Person Name
Luigi Formisano
Contact Person Email
luigi.formisano1@unina.it
Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
Medical Oncology and Haematology
Principal Investigator Name
Giuseppe Procopio
Principal Investigator Email
Giuseppe.Procopio@istitutotumori.mi.it
Contact Person Name
Giuseppe Procopio
Site Name
IRCCS Ospedale Policlinico San Martino
Department Name
Medical Oncology
Principal Investigator Name
Giuseppe Fornarini
Principal Investigator Email
giuseppe.fornarini@hsanmartino.it
Contact Person Name
Giuseppe Fornarini
Site Name
Azienda Ospedaliera S Maria Di Terni
Department Name
Medical Oncology
Principal Investigator Name
Sergio Bracarda
Principal Investigator Email
s.bracarda@aospterni.it
Contact Person Name
Sergio Bracarda
Contact Person Email
s.bracarda@aospterni.it
Site Name
Azienda Ospedaliero Universitaria Pisana
Department Name
U.O. Oncology
Principal Investigator Name
Gianluca Masi
Principal Investigator Email
gianlucamasi72@gmail.com
Contact Person Name
Gianluca Masi
Contact Person Email
gianlucamasi72@gmail.com
Site Name
Azienda Ospedaliera Per L'Emergenza Cannizzaro
Department Name
Medical Oncology
Principal Investigator Name
Giuseppa Scandurra
Principal Investigator Email
giuseppascandurra@pec.ordinemedct.it
Contact Person Name
Giuseppa Scandurra

France

Earliest CTIS Part Ii Submission Date
23-01-2025
Latest Decision Or Authorization Date
07-01-2026
Processing Time Days
349
Number Of Sites
9
Number Of Participants
21

Sites

Site Name
Institut De Cancerologie De L Ouest
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Jean-Sebastien FRENEL
Principal Investigator Email
jean-sebastien.frenel@ico.unicancer.fr
Contact Person Name
Jean-Sebastien FRENEL
Site Name
Groupe Hospitalier Diaconesses Croix Saint Simon
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Antoine ANGELERGUES
Principal Investigator Email
aangelergues@hopital-dcss.org
Contact Person Name
Antoine ANGELERGUES
Contact Person Email
aangelergues@hopital-dcss.org
Site Name
Oncopole Claudius Regaud
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Carlos Alberto GOMEZ-ROCA
Principal Investigator Email
gomez-roca.carlos@iuct-oncopole.fr
Contact Person Name
Carlos Alberto GOMEZ-ROCA
Site Name
Centre Francois Baclesse
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Florence JOLY
Principal Investigator Email
f.joly@baclesse.unicancer.fr
Contact Person Name
Florence JOLY
Contact Person Email
f.joly@baclesse.unicancer.fr
Site Name
Centr Georges Francois Leclerc
Department Name
MEDECINE INTERNE
Principal Investigator Name
François GHIRINGHELLI
Principal Investigator Email
fghiringhelli@cgfl.fr
Contact Person Name
François GHIRINGHELLI
Contact Person Email
fghiringhelli@cgfl.fr
Site Name
Centre Oscar Lambret
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Cyril ABDEDDAIM
Principal Investigator Email
c-abdeddaim@o-lambret.fr
Contact Person Name
Cyril ABDEDDAIM
Contact Person Email
c-abdeddaim@o-lambret.fr
Site Name
Institut Gustave Roussy
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Laurence ALBIGES
Principal Investigator Email
laurence.albiges@gustaveroussy.fr
Contact Person Name
Laurence ALBIGES
Site Name
CARIO Centre Armoricain de Radiotherapie D'Imagerie medicale et D'Oncologie
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Anne-Claire HARDY-BESSARD
Principal Investigator Email
ac.hardy@cario-sante.fr
Contact Person Name
Anne-Claire HARDY-BESSARD
Contact Person Email
ac.hardy@cario-sante.fr
Site Name
Centre Leon Berard
Department Name
ONCOLOGIE OPTION MEDICALE
Principal Investigator Name
Aude FLECHON
Principal Investigator Email
aude.flechon@lyon.unicancer.fr
Contact Person Name
Aude FLECHON
Contact Person Email
aude.flechon@lyon.unicancer.fr

Sponsor

Primary sponsor

Full Name
Daiichi Sankyo Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
WCG Clinical Inc.
Responsibilities
sponsorDuties codes: ["8"]
Name
Pharmaceutical Product Development LLC
Responsibilities
sponsorDuties codes: ["4"]
Name
IQVIA Limited
Responsibilities
sponsorDuties codes: ["1","12","2","5"]
Name
Suvoda LLC
Responsibilities
sponsorDuties codes: ["3"]
Name
Bioclinica Inc.
Responsibilities
sponsorDuties code: 15; value: Independent central imaging reviewer; ILD Adjudication Committee
Name
Medidata Solutions Inc.
Responsibilities
sponsorDuties code: 7

Third parties

  • {"country":"United States","full_name":"WCG Clinical Inc.","duties_or_roles":"sponsorDuties codes: [\"8\"]","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Teckro Limited","duties_or_roles":"Site Engagement Platform (sponsorDuties code: 15)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Suvoda LLC","duties_or_roles":"sponsorDuties codes: [\"3\"]","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Pharmaceutical Product Development LLC","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Guardant Health Inc.","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Ventana Medical Systems Inc.","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"sponsorDuties code: 15; value: Independent central imaging reviewer; ILD Adjudication Committee","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"sponsorDuties codes: [\"1\",\"12\",\"2\",\"5\"]","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Fisher Bioservices Inc.","duties_or_roles":"sponsorDuties value: Long term storage (code: 15)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"sponsorDuties code: 7","organisation_type":"Non-Pharmaceutical company"}

Investigational products

Investigational Product Name
Raludotatug Deruxtecan
Active Substance
RALUDOTATUG DERUXTECAN
Modality
ADC|Monoclonal antibody
Routes Of Administration
Intravenous infusion
Route
Intravenous infusion
Authorisation Status
prodAuthStatus: 1

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