Clinical trial • Phase II • Neurology

PRASINEZUMAB for Parkinson's disease (early idiopathic)

Phase II trial of PRASINEZUMAB for Parkinson's disease (early idiopathic).

Overview

Trial Therapeutic Area
Neurology
Trial Disease
Parkinson's disease (early idiopathic)
Trial Stage
Phase II
Drug Modality
Monoclonal antibody

Key dates

Initial CTIS Submission Date
21-12-2023
First CTIS Authorization Date
19-03-2024

Trial design

Randomised, open-label, placebo intravenous infusion q4w (placebo arm) versus ro7046015 (prasinezumab) two active dose arms: high dose — 4500 mg for body weight ≥ 65 kg or 3500 mg for body weight < 65 kg, iv once every four weeks (q4w); low dose — 1500 mg iv q4w.-controlled Phase II trial across 26 sites in Austria, France, Germany and others.

Randomised
Yes
Open Label
Yes
Comparator
Placebo intravenous infusion Q4W (placebo arm) versus RO7046015 (prasinezumab) two active dose arms: high dose — 4500 mg for body weight ≥ 65 kg or 3500 mg for body weight < 65 kg, IV once every four weeks (Q4W); low dose — 1500 mg IV Q4W.
Single Multiple Or Escalation Dose Combined
Yes
Target Sample Size
214
Trial Duration For Participant
364

Stratification factors

  • Sex
  • Age group
  • Prior background therapy with MAO-B inhibitor (untreated vs treated)
  • Dopaminergic therapy since start of study (Yes vs No)

Eligibility

Recruits 214 Vulnerable population selected (isVulnerablePopulationSelected = true); no details on consent or assent handling are provided in the available record..

Vulnerable Population
Vulnerable population selected (isVulnerablePopulationSelected = true); no details on consent or assent handling are provided in the available record.

Inclusion criteria

  • {"criterion_text":"- A screening brain DaT-SPECT consistent with PD (central reading)\n- Clinical status does not require dopaminergic PD medication and is not expected to require dopaminergic treatment within 52 weeks from baseline\n- If presently being treated for PD, a stable dose of MAO-B inhibitor (rasagiline or selegiline) for at least 90 days prior to baseline and not expected to change within 52 weeks.\n- Idiopathic PD with bradykinesia plus one of the other cardinal signs of PD (resting tremor, rigidity) being present, without any other known or suspected cause of PD untreated or treated with MAO-B inhibitor\n- A diagnosis of PD for 2 years or less at screening\n- Hoehn and Yahr Stage I or II"}

Exclusion criteria

  • {"criterion_text":"- A diagnosis of a significant CNS disease other than Parkinson's disease; history of repeated head injury; history of epilepsy or seizure disorder other than febrile seizures as a child\n- Mini Mental State Examination (MMSE) </=25\n- History of or screening brain magnetic resonance imaging (MRI) scan indicative of clinically significant abnormality\n- Medical history indicating a Parkinson syndrome other than idiopathic PD, including but not limited to, progressive supranuclear gaze palsy, multiple system atrophy, drug-induced parkinsonism, essential tremor, primary dystonia\n- Known carriers of certain familial PD genes (as specified in study protocol)\n- History of PD related freezing episodes or falls"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- 1. Change in total MDS-UPDRS score (sum of Parts I, II and III) from baseline at Week 52.","definition_or_measurement_approach":"Change from baseline at Week 52, measured by the Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Total Score (sum of Parts I, II and III)."}

Secondary endpoints

  • {"endpoint_text":"- 1. Change from baseline in MDS-UPDRS Part IA, Part IB, Part I total, Part II total, Part III total and Part III subscores","definition_or_measurement_approach":"Change from baseline in specified MDS-UPDRS parts and subscores."}
  • {"endpoint_text":"- 2. Change from baseline in Dopamine transporter imaging with single photon emission computed tomography (DaT-SPECT) in ipsilateral (to the clinically dominant side) putamen","definition_or_measurement_approach":"Change from baseline in DaT-SPECT uptake in the ipsilateral putamen (to the clinically-dominant side)."}
  • {"endpoint_text":"- 3. Change from baseline in Montreal Cognitive Assessment (MoCA) total score","definition_or_measurement_approach":"Change from baseline in total MoCA score."}
  • {"endpoint_text":"- 4. Change from baseline in Clinical Global Impression (CGI-I)","definition_or_measurement_approach":"Change from baseline in CGI-Improvement score."}
  • {"endpoint_text":"- 5. Change from baseline in Patient Global Impression of change (PGIC)","definition_or_measurement_approach":"Change from baseline in PGIC."}
  • {"endpoint_text":"- 6. Change from baseline in Schwab and England Activities of Daily Living (SE-ADL)","definition_or_measurement_approach":"Change from baseline in SE-ADL score."}
  • {"endpoint_text":"- 7. Time to worsening in motor or non-motor symptoms as measured in MDS-UPDRS","definition_or_measurement_approach":"Time-to-event endpoint: time to worsening as determined by MDS-UPDRS measures."}
  • {"endpoint_text":"- 8. Time to start of dopaminergic PD treatment (levodopa or dopamine-agonists)","definition_or_measurement_approach":"Time-to-event: time from baseline to initiation of dopaminergic PD treatment (levodopa or dopamine agonists)."}
  • {"endpoint_text":"- 9. Incidence and severity of adverse events (AEs) and serious AEs (SAEs)","definition_or_measurement_approach":"Incidence and severity assessment of AEs and SAEs as reported during the study."}
  • {"endpoint_text":"- 10. Incidence of Anti-drug antibodies (ADAs)","definition_or_measurement_approach":"Incidence of detected anti-drug antibodies during treatment."}
  • {"endpoint_text":"- 11. Population and individual primary PK parameter estimations","definition_or_measurement_approach":"Population and individual pharmacokinetic parameter estimations (PK analysis)."}

Recruitment

Registry Or Advocacy Recruitment
True, Michael J. Fox Foundation (MJFF)
Digital Remote Recruitment
True; recruitment/participant materials include web resources (Site web PASADENA, Site web MJFF), smartphone ICF and video/tablet instruction materials as indicated by document titles.
Planned Sample Size
214
Recruitment Window Months
100
Consent Approach
Subject information sheets and informed consent forms (L1 SIS and ICF) are provided; translated/document versions present for French and Spanish in the document list. No explicit details on assent, age-specific documents, or exact consent provider processes are provided in the available record.

Geography

Total Number Of Sites
26
Total Number Of Participants
238

Austria

Earliest CTIS Part Ii Submission Date
07-12-2023
Latest Decision Or Authorization Date
22-12-2025
Processing Time Days
746
Number Of Sites
1
Number Of Participants
6

Sites

Site Name
Medizinische Universitaet Innsbruck
Department Name
Department of Neurology
Principal Investigator Name
Klaus Seppi
Principal Investigator Email
klaus.seppi@i-med.ac.at
Contact Person Name
Klaus Seppi
Contact Person Email
klaus.seppi@i-med.ac.at

France

Earliest CTIS Part Ii Submission Date
23-02-2024
Latest Decision Or Authorization Date
24-10-2025
Processing Time Days
609
Number Of Sites
10
Number Of Participants
92

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Centre d’Investigation Clinique Henri Mondor
Principal Investigator Name
Philippe REMY
Principal Investigator Email
neuro.philippe.remy@aphp.fr
Contact Person Name
Philippe REMY
Contact Person Email
neuro.philippe.remy@aphp.fr
Site Name
Centre Hospitalier Universitaire Grenoble Alpes
Department Name
CIC 406 – Centre d’Investigation Clinique (CIC)
Principal Investigator Name
Elena MORO
Principal Investigator Email
e.moro@chu-grenoble.fr
Contact Person Name
Elena MORO
Contact Person Email
e.moro@chu-grenoble.fr
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Centre d’Investigation Clinique
Principal Investigator Name
Isabelle BENATRU
Principal Investigator Email
isabelle.benatru@chu-poitiers.fr
Contact Person Name
Isabelle BENATRU
Site Name
CHU Gabriel-Montpied
Department Name
Service de Neurologie
Principal Investigator Name
Ana Raquel MARQUES
Principal Investigator Email
ar_marques@chu-clermontferrand.fr
Contact Person Name
Ana Raquel MARQUES
Site Name
Pellegrin Hospital
Department Name
Centre d’Investigation Clinique
Principal Investigator Name
Wassilios MEISSNER
Principal Investigator Email
wassilios.meissner@chu-bordeaux.fr
Contact Person Name
Wassilios MEISSNER
Site Name
Hôpital de la Timone
Department Name
Service de Neurologie et pathologie du mouvement
Principal Investigator Name
Jean-Philippe AZULAY
Principal Investigator Email
jean-philippe.azulay@ap-hm.fr
Contact Person Name
Jean-Philippe AZULAY
Contact Person Email
jean-philippe.azulay@ap-hm.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Centre d’Investigation Clinique – CIC 1436
Principal Investigator Name
Olivier RASCOL
Principal Investigator Email
olivier.rascol@univ-tlse3.fr
Contact Person Name
Olivier RASCOL
Contact Person Email
olivier.rascol@univ-tlse3.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
CIC Neurosciences, Bâtiment ICM
Principal Investigator Name
Jean-Christophe CORVOL
Principal Investigator Email
jean-christophe.corvol@psl.aphp.fr
Contact Person Name
Jean-Christophe CORVOL
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Service de Neurologie
Principal Investigator Name
Caroline BAYREUTHER-GIORDANA
Principal Investigator Email
bayreuther.c@chu-nice.fr
Contact Person Name
Caroline BAYREUTHER-GIORDANA
Contact Person Email
bayreuther.c@chu-nice.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
CIC, Service de Neurologie
Principal Investigator Name
Philippe DAMIER
Principal Investigator Email
philippe.damier@chu-nantes.fr
Contact Person Name
Philippe DAMIER
Contact Person Email
philippe.damier@chu-nantes.fr

Germany

Earliest CTIS Part Ii Submission Date
07-12-2023
Latest Decision Or Authorization Date
12-05-2026
Processing Time Days
887
Number Of Sites
6
Number Of Participants
65

Sites

Site Name
Universitaet Leipzig
Department Name
Klinik für Neurologie
Principal Investigator Name
Joseph Classen
Principal Investigator Email
Joseph.Classen@medizin.uni-leipzig.de
Contact Person Name
Joseph Classen
Site Name
Paracelsus-Kliniken Deutschland GmbH & Co. KGaA
Department Name
Zentrum f. Parkinson Syndrome und Bewegungsstörungen
Principal Investigator Name
Brit Mollenhauer
Principal Investigator Email
brit.mollenhauer@pkd.de
Contact Person Name
Brit Mollenhauer
Contact Person Email
brit.mollenhauer@pkd.de
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Zentrum für Neurologie, Abteilung für Neurodegenerative Erkrankungen
Principal Investigator Name
Kathrin Brockmann
Principal Investigator Email
kathrin.brockmann@uni-tuebingen.de
Contact Person Name
Kathrin Brockmann
Site Name
Universitaetsklinikum Ulm AöR
Department Name
Klinik für Neurologie
Principal Investigator Name
Georg Bernhard Landwehrmeyer
Principal Investigator Email
Bernhard.landwehmeyer@uni-ulm.de
Contact Person Name
Georg Bernhard Landwehrmeyer
Site Name
Universitaetsklinikum Duesseldorf AöR
Department Name
Klinik f. Neurologie, Zentrum f. Bewegungsstörungen und Neuromodulation
Principal Investigator Name
Alfons Schnitzler
Principal Investigator Email
Alfons.schnitzler@hhu.de
Contact Person Name
Alfons Schnitzler
Contact Person Email
Alfons.schnitzler@hhu.de
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
Campus Mitte, Klinik für Neurologie
Principal Investigator Name
Andrea Kühn
Principal Investigator Email
Andrea.kuehn@charite.de
Contact Person Name
Andrea Kühn
Contact Person Email
Andrea.kuehn@charite.de

Spain

Earliest CTIS Part Ii Submission Date
07-12-2023
Latest Decision Or Authorization Date
13-04-2026
Processing Time Days
858
Number Of Sites
9
Number Of Participants
75

Sites

Site Name
Hospital Universitario De La Princesa
Department Name
Neurology
Principal Investigator Name
Lydia López Manzanares
Principal Investigator Email
lydialopez@hotmail.com
Contact Person Name
Lydia López Manzanares
Contact Person Email
lydialopez@hotmail.com
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Movement Disorders Unit
Principal Investigator Name
Jaime Kulisevsky Bojarski
Principal Investigator Email
jkulisevsky@santpau.cat
Contact Person Name
Jaime Kulisevsky Bojarski
Contact Person Email
jkulisevsky@santpau.cat
Site Name
Hospital Universitario Virgen De La Macarena
Department Name
Neurology
Principal Investigator Name
Julio Dotor García-Soto
Principal Investigator Email
juliodotor@gmail.com
Contact Person Name
Julio Dotor García-Soto
Contact Person Email
juliodotor@gmail.com
Site Name
Clinica Universidad De Navarra
Department Name
Neurology
Principal Investigator Name
María Rosario Luquin Piudo
Principal Investigator Email
rluquin@unav.es
Contact Person Name
María Rosario Luquin Piudo
Contact Person Email
rluquin@unav.es
Site Name
Hospital Universitario Fundacion Alcorcon
Department Name
Neurology
Principal Investigator Name
Lydia Vela Desojo
Principal Investigator Email
lvela@fhalcorcon.es
Contact Person Name
Lydia Vela Desojo
Contact Person Email
lvela@fhalcorcon.es
Site Name
Hospital Universitari General De Catalunya
Department Name
Neurology
Principal Investigator Name
Ernest Balaguer Martínez
Principal Investigator Email
a.balaguer@udic.es
Contact Person Name
Ernest Balaguer Martínez
Contact Person Email
a.balaguer@udic.es
Site Name
Hospital Clinic De Barcelona
Department Name
Movement Disorder Unit
Principal Investigator Name
Francesc Valldeoriola Serra
Principal Investigator Email
fvallde@clinic.cat
Contact Person Name
Francesc Valldeoriola Serra
Contact Person Email
fvallde@clinic.cat
Site Name
Hospital Universitari Vall D Hebron
Department Name
Neurology
Principal Investigator Name
Jorge Hernández-Vara
Principal Investigator Email
jorherna@vhebron.net
Contact Person Name
Jorge Hernández-Vara
Contact Person Email
jorherna@vhebron.net
Site Name
Policlinica Gipuzkoa S.A.
Department Name
Neurology
Principal Investigator Name
Gurutz Linazasoro Cristobal
Principal Investigator Email
Glinazasoro@inbiomed.org
Contact Person Name
Gurutz Linazasoro Cristobal
Contact Person Email
Glinazasoro@inbiomed.org

Sponsor

Primary sponsor

Full Name
F. Hoffmann-La Roche AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
Syneos Health Netherlands B.V.
Responsibilities
Global CRO

Third parties

  • {"country":"Canada","full_name":"Neurorx Research Inc.","duties_or_roles":"MRI Imaging","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"4","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Netherlands","full_name":"Syneos Health Netherlands B.V.","duties_or_roles":"Global CRO","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"WCG Clinical Inc.","duties_or_roles":"Scales and training","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Endpoint Clinical Inc.","duties_or_roles":"Randomization","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Biotel Research LLC","duties_or_roles":"ECG Provider","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Charles River Laboratories Inc.","duties_or_roles":"Analytical Laboratory (PK, ADA)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Invicro LLC","duties_or_roles":"DaT-SPECT","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
RO7046015 (prasinezumab / PRX002)
Active Substance
PRASINEZUMAB
Modality
Monoclonal antibody
Routes Of Administration
Intravenous infusion
Route
Intravenous infusion
Starting Dose
1500 mg (low dose); 4500 mg for body weight ≥ 65 kg (high dose); 3500 mg for body weight < 65 kg (high dose)
Dose Levels
1500 mg; 3500 mg; 4500 mg
Frequency
Once every four weeks (Q4W)
Maximum Dose
4500 mg

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