Clinical trial • Phase I/II • Oncology

PEMBROLIZUMAB for Metastatic colorectal cancer | Malignant solid tumor

Phase I/II trial of PEMBROLIZUMAB for Metastatic colorectal cancer | Malignant solid tumor. Randomised, adaptive. 182 participants.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Metastatic colorectal cancer | Malignant solid tumor
Trial Stage
Phase I/II
Drug Modality
Bispecific antibody | Monoclonal antibody | Small molecule

Key dates

Initial CTIS Submission Date
03-10-2024
First CTIS Authorization Date
22-10-2024

Trial design

Randomised, adaptive Phase I/II trial across 21 sites in Spain, Belgium, France and others.

Randomised
Yes
Adaptive
Yes
Single Multiple Or Escalation Dose Combined
Yes
Target Sample Size
182

Eligibility

Recruits 182 Vulnerable population flag is set for the trial. All participants must provide a signed informed consent form prior to any study procedures (age ≥18). No assent process or enrolment of minors is described in the provided data..

Pregnancy Exclusion
Pregnant or breastfeeding patients; patients of childbearing potential must use highly effective contraception methods prior to study entry, for the duration of study participation, and for 6 months after the last dose of petosemtamab.
Vulnerable Population
Vulnerable population flag is set for the trial. All participants must provide a signed informed consent form prior to any study procedures (age ≥18). No assent process or enrolment of minors is described in the provided data.

Inclusion criteria

  • {"criterion_text":"- Signed informed consent form (ICF) before initiation of any study procedures"}
  • {"criterion_text":"- Age ≥18 years at signing of ICF"}
  • {"criterion_text":"- FIRST-LINE HNSCC: patients eligible to receive pembrolizumab as first-line monotherapy with tumors expressing PD-L1, CPS ≥1"}
  • {"criterion_text":"- SECOND-/THIRD-LINE HNSCC PATIENTS: patients who have progressed on or after, or are intolerant to, anti-PD-(L)1 therapy as monotherapy or in combination with other agents, and have progressed to a platinum-based chemotherapy"}
  • {"criterion_text":"- 1L/2L mCRC: Patients should have been previously diagnosed with histologically or cytologically confirmed unresectable or metastatic adenocarcinoma of the colon or rectum. Patients must be RAS/RAF wild type and naive to prior anti-EGFR therapy"}
  • {"criterion_text":"- Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1"}
  • {"criterion_text":"- Adequate cardiac and organ function"}

Exclusion criteria

  • {"criterion_text":"- Central nervous system metastases that are untreated or symptomatic, or require radiation, surgery, or continued steroid therapy to control symptoms within 14 days of study entry"}
  • {"criterion_text":"- History of hypersensitivity reaction or any toxicity attributed to human proteins or any of the excipients that warranted permanent cessation of these agents"}
  • {"criterion_text":"- Uncontrolled hypertension with appropriate treatment, or unstable angina"}
  • {"criterion_text":"- History of congestive heart failure or serious cardiac arrhythmia requiring treatment (except atrial fibrillation, paroxysmal supraventricular tachycardia)"}
  • {"criterion_text":"- History of prior malignancies with the exception of excised cervical intraepithelial neoplasia or nonmelanoma skin cancer, or curatively treated cancer deemed at low risk for recurrence with no evidence of disease for at least 3 years"}
  • {"criterion_text":"- Patients with a history of interstitial lung disease (ILD) (eg, pneumonitis or pulmonary fibrosis), or evidence of ILD on baseline chest computerized tomography (CT) scan"}
  • {"criterion_text":"- Pregnant or breastfeeding patients; patients of childbearing potential must use highly effective contraception methods prior to study entry, for the duration of study participation, and for 6 months after the last dose of petosemtamab."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Objective Response Rate (ORR)","definition_or_measurement_approach":"Not specified in the provided data"}
  • {"endpoint_text":"- Frequency and severity of adverse events, serious adverse events, treatment discontinuations and modifications","definition_or_measurement_approach":"Not specified in the provided data"}

Secondary endpoints

  • {"endpoint_text":"- Pharmacokinetic parameters (CEOI, Cmax, C0h, AUC, CL, Vss, tmax and t1/2,) and population pharmacokinetics","definition_or_measurement_approach":"Measurement of PK parameters: CEOI, Cmax, C0h, AUC, CL, Vss, tmax, t1/2 and population PK analyses as listed"}
  • {"endpoint_text":"- Progression-Free Survival (PFS) and Duration of Response (DOR)","definition_or_measurement_approach":"Not specified in the provided data"}
  • {"endpoint_text":"- Overall Survival (OS)","definition_or_measurement_approach":"Not specified in the provided data"}

Recruitment

Planned Sample Size
395
Recruitment Window Months
116
Consent Approach
Participants (age ≥18) must sign a written informed consent form (ICF) prior to any study procedures (inclusion criterion). Country-specific ICF/SIS documents are provided; available language-specific ICFs in the document list include Spanish, French, Dutch and Italian versions (country-specific versions noted). No assent process for minors is described (minors excluded).

Geography

Total Number Of Sites
21
Total Number Of Participants
395

Spain

Earliest CTIS Part Ii Submission Date
17-10-2024
Latest Decision Or Authorization Date
25-10-2024
Processing Time Days
8
Number Of Sites
5
Number Of Participants
111

Sites

Site Name
Hospital Universitari Vall D Hebron
Department Name
Oncology
Principal Investigator Name
Josep Tabernero
Principal Investigator Email
jtabernero@vhio.net
Contact Person Name
Josep Tabernero
Contact Person Email
jtabernero@vhio.net
Site Name
Hospital Universitario De Navarra
Department Name
Oncology
Principal Investigator Name
Virginia Arrazubi
Principal Investigator Email
virginia.arrazubi.arrula@navarra.es
Contact Person Name
Virginia Arrazubi
Site Name
Fundacion Instituto Valenciano De Oncologia
Department Name
Oncology
Principal Investigator Name
Hector Aguilar
Principal Investigator Email
haguilar@fivo.org
Contact Person Name
Hector Aguilar
Contact Person Email
haguilar@fivo.org
Site Name
Clinica Universidad De Navarra
Department Name
Oncology
Principal Investigator Name
José Maria Lopez-Picazo
Principal Investigator Email
jlpicazo@unav.es
Contact Person Name
José Maria Lopez-Picazo
Contact Person Email
jlpicazo@unav.es
Site Name
Hospital Universitario 12 De Octubre
Department Name
Oncology
Principal Investigator Name
Rocio Carbonero
Principal Investigator Email
rgcarbonero@gmail.com
Contact Person Name
Rocio Carbonero
Contact Person Email
rgcarbonero@gmail.com

Belgium

Earliest CTIS Part Ii Submission Date
17-10-2024
Latest Decision Or Authorization Date
24-10-2024
Processing Time Days
7
Number Of Sites
4
Number Of Participants
34

Sites

Site Name
Universitair Ziekenhuis Gent
Department Name
Oncology
Principal Investigator Name
Michael Saerens
Principal Investigator Email
michael.saerens@uzgent.be
Contact Person Name
Michael Saerens
Contact Person Email
michael.saerens@uzgent.be
Site Name
Centre Hospitalier Universitaire Dinant Godinne Sainte-Elisabeth-UCL-Namur
Department Name
Oncology
Principal Investigator Name
Stéphanie Henry
Principal Investigator Email
stephanie.henry@uclouvain.be
Contact Person Name
Stéphanie Henry
Contact Person Email
stephanie.henry@uclouvain.be
Site Name
Institut Jules Bordet
Department Name
Oncology
Principal Investigator Name
Christiane Jungels
Principal Investigator Email
christiane.jungels@hubruxelles.be
Contact Person Name
Christiane Jungels
Site Name
Cliniques Universitaires Saint-Luc
Department Name
Oncology
Principal Investigator Name
Marc Van den Eynde
Principal Investigator Email
marc.vandeneynde@saintluc.uclouvain.be
Contact Person Name
Marc Van den Eynde

France

Earliest CTIS Part Ii Submission Date
17-10-2024
Latest Decision Or Authorization Date
24-10-2024
Processing Time Days
7
Number Of Sites
8
Number Of Participants
206

Sites

Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Oncologie Médicale
Principal Investigator Name
Amaury Daste
Principal Investigator Email
amaury.daste@chu-bordeaux.fr
Contact Person Name
Amaury Daste
Contact Person Email
amaury.daste@chu-bordeaux.fr
Site Name
Centre Leon Berard
Department Name
Oncologie
Principal Investigator Name
Jérôme Fayette
Principal Investigator Email
jerome.fayette@lyon.unicancer.fr
Contact Person Name
Jérôme Fayette
Site Name
Institut Curie
Department Name
Oncologie
Principal Investigator Name
Edith Borcoman
Principal Investigator Email
edith.borcoman@curie.fr
Contact Person Name
Edith Borcoman
Contact Person Email
edith.borcoman@curie.fr
Site Name
Institut Gustave Roussy
Department Name
Drug development (DITEP)
Principal Investigator Name
Antoine Hollebecque
Principal Investigator Email
antoine.hollebecque@gustaveroussy.fr
Contact Person Name
Antoine Hollebecque
Site Name
Hoptial La Timone
Department Name
Oncologie médicale
Principal Investigator Name
Sébastien Salas
Principal Investigator Email
sebastien.salas@ap-hm.fr
Contact Person Name
Sébastien Salas
Contact Person Email
sebastien.salas@ap-hm.fr
Site Name
Centre Antoine Lacassagne
Department Name
Unité de phase précoce
Principal Investigator Name
Esma Saada-Bouzid
Principal Investigator Email
esma.saada-bouzid@nice.unicancer.fr
Contact Person Name
Esma Saada-Bouzid
Site Name
Institut Regional Du Cancer De Montpellier
Department Name
Oncologie médicale
Principal Investigator Name
Thibault Mazard
Principal Investigator Email
Thibault.Mazard@icm.unicancer.fr
Contact Person Name
Thibault Mazard
Site Name
Centre Henri Becquerel
Department Name
Oncologie médiacale
Principal Investigator Name
Florian Clatot
Principal Investigator Email
florian.clatot@chb.unicancer.fr
Contact Person Name
Florian Clatot

Italy

Earliest CTIS Part Ii Submission Date
22-09-2025
Latest Decision Or Authorization Date
21-10-2025
Processing Time Days
29
Number Of Sites
1
Number Of Participants
10

Sites

Site Name
ASST Grande Ospedale Metropolitano Niguarda
Department Name
Oncology
Principal Investigator Name
Andrea Sartore Bianchi
Principal Investigator Email
andrea.sartorebianchi@ospedaleniguarda.it
Contact Person Name
Andrea Sartore Bianchi

Netherlands

Earliest CTIS Part Ii Submission Date
17-10-2024
Latest Decision Or Authorization Date
22-10-2024
Processing Time Days
5
Number Of Sites
3
Number Of Participants
34

Sites

Site Name
Het Nederlands Kanker Instituut-Antoni van Leeuwenhoek Ziekenhuis Stichting
Department Name
Oncology
Principal Investigator Name
Marieke Vollebergh
Principal Investigator Email
m.vollebergh@nki.nl
Contact Person Name
Marieke Vollebergh
Contact Person Email
m.vollebergh@nki.nl
Site Name
Radboud universitair medisch centrum / RADBOUDUMC
Department Name
Oncology
Principal Investigator Name
Carla van Herpen
Principal Investigator Email
Carla.vanHerpen@radboudumc.nl
Contact Person Name
Carla van Herpen
Contact Person Email
Carla.vanHerpen@radboudumc.nl
Site Name
Universitair Medisch Centrum Utrecht
Department Name
Oncology
Principal Investigator Name
Lot Devriese
Principal Investigator Email
l.a.devriese@umcutrecht.nl
Contact Person Name
Lot Devriese
Contact Person Email
l.a.devriese@umcutrecht.nl

Sponsor

Primary sponsor

Full Name
Merus B.V.
Organisation Type
Pharmaceutical company
Country Of Registered Address
Netherlands

Contract research organisations

Name
Oncology Therapeutic Development
Responsibilities
sponsor duties codes: [1,11,12,2,5,9] (listed as third party duties; also referenced as CRO in serious breach documentation)
Name
Almac Clinical Services Limited
Responsibilities
sponsor duties codes: [3]
Name
Medpace UK Limited
Responsibilities
sponsor duties codes: [15 (SAE management and data entry), 8]
Name
Syneos Health Inc.
Responsibilities
sponsor duties codes: [7]
Name
P95
Responsibilities
sponsor duties codes: [10,6,7]

Third parties

  • {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"codes: [4]","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"France","full_name":"Oncology Therapeutic Development","duties_or_roles":"codes: [1,11,12,2,5,9]","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Guardant Health Inc.","duties_or_roles":"codes: [4]","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"France","full_name":"Median Technologies","duties_or_roles":"codes: [15] (Medical image analysis/ review - X-ray, MRI, ultrasound, etc.)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Syneos Health Inc.","duties_or_roles":"codes: [7]","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom (Northern Ireland)","full_name":"Almac Clinical Services Limited","duties_or_roles":"codes: [3]","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Medpace UK Limited","duties_or_roles":"codes: [15 (SAE management and data entry), 8]","organisation_type":"Pharmaceutical company"}
  • {"country":"Belgium","full_name":"P95","duties_or_roles":"codes: [10,6,7]","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
KEYTRUDA 25 mg/mL concentrate for solution for infusion
Active Substance
PEMBROLIZUMAB
Modality
Monoclonal antibody
Routes Of Administration
Intravenous administration
Route
Intravenous
Authorisation Status
Authorised
Investigational Product Name
PETOSEMTAMAB (MCLA-158)
Active Substance
PETOSEMTAMAB
Modality
Bispecific antibody
Routes Of Administration
Intravenous
Route
Intravenous
Authorisation Status
Investigational (no MA)
Investigational Product Name
OXALIPLATIN
Active Substance
OXALIPLATIN
Modality
Small molecule
Routes Of Administration
Intravenous administration
Route
Intravenous
Authorisation Status
Authorised
Investigational Product Name
FLUOROURACIL
Active Substance
FLUOROURACIL
Modality
Small molecule
Routes Of Administration
Intravenous bolus injection / IV infusion
Route
Intravenous
Authorisation Status
Authorised
Investigational Product Name
CALCIUM FOLINATE
Active Substance
CALCIUM FOLINATE
Modality
Small molecule
Routes Of Administration
Intravenous administration
Route
Intravenous
Authorisation Status
Authorised
Investigational Product Name
IRINOTECAN
Active Substance
IRINOTECAN
Modality
Small molecule
Routes Of Administration
Intravenous administration
Route
Intravenous
Authorisation Status
Authorised
Combination Treatment
Yes

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